NCT03189706

Brief Summary

The purpose of this study is to find out whether an experimental drug called Hu3F8 can be given with the chemotherapy drugs irinotecan and temozolomide and another drug called GM-CSF. The investigators want to find out if this combination is safe and what effect it has on the participant and the disease.

Trial Health

55
Monitor

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Trial has exceeded expected completion date
Enrollment
48

participants targeted

Target at P50-P75 for early_phase_1

Timeline
Completed

Started Jun 2017

Longer than P75 for early_phase_1

Geographic Reach
1 country

1 active site

Status
active not recruiting

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

June 12, 2017

Completed
1 day until next milestone

First Submitted

Initial submission to the registry

June 13, 2017

Completed
3 days until next milestone

First Posted

Study publicly available on registry

June 16, 2017

Completed
9 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

June 1, 2026

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

June 1, 2026

Completed
Last Updated

July 2, 2025

Status Verified

July 1, 2025

Enrollment Period

9 years

First QC Date

June 13, 2017

Last Update Submit

July 1, 2025

Conditions

Keywords

Hu3F8IrinotecanTemozolomideSargramostimChemoimmunotherapy17-251

Outcome Measures

Primary Outcomes (2)

  • Number of participants with treatment-related adverse events as assessed by CTCAE v4.0

    The regimen will be considered safe if there are no toxicities requiring discontinuation of therapy in at least 9/10 patients during the first two cycles.

    2 years

  • response rate (CR+PR)

    Response assessment will be based on the best response over the course of four cycles. Disease response for NB will use the International NB Response Criteria. Patients who withdraw from the study prior to cycle 4 with \< partial response will also not be considered evaluable for response and will be replaced.

    2 years

Study Arms (1)

Hu3F8, Irinotecan/Temozolomide and Sargramostim (HITS)

EXPERIMENTAL

Each cycle consists of four doses of hu3F8, five doses each of irinotecan and temozolomide and five doses of GM-CSF.

Drug: IrinotecanDrug: temozolomideBiological: Hu3F8Drug: GM-CSF

Interventions

50mg/m\^2/day IV will be administered from day 1-5

Hu3F8, Irinotecan/Temozolomide and Sargramostim (HITS)

(given concurrently with Irinotecan) 150mg/m\^2/day orally

Hu3F8, Irinotecan/Temozolomide and Sargramostim (HITS)
Hu3F8BIOLOGICAL

2.25mg/kg IV will be administered on days 2, 4, 8 and 10

Hu3F8, Irinotecan/Temozolomide and Sargramostim (HITS)
GM-CSFDRUG

250mcg/m2/day SC will be administered on days 6-10

Hu3F8, Irinotecan/Temozolomide and Sargramostim (HITS)

Eligibility Criteria

Sexall
Healthy VolunteersNo
Age GroupsChild (0-17), Adult (18-64), Older Adult (65+)

You may qualify if:

  • Diagnosis of NB as defined by international criteria,.e., histopathology (confirmed by the MSK Department of Pathology) or bone marrow metastases plus high urine catecholamine levels
  • High-risk NB as defined as any of the following:
  • Stage 4 with MYCN amplification (any age)
  • Stage 4 without MYCN amplification (\>1.5 years of age)
  • Stage 3 with MYCN amplification (unresectable; any age)
  • Stage 4S with MYCN amplification (any age)
  • Patients fulfill one of the following criteria:
  • Have evidence of soft tissue disease OR
  • If they only have osteomedullary disease at protocol enrollment, they should have:
  • Had previously received Hu3F8+GMCSF therapy AND have had less than a complete response to it OR
  • Had progressed progressive disease after their most recent anti-neuroblastoma therapeutic regimen
  • Patients must have evaluable (microscopic marrow metastasis, elevated tumor markers, positive MIBG or PET scans) or measurable (CT, MRI) disease documented after completion of prior systemic therapy.
  • Prior treatment with murine and hu3F8 is allowed.
  • Prior treatment with irinotecan or temozolomide is permitted.
  • Patients with prior m3F8, hu3F8, ch14.18 or hu14.18 treatment must have a negative HAHA antibody titer. Human anti-mouse antibody positivity is allowed.
  • +1 more criteria

You may not qualify if:

  • Patients with CR/VGPR disease
  • Existing severe major organ dysfunction, i.e., renal, cardiac, hepatic, neurologic, pulmonary, or gastrointestinal toxicity ≥ grade 3 except for hearing loss, alopecia, anorexia, nausea, and hypomagnesemia from TPN, which may be grade 3
  • ANC \< 500/uL
  • Platelet count \<30K/uL
  • History of allergy to mouse proteins
  • Active life-threatening infection
  • Inability to comply with protocol requirements
  • Women who are pregnant or breast-feeding

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (1)

Memorial Sloan Kettering Cancer Center

New York, New York, 10065, United States

Location

Related Links

MeSH Terms

Conditions

Neuroblastoma

Interventions

IrinotecanTemozolomidenaxitamabGranulocyte-Macrophage Colony-Stimulating Factor

Condition Hierarchy (Ancestors)

Neuroectodermal Tumors, Primitive, PeripheralNeuroectodermal Tumors, PrimitiveNeoplasms, NeuroepithelialNeuroectodermal TumorsNeoplasms, Germ Cell and EmbryonalNeoplasms by Histologic TypeNeoplasmsNeoplasms, Glandular and EpithelialNeoplasms, Nerve Tissue

Intervention Hierarchy (Ancestors)

CamptothecinAlkaloidsHeterocyclic CompoundsDacarbazineTriazenesOrganic ChemicalsImidazolesAzolesHeterocyclic Compounds, 1-RingColony-Stimulating FactorsGlycoproteinsGlycoconjugatesCarbohydratesHematopoietic Cell Growth FactorsCytokinesIntercellular Signaling Peptides and ProteinsPeptidesAmino Acids, Peptides, and ProteinsProteinsBiological Factors

Study Officials

  • Shakeel Modak, MD

    Memorial Sloan Kettering Cancer Center

    PRINCIPAL INVESTIGATOR

Study Design

Study Type
interventional
Phase
early phase 1
Allocation
NA
Masking
NONE
Purpose
TREATMENT
Intervention Model
SINGLE GROUP
Model Details: This is a pilot study of HITS in patients with resistant NB.
Sponsor Type
OTHER
Responsible Party
SPONSOR

Study Record Dates

First Submitted

June 13, 2017

First Posted

June 16, 2017

Study Start

June 12, 2017

Primary Completion

June 1, 2026

Study Completion

June 1, 2026

Last Updated

July 2, 2025

Record last verified: 2025-07

Data Sharing

IPD Sharing
Will share

Memorial Sloan Kettering Cancer Center supports the international committee of medical journal editors (ICMJE) and the ethical obligation of responsible sharing of data from clinical trials. The protocol summary, a statistical summary, and informed consent form will be made available on clinicaltrials.gov when required as a condition of Federal awards, other agreements supporting the research and/or as otherwise required. Requests for deidentified individual participant data can be made beginning 12 months after publication and for up to 36 months post publication. Deidentified individual participant data reported in the manuscript will be shared under the terms of a Data Use Agreement and may only be used for approved proposals. Requests may be made to: crdatashare@mskcc.org.

Shared Documents
SAP

Locations