NCT03121586

Brief Summary

To evaluate the long-term safety and tolerability of pimavanserin after 52 weeks of adjunctive treatment in subjects with schizophrenia

Trial Health

68
Monitor

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Strong global presence with extensive site network
Enrollment
995

participants targeted

Target at P75+ for phase_3 schizophrenia

Timeline
Completed

Started Jan 2017

Longer than P75 for phase_3 schizophrenia

Geographic Reach
14 countries

161 active sites

Status
terminated

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

January 1, 2017

Completed
3 months until next milestone

First Submitted

Initial submission to the registry

April 13, 2017

Completed
7 days until next milestone

First Posted

Study publicly available on registry

April 20, 2017

Completed
7 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

April 30, 2024

Completed
1 month until next milestone

Study Completion

Last participant's last visit for all outcomes

May 30, 2024

Completed
1.2 years until next milestone

Results Posted

Study results publicly available

August 24, 2025

Completed
Last Updated

August 24, 2025

Status Verified

July 1, 2025

Enrollment Period

7.3 years

First QC Date

April 13, 2017

Results QC Date

May 14, 2025

Last Update Submit

August 6, 2025

Conditions

Outcome Measures

Primary Outcomes (1)

  • Treatment Emergent Adverse Events

    Number of patients with treatment emergent adverse events

    Treatment period (52 weeks) and follow-up period (30 days): planned total of 56 weeks. Since the study was prematurely terminated, the reporting period was shortened; AEs were assessed to the end of treatment, at a mean duration of 319 days (or 46 weeks).

Study Arms (1)

Drug - Pimavanserin

EXPERIMENTAL

Pimavanserin 34 mg, 20 mg, or 10 mg, + background antipsychotic, taken once daily by mouth

Drug: Pimavanserin

Interventions

Pimavanserin 10 mg, tablet, taken as one 10 mg tablets, once daily by mouth, OR Pimavanserin 20 mg, tablet, taken as two 10 mg tablets, once daily by mouth, OR Pimavanserin 34 mg, tablet, taken as two 17 mg tablets, once daily by mouth

Drug - Pimavanserin

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Patient is able to understand and provide signed informed consent
  • Has a caregiver or some other identified responsible person (e.g., family member, social worker, caseworker, or nurse) considered reliable by the Investigator in providing support to the subject to help ensure compliance with study treatment, study visits, and protocol procedures and who is also able to provide input helpful for completing study rating scale
  • Is completing the Week 6 visit in Study ACP-103-034 or the Week 26 visit in Study ACP-103-038 or 064 while continuing to take his/her assigned dose of blinded study drug and may, in the Investigator's opinion, benefit from continued adjunctive treatment with pimavanserin to a antipsychotic
  • If the subject is female, she must not be pregnant or breastfeeding. She must also be of non-childbearing potential (defined as either surgically sterilized or at least 1 year postmenopausal) or must agree to use two clinically acceptable methods of contraception
  • The main background antipsychotic with which the subject is being treated must continue to be on one of the antipsychotics listed below:
  • Aripiprazole
  • Aripiprazole long-acting injectables:
  • Abilify Maintena®
  • Aristada®
  • Asenapine
  • Risperidone
  • Risperidone long-acting injection
  • Olanzapine
  • Paliperidone extended release (ER) (≤9 mg)
  • Paliperidone palmitate
  • +8 more criteria

You may not qualify if:

  • Patient is judged by the Investigator or the Medical Monitor to be inappropriate for the study (e.g., significantly noncompliant in Studies ACP-103-034, -038, or -064)
  • A urine drug screen (UDS) result at Baseline that indicates the presence of any tested prohibited substance of potential abuse
  • Subjects from Studies 034 and 038 with a result indicating the presence of marijuana are permitted, if allowed by medical regulations, if they agree to abstain from marijuana use during the study and the medical monitor approves the subject's participation
  • Subjects from Study 064 with a result indicating the presence of marijuana are not permitted in the study
  • Is taking a medication or drug or other substance that is prohibited according to this protocol
  • Known family or personal history or symptoms of long QT syndrome or risk factors for torsade de pointes and/or sudden death, including symptomatic bradycardia, hypokalemia or hypomagnesemia, and the presence of congenital prolongation of the QT interval
  • Patient has current evidence of a serious and/or unstable psychiatric, neurologic, cardiovascular, respiratory, gastrointestinal, renal, hepatic, hematologic, or other medical disorder, including cancer or malignancies, which would affect the patient's ability to participate in the study.
  • Patients will be evaluated at screening to ensure that all criteria for study participation are met. Patients may be excluded from the study based on these assessments (and specifically if it is determined that their baseline health and psychiatric condition do not meet all pre-specified entry criteria).

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (161)

171-Alea Research Institute

Phoenix, Arizona, 85012, United States

Location

156-Woodland International Research Group, LLC

Little Rock, Arkansas, 72211, United States

Location

111-Woodland Research Northwest, LLC

Rogers, Arkansas, 72758, United States

Location

167-CITrials - Bellflower

Bellflower, California, 90706, United States

Location

105-ProScience Research Group

Culver City, California, 90230, United States

Location

123-Synergy San Diego

Lemon Grove, California, 91945, United States

Location

164-Artemis Institute for Clinical Research

San Diego, California, 92103, United States

Location

165-CITrials

Santa Ana, California, 92705, United States

Location

108-Collaborative Nueroscience Network, LLC

Torrance, California, 90502, United States

Location

125-Galiz Research

Hialeah, Florida, 33016, United States

Location

137-Innovative Clinical Research, Inc.

Lauderhill, Florida, 33319, United States

Location

146-Premier Clinical Research Institute, Inc.

Miami, Florida, 33122, United States

Location

162-Synexus Clinical Research, Inc.

Atlanta, Georgia, 30328, United States

Location

168-Atlanta Center for Medical Research

Atlanta, Georgia, 30331, United States

Location

102-Northwest Behavioral Research Center

Marietta, Georgia, 30060, United States

Location

114-Northwestern University

Chicago, Illinois, 60611, United States

Location

101-American Medical Research

Chicago, Illinois, 60612, United States

Location

130-Alexian Brothers Center for Psychiatric Research

Hoffman Estates, Illinois, 60169, United States

Location

118-Lake Charles Clinical Trials

Lake Charles, Louisiana, 70629, United States

Location

124-Altea Research Institute

Las Vegas, Nevada, 89102, United States

Location

141-Hassman Research Institute

Berlin, New Jersey, 08009, United States

Location

153-Albuquerque Neuroscience Inc.

Albuquerque, New Mexico, 87109, United States

Location

104-Neurobehavioral Research, Inc.

Cedarhurst, New York, 11516, United States

Location

140-Synexus Clinical Research, Inc - 140

Jamaica, New York, 11432, United States

Location

128-Finger Lakes Clinical Research

Rochester, New York, 14618, United States

Location

106-New Hope Clinical Research

Charlotte, North Carolina, 28211, United States

Location

145-Carolina Behavioral Care

Durham, North Carolina, 27704, United States

Location

110-Cutting Edge Research Group

Oklahoma City, Oklahoma, 73116, United States

Location

170-Suburban Research Associates

Downingtown, Pennsylvania, 19335, United States

Location

127-University Hills Clinical Research

Irving, Texas, 75062, United States

Location

103-Pillar Clinical Research, LLC

Richardson, Texas, 75080, United States

Location

115-Psychiatric and Behavioral Solutions LLC

Salt Lake City, Utah, 84105, United States

Location

610-Clinica Privada Banfield S.A.

Buenos Aires, Argentina

Location

625-NOVAIN Neurociencias Group

Buenos Aires, Argentina

Location

603-Fundación para el Estudio y Tratamiento de las Enfermedades Mentales - FETEM

Ciudad Autonoma Buenos Aires, Argentina

Location

601-CENydET- Centro Neurobiologico y de Estres Traumatico-Biopsychomedical Research Group SRL

Ciudad Autonoma de Buenos Aire, Argentina

Location

602-FunDamoS

Ciudad Autonoma de Buenos Aire, Argentina

Location

622-Instituto Medico Damic Srl

Córdoba, Argentina

Location

624-Centro Especializado en Neurociencias CEN

Córdoba, Argentina

Location

626-Sanatorio Prof. Leon S. Morra S.A.

Córdoba, Argentina

Location

617-INSA Instituto de Neurociencias San Agustin S.A.

La Plata, Argentina

Location

623-Clinica Privada de Salud Mental Santa Teresa de Avila

La Plata, Argentina

Location

607-Resolution Psicopharmacology Research Institute

Mendoza, Argentina

Location

454-Mental Health Centre 'Prof. Dr. Ivan Temkov', EOOD

Burgas, 8000, Bulgaria

Location

533-State Psychiatric Hospital - Kardzhali, EOOD

Kardzhali, 6600, Bulgaria

Location

532-MHAT "Dr. Hristo Stambolski", EOOD

Kazanlak, Bulgaria

Location

569-State Psychiatric Hospital - Lovech

Lovech, 5500, Bulgaria

Location

406-State Psychiatric Hospital - Pazardzhik AD

Pazardzhik, 4400, Bulgaria

Location

535-UMHAT 'Dr. Georgi Stranski', EAD

Pleven, Bulgaria

Location

586-Medical Center Mentalcare OOD

Plovdiv, 4004, Bulgaria

Location

563-MC-Hipokrat-N E00D

Plovdiv, 4028, Bulgaria

Location

403-University Multiprofile hospital for activated treatment Sveti Georgi, Clinic of psychiatry

Plovdiv, Bulgaria

Location

592-Medical center Spectar - Plovdiv EOOD

Plovdiv, Bulgaria

Location

570-Medical Centre "Sveti Naum"

Sofia, 1113, Bulgaria

Location

497-MHC - Sofia, EOOD

Sofia, 1202, Bulgaria

Location

526-DCC "Sv. Vrach and Sv. Sv. Kuzma and Damyan", OOD

Sofia, 1408, Bulgaria

Location

402-Military Medical Academy, Multiprofile Hospital for Actie Treatment - Sofia

Sofia, 1431, Bulgaria

Location

405-UMHAT "Alexandrovska" EAD

Sofia, 1431, Bulgaria

Location

568-Medical Center Hera EOOD

Sofia, 1510, Bulgaria

Location

528-Medical Center Intermedica, OOD

Sofia, 1680, Bulgaria

Location

404-MHAT-Targovishte, AD

Targovishte, 7700, Bulgaria

Location

590-State Psychiatric Hospital - Tzarev Brod

Tsarev Brod, Bulgaria

Location

498-DCC "Mladost M" - Varna, OOD

Varna, 9020, Bulgaria

Location

455-Mental Health Center - Veliko Tarnovo EOOD

Veliko Tarnovo, 5000, Bulgaria

Location

401-Mental Health Center-Vratsa EOOD

Vratsa, 3000, Bulgaria

Location

Chatham-Kent Clinical Trials Research Ctr

Chatham, Ontario, N7L1C1, Canada

Location

351-McGill University Health Ctr Allan Memorial Int.

Montreal, Quebec, H3A 1A1, Canada

Location

356-Chatham-Kent Clinical Trials Research Ctr

Chatham, N7L 1C1, Canada

Location

536 - Clinic for psychiatry Vrapce

Zagreb, Croatia

Location

537 - Clinic for psychiatry Vrapce

Zagreb, Croatia

Location

550-Clinic for psychiatry Vrapce

Zagreb, Croatia

Location

557 - Clinic for psychiatry Vrapce

Zagreb, Croatia

Location

594-Klinika za psihijatriju Sveti Ivan, n/p Igor Filipčić or Marija Zelenika

Zagreb, Croatia

Location

512-NeuropsychiatrieHK s.r.o.

Hradec Králové, 50341, Czechia

Location

583-Narodni ustav dusevniho zdravi

Klecany, Czechia

Location

519-A-SHINE s.r.o.

Pilsen, 31200, Czechia

Location

513-CLINTRIAL s.r.o.

Prague, 10000, Czechia

Location

499-MUDr. Tibor Miklos

Prague, 10600, Czechia

Location

511-Psychiatrie Ricany s.r.o.

Říčany, 25101, Czechia

Location

410-Dr. Máthé és Társa Bt.

Kalocsa, Bács-Kiskun Megye, 6300, Hungary

Location

411-ÓBudai Egészségűgyi Centrum Kft

Budapest, Pest County, 1036, Hungary

Location

456-Semmelweis University Department of Psychiatry and Psychotherapy

Budapest, Pest County, 1083, Hungary

Location

520-Nyiro Gyula Korhaz - Orszagos Pszichiatriai es Addiktologiai Intezet

Budapest, 1135, Hungary

Location

440-PsychoTech Kft.

Pécs, 7633, Hungary

Location

566-Ospedale San Raffaele (San Raffaele Turro)

Milan, Italy

Location

553-AO Città della Salute e della Scienza di Torino

Torino, Italy

Location

483-Romuvos klinika, UAB

Kaunas, LT-44279, Lithuania

Location

518-Kaunas City Outpatient Clinic, Public Institution

Kaunas, LT-48259, Lithuania

Location

484-Medical Center Puriena JSC

Šilutė, Lithuania

Location

517-Zirmunai Mental Health Center, Public Institution

Vilnius, 09112, Lithuania

Location

525-Podlaskie Centrum Psychogeriatrii

Bialystok, 15-756, Poland

Location

502-Przychodnia Srodmiescie Sp. z o. o.

Bydgoszcz, 85-080, Poland

Location

579-Centrum Badan Klinicznych P.I. House Sp. z o.o.

Gdansk, 80-546, Poland

Location

501-Specjalistyczna Praktyka Lekarska Marek Domański

Lublin, 20-582, Poland

Location

578-MSCZ im. Prof. J. Mazurkiewicza

Pruszków, Poland

Location

505-GUZ Lipetsk Regional psychoneurological Hospital #1

Plekhanovo, Lipetsk Oblast, 399313, Russia

Location

417-State Budget Healthcare Institution of Stavropol Region (Regional Specialized Psychiatric Hospital #2)

Tonnel’nyy, Stavropol Kray, 357034, Russia

Location

418-State Budget Healthcare Institution of Arkhangelsk Region "Arkhangelsk Clinical Psychiatric Hospital"

Arkhangelsk, 163530, Russia

Location

459-Federal State Budgetary Research Institution "Mental Health Science Center"

Moscow, 115522, Russia

Location

573-SBIH of Moscow "Psychiatric Clinical Hospital # 4 n.a. P.B. Gannushkin" Short name: PCH N4 n.a. P.B.Gannushkin

Moscow, Russia

Location

581-SBIH of Moscow "Psych Clinical Hospital #1 N.A. Alekseev"

Moscow, Russia

Location

419-State municipal healthcare Institution "Leningrad region psychoneurological center"

Saint Petersburg, 188820, Russia

Location

415-Saint-Petersburg State Healthcare Institution "Saint Nicolas Wonderworker Psychiatric Hospital"

Saint Petersburg, 190121, Russia

Location

571-St. Petersburg SHI "Psychoneurological Dispensary #10"

Saint Petersburg, 190121, Russia

Location

451-V. M. Bekhterev National Research Medical Center For Psychiatry and Neurology

Saint Petersburg, 192019, Russia

Location

453-"Saint-Petersburg Scientific Research Psychoneurological Institute n.a. V.M. Bekhterev"

Saint Petersburg, 192019, Russia

Location

465-"Saint-Petersburg Scientific Research Psychoneurological Institute N.A. V.M. Bekhterev"

Saint Petersburg, 192019, Russia

Location

495-FSBI "National Medical Scientifi Center of Psychiatry and Neurology n.a. V.M. Bekhterev" MoH

Saint Petersburg, 192019, Russia

Location

464-Saint Petersburg State Budget Healthcare Institution "City Psychiatric Hospital No. 6 (Inpatient Department with Treatment Center)"

Saint Petersburg, 193167, Russia

Location

443-Saint-Petersburg State Budget Healthcare Institution "Psychoneurological Center #5"

Saint Petersburg, 195112, Russia

Location

444-SPHI "City Mental Hospital #3 n.a. I.I Skvortsov-Stepanov"

Saint Petersburg, 197341, Russia

Location

452-Saint Petersburg State Public Institution of Healthcare "City Psychiatric Hospital #3 n.a.I.I. Skvortsov-Stepanov

Saint Petersburg, 197341, Russia

Location

496-SPHI "City Mental Hospital #3 n.a. I.I Skvortsov-Stepanov

Saint Petersburg, 197341, Russia

Location

458-State Budget Healthcare Institution "Samara Psychiatric Hospital"

Saint Petersburg, 443016, Russia

Location

416-FSBEI HE "Smolensk State Medical University" of the MoH of the RF

Smolensk, 214019, Russia

Location

420-"Podderzhka" Research and Educational Center of Psychotherapy Limited Liability Company

Stavropol, 355000, Russia

Location

572-Klinika StoLet" Ltd.

Tomsk, Russia

Location

466-OOO "Lion-Med"

Voronezh, 394024, Russia

Location

422-State Budget Healthcare Institution of Yaroslavl Region "Yaroslavl Region Clinical Psychiatric Hospital"

Yaroslavl, 150003, Russia

Location

428-Clinical center of Serbia

Belgrade, 11 000, Serbia

Location

424-Institute of Mental health

Belgrade, 11000, Serbia

Location

425-Clinical Hospital Center "Dr. Dragisa Misovic-Dedinje", Clinic of Psychiatry

Belgrade, 11000, Serbia

Location

471-Clinic for Psychiatric Diseases "Dr Laza Lazarevic"

Belgrade, 11000, Serbia

Location

524-General Hospital Euromedik

Belgrade, 11000, Serbia

Location

587-Institute of Mental Health

Belgrade, 11000, Serbia

Location

584-Clinic for Psychiatry, Clinical Canter of Serbia

Belgrade, Serbia

Location

472-Special Hospital for Psychiatric Diseases "Kovin"

Kovin, 26220, Serbia

Location

493-Special Neuropsychiatric Hospital Kovin

Kovin, 26220, Serbia

Location

423-Clinical Center Kragujevac

Kragujevac, 34 000, Serbia

Location

429-Clinical Center Kragujevac, Clinic of Psychiatry

Kragujevac, 34 000, Serbia

Location

430-Psychiatric Clinic, Clinical Center Kragujevac

Kragujevac, Serbia

Location

427-Clinical Center Nis, Clinic of Mental Health

Niš, 18 000, Serbia

Location

585-Special Hospital for Psychiatric Diseases "Gornja Toponica"

Niš, Serbia

Location

593-Specialized Hospital for Neuropsychiatric Diseases "Sveti Vracevi"

Novi Kneževac, Serbia

Location

476-FIDMAG Germanes Hospitalaries

Barcelona, 08830, Spain

Location

574-Hospital Clinic de Barcelona

Barcelona, Spain

Location

588-Institucion Hospitalaria Hestia Palau - Ensayos clinicos

Barcelona, Spain

Location

475-Hospital Gregorio Marañon

Madrid, 28007, Spain

Location

575-Hospital Universitario 12 de Octubre

Madrid, Spain

Location

494-CSM La Corredoria

Oviedo, 33011, Spain

Location

431-Centro de Salud Parquesol, 2ª planta - Servicio de Psiquiatria

Valladolid, 47016, Spain

Location

529-Hospital Provincial de Zamora

Zamora, 49021, Spain

Location

438-Communal Establishment "Odesa Regional Psychiatric Hospital #2"

Odesa, Oblast, 67513, Ukraine

Location

462-Communal Establishment "I.I. Mechnykov Dnipropetrovsk Regional Clinical Hospital"

Dnipro, 49005, Ukraine

Location

510-CI of Kyiv RC Regional Psychiatric-Narcological Medical Association, Depart #10 (male), Dept #2 (female)

Hlevakha, 08631, Ukraine

Location

433-SI "Institute of Neurology, Psychiatry and Narcology of National Academy of Medical Sciences of Ukraine"

Kharkiv, 61068, Ukraine

Location

434-State Institution "Institute of Neurology, Psychiatry and Narcology of NAMS of Ukraine", Department of Urgent Psychiatry and Narcology

Kharkiv, 61068, Ukraine

Location

582-SI Institute of Neurology,Psychiatry&Narcology of NAMSU

Kharkiv, 61068, Ukraine

Location

567-CIH Kharkiv Regional Clinical Psychiatric Hospital #3 Psychiatric Department of Primary Psychotic Episod Short Site name: CIH KRCPH #3 PD of PPE

Kharkiv, Ukraine

Location

461-Kherson Regional Psychiatric Hospital

Kherson, 73488, Ukraine

Location

507-Main Military Clinical Hospital of MDU

Kyiv, 01133, Ukraine

Location

447-Ukrainian Scientific Research Institute of Social and Forensic Psychiatry and Narcology of Ministry of Healthcare of Ukraine

Kyiv, 04080, Ukraine

Location

Kyiv Regional Medical Incorporation Psychiatry Center of Novel Treatment and Rehabilitation of Psychotic Disorders, Department #29, Department #30

Kyiv, 04080, Ukraine

Location

460-Kyiv City Psychoneurological Hospital #3, General Psychiatry Department No. 2

Kyiv, 08631, Ukraine

Location

435-Kyiv Regional Medical Incorporation "Psychiatry". Center of Novel Treatment and Rehabilitation of Psychotic disorders, build 5, Department #30

Kyiv, Ukraine

Location

564-Regional Clinical Psychiatric Hospital

Nove, Ukraine

Location

509-CI Odesa Regional Medical Centre of Mental Health

Odesa, 65014, Ukraine

Location

508-CI Cherkasy Regional Psychiatric Hospital of ChRC Female Dept #11, Male Dept #12

Smila, 20708, Ukraine

Location

591-Municipal non-profit enterprise "Transcarpathian Regional Medical Center of Mental Health and Medicine of Addictions" of the Transcarpathian Regional Council, Department of psychiatry

Uzhhorod, Ukraine

Location

Communal Establishment "Acad. O.I. Iushchenko Vinnytsia Regional Psychoneurologic Hospital"

Vinnytsia, 21005, Ukraine

Location

432-Municipal Institution "Vinnytsya Regional Psychoneurological Hospital n.a. Acad. O.I. Yushchenko", Male Department No 14, Female Department No 15, Vinnytsya National Medical University n.a. M.I. Pyrogov, Dept of Psychiatry, Narcology and Psychothera

Vinnytsia, Ukraine

Location

MeSH Terms

Conditions

Schizophrenia

Interventions

pimavanserin

Condition Hierarchy (Ancestors)

Schizophrenia Spectrum and Other Psychotic DisordersMental Disorders

Limitations and Caveats

The study was terminated prematurely by the sponsor for business reasons.

Results Point of Contact

Title
Sr. Dir. Medical Information and Medical Communications
Organization
Acadia Pharmaceuticals Inc.

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 3
Allocation
NA
Masking
NONE
Purpose
TREATMENT
Intervention Model
SINGLE GROUP
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

April 13, 2017

First Posted

April 20, 2017

Study Start

January 1, 2017

Primary Completion

April 30, 2024

Study Completion

May 30, 2024

Last Updated

August 24, 2025

Results First Posted

August 24, 2025

Record last verified: 2025-07

Data Sharing

IPD Sharing
Will not share

Locations