NCT03038880

Brief Summary

This was a Phase II, multicenter, randomized, active comparator-controlled, 52-week study to investigate the efficacy, safety and pharmacokinetics of faricimab (RO6867461; RG7716) administered with extended dosing regimens in treatment-naive participants with neovascular age related macular degeneration (nAMD). Only one eye was chosen as the study eye.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
76

participants targeted

Target at P50-P75 for phase_2

Timeline
Completed

Started Jan 2017

Shorter than P25 for phase_2

Geographic Reach
1 country

25 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

January 27, 2017

Completed
4 days until next milestone

First Submitted

Initial submission to the registry

January 31, 2017

Completed
1 day until next milestone

First Posted

Study publicly available on registry

February 1, 2017

Completed
11 months until next milestone

Primary Completion

Last participant's last visit for primary outcome

January 11, 2018

Completed
3 months until next milestone

Study Completion

Last participant's last visit for all outcomes

March 29, 2018

Completed
2.8 years until next milestone

Results Posted

Study results publicly available

January 5, 2021

Completed
Last Updated

January 5, 2021

Status Verified

December 1, 2020

Enrollment Period

12 months

First QC Date

January 31, 2017

Results QC Date

December 9, 2020

Last Update Submit

December 9, 2020

Conditions

Outcome Measures

Primary Outcomes (1)

  • Mean Change From Baseline in Best Corrected Visual Acuity (BCVA) at Week 40, Using the Early Treatment Diabetic Retinopathy Study (ETDRS) BCVA Charts

    Best corrected visual acuity (BCVA) at a starting test distance of 4 meters was measured using a set of three Precision VisionTM or Lighthouse distance acuity charts (modified ETDRS Charts 1, 2, and R) prior to dilating eyes by a trained and certified visual acuity examiner. The BCVA examiner was masked to study eye and treatment assignment and only performed the refraction and BCVA assessment. The BCVA examiner was also masked to the BCVA letter scores of a participant's previous visits and could only know the refraction data from previous visits. The BCVA letter score ranges from 0 to 100 (best score attainable), and a gain in BCVA letter score from baseline indicates an improvement in visual acuity. The analysis was performed using a Mixed Model for Repeated Measurement (MMRM) model, which included an unstructured covariance and the categorical covariates of treatment group, visit, and visit by treatment group interaction and the continuous covariate of baseline BCVA.

    Baseline, Week 40

Secondary Outcomes (18)

  • Mean Change From Baseline in BCVA at Specified Timepoints, Using the ETDRS BCVA Charts

    Baseline, Day 7, Weeks 4, 8, 12, 16, 20, 24, 28, 32, 36, 40, 44, 48, and 52

  • Number and Percentage of Participants Gaining Greater Than or Equal to (≥)15, ≥10, ≥5, or ≥0 Letters From Baseline in BCVA at Specified Timepoints

    Baseline, Day 7, Weeks 4, 8, 12, 16, 20, 24, 28, 32, 36, 40, 44, 48, and 52

  • Percentage of Participants Gaining ≥15 Letters From Baseline in BCVA at Specified Timepoints

    Baseline, Day 7, Weeks 4, 8, 12, 16, 20, 24, 28, 32, 36, 40, 44, 48, and 52

  • Number and Percentage of Participants Not Losing ≥15, ≥10, ≥5, or ≥0 Letters From Baseline in BCVA at Specified Timepoints

    Baseline, Day 7, Weeks 4, 8, 12, 16, 20, 24, 28, 32, 36, 40, 44, 48, and 52

  • Percentage of Participants Not Losing ≥15 Letters From Baseline in BCVA at Specified Timepoints

    Baseline, Day 7, Weeks 4, 8, 12, 16, 20, 24, 28, 32, 36, 40, 44, 48, and 52

  • +13 more secondary outcomes

Study Arms (3)

6 mg Faricimab Q12W

EXPERIMENTAL

6 mg faricimab was given by intravitreal (IVT) injection once every 4 weeks (Q4W) up to Week 12 (4 injections), followed by 6 mg faricimab IVT injection once every 12 weeks (Q12W) from Week 24 up to Week 48 (injections at Weeks 24, 36, and 48; 3 injections).

Drug: FaricimabDrug: Sham Procedure

6 mg Faricimab Q16W

EXPERIMENTAL

6 mg faricimab was administered by IVT injection once every 4 weeks (Q4W) up to Week 12 (4 injections), followed by no doses up to Week 24 when a protocol-defined assessment of disease activity was performed. Participants with disease activity at Week 24 initiated 6 mg faricimab IVT Q12W dosing, and participants without disease activity at Week 24 initiated 6 mg faricimab IVT once every 16 weeks (Q16W) dosing for the remainder of the study.

Drug: FaricimabDrug: Sham Procedure

0.5 mg Ranibizumab Q4W

ACTIVE COMPARATOR

0.5 mg of ranibizumab was administered by IVT injection once every 4 weeks (Q4W) for 48 weeks (13 injections).

Drug: Ranibizumab

Interventions

Faricimab was administered via IVT injections as specified during the treatment period.

Also known as: RO6867461, RG7716
6 mg Faricimab Q12W6 mg Faricimab Q16W

Ranibizumab was administered via IVT injections as specified during the treatment period.

Also known as: Lucentis®
0.5 mg Ranibizumab Q4W

The sham was a procedure that mimicked an IVT injection and involved the blunt end of an empty syringe (without a needle) being pressed against the anesthetized eye. It was administered to participants in the faricimab treatments arms at applicable visits to maintain masking among treatment arms.

6 mg Faricimab Q12W6 mg Faricimab Q16W

Eligibility Criteria

Age50 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Treatment-naive CNV secondary to AMD (nAMD)
  • Subfoveal or juxtafoveal CNV with a subfoveal component related to the CNV activity by fundus fluorescein angiography (FFA) or spectral-domain optical coherence tomography (SD-OCT; as evidenced by subretinal fluid, subretinal hyperreflective material, evidence of leakage, or hemorrhage)
  • CNV lesion of all types with: total lesion size (including blood, atrophy, fibrosis, and neovascularization) of 6 disc areas or less by FFA; and CNV component area of at least 50% of total lesion size by FFA; and active CNV confirmed by FFA (evidence of leakage); and CNV exudation confirmed by SD-OCT (presence of fluid)
  • BCVA letter score of 73 to 24 letters (inclusive) on ETDRS-like charts (20/40-20/320 Snellen equivalent) on day 1
  • Clear ocular media and adequate pupillary dilatation to allow acquisition of good-quality retinal images to confirm diagnosis

You may not qualify if:

  • CNV due to causes other than AMD, such as ocular histoplasmosis, trauma, pathological myopia, angioid streaks, choroidal rupture, or uveitis
  • Central serous chorioretinopathy at screening
  • Retinal pigment epithelial tear involving the macula
  • On FFA: subretinal hemorrhage, fibrosis, or atrophy of more than (\>)50% of the total lesion area and/or that involves the fovea
  • Any prior or concomitant treatment for CNV including (but not restricted to) IVT treatment (steroids, anti-VEGF, tissue plasminogen activator, ocriplasmin, C3F8 gas, air), periocular pharmacological intervention, argon laser photocoagulation, verteporfin photodynamic therapy, diode laser, transpupillary thermotherapy, or surgical intervention
  • Cataract surgery within 3 months of baseline assessments
  • Any other intraocular surgery (pars plana vitrectomy, glaucoma surgery, corneal transplant, radiotherapy)
  • Prior IVT treatment (including anti-VEGF medication) except for management of cataract complication with steroid IVT treatment
  • Prior periocular pharmacological intervention for other retinal diseases
  • Any concurrent intraocular condition in the study eye (eg, amblyopia, aphakia, retinal detachment, cataract, diabetic retinopathy or maculopathy, or epiretinal membrane with traction) that, in the opinion of the investigator, could either reduce the potential for visual improvement or require medical or surgical intervention during the course of the study
  • Active intraocular inflammation (grade trace or above) in the study eye on day 1 (before randomization)
  • Current vitreous hemorrhage in the study eye
  • Uncontrolled glaucoma (eg, progressive loss of visual fields or defined as IOP ≥25 mm Hg despite treatment with antiglaucoma medication) in the study eye
  • Spherical equivalent of refractive error demonstrating more than 8 diopters of myopia in the study eye
  • History of idiopathic or autoimmune-associated uveitis in either eye
  • +8 more criteria

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (25)

Retinal Consultants of Arizona

Phoenix, Arizona, 85053, United States

Location

Retina Associates Southwest PC

Tucson, Arizona, 85704, United States

Location

California Retina Consultants

Bakersfield, California, 93309, United States

Location

Retinal Diagnostic Center

Campbell, California, 95008, United States

Location

Retina Consultants of Southern Colorado PC; Clinical Research Department

Colorado Springs, Colorado, 80909-1183, United States

Location

Rand Eye

Deerfield Beach, Florida, 33064, United States

Location

Florida Eye Associates

Melbourne, Florida, 32901, United States

Location

Retina Vitreous Assoc of FL

St. Petersburg, Florida, 33711, United States

Location

Southern Vitreoretinal Assoc

Tallahassee, Florida, 32308, United States

Location

Southeast Retina Center

Augusta, Georgia, 30909, United States

Location

Midwest Eye Institute

Indianapolis, Indiana, 46290, United States

Location

Wolfe Eye Clinic

West Des Moines, Iowa, 50266, United States

Location

The Retina Care Center

Baltimore, Maryland, 21209, United States

Location

Vitreo Retinal Surgery

Minneapolis, Minnesota, 55435, United States

Location

Sierra Eye Associates

Reno, Nevada, 89502, United States

Location

Eye Associates of New Mexico

Albuquerque, New Mexico, 87109, United States

Location

Vitreoretinal Consultants

Great Neck, New York, 11021, United States

Location

Oregon Retina, LLP

Eugene, Oregon, 97401, United States

Location

Retina Northwest

Portland, Oregon, 97221, United States

Location

Charles Retina Institute

Germantown, Tennessee, 38138, United States

Location

Retina Res Institute of Texas

Abilene, Texas, 79606, United States

Location

Texas Retina Associates

Arlington, Texas, 76012, United States

Location

Retina Research Center

Austin, Texas, 78750, United States

Location

Strategic Clinical Research Group, LLC

Willow Park, Texas, 76087, United States

Location

Retina Associates of Utah

Salt Lake City, Utah, 84107, United States

Location

Related Publications (1)

  • Khanani AM, Patel SS, Ferrone PJ, Osborne A, Sahni J, Grzeschik S, Basu K, Ehrlich JS, Haskova Z, Dugel PU. Efficacy of Every Four Monthly and Quarterly Dosing of Faricimab vs Ranibizumab in Neovascular Age-Related Macular Degeneration: The STAIRWAY Phase 2 Randomized Clinical Trial. JAMA Ophthalmol. 2020 Sep 1;138(9):964-972. doi: 10.1001/jamaophthalmol.2020.2699.

MeSH Terms

Conditions

Choroidal NeovascularizationMacular Degeneration

Interventions

faricimabRanibizumab

Condition Hierarchy (Ancestors)

Choroid DiseasesUveal DiseasesEye DiseasesNeovascularization, PathologicMetaplasiaPathologic ProcessesPathological Conditions, Signs and SymptomsRetinal DegenerationRetinal Diseases

Intervention Hierarchy (Ancestors)

Antibodies, Monoclonal, HumanizedAntibodies, MonoclonalAntibodiesImmunoglobulinsImmunoproteinsBlood ProteinsProteinsAmino Acids, Peptides, and ProteinsSerum GlobulinsGlobulins

Limitations and Caveats

Interpretability of the imaging endpoints is limited by the relatively small sample size of the study and imbalances between the arms at baseline. Formal comparisons could not be performed across the treatment arms.

Results Point of Contact

Title
Medical Communications
Organization
Hoffmann-La Roche

Study Officials

  • Clinical Trials

    Hoffmann-La Roche

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
DOUBLE
Who Masked
PARTICIPANT, OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

January 31, 2017

First Posted

February 1, 2017

Study Start

January 27, 2017

Primary Completion

January 11, 2018

Study Completion

March 29, 2018

Last Updated

January 5, 2021

Results First Posted

January 5, 2021

Record last verified: 2020-12

Locations