NCT02953301

Brief Summary

The purpose of this study is to determine whether resminostat will be able to delay or prevent worsening of disease in patients with advanced stage mycosis fungoides or Sézary Syndrome that have recently achieved disease control with previous systemic therapy.

Trial Health

98
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
201

participants targeted

Target at P75+ for phase_2

Timeline
Completed

Started Nov 2016

Longer than P75 for phase_2

Geographic Reach
12 countries

54 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

October 26, 2016

Completed
6 days until next milestone

Study Start

First participant enrolled

November 1, 2016

Completed
1 day until next milestone

First Posted

Study publicly available on registry

November 2, 2016

Completed
6.3 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

March 1, 2023

Completed
1.4 years until next milestone

Study Completion

Last participant's last visit for all outcomes

August 1, 2024

Completed
Last Updated

August 30, 2024

Status Verified

August 1, 2024

Enrollment Period

6.3 years

First QC Date

October 26, 2016

Last Update Submit

August 29, 2024

Conditions

Keywords

Cutaneous T-Cell Lymphoma (CTLC)Maintenanceresminostat4SCHDACMycosis FungoidesSézary Syndrome

Outcome Measures

Primary Outcomes (1)

  • PFS (Progression-free survival)

    The primary objective is to determine if maintenance treatment with resminostat increases progression free survival (PFS) compared to placebo in patients with advanced stage (Stage IIB-IVB) MF or SS that have achieved disease control (complete response \[CR\], partial response \[PR\] or stable disease \[SD\]) with previous systemic therapy.

    From date of randomization until the date of first documented progression or date of death from any cause, whichever came first, up to approximately 32 months

Secondary Outcomes (1)

  • TTSW (Time to symptom worsening): pruritus

    From date of randomisation to first date that criteria for symptom (pruritus) worsening have been met, up to approximately 32 months. Symptom worsening is defined as an increase of a minimum of 3 points on the visual analogue itching scale

Other Outcomes (10)

  • TTP (Time to progression)

    From date of randomization until the date of first documented progression, up to approximately 32 months

  • TTNT (Time to next treatment)

    From date of randomisation to first date that new treatment is received, up to approximately 44 months.

  • PFS2, PFS3 (Progression-free survival 2, 3)

    From date of start of subsequent treatment to date of progression or death due to any cause in the absence of documented PD whilst receiving second and third line therapy, respectively, up to approximately 44 months

  • +7 more other outcomes

Study Arms (2)

resminostat

EXPERIMENTAL

3 x 200 mg tablets p.o., 5 days treatment followed by 9 days rest (cycles until progress or unacceptable toxicity)

Drug: resminostat

Placebo

PLACEBO COMPARATOR

3 tablets p.o. matching verum, 5 days treatment followed by 9 days rest (cycles until progress or unacceptable toxicity)

Drug: Placebo

Interventions

Also known as: 4SC-201
resminostat
Placebo

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Patients with histologically confirmed MF (Stage IIB-IVB) or SS in an ongoing complete response (CR), partial response (PR) or stable disease (SD) after at least one prior systemic therapy according to local standards (including but not limited to α-interferon, bexarotene, total skin electron beam irradiation, chemotherapy) \[the most recent systemic therapy must have been completed as planned or stopped due to unacceptable toxicity 2-12 weeks prior to randomisation\]
  • Eastern Cooperative Oncology Group (ECOG) status score 0-2
  • Adequate haematological, hepatic and renal function

You may not qualify if:

  • Patients with progressive disease (PD)
  • Baseline corrected QT (QTc) interval \> 500 milliseconds
  • Concurrent use of any other specific anti-tumour therapy including psoralen photo chemotherapy (PUVA), chemotherapy, immunotherapy, hormonal therapy, radiation therapy, or experimental medications

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (54)

Medizinische Universität Graz

Graz, Austria

Location

Medizinische Universität Wien

Vienna, Austria

Location

Cliniques Universitaires Saint-Luc

Brussels, Belgium

Location

Universitaire Ziekenhuizen

Leuven, Belgium

Location

Centre Hospitalier Universitaire (CHU) de Bordeaux - Hôpital Saint-André

Bordeaux, France

Location

CHU Estaing

Clermont-Ferrand, France

Location

Centre Hospitalier Lyon-Sud

Lyon, France

Location

Chu Paris-Gh St-Louis Lariboisiere F.Widal Hopital

Paris, France

Location

Hopital Robert Debre - CHU de Reims

Reims, France

Location

Charité - Universitaetsmedizin Berlin

Berlin, Germany

Location

Universitaetsklinikum Bochum - St. Josef-Hospital

Bochum, Germany

Location

Elbekliniken Buxtehude

Buxtehude, Germany

Location

Uniklinik Köln

Cologne, Germany

Location

Klinikum Dortmund

Dortmund, Germany

Location

SRH Wald-Klinikum Gera

Gera, Germany

Location

Universitätsmedizin Göttingen

Göttingen, Germany

Location

Universitaetsklinikum Halle

Halle, Germany

Location

Universitaetsklinikum Hamburg-Eppendorf

Hamburg, Germany

Location

Universitaetsklinikum Schleswig-Holstein (UKSH), Campus Kiel

Kiel, Germany

Location

HELIOS Klinikum

Krefeld, Germany

Location

Klinikum der Stadt Ludwigshafen am Rhein

Ludwigshafen am Rhein, Germany

Location

Universitätsklinikum Schleswig-Holstein

Lübeck, Germany

Location

Universitätsklinikum Mannheim

Mannheim, Germany

Location

Johannes Wesling Klinikum Minden

Minden, Germany

Location

Universitäts-Hautklinik Tübingen

Tübingen, Germany

Location

Universitätsklinikum Ulm

Ulm, Germany

Location

ATTIKON Hospital and Cutaneous Lymphoma Clinic

Athens, Greece

Location

Universita Di Firenze

Florence, Italy

Location

Fondazione IRCCS Ca' Granda Ospedale Maggiore Policlinico

Milan, Italy

Location

Universita Cattolica del Sacro Cuore

Roma, Italy

Location

IFO San Gallicano

Rome, Italy

Location

Ospedale Molinette

Turin, Italy

Location

Niigata University Medical and Dental Hospital

Niigata, Japan

Location

Okayama University Hospital

Okayama, Japan

Location

Tohoku University Hospital

Sendai, Japan

Location

Hamamatsu University School of Medicine

Shizuoka, Japan

Location

University of Tsukuba Hospital

Tsukuba, Japan

Location

Leids Universitair Medisch Centrum (LUMC)

Leiden, Netherlands

Location

Medical University of Gdansk

Gdansk, Poland

Location

SP ZOZ Szpital Uniwersytecki w Krakowie

Krakow, Poland

Location

Uniwersytecki Szpital Kliniczny im. WAM - CSW

Lodz, Poland

Location

Centrum Onkologii-Instytut im. Marii Sklodowskiej-Curie

Warsaw, Poland

Location

Hospital Del Mar

Barcelona, Spain

Location

Hospital Duran i Reynals

Barcelona, Spain

Location

Hospital Universitario 12 de Octubre

Madrid, Spain

Location

Hospital Uni. Nuestra Senora de Candelaria

Santa Cruz de Tenerife, Spain

Location

Hospital General Universitario

Valencia, Spain

Location

Centre hospitalier universitaire vaudois (CHUV)

Lausanne, Switzerland

Location

Kantonsspital St. Gallen

Sankt Gallen, Switzerland

Location

Universitätsspital Zürich

Zurich, Switzerland

Location

University Hospital

Birmingham, United Kingdom

Location

Beatson West of Scotland Cancer Centre

Glasgow, United Kingdom

Location

St John's Institute Of Dermatology - Guy's & St Thomas' Nhs Foundation Trust

London, United Kingdom

Location

Christie Hospital

Manchester, United Kingdom

Location

Related Publications (1)

  • Valipour A, Jager M, Wu P, Schmitt J, Bunch C, Weberschock T. Interventions for mycosis fungoides. Cochrane Database Syst Rev. 2020 Jul 7;7(7):CD008946. doi: 10.1002/14651858.CD008946.pub3.

MeSH Terms

Conditions

Mycosis FungoidesSezary SyndromeLymphoma, T-Cell, Cutaneous

Interventions

resminostat

Condition Hierarchy (Ancestors)

Lymphoma, T-CellLymphoma, Non-HodgkinLymphomaNeoplasms by Histologic TypeNeoplasmsLymphoproliferative DisordersLymphatic DiseasesHemic and Lymphatic DiseasesImmunoproliferative DisordersImmune System Diseases

Study Officials

  • Rudolf Stadler, Prof.

    Johannes Wesling Klinikum, Minden, Germany

    PRINCIPAL INVESTIGATOR

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
TRIPLE
Who Masked
PARTICIPANT, INVESTIGATOR, OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

October 26, 2016

First Posted

November 2, 2016

Study Start

November 1, 2016

Primary Completion

March 1, 2023

Study Completion

August 1, 2024

Last Updated

August 30, 2024

Record last verified: 2024-08

Data Sharing

IPD Sharing
Will not share

Locations