NCT02948543

Brief Summary

Open label, randomised phase 3 trial of the addition of Mitomycin to BCG as adjuvant intravesical therapy for high-risk, non-muscle-invasive bladder cancer. The study aim is to compare disease-free survival between treatment arms: BCG alone versus Mitomycin in addition to BCG.

Trial Health

47
At Risk

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Trial has exceeded expected completion date
Enrollment
501

participants targeted

Target at P50-P75 for phase_3

Timeline
Completed

Started Jul 2013

Longer than P75 for phase_3

Geographic Reach
2 countries

17 active sites

Status
unknown

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

July 1, 2013

Completed
3.1 years until next milestone

First Submitted

Initial submission to the registry

August 1, 2016

Completed
3 months until next milestone

First Posted

Study publicly available on registry

October 28, 2016

Completed
8.1 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

December 1, 2024

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

December 1, 2024

Completed
Last Updated

June 18, 2023

Status Verified

June 1, 2023

Enrollment Period

11.4 years

First QC Date

August 1, 2016

Last Update Submit

June 14, 2023

Conditions

Outcome Measures

Primary Outcomes (1)

  • Disease free survival (death or recurrence)

    Measured from the date of randomisation until the date of disease recurrence, upper tract disease is first evident, or the date of death, or until the date last known to be alive and without disease recurrence. Assessed via cystoscopy.

    Up to 5 years

Secondary Outcomes (8)

  • Activity (Clear cystoscopy at 3 months)

    At 3 months after patient randomised

  • Time to recurrence (recurrence)

    Up to 5 years

  • Time to progression (disease progression)

    Up to 5 years

  • Safety (Adverse events graded according to CTC AE V4.0)

    Measured before day 1 of each instillation during treatment.

  • Health-Related Quality of Life

    Up to 5 years from the date of randomisation

  • +3 more secondary outcomes

Other Outcomes (1)

  • Exploratory Tissue Biomarker Investigation

    Baseline

Study Arms (2)

Treatment (Arm B):Intravesical BCG + MM

EXPERIMENTAL

Induction (weekly x 9); and followed by Maintenance (monthly x 9) beginning 3 months after randomisation. Dosage of Bacillus of Calmette-Guerin (BCG) dependent on preferred brand of BCG by participating institution. Either 2-8 x 10\^8 CFU for OncoTICE or, 81mg for ImmuCYST and TheraCys. Prior to treatment commencement, investigators should nominate which BCG brand will be used. The same brand of BCG must be used for all treatment administered to an individual participant throughout the study. Dosage of Mitomycin (MM) fixed at 40mg per instillation.

Biological: Bacillus of Calmette-Guerin (BCG)Drug: Mitomycin (MM)

Treatment (Arm A): Intravesical BCG

OTHER

Induction (weekly x 6); and followed by Maintenance (monthly x 10) beginning 3 months after randomisation. Dosage of Bacillus of Calmette-Guerin (BCG) dependent on preferred brand of BCG by participating institution. Either 2-8 x 10\^8 CFU for OncoTICE or, 81mg for ImmuCYST and TheraCys. Prior to treatment commencement, investigators should nominate which BCG brand will be used. The same brand of BCG must be used for all treatment administered to an individual participant throughout the study.

Biological: Bacillus of Calmette-Guerin (BCG)

Interventions

A strain of tubercle bacillus which modifies biologic response.

Also known as: OncoTICE, ImmuCYST, TheraCys
Treatment (Arm A): Intravesical BCGTreatment (Arm B):Intravesical BCG + MM

An antibiotic produced by a soil actinomycete which inhibits DNA synthesis.

Treatment (Arm B):Intravesical BCG + MM

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Males or females with confirmed high grade pTa or stage pT1 (any grade) non-muscle invasive bladder cancer on initial or re-resection histology (concurrent carcinoma in situ is allowed).
  • Age \>= 18 yrs
  • No macroscopically visible disease at cystoscopy within 8 weeks prior to randomisation. This may be either the initial Transurethral Resection of the Bladder Tumour (TURBT) at which the primary tumour was completely resected, or a planned second cystoscopy and/or re-resection done within 8 weeks of the initial TURBT.
  • ECOG Performance Status of 0-2
  • Adequate bone marrow, renal and liver function confirmed by pre-randomisation blood tests.
  • Study treatment both planned and able to start within 4 weeks of randomisation
  • Has completed the HRQL questionnaires or is unable to complete them because of literacy, insufficient English or limited vision
  • Willing and able to comply with all study requirements, including treatment, timing and/or nature of all required assessments
  • Signed, written informed consent

You may not qualify if:

  • Contraindications or hypersensitivity to investigational products, BCG and Mitomycin
  • Prior treatment with any other intravesical agent including BCG or Mitomycin (excludes single doses given post TURBT)
  • Current or past transitional cell carcinoma (TCC) of the upper urinary tract
  • Prior muscle-invasive (stage T2 or higher) transitional-cell carcinoma of the bladder
  • Bladder dysfunction precluding intravesical therapy eg. Severe urinary incontinence or overactive or spastic bladder
  • Life expectancy \< 3 months
  • Congenital or acquired immune deficiencies, whether due to a concurrent disease (e.g. acquired immune deficiency syndrome (AIDS), leukaemia, lymphoma) or immunosuppressive therapy (e.g. corticosteroids), or cancer therapy (cytotoxic drugs, radiation)
  • Prior radiotherapy of the pelvis
  • Prior or current treatment with radiotherapy-response or biological-response modifiers
  • Clinical evidence of existing active tuberculosis
  • History of another malignancy within 5 years prior to registration. Patients with non-melanomatous carcinoma of the skin are eligible for this study.
  • Serious medical or psychiatric conditions that might limit the ability of the patient to comply with the protocol.
  • Pregnancy, lactation, or inadequate contraception. Women must be post menopausal, infertile, or use a reliable means of contraception. Women of childbearing potential must have a negative pregnancy test done within 7 days prior to registration. Men must have been surgically sterilised or use a (double if required) barrier method of contraception.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (17)

Concord Repatriation General Hospital

Concord, New South Wales, 2139, Australia

Location

Nepean Hospital

Kingswood, New South Wales, 2747, Australia

Location

Southside Cancer Care Centre

Miranda, New South Wales, 2228, Australia

Location

John Hunter Hospital

New Lambton Heights, New South Wales, 2305, Australia

Location

GenesisCare

St Leonards, New South Wales, 2065, Australia

Location

The Tweed Hospital

Tweed Heads, New South Wales, 2485, Australia

Location

Sydney Adventist Hospital

Wahroonga, New South Wales, 2076, Australia

Location

Westmead Hospital

Westmead, New South Wales, 2145, Australia

Location

Redcliffe Hospital

Redcliffe, Queensland, 4020, Australia

Location

Footscray Hospital

Footscray, Victoria, 3011, Australia

Location

Frankston Hospital

Frankston, Victoria, 3199, Australia

Location

Austin Health - Austin Hospital

Heidelberg, Victoria, 3084, Australia

Location

The Alfred Hospital

Melbourne, Victoria, 3004, Australia

Location

Royal Melbourne Hospital - City Campus

Parkville, Victoria, 3050, Australia

Location

Epworth Healthcare

Richmond, Victoria, 3121, Australia

Location

Fiona Stanley Hospital

Murdoch, Western Australia, 6150, Australia

Location

Nottingham City Hospital - City Campus

Nottingham, NG7 2UH, United Kingdom

Location

MeSH Terms

Conditions

Urinary Bladder Neoplasms

Interventions

BCG VaccineBCG ConnaughtMitomycin

Condition Hierarchy (Ancestors)

Urologic NeoplasmsUrogenital NeoplasmsNeoplasms by SiteNeoplasmsFemale Urogenital DiseasesFemale Urogenital Diseases and Pregnancy ComplicationsUrogenital DiseasesUrinary Bladder DiseasesUrologic DiseasesMale Urogenital Diseases

Intervention Hierarchy (Ancestors)

Tuberculosis VaccinesBacterial VaccinesVaccinesBiological ProductsComplex MixturesMitomycinsIndolequinonesQuinonesOrganic ChemicalsAzirinesHeterocyclic Compounds, 1-RingHeterocyclic CompoundsIndolesHeterocyclic Compounds, 2-RingHeterocyclic Compounds, Fused-Ring

Study Officials

  • Dickon Hayne

    Fiona Stanley Hospital

    STUDY CHAIR

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
OTHER
Responsible Party
SPONSOR

Study Record Dates

First Submitted

August 1, 2016

First Posted

October 28, 2016

Study Start

July 1, 2013

Primary Completion

December 1, 2024

Study Completion

December 1, 2024

Last Updated

June 18, 2023

Record last verified: 2023-06

Locations