NCT02872714

Brief Summary

The purpose of this study is to evaluate the overall response rate (ORR) of pemigatinib as a monotherapy in the treatment of metastatic or surgically unresectable urothelial carcinoma harboring FGF/FGFR alterations.

Trial Health

98
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
263

participants targeted

Target at P75+ for phase_2

Timeline
Completed

Started Jan 2017

Longer than P75 for phase_2

Geographic Reach
11 countries

96 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

August 16, 2016

Completed
3 days until next milestone

First Posted

Study publicly available on registry

August 19, 2016

Completed
5 months until next milestone

Study Start

First participant enrolled

January 12, 2017

Completed
5.1 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

February 1, 2022

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

February 1, 2022

Completed
1.1 years until next milestone

Results Posted

Study results publicly available

March 24, 2023

Completed
Last Updated

August 14, 2025

Status Verified

August 1, 2025

Enrollment Period

5.1 years

First QC Date

August 16, 2016

Results QC Date

January 30, 2023

Last Update Submit

August 12, 2025

Conditions

Keywords

Urothelial carcinomafibroblast growth factor (FGF)fibroblast growth factor receptor (FGFR)FGF/FGFR alterations

Outcome Measures

Primary Outcomes (1)

  • Objective Response Rate (ORR) in Participants With FGFR3 Mutations or Fusions on a CD Regimen

    ORR was defined as the percentage of participants with a best overall response of complete response (CR) or partial response (PR) at any post-Baseline visit prior to first progressive disease (PD), per Response Evaluation Criteria in Solid Tumors (RECIST) version 1.1 (v1.1). CR: disappearance of all target and non-target lesions and no appearance of any new lesions. Any pathological lymph nodes (whether target or non-target) must have a reduction in the short axis to \<10 millimeters (mm). PR: complete disappearance or at least a 30% decrease in the sum of the diameters of target lesions, taking as a reference the baseline sum diameters, no new lesions, and no progression of non-target lesions. Response was based on review of scans by an independent centralized radiological review committee. Response was confirmed.

    up to 1138 days

Secondary Outcomes (7)

  • ORR in Participants With FGFR3 Mutations or Fusions on an ID Regimen

    up to 817 days

  • ORR in Participants With All Other FGF/FGFR Alterations

    up to 1198 days

  • ORR in All Participants on an ID or CD Regimen in Combined Cohorts

    up to 1198 days

  • Number of Participants With Any Treatment-emergent Adverse Event (TEAE)

    up to approximately 25 weeks

  • Progression-free Survival (PFS)

    up to 1138 days

  • +2 more secondary outcomes

Study Arms (3)

Cohort A-ID (Intermittent Dose) Pemigatinib

EXPERIMENTAL

Pemigatinib in subjects with FGFR3 mutations or fusions.

Drug: pemigatinib

Cohort A-CD (Continuous Dose) Pemigatinib

EXPERIMENTAL

Pemigatinib in subjects with FGFR3 mutations or fusions.

Drug: pemigatinib

Cohort B Pemigatinib

EXPERIMENTAL

Pemigatinib in subjects with other FGF/FGFR alterations.

Drug: pemigatinib

Interventions

Pemigatinib once a day by mouth for 2 consecutive weeks and 1 week off therapy.

Also known as: INCB054828
Cohort A-ID (Intermittent Dose) PemigatinibCohort B Pemigatinib

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • years and older in Japan
  • Histologically documented metastatic or surgically unresectable urothelial carcinoma; may include primary site from urethra, ureters, upper tract, renal pelvis, and bladder.
  • Eastern Cooperative Oncology Group (ECOG) performance status of 0-2.
  • Life expectancy ≥ 12 weeks.
  • Radiographically measurable per RECIST v1.1.
  • Documented FGF/FGFR alteration and have either 1a) failed at least 1 previous treatment for their metastatic or surgically unresectable urothelial carcinoma (ie, chemotherapy, immunotherapy) or 1b) have not received chemotherapy due to poor ECOG status or 2) have insufficient renal function.

You may not qualify if:

  • Prior receipt of a selective FGFR inhibitor.
  • Use of any potent CYP3A4 inhibitors or inducers within 14 days or 5 half-lives (whichever is shorter) before the first dose of study drug.
  • Inability or unwillingness to swallow pemigatinib or significant gastrointestinal disorder(s) that could interfere with the absorption, metabolism, or excretion of pemigatinib.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (96)

Arizona Oncology Associates (Wilmot)

Tucson, Arizona, 85711, United States

Location

Sharp Memorial Hospital

San Diego, California, 92123, United States

Location

UCSF Helen Diller Family Comprehensive Care Center

San Francisco, California, 94158, United States

Location

Rocky Mountain Cancer Centers

Boulder, Colorado, 80303, United States

Location

Calaway-Young Cancer Center at Valley View Hospital

Glenwood Springs, Colorado, 81601, United States

Location

Mount Sinai Medical Center

Miami Beach, Florida, 33140, United States

Location

Florida Hospital Cancer Institute

Orlando, Florida, 32804, United States

Location

Emory University School of Medicine

Atlanta, Georgia, 30322, United States

Location

University of Maryland, Greenebaum Cancer Center

Baltimore, Maryland, 21201, United States

Location

Lahey Clinic Inc. - PARENT ACCOUNT

Burlington, Massachusetts, 01805, United States

Location

Minnesota Oncology Hematology, P.A.

Woodbury, Minnesota, 55125, United States

Location

GU Research Network

Omaha, Nebraska, 68130, United States

Location

TRIO - Comprehensive Cancer Centers of Nevada

Las Vegas, Nevada, 89169-3321, United States

Location

New York Oncology Hematology, P.C.

Albany, New York, 12208, United States

Location

Northwell Cancer Institute

New Hyde Park, New York, 11042, United States

Location

University of Rochester

Rochester, New York, 14642, United States

Location

University of North Carolina at Chapel Hill

Chapel Hill, North Carolina, 27514, United States

Location

Oncology Hematology Care, Inc.

Cincinnati, Ohio, 45242, United States

Location

Oregon Health & Science University

Portland, Oregon, 97229, United States

Location

Compass Oncology the Northwest Cancer Specialists

Tualatin, Oregon, 97062, United States

Location

St. Luke's Hospital

Bethlehem, Pennsylvania, 18015, United States

Location

VA Pittsburgh Healthcare System

Pittsburgh, Pennsylvania, 15240, United States

Location

Carolina Urologic Research Center

Myrtle Beach, South Carolina, 29572, United States

Location

Vanderbilt University Medical Center

Nashville, Tennessee, 37232, United States

Location

Texas Oncology, P.A. - Austin

Austin, Texas, 78731, United States

Location

Texas Oncology - Baylor Charles A. Sammons

Dallas, Texas, 75246, United States

Location

Texas Oncology

Houston, Texas, 77024, United States

Location

Texas Oncology, P.A. - Sherman

Sherman, Texas, 75090, United States

Location

Baylor Scott & White Health

Temple, Texas, 76508, United States

Location

Huntsman Cancer Institute

Salt Lake City, Utah, 84112, United States

Location

Virginia Oncology Associates - Hampton

Norfolk, Virginia, 23502, United States

Location

Northwest Medical Specialties, PLLC

Tacoma, Washington, 98405, United States

Location

University of Wisconsic Hospital and Clinic

Madison, Wisconsin, 53792, United States

Location

Medical College of Wisconsin

Milwaukee, Wisconsin, 53226, United States

Location

UZ Antwerpen

Edegem, 2650, Belgium

Location

AZ Sint-Lucas - Campus Sint-Lucas

Ghent, 9000, Belgium

Location

AZ Groeninge Campus Loofstraat

Kortrijk, 8500, Belgium

Location

AZ Delta

Roeselare, 8800, Belgium

Location

Rigshospitalet

Copenhagen, 2100, Denmark

Location

CHU Besançon - Hôpital Jean Minjoz

Besançon, Doubs, 25030, France

Location

Groupe Hospitalier Saint André - Hôpital Saint André

Bordeaux, Gironde, 33075, France

Location

Institut Claudius Regaud-Oncopole

Toulouse, Haute Garonne, 31059, France

Location

ICO - Site René Gauducheau

Saint-Herblain, Loire Atlantique, 44805, France

Location

ICO - Site Paul Papin

Angers, Maine Et Loire, 49933, France

Location

Hopital Saint Louis

Paris, Paris, 75010, France

Location

Centre Leon Berard

Lyon, Rhone, 69373, France

Location

CHU Strasbourg - Nouvel HĂ´pital Civil

Strasbourg, Rhone, 67091, France

Location

Groupe Hospitalier Pitie-Salpetriere

Paris, 75571, France

Location

Institut Gustave Roussy

Villejuif, 94805, France

Location

Charite Universitaetsmedizin Berlin - Campus Benjamin Franklin

Berlin, 12200, Germany

Location

Universitaetsklinikum Koeln

Cologne, 50937, Germany

Location

Klinikum Dresden Standort Dresden-Friedrichstadt

Dresden, 01067, Germany

Location

Universitaetsklinikum Carl Gustav Carus TU Dresden

Dresden, 01307, Germany

Location

Universitaetsklinikum Hamburg-Eppendorf

Hamburg, 20246, Germany

Location

Universitaetsmedizin der Johannes Gutenberg-Universitaet Mainz

Mainz, 55131, Germany

Location

Universitaetsklinikum Muenster

MĂ¼nster, 48149, Germany

Location

Studienpraxis Urologie Drs. Feyerabend

NĂ¼rtingen, 72622, Germany

Location

Universitaetsklinikum Tuebingen

TĂ¼bingen, 72076, Germany

Location

Soroka University Medical Center

Beersheba, 8410101, Israel

Location

Assaf Harofeh Medical Center

Be’er Ya‘aqov, 70300, Israel

Location

Meir Medical Center

Kfar Saba, 4428126, Israel

Location

Chaim Sheba Medical Center

Ramat Gan, 52656, Israel

Location

Tel Aviv Sourasky Medical Center

Tel Aviv, 64239, Israel

Location

Azienda Ospedaliera Universitaria Policlinico Sant'Orsola Malpighi

Bologna, 40138, Italy

Location

Fondazione Del Piemonte Per L'Oncologia IRCC Candiolo

Candiolo, 20133, Italy

Location

Fondazione IRCCS Istituto Nazionale dei Tumori

Milan, 20133, Italy

Location

Azienda Ospedaliera Di Rilievo Nazionale A. Cardarellio

Napoli, 80131, Italy

Location

Ospedale degli Infermi

Rimini, 47923, Italy

Location

University Campus Bio-Medico di Roma

Rome, 00128, Italy

Location

IRCCS Ospedale Casa Sollievo della Sofferenza

San Giovanni Rotondo, 71013, Italy

Location

A.O.U. Senese Policlinico Santa Maria alle Scotte

Siena, 53100, Italy

Location

San Camillo-Forlanini Hospital

Siena, 53100, Italy

Location

Kyushu University Hospital

Fukuoka, 8128582, Japan

Location

Saitama Medical University International Medical Center

Hidaka-shi, 350-1298, Japan

Location

Hirosaki University Hospital

Hirosaki-shi, 036-8563, Japan

Location

Teikyo University Hospital

Itabashi-ku, 173-8606, Japan

Location

Nihon University Itabashi Hospital

Itabashi-ku, 173-8610, Japan

Location

Nara Medical University Hospital

Kashihara-shi, 634-8522, Japan

Location

Osaka International Cancer Institute

Osaka, 541-8567, Japan

Location

Saitama Cancer Center

Saitama, 362-0806, Japan

Location

Osaka University Hospital

Suita-shi, 565-0871, Japan

Location

Jichi Medical University Hospital

Tochigi, 329-0498, Japan

Location

VU Medisch Centrum

Amsterdam, 1081 HV, Netherlands

Location

Zorgsaam Ziekenhuis

Terneuzen, 4535 PA, Netherlands

Location

HagaZiekenhuis Van Den Haag

The Hague, Netherlands

Location

Viecuri Medisch Centrum

Venlo, 5912 BL, Netherlands

Location

Clinica Universidad de Navarra

Pamplona, Navarre, 31008, Spain

Location

Hospital Universitari Vall d'Hebron

Barcelona, 08035, Spain

Location

ICO Girona - Hospital Universitari de Girona Dr. Josep Trueta

Girona, 17007, Spain

Location

Centro Integral Oncologico Clara Campal

Madrid, 28050, Spain

Location

University College London Hospitals

London, Greater London, NW1 2PG, United Kingdom

Location

Guy's Hospital

London, Greater London, SE1 9RT, United Kingdom

Location

Charing Cross Hospital

London, Greater London, W6 8RF, United Kingdom

Location

Nottingham University Hospitals City Campus

Nottingham, Nottinghamshire, NG5 1PB, United Kingdom

Location

Beatson West of Scotland Cancer Centre

Glasgow, Strathclyde, G12 OYN, United Kingdom

Location

Queen Elizabeth Hospital

Birmingham, West Midlands, B15 2TH, United Kingdom

Location

Related Publications (2)

  • Zhang C, Huang MN, Shan JQ, Hu ZJ, Li ZW, Liu JY. Pemigatinib, a selective FGFR inhibitor overcomes ABCB1-mediated multidrug resistance in cancer cells. Biochem Biophys Res Commun. 2024 Jan 8;691:149314. doi: 10.1016/j.bbrc.2023.149314. Epub 2023 Nov 24.

  • Necchi A, Pouessel D, Leibowitz R, Gupta S, Flechon A, Garcia-Donas J, Bilen MA, Debruyne PR, Milowsky MI, Friedlander T, Maio M, Gilmartin A, Li X, Veronese ML, Loriot Y. Pemigatinib for metastatic or surgically unresectable urothelial carcinoma with FGF/FGFR genomic alterations: final results from FIGHT-201. Ann Oncol. 2024 Feb;35(2):200-210. doi: 10.1016/j.annonc.2023.10.794. Epub 2023 Nov 11.

MeSH Terms

Conditions

Carcinoma, Transitional CellAcrocephalosyndactylia

Interventions

pemigatinib

Condition Hierarchy (Ancestors)

CarcinomaNeoplasms, Glandular and EpithelialNeoplasms by Histologic TypeNeoplasmsCraniosynostosesSynostosisDysostosesBone Diseases, DevelopmentalBone DiseasesMusculoskeletal DiseasesSyndactylyCraniofacial AbnormalitiesMusculoskeletal AbnormalitiesLimb Deformities, CongenitalCongenital AbnormalitiesCongenital, Hereditary, and Neonatal Diseases and Abnormalities

Results Point of Contact

Title
Study Director
Organization
Incyte Corporation

Study Officials

  • Ekaterine Asatiani, MD

    Incyte Corporation

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR
Expanded Access
Yes

Study Record Dates

First Submitted

August 16, 2016

First Posted

August 19, 2016

Study Start

January 12, 2017

Primary Completion

February 1, 2022

Study Completion

February 1, 2022

Last Updated

August 14, 2025

Results First Posted

March 24, 2023

Record last verified: 2025-08

Data Sharing

IPD Sharing
Will share

Incyte shares data with qualified external researchers after a research proposal is submitted. These requests are reviewed and approved by a review panel on the basis of scientific merit. All data provided is anonymized to respect the privacy of patients who have participated in the trial in line with applicable laws and regulations. The trial data availability is according to the criteria and process described on https://www.incyte.com/our-company/compliance-and-transparency

Shared Documents
STUDY PROTOCOL, SAP
Time Frame
Data will be shared after the primary publication or 2 years after the study has ended for market authorized products and indications.
Access Criteria
Data from eligible studies will be shared with qualified researchers according to the criteria and process described in the Data Sharing section of the www.incyteclinicaltrials.com website. For approved requests, the researchers will be granted access to anonymized data under the terms of a data sharing agreement.
More information

Locations