NCT02807285

Brief Summary

The primary objective of this expanded access program is to provide ocrelizumab as treatment for eligible participants with primary progressive multiple sclerosis (PPMS) before it is commercially available in the United States (U.S.) for the indication of PPMS.

Trial Health

55
Monitor

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Geographic Reach
1 country

56 active sites

Status
unknown

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

June 16, 2016

Completed
5 days until next milestone

First Posted

Study publicly available on registry

June 21, 2016

Completed
Last Updated

September 7, 2017

Status Verified

September 1, 2017

First QC Date

June 16, 2016

Last Update Submit

September 4, 2017

Conditions

Interventions

Participants will receive 600 mg ocrelizumab as two 300 mg infusions separated by 14 days, every 24 weeks.

Also known as: RO4964913

Eligibility Criteria

Age18 Years - 55 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64)

You may qualify if:

  • Age 18 to 55 years (inclusive)
  • Diagnosis of PPMS in accordance with the revised 2010 McDonald criteria and the presence or documented history of cerebrospinal fluid oligoclonal bands by isoelectric focusing or elevated immunoglobulin G (IgG) index
  • Expanded Disability Status Score (EDSS) of 2.0 to 6.5 points at screening
  • For women of childbearing potential: agreement to remain abstinent (refrain from heterosexual intercourse) or use contraceptive methods that result in a failure rate of less than (\<)1 percent (%) per year during the treatment period and for at least 24 weeks after the last dose of study treatment or until their B-cells have repleted, whichever is longer

You may not qualify if:

  • History of relapsing-remitting multiple sclerosis (RRMS), progressive relapsing multiple sclerosis (PRMS) or secondary progressive multiple sclerosis (SPMS) at screening
  • History of severe allergic or anaphylactic reactions to humanized or murine monoclonal antibodies
  • History or known presence of recurrent or chronic infection
  • History of recurrent aspiration pneumonia requiring antibiotic therapy
  • History of cancer, including solid tumors and hematological malignancies (except basal cell, in situ squamous cell carcinomas of the skin, and in situ carcinoma of the cervix of the uterus that have been excised and resolved with documented clean margins on pathology)
  • History of or currently active primary or secondary immunodeficiency
  • History of coagulation disorders because ocrelizumab is administered via infusion
  • Known presence or history of other neurologic disorders
  • Significant, uncontrolled disease, such as cardiovascular (including cardiac arrhythmia), pulmonary (including chronic obstructive pulmonary disease), renal, hepatic, endocrine, gastrointestinal, or any other significant disease
  • Congestive heart failure
  • Known active bacterial, viral, fungal, mycobacterial infection, or other infection
  • Any concomitant disease that may require chronic treatment with systemic corticosteroids or immunosuppressants during the course of the expanded access program (EAP)
  • Contraindications for or intolerance to oral or IV corticosteroids, including IV methylprednisolone
  • Treatment with therapies approved for relapsing forms of Multiple Sclerosis (MS), including: Beta interferons, glatiramer acetate, fingolimod (Gilenya®), teriflunomide (Aubagio®), dimethyl fumarate (Tecfidera®), IV immunoglobulin, plasmapheresis, or other immunomodulatory therapies within 12 weeks prior to enrollment (Participants should not be excluded from the EAP due to previous treatment with rituximab)
  • Participants who have received fingolimod (Gilenya®) or dimethyl fumarate (Tecfidera®) if their lymphocyte count is not within normal values
  • +3 more criteria

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (56)

Phoenix Neurological Associates Ltd

Phoenix, Arizona, 85006, United States

Location

Territory Neurology and Research Institute

Tucson, Arizona, 85704, United States

Location

Mercy Medical Group; MS Centre Nurse

Carmichael, California, 95608, United States

Location

Scripps Clinic

La Jolla, California, 92037, United States

Location

MS Center of Southern California

Newport Beach, California, 92663, United States

Location

Stanford University

Palo Alto, California, 94304, United States

Location

Neuro-Therapeutics Inc.

Pasadena, California, 91105, United States

Location

UCSF- Multiple Sclerosis Centre; Department of Neurology

San Francisco, California, 94158, United States

Location

University Of Colorado

Aurora, Colorado, 80045, United States

Location

Advanced Neurology of Colorado, LLC

Fort Collins, Colorado, 80528, United States

Location

Associated Neurologists of Southern CT PC

Fairfield, Connecticut, 06824, United States

Location

Neurology Associates

Norwich, Connecticut, 06360, United States

Location

University of Miami Miller School of Medicine; Clinical Reseach Building

Miami, Florida, 33136, United States

Location

Neurological Services of Orlando

Orlando, Florida, 32806, United States

Location

Infinity Clinical Research, LLC

Sunrise, Florida, 33351, United States

Location

University of South Florida

Tampa, Florida, 33612, United States

Location

MS Center of Vero Beach

Vero Beach, Florida, 32960, United States

Location

Consultants in Neurology Ltd

Northbrook, Illinois, 60062, United States

Location

Fort Wayne Neurological Center

Fort Wayne, Indiana, 46805, United States

Location

Indiana University

Indianapolis, Indiana, 46202, United States

Location

University of Kansas Medical Center

Kansas City, Kansas, 66160, United States

Location

Norton Neurology Services

Louisville, Kentucky, 40207, United States

Location

Steward St. Elizabeth's Medical Center

Boston, Massachusetts, 02135, United States

Location

Wayne State Uni /Detroit Medical Center

Detroit, Michigan, 48201, United States

Location

Henry Ford Health System

Detroit, Michigan, 48202, United States

Location

Michigan Institute for Neurological Disorders

Farmington Hills, Michigan, 48334, United States

Location

The Minneapolis Clinic of Neurology

Golden Valley, Minnesota, 55422, United States

Location

Washington University

St Louis, Missouri, 63110, United States

Location

University of Nebraska Medical Center

Omaha, Nebraska, 68198-9450, United States

Location

Rutgers New Jersey Medical School

Newark, New Jersey, 07103, United States

Location

Holy Name Hospital

Teaneck, New Jersey, 07666, United States

Location

Icahn School of Medicine at Mount Sinai

New York, New York, 10029, United States

Location

South Shore Neurologic Associates P.C.

Patchogue, New York, 11772, United States

Location

Stony Brook University Medical Center

Stony Brook, New York, 11794, United States

Location

Carolinas Healthcare System

Charlotte, North Carolina, 28208, United States

Location

Raleigh Neurology Associates

Raleigh, North Carolina, 27607-6520, United States

Location

University of Cincinnati

Cincinnati, Ohio, 45203-0542, United States

Location

Cleveland Clinic

Cleveland, Ohio, 44195, United States

Location

The Ohio State University Wexner Medical Center; Department of Neurology

Columbus, Ohio, 43210, United States

Location

Neurology and Neuroscience Assoc., Inc.

Westerville, Ohio, 43081, United States

Location

Oklahoma Medical Research Foundation; MS Center of Excellence

Oklahoma City, Oklahoma, 73104, United States

Location

Providence Multiple Sclerosis Center

Portland, Oregon, 97225, United States

Location

University of Pennsylvania

Philadelphia, Pennsylvania, 19104, United States

Location

University of Pittsburgh

Pittsburgh, Pennsylvania, 15213, United States

Location

Abington Neurological Associates

Willow Grove, Pennsylvania, 19090, United States

Location

The Neurology Foundation, Inc.

Providence, Rhode Island, 02905, United States

Location

Sibyl Wray MD Neurology PC

Knoxville, Tennessee, 37934, United States

Location

Advanced Neurosciences Institute

Nashville, Tennessee, 37205, United States

Location

University Of Texas Health Science Center Houston

Houston, Texas, 77030, United States

Location

Central Texas Neurology Consultants

Round Rock, Texas, 78681, United States

Location

Neurology Center of San Antonio

San Antonio, Texas, 78212, United States

Location

University of Vermont

Burlington, Vermont, 05401, United States

Location

Neurological Associates Inc; Clinical Research

Richmond, Virginia, 23236, United States

Location

Swedish Neuroscience Institute; Multiple Sclerosis Center

Seattle, Washington, 98122, United States

Location

Multicare Neuroscience Center of Washington

Tacoma, Washington, 98405, United States

Location

Columbia St. Mary's Hospital System

Milwaukee, Wisconsin, 53211, United States

Location

MeSH Terms

Conditions

Multiple Sclerosis

Interventions

ocrelizumab

Condition Hierarchy (Ancestors)

Demyelinating Autoimmune Diseases, CNSAutoimmune Diseases of the Nervous SystemNervous System DiseasesDemyelinating DiseasesAutoimmune DiseasesImmune System Diseases

Study Officials

  • Clinical Trials

    Hoffmann-La Roche

    STUDY DIRECTOR

Study Design

Study Type
expanded access
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

June 16, 2016

First Posted

June 21, 2016

Last Updated

September 7, 2017

Record last verified: 2017-09

Locations