NCT02799745

Brief Summary

The primary purpose of this study was to compare the time to prostate cancer progression (pathological or therapeutic progression) between patients treated with enzalutamide versus patients undergoing active surveillance.

Trial Health

90
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
227

participants targeted

Target at P75+ for phase_2 prostate-cancer

Timeline
Completed

Started Jun 2016

Geographic Reach
2 countries

54 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

February 29, 2016

Completed
3 months until next milestone

Study Start

First participant enrolled

June 9, 2016

Completed
6 days until next milestone

First Posted

Study publicly available on registry

June 15, 2016

Completed
4.2 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

August 28, 2020

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

August 28, 2020

Completed
1.2 years until next milestone

Results Posted

Study results publicly available

November 10, 2021

Completed
Last Updated

December 6, 2024

Status Verified

November 1, 2024

Enrollment Period

4.2 years

First QC Date

February 29, 2016

Results QC Date

August 27, 2021

Last Update Submit

November 19, 2024

Conditions

Keywords

Therapeutic Cancer ProgressionPathological Cancer ProgressionEnzalutamideProstate CancerActive surveillance

Outcome Measures

Primary Outcomes (1)

  • Time to Prostate Cancer Progression

    Time to cancer prostate progression (pathological or therapeutic): time (in months) from date of randomization until the date of cancer progression (pathological or therapeutic). Pathological progression: increase in primary or secondary Gleason pattern by greater than or equal (\>=) 1 or higher proportion of cancer positive cores (\>=15 percent \[%\] increase). Therapeutic progression: earliest occurrence of primary therapy for prostate cancer (prostatectomy/radiation/focal therapy/systemic therapy). Medians and 95% CIs were calculated with the Kaplan-Meier (KM) method. Participants with no cancer progression at the time of study completion, discontinuation or death were censored at the last assessment date. Participants switching therapy during the study were censored at the time of the initial therapy switch, and participants discontinuing therapy were censored at the time of study discontinuation.

    From the date of randomization until the date of the cancer progression (pathological or therapeutic) (up to study completion date, 28 Aug 2020; approximately 50 months)

Secondary Outcomes (12)

  • Number of Participants With Adverse Events (AEs)

    From date of first dose of enzalutamide or randomization until end of study (up to study completion date, 28 Aug 2020; approximately 50 months)

  • Percentage of Participants Reported Negative Biopsies for Cancer

    At the end of months 12 and 24

  • Change From Baseline in Percent of Cancer Positive Cores at Month 12 and 24

    Baseline, months 12 and 24

  • Time to Prostate-specific Antigen (PSA) Progression

    From date of randomization or first dose of enzalutamide until date of PSA progression (pathological or therapeutic) (up to study completion date=28 Aug 2020, median duration: 14.82 months for "Enzalutamide", 8.80 months for "Active Surveillance")

  • Percentage of Participants With Secondary Rise in Serum PSA

    At the end of months 12, 24 and at the end of study (up to study completion date, 28 Aug 2020, approximately 50 months)

  • +7 more secondary outcomes

Study Arms (2)

Enzalutamide

ACTIVE COMPARATOR

Participants received 160-milligrams (mg) enzalutamide administered as four 40-mg capsules, orally once daily for 1 year of treatment period. Following the 1-year treatment period, all participants were followed for 1 additional year. Post the 1-year follow-up period, participants then started the continued follow-up period, in which, participants were followed up every 3 months for these 2 years, after which follow-up was either every 6 months up to 36 months or until the end of study (total duration of follow up in the study was approximately up to 35.9 months).

Drug: Enzalutamide

Active Surveillance (AS)

OTHER

Participants did not receive any study treatment in this arm but were on continued active surveillance (AS) for 1 year of treatment period. Following the 1-year treatment period, all participants were followed for 1 additional year. Post the 1-year follow up, participants then started the continued follow-up period, in which, participants were followed up every 3 months for these 2 years, after which follow-up was either every 6 months up to 36 months or until the end of study (total duration of follow up in the study was approximately up to 35.9 months).

Other: Active Surveillance

Interventions

Oral

Also known as: MDV3100, Xtandi
Enzalutamide
Active Surveillance (AS)

Eligibility Criteria

Age18 Years+
Sexmale
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Histologically proven adenocarcinoma of the prostate diagnosed (with ≥10 core biopsy) within 6 months of screening. The biopsy that was used for this diagnosis must be submitted for central pathology review.
  • Prostate cancer categorized (as determined by central pathology review) as low risk is defined as T1c-T2a, PSA\<10, N0, M0 (or presumed N0, M0 if CT/bone scan not done due to low risk of metastases), GS ≤ 6, ECOG status ≤2 and estimated life expectancy \>5 years OR intermediate risk is defined as T2b-T2c, PSA\<20, N0, M0 (or presumed N0, M0 if CT/bone scan not done), GS ≤7 (3+4 pattern only), ECOG status ≤ 2 and estimated life expectancy \> 5 years. Prostate cancer categorized (as determined by central pathology review) to the very low risk category (T1c, GS ≤6, PSA \<10 ng/mL, fewer than 3 prostate biopsy cores positive,
  • ≤50% cancer in any core, PSA density \<0.15 ng/mL/g) is not included.
  • Ability to swallow study drugs and to comply with study requirements throughout the study
  • Institutional Review Board (IRB)-/Independent Ethics Committee (IEC)-approved written Informed Consent and privacy language as per national regulations must be obtained from the subject or legally authorized representative prior to any study-related procedures
  • Throughout study, male subject and a female partner who is of childbearing potential must use two acceptable methods of birth control (one of which must include a condom barrier method of contraception) starting at screening and continuing throughout the study period and for three months after the final study drug administration. Two acceptable methods of birth control thus include the following:
  • Condom (barrier method of contraception) AND
  • One of the following is required:
  • i. Established use of oral, injected or implanted hormonal methods of contraception by the female partner; ii. Placement of an intrauterine device or intrauterine system by the female partner; iii. Additional barrier method: Occlusive cap (diaphragm or cervical/vault caps) with spermicidal foam / gel / film / cream / suppository by the female partner; iv. Tubal ligation in the female partner.
  • Must not donate sperm starting at screening throughout the study period and for 90 days after the final study drug administration.

You may not qualify if:

  • Prior radiotherapy, surgery, chemotherapy, or hormonal therapy for prostate cancer
  • Very low risk category (T1c, GS ≤6, PSA \<10 ng/mL, fewer than 3 prostate biopsy cores positive, ≤50% cancer in any core, PSA density \<0.15 ng/mL/g)
  • Prior transurethral resection of the prostate or prior transurethral microwave thermotherapy of the prostate
  • Use of oral glucocorticoids within 1 month of screening
  • Use of 5 alpha reductase inhibitor within 1 month of screening or total use, within the last two years prior to screening, of \>3 months
  • Presence of metastatic disease
  • History of seizure or any condition that may predispose to seizures at any time in the past. History of loss of consciousness or transient ischemic attack within 12 months of screening
  • Absolute neutrophil count \< 1,500/μL, platelet count \< 100,000/μL, or hemoglobin \< 6.2 mmol/L (10 g/dL) at screening
  • Total bilirubin \>1.5 times the upper limit of normal (ULN) or alanine aminotransferase (ALT) or aspartate aminotransferase (AST) ≥ 2.5 X ULN at screening
  • Creatinine \> 177 μmol/L (\> 2 mg/dL) at screening
  • Albumin \< 30 g/L (3.0 g/dL) at screening
  • Major surgery within 4 weeks prior to Randomization Visit
  • Clinically significant cardiovascular disease including:
  • Myocardial infarction or uncontrolled angina within 6 months
  • Congestive heart failure New York Heart Association (NYHA) class 3 or 4
  • +7 more criteria

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (54)

Site US10034

Birmingham, Alabama, 35223, United States

Location

Site US10024

Homewood, Alabama, 35209, United States

Location

Site US10007

Tucson, Arizona, 85704, United States

Location

Site US10055

Tucson, Arizona, 85741, United States

Location

Site US10004

Los Angeles, California, 90048, United States

Location

Site US10026

Sacramento, California, 95670, United States

Location

Site US10010

San Diego, California, 92123, United States

Location

Site US10051

Aurora, Colorado, 80045, United States

Location

Site US10029

Denver, Colorado, 80211, United States

Location

Site US10054

Denver, Colorado, 80220, United States

Location

Site US10072

Bradenton, Florida, 34205, United States

Location

Site US10057

Lakeland, Florida, 33805, United States

Location

Site US10038

Chicago, Illinois, 60611, United States

Location

Site US10062

Chicago, Illinois, 60612, United States

Location

Site US10074

Chicago, Illinois, 60612, United States

Location

Site US10018

Glenview, Illinois, 60026, United States

Location

Site US10071

Lake Barrington, Illinois, 60010, United States

Location

Site US10046

Carmel, Indiana, 46033, United States

Location

Site US10009

Jeffersonville, Indiana, 47130, United States

Location

Site US10037

New Orleans, Louisiana, 70112, United States

Location

Site US10006

Shreveport, Louisiana, 71106, United States

Location

Site US10001

Towson, Maryland, 21204, United States

Location

Site US10032

Boston, Massachusetts, 02111, United States

Location

Site US10008

Troy, Michigan, 48084, United States

Location

Site US10069

Lincoln, Nebraska, 68516, United States

Location

Site US10044

Omaha, Nebraska, 68114, United States

Location

Site US10067

Omaha, Nebraska, 68130, United States

Location

Site US10061

Lebanon, New Hampshire, 03756, United States

Location

Site US10049

Morristown, New Jersey, 07962, United States

Location

Site US10043

Voorhees Township, New Jersey, 08043, United States

Location

Site US10068

Brooklyn, New York, 11215, United States

Location

Site US10050

Cheektowaga, New York, 14225, United States

Location

Site US10030

Garden City, New York, 11530, United States

Location

Site US10028

Poughkeepsie, New York, 12601, United States

Location

Site US10021

Syracuse, New York, 13210, United States

Location

Site US10022

Syracuse, New York, 13210, United States

Location

Site US10047

Gastonia, North Carolina, 28053, United States

Location

Site US10045

Cleveland, Ohio, 44195, United States

Location

Site US10015

Middleburg Heights, Ohio, 44130, United States

Location

Site US10053

Oklahoma City, Oklahoma, 73104, United States

Location

Site US10063

Bala-Cynwyd, Pennsylvania, 19004, United States

Location

Site US10052

Lancaster, Pennsylvania, 17604, United States

Location

Site US10014

Warwick, Rhode Island, 02886, United States

Location

Site US10019

Myrtle Beach, South Carolina, 29572, United States

Location

Site US10011

Nashville, Tennessee, 37209, United States

Location

Site US10056

Dallas, Texas, 75231, United States

Location

Site US10036

Houston, Texas, 77027, United States

Location

Site US10035

San Antonio, Texas, 78229, United States

Location

Site US10058

Richmond, Virginia, 23235, United States

Location

Site US10017

Milwaukee, Wisconsin, 53226, United States

Location

Site CA15005

Abbotsford, British Columbia, V2S 3N6, Canada

Location

Site CA15004

Halifax, Nova Scotia, B3H 2Y9, Canada

Location

Site CA15001

Toronto, Ontario, M4N3M5, Canada

Location

Site CA15003

Toronto, Ontario, M5G2M9, Canada

Location

Related Publications (3)

  • Handa N, Shore ND, Cooperberg MR, Davicioni E, Zhao X, Elsouda D, Liu Y, Proudfoot JA, Kuperman G, Russell D, Iwata KK, Schaeffer EM, Ross A. Transcriptome profiling of prostatic tumours from ENACT trial patients with or without enzalutamide. BJU Int. 2025 Nov;136(5):920-929. doi: 10.1111/bju.16861. Epub 2025 Jul 31.

  • Ross AE, Iwata KK, Elsouda D, Hairston J, Russell D, Davicioni E, Proudfoot JA, Shore ND, Schaeffer EM. Transcriptome-Based Prognostic and Predictive Biomarker Analysis of ENACT: A Randomized Controlled Trial of Enzalutamide in Men Undergoing Active Surveillance. JCO Precis Oncol. 2024 Apr;8:e2300603. doi: 10.1200/PO.23.00603.

  • Shore ND, Renzulli J, Fleshner NE, Hollowell CMP, Vourganti S, Silberstein J, Siddiqui R, Hairston J, Elsouda D, Russell D, Cooperberg MR, Tomlins SA. Enzalutamide Monotherapy vs Active Surveillance in Patients With Low-risk or Intermediate-risk Localized Prostate Cancer: The ENACT Randomized Clinical Trial. JAMA Oncol. 2022 Aug 1;8(8):1128-1136. doi: 10.1001/jamaoncol.2022.1641.

Related Links

MeSH Terms

Conditions

Prostatic Neoplasms

Interventions

enzalutamideWatchful Waiting

Condition Hierarchy (Ancestors)

Genital Neoplasms, MaleUrogenital NeoplasmsNeoplasms by SiteNeoplasmsGenital Diseases, MaleGenital DiseasesUrogenital DiseasesProstatic DiseasesMale Urogenital Diseases

Intervention Hierarchy (Ancestors)

Outcome Assessment, Health CareOutcome and Process Assessment, Health CareQuality of Health CareHealth Services Administration

Results Point of Contact

Title
Clinical Trial Disclosure
Organization
Astellas Pharma Global Development, Inc.

Study Officials

  • Medical Director

    Astellas Pharma Global Development, Inc.

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

February 29, 2016

First Posted

June 15, 2016

Study Start

June 9, 2016

Primary Completion

August 28, 2020

Study Completion

August 28, 2020

Last Updated

December 6, 2024

Results First Posted

November 10, 2021

Record last verified: 2024-11

Data Sharing

IPD Sharing
Will share

Access to anonymized individual participant level data collected during the study, in addition to study-related supporting documentation, is planned for studies conducted with approved product indications and formulations, as well as products terminated during development. Studies conducted with product indications or formulations that remain active in development are assessed after study completion to determine if Individual Participant Data can be shared. Further details on Astellas' data sharing policy can be found at https://www.clinicaltrials.astellas.com/transparency/.

Shared Documents
STUDY PROTOCOL, SAP, CSR
Time Frame
Access to participant level data is offered to researchers after publication of the primary manuscript (if applicable) and is available as long as Astellas has legal authority to provide the data.
Access Criteria
Researchers must submit a proposal to conduct a scientifically relevant analysis of the study data. The research proposal is reviewed by an Independent Research Panel. If the proposal is approved, access to the study data is provided in a secure data sharing environment after receipt of a signed Data Sharing Agreement.
More information

Locations