NCT02753946

Brief Summary

The purpose of the study is to demonstrate the safety and efficacy of ZTI-01 (IV fosfomycin) as non-inferior to piperacillin/tazobactam in overall success (clinical cure and microbiologic eradication) for the treatment of hospitalized patients with complicated urinary tract infections (cUTI) or acute pyelonephritis (AP).

Trial Health

98
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
465

participants targeted

Target at P75+ for phase_2

Timeline
Completed

Started Apr 2016

Shorter than P25 for phase_2

Geographic Reach
16 countries

68 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

April 1, 2016

Completed
12 days until next milestone

First Submitted

Initial submission to the registry

April 13, 2016

Completed
15 days until next milestone

First Posted

Study publicly available on registry

April 28, 2016

Completed
9 months until next milestone

Primary Completion

Last participant's last visit for primary outcome

January 12, 2017

Completed
5 months until next milestone

Study Completion

Last participant's last visit for all outcomes

May 30, 2017

Completed
1.5 years until next milestone

Results Posted

Study results publicly available

December 11, 2018

Completed
Last Updated

March 7, 2019

Status Verified

March 1, 2019

Enrollment Period

10 months

First QC Date

April 13, 2016

Results QC Date

November 16, 2018

Last Update Submit

March 5, 2019

Conditions

Outcome Measures

Primary Outcomes (1)

  • Number of Patients With an Overall Success

    Clinical cure (resolution or significant improvement in signs and symptoms) and microbiologic eradication (baseline pathogen) in m-MITT population

    TOC Visit (Day 19)

Secondary Outcomes (2)

  • Number of Patients With a Response of Clinical Cure in Various Protocol Populations

    TOC Visit (Day 19)

  • Number of Patients With a Response of Microbiologic Eradication

    TOC Visit (Day 19)

Study Arms (2)

ZTI-01

EXPERIMENTAL

6 g ZTI-01 (IV fosfomycin) intravenously administered every 8 hours (18g total daily dose for 7-14 calendar days)

Drug: ZTI-01

piperacillin tazobactam

ACTIVE COMPARATOR

4.5 g piperacillin/tazobactam (4 g piperacillin/0.5 g tazobactam) intravenously administered every 8 hours (13.5g total daily dose for 7-14 calendar days)

Drug: Piperacillin-tazobactam

Interventions

ZTI-01DRUG

6g ZTI-01 intravenous infusion TID q8 hours

Also known as: disodium fosfomycin
ZTI-01

4.5g piperacillin-tazobactam intravenous infusion TID q8 hours

Also known as: piperacillin-tazobactam combination product
piperacillin tazobactam

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • A signed informed consent form (ICF);
  • Male or female, at least 18 years of age;
  • Diagnosis requires hospitalization and treatment with intravenous (IV) antibiotics;
  • Documented or suspected cUTI or AP including at least 2 protocol defined signs and symptoms and a urine specimen with evidence of pyuria plus at least one protocol defined associated risk
  • Pretreatment baseline urine culture specimen
  • Expectation that any implanted urinary instrumentation will be removed or replaced not longer than 24 hours, after randomization;
  • Expectation that patient will survive anticipated duration of the study;
  • Patient requires initial hospitalization to manage the cUTI or AP;
  • Women of childbearing potential have had a negative pregnancy test before randomization and be willing to consistently use a highly effective method of contraception
  • Male study participants will be required to use condoms with a spermicide throughout study

You may not qualify if:

  • Presence of any of the following conditions: perinephric abscess, renal corticomedullary abscess, uncomplicated urinary tract infection, recent history of trauma to the pelvis or urinary tract, polycystic kidney disease, chronic vesicoureteral reflux, previous or planned renal transplantation; patients receiving dialysis/hemodialysis/CVVH, previous or planned cystectomy or ileal loop surgery; known or suspected infection; caused by pathogen resistant to study treatment antibiotics
  • Presence of suspected or confirmed acute bacterial prostatitis, orchitis, epididymitis, or chronic bacterial prostatitis as determined by history and/or physical examination;
  • Gross hematuria requiring intervention;
  • Urinary tract surgery within 7 days prior to randomization or urinary tract surgery planned during the study period;
  • Creatinine clearance \<20 mL/min using the Cockcroft-Gault formula;
  • Non-renal source of infection such as endocarditis, osteomyelitis, abscess, meningitis, or pneumonia diagnosed within 7 days prior to randomization;
  • Signs of severe sepsis as defined per protocol;
  • Pregnant or breastfeeding women;
  • Known seizure disorder requiring current treatment with anti-seizure medication which would prohibit the patient from complying with the protocol;
  • Cancer chemotherapy, immunosuppressive medications for transplantation, or medications for rejection of transplantation with 30 days of randomization;
  • Significant hepatic disease or dysfunction, including known acute viral hepatitis or hepatic encephalopathy;
  • ALT/AST \>5 × ULN or total bilirubin \>3 × ULN at Screening;
  • Receipt of any potentially-effective systemic antibiotic with activity against Gram-negative uropathogens for more than 24 hours within the 72-hour window prior to randomization (exceptions defined in protocol);
  • Requirement for additional systemic antibiotic therapy (other than study drug) or antifungal therapy for vaginal candidiasis;
  • Likely to require the use of an antibiotic for cUTI or AP prophylaxis during the study;
  • +10 more criteria

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (68)

Unknown Facility

Pensacola, Florida, United States

Location

Unknown Facility

Augusta, Georgia, United States

Location

Unknown Facility

Columbus, Georgia, United States

Location

Unknown Facility

Boylston, Massachusetts, United States

Location

Unknown Facility

St Louis, Missouri, United States

Location

Unknown Facility

Butte, Montana, United States

Location

Unknown Facility

Brest, Belarus

Location

Unknown Facility

Grodno, Belarus

Location

Unknown Facility

Homyel, Belarus

Location

Unknown Facility

Minsk, Belarus

Location

Unknown Facility

Vitebsk, Belarus

Location

Unknown Facility

Plovdiv, Bulgaria

Location

Unknown Facility

Sofia, Bulgaria

Location

Unknown Facility

Slavonski Brod, Croatia

Location

Unknown Facility

Split, Croatia

Location

Unknown Facility

Zagreb, Croatia

Location

Unknown Facility

Brno, Czechia

Location

Unknown Facility

Hradec Králové, Czechia

Location

Unknown Facility

Liberec, Czechia

Location

Unknown Facility

Kohtla-Järve, Estonia

Location

Unknown Facility

Tallinn, Estonia

Location

Unknown Facility

Batumi, Georgia

Location

Unknown Facility

Kutaisi, Georgia

Location

Unknown Facility

Tbilisi, Georgia

Location

Unknown Facility

Ampelokipoi, Greece

Location

Unknown Facility

Athens, Greece

Location

Unknown Facility

Thessaloniki, Greece

Location

Unknown Facility

Budapest, Hungary

Location

Unknown Facility

Miskolc, Hungary

Location

Unknown Facility

Nagykanizsa, Hungary

Location

Unknown Facility

Pécs, Hungary

Location

Unknown Facility

Szekszárd, Hungary

Location

Unknown Facility

Szentes, Hungary

Location

Unknown Facility

Riga, Latvia

Location

Unknown Facility

Valmiera, Latvia

Location

Unknown Facility

Kaunas, Lithuania

Location

Unknown Facility

Klaipėda, Lithuania

Location

Unknown Facility

Vilnius, Lithuania

Location

Unknown Facility

Bielsko-Biala, Poland

Location

Unknown Facility

Krakow, Poland

Location

Unknown Facility

Lodz, Poland

Location

Unknown Facility

Piaseczno, Poland

Location

Unknown Facility

Tychy, Poland

Location

Unknown Facility

Wroclaw, Poland

Location

Unknown Facility

Zamość, Poland

Location

Unknown Facility

Bucharest, Romania

Location

Unknown Facility

Craiova, Romania

Location

Unknown Facility

Oradea, Romania

Location

Unknown Facility

Krasnoyarsk, Russia

Location

Unknown Facility

Moscow, Russia

Location

Unknown Facility

Moscow, Zelenograd, Russia

Location

Unknown Facility

Nizhny Novgorod, Russia

Location

Unknown Facility

Novosibirsk, Russia

Location

Unknown Facility

Penza, Russia

Location

Unknown Facility

Rostov-on-Don, Russia

Location

Unknown Facility

Saint Petersburg, Russia

Location

Unknown Facility

Saratov, Russia

Location

Unknown Facility

Smolensk, Russia

Location

Unknown Facility

Vsevolozhsk, Russia

Location

Unknown Facility

Martin, Slovakia

Location

Unknown Facility

Poprad, Slovakia

Location

Unknown Facility

Žilina, Slovakia

Location

Unknown Facility

Chernihiv, Ukraine

Location

Unknown Facility

Dnipropetrovsk, Ukraine

Location

Unknown Facility

Kharkiv, Ukraine

Location

Unknown Facility

Kyiv, Ukraine

Location

Unknown Facility

Odesa, Ukraine

Location

Unknown Facility

Zaporizhzhia, Ukraine

Location

Related Publications (1)

  • Kaye KS, Rice LB, Dane AL, Stus V, Sagan O, Fedosiuk E, Das AF, Skarinsky D, Eckburg PB, Ellis-Grosse EJ. Fosfomycin for Injection (ZTI-01) Versus Piperacillin-tazobactam for the Treatment of Complicated Urinary Tract Infection Including Acute Pyelonephritis: ZEUS, A Phase 2/3 Randomized Trial. Clin Infect Dis. 2019 Nov 27;69(12):2045-2056. doi: 10.1093/cid/ciz181.

MeSH Terms

Interventions

Piperacillin, Tazobactam Drug Combination

Intervention Hierarchy (Ancestors)

TazobactamPenicillanic AcidPenicillinsbeta-LactamsLactamsAmidesOrganic ChemicalsPiperacillinAmpicillinPenicillin GSulfur CompoundsSulfonesHeterocyclic Compounds, 2-RingHeterocyclic Compounds, Fused-RingHeterocyclic CompoundsDrug CombinationsPharmaceutical Preparations

Results Point of Contact

Title
Chief Medical Officer
Organization
Nabriva Therapeutics plc

Study Officials

  • Evelyn J Ellis-Grosse, PhD

    Zavante Therapeutics, Inc.

    STUDY CHAIR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
GT60
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
QUADRUPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR, OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

April 13, 2016

First Posted

April 28, 2016

Study Start

April 1, 2016

Primary Completion

January 12, 2017

Study Completion

May 30, 2017

Last Updated

March 7, 2019

Results First Posted

December 11, 2018

Record last verified: 2019-03

Data Sharing

IPD Sharing
Will share

Individual IPD data will be shared in listings with FDA, IRB/ECs, Data Monitoring Committee

Shared Documents
STUDY PROTOCOL, SAP, ICF, CSR, ANALYTIC CODE
Time Frame
ongoing submissions to IND
Access Criteria
IND/NDA submission, CTA submissions

Locations