NCT02693171

Brief Summary

The purpose of this study was to assess the incidence of human anti-chimeric antibody (HACA) in high-risk neuroblastoma patients treated with Unituxin combination therapy.

Trial Health

57
Monitor

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
13

participants targeted

Target at below P25 for all trials

Timeline
Completed

Started Mar 2016

Shorter than P25 for all trials

Geographic Reach
1 country

18 active sites

Status
terminated

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

February 23, 2016

Completed
3 days until next milestone

First Posted

Study publicly available on registry

February 26, 2016

Completed
18 days until next milestone

Study Start

First participant enrolled

March 15, 2016

Completed
9 months until next milestone

Primary Completion

Last participant's last visit for primary outcome

December 19, 2016

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

December 19, 2016

Completed
2.6 years until next milestone

Results Posted

Study results publicly available

August 5, 2019

Completed
Last Updated

August 5, 2019

Status Verified

June 1, 2019

Enrollment Period

9 months

First QC Date

February 23, 2016

Results QC Date

February 12, 2018

Last Update Submit

June 11, 2019

Conditions

Outcome Measures

Primary Outcomes (1)

  • To Determine the Incidence of Human Anti-chimeric Antibody (HACA) in High-risk Neuroblastoma Patients Treated With Unituxin Combination Therapy.

    Seven blood samples were collected at the following time points for the evaluation of HACA levels: * Course 1- Prior to the first Unituxin infusion * Course 2- Prior to the first Unituxin infusion * Course 3- Prior to the first Unituxin infusion * Course 4- Prior to the first Unituxin infusion * Course 5- Prior to the first Unituxin infusion * Course 6- Prior to the first dose of 13-cis-retinoic acid (RA) * Study termination (approximately 2 weeks following the final 13-cis-retinoic acid dose)

    Approximately 6 months

Secondary Outcomes (3)

  • To Determine the Incidence of Targeted Immune-related Adverse Events (AEs) During Treatment With Dinutuximab Combination Therapy in High-risk Neuroblastoma Subjects.

    Approximately 6 months

  • To Determine the Incidence of Neutralizing Antibody (NAb) in Patients With Human Anti-chimeric Antibody (HACA) Positive Samples.

    Approximately 6 months

  • To Determine the Effect of HACA on Dinutuximab Plasma Concentrations.

    Approximately 6 months

Study Arms (1)

Dinutuximab administered for 5 cycles

High-risk neuroblastoma patient treated with Unituxin as standard of care

Drug: Dinutuximab

Interventions

Unituxin was administered along with cytokines according to the prescribing information

Also known as: Unituxin®
Dinutuximab administered for 5 cycles

Eligibility Criteria

Age1 Year - 18 Years
Sexall
Healthy VolunteersNo
Age GroupsChild (0-17), Adult (18-64)
Sampling MethodNon-Probability Sample
Study Population

High-risk neuroblastoma patients prescribed Unituxin

You may qualify if:

  • Patient had been diagnosed with high-risk neuroblastoma.
  • Patient had been prescribed Unituxin and plans to start Unituxin therapy within 30 days of study entry.
  • Patient started Unituxin therapy no later than 200 days after Autologous Stem Cell Transplantation (ASCT).
  • Written informed consent / assent was obtained in accordance with institutional and International Conference on Harmonisation (ICH) guidelines.

You may not qualify if:

  • Patient had received prior anti-disialoganglioside (anti-GD2) antibody therapy.
  • Patient had participated in an investigational clinical trial with tumor therapeutic intent within 30 days of informed consent.
  • Patient underwent Autologous Stem Cell Transplantation (ASCT) more than 200 days prior to receiving Unituxin therapy.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (18)

University Of Alabama At Birmingham

Birmingham, Alabama, 35233, United States

Location

Arkansas Children's Hospital

Little Rock, Arkansas, 72202, United States

Location

Children's Hospital Los Angeles

Los Angeles, California, 90027, United States

Location

Children's Hospital of Orange County

Orange, California, 92868, United States

Location

Rady Children's Hospital- San Diego

San Diego, California, 92123, United States

Location

University of Chicago

Chicago, Illinois, 60637, United States

Location

Dana Farber Cancer Institute

Boston, Massachusetts, 02215, United States

Location

University of Michigan - C S Mott Children's Hospital

Ann Arbor, Michigan, 48109, United States

Location

Children's Hospitals and Clinics of Minnesota - Minneapolis

Minneapolis, Minnesota, 55404, United States

Location

Children's Mercy Hospital

Kansas City, Missouri, 64108, United States

Location

Columbia University Medical Center

New York, New York, 10032, United States

Location

Carolinas Medical Center / Levine Children's Hospital

Charlotte, North Carolina, 28203, United States

Location

Duke University Medical Center

Durham, North Carolina, 27710, United States

Location

Nationwide Children's Hospital

Columbus, Ohio, 43205, United States

Location

Penn State Hershey Children's Hospital

Hershey, Pennsylvania, 17033, United States

Location

Vanderbilt-Ingram Cancer Center

Nashville, Tennessee, 37232, United States

Location

Cook Children's Health Care System

Fort Worth, Texas, 76104, United States

Location

Seattle Children's Hospital

Seattle, Washington, 98105, United States

Location

MeSH Terms

Conditions

Neuroblastoma

Interventions

dinutuximab

Condition Hierarchy (Ancestors)

Neuroectodermal Tumors, Primitive, PeripheralNeuroectodermal Tumors, PrimitiveNeoplasms, NeuroepithelialNeuroectodermal TumorsNeoplasms, Germ Cell and EmbryonalNeoplasms by Histologic TypeNeoplasmsNeoplasms, Glandular and EpithelialNeoplasms, Nerve Tissue

Results Point of Contact

Title
Odette Jordan, MD, PMP
Organization
United Therapeutics Corp.

Study Officials

  • Ami Desai, MD

    Children's Hospital of Philadelphia

    STUDY CHAIR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
observational
Observational Model
COHORT
Time Perspective
PROSPECTIVE
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

February 23, 2016

First Posted

February 26, 2016

Study Start

March 15, 2016

Primary Completion

December 19, 2016

Study Completion

December 19, 2016

Last Updated

August 5, 2019

Results First Posted

August 5, 2019

Record last verified: 2019-06

Data Sharing

IPD Sharing
Will not share

Locations