NCT02677701

Brief Summary

This is a study to examine the effect of combining chronic oral azithromycin with inhaled tobramycin in adolescent and adult subjects with cystic fibrosis who are chronically infected with P. aeruginosa.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
119

participants targeted

Target at P50-P75 for phase_4

Timeline
Completed

Started Oct 2016

Typical duration for phase_4

Geographic Reach
1 country

39 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

January 29, 2016

Completed
11 days until next milestone

First Posted

Study publicly available on registry

February 9, 2016

Completed
9 months until next milestone

Study Start

First participant enrolled

October 21, 2016

Completed
3.3 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

February 13, 2020

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

February 13, 2020

Completed
1 year until next milestone

Results Posted

Study results publicly available

March 1, 2021

Completed
Last Updated

June 28, 2021

Status Verified

June 1, 2021

Enrollment Period

3.3 years

First QC Date

January 29, 2016

Results QC Date

February 9, 2021

Last Update Submit

June 3, 2021

Conditions

Outcome Measures

Primary Outcomes (1)

  • Relative Change in Lung Function

    Relative change in FEV1 volume (L) from enrollment at week 0 to the end of the 4-week period with inhaled tobramycin at week 6

    baseline (week 0) to week 6 (6 week period)

Secondary Outcomes (3)

  • Relative Change in Lung Function

    week 2 to week 6 (4 week period)

  • Change in Cystic Fibrosis Respiratory Symptom Diary - Chronic Respiratory Infection Symptom Score (CFRSD-CRISS)

    baseline (week 0) to week 6 (6 week period)

  • Change in Cystic Fibrosis Questionnaire - Revised Respiratory Symptom Score (CFQ-R RSS)

    baseline (week 0) to week 6 (6 week period)

Other Outcomes (1)

  • Change in Sputum Pseudomonas Aeruginosa Bacterial Density

    baseline (week 0) to week 6 (6 week period)

Study Arms (2)

azithromycin

ACTIVE COMPARATOR

azithromycin 500mg tablet over-encapsulated to match placebo in appearance, taken by mouth thrice weekly for 6 weeks

Drug: azithromycinDrug: inhaled tobramycin

placebo

PLACEBO COMPARATOR

encapsulated placebo taken by mouth thrice weekly for 6 weeks

Drug: placebo (for azithromycin)Drug: inhaled tobramycin

Interventions

500mg tablet over-encapsulated to match placebo

Also known as: Zithromax
azithromycin

clinically prescribed inhaled tobramycin used by subjects participating in the study

azithromycinplacebo

Eligibility Criteria

Age12 Years+
Sexall
Healthy VolunteersNo
Age GroupsChild (0-17), Adult (18-64), Older Adult (65+)

You may qualify if:

  • years old or older
  • documented diagnosis of cystic fibrosis
  • written informed consent (and assent when applicable)
  • at least two respiratory cultures growing P. aeruginosa within the last 12 months
  • FEV1% predicted between 25-100%
  • use of at least two cycles of inhaled tobramycin within the last 24 weeks
  • Off TISP and other inhaled anti-pseudomonal antibiotics for at least 2 weeks at Visit 1 and remain off of any inhaled antibiotics for an additional 2 weeks before starting inhaled tobramycin
  • most recent liver function test results less than 4 times the upper limit of normal, obtained within the last 12 months
  • prior or current use of azithromycin for at least four consecutive weeks
  • stable clinical status and therapeutic regimen

You may not qualify if:

  • weight \<40 kg
  • positive pregnancy test, lactating, or unwillingness to practice a pre-defined form of contraception, which includes abstinence
  • inability to perform reproducible spirometry
  • inability or unwillingness to cycle off of inhaled tobramycin for one 4-week period and without use of any additional inhaled antibiotics
  • respiratory culture with Burkholderia cepacia complex species within 24 months or with nontuberculous mycobacteria within 18 months of screening
  • use of intravenous or oral anti-pseudomonal antibiotics within 4 weeks of screening
  • use of investigational therapy within 4 weeks of screening
  • use of systemic corticosteroids equivalent to a daily dose more than 10mg of prednisone
  • use of nelfinavir, warfarin, haloperidol, or methadone (concern of drug interaction with azithromycin)
  • initiation of cystic fibrosis transmembrane conductance regulator (CFTR) modulator therapy within 30 days
  • ECG abnormality at screening requiring prompt further medical attention, or QTc interval \>480 msec for males and \>486 msec for females
  • any other condition that, in the opinion of the site investigator, would compromise the safety of the subject or quality of the data

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (39)

Children's Hospital of Los Angeles

Los Angeles, California, 90027, United States

Location

Stanford University Medical Center

Palo Alto, California, 94025, United States

Location

Rady Children's Hospital and Health Center at the University of California San Diego

San Diego, California, 92123, United States

Location

National Jewish Health

Denver, Colorado, 80206, United States

Location

Yale University School of Medicine

New Haven, Connecticut, 06520, United States

Location

University of Florida

Gainesville, Florida, 32610, United States

Location

The Nemours Children's Clinic - Orlando

Orlando, Florida, 32806, United States

Location

Nemours Children's Clinic - Pensacola

Pensacola, Florida, 32504, United States

Location

Saint Luke's Cystic Fibrosis Center of Idaho

Boise, Idaho, 83712, United States

Location

Northwestern University

Chicago, Illinois, 60208, United States

Location

Saint Francis Medical Center

Peoria, Illinois, 61637, United States

Location

Riley Hospital for Children

Indianapolis, Indiana, 46202, United States

Location

Maine Medical Partners Pediatric Specialty Care

Portland, Maine, 04102, United States

Location

Johns Hopkins University

Baltimore, Maryland, 21287, United States

Location

Boston Children's Hospital

Boston, Massachusetts, 02115, United States

Location

University of Massachusetts Memorial Health Care

Worcester, Massachusetts, 01655, United States

Location

University of Michigan Health System

Ann Arbor, Michigan, 48109, United States

Location

Helen DeVos Children's Hospital

Grand Rapids, Michigan, 49503, United States

Location

The Minnesota Cystic Fibrosis Center

Minneapolis, Minnesota, 55455, United States

Location

Children's Mercy Kansas City

Kansas City, Missouri, 64108, United States

Location

Cardinal Glennon Children's Medical Center

St Louis, Missouri, 63104, United States

Location

St. Louis Children's Hospital

St Louis, Missouri, 63110, United States

Location

Monmouth Medical Center

Long Branch, New Jersey, 07740, United States

Location

Beth Israel Medical Center

New York, New York, 10003, United States

Location

Children's Hospital of New York

New York, New York, 10032, United States

Location

University of Rochester Medical Center Strong Memorial

Rochester, New York, 14642, United States

Location

University of North Carolina at Chapel Hill

Chapel Hill, North Carolina, 27599, United States

Location

Cincinnati Children's Hospital Medical Center

Cincinnati, Ohio, 45229, United States

Location

University Hospitals Case Medical Center/Rainbow Babies and Children's Hospital

Cleveland, Ohio, 44106, United States

Location

Dayton Children's Hospital

Dayton, Ohio, 45404, United States

Location

Oregon Health Sciences University

Portland, Oregon, 97239, United States

Location

Hershey Medical Center Pennsylvania State University

Hershey, Pennsylvania, 17033, United States

Location

St. Christopher's Hospital for Children

Philadelphia, Pennsylvania, 19134, United States

Location

Children's Hospital of Pittsburgh of UPMC

Pittsburgh, Pennsylvania, 15224, United States

Location

Cook Children's Medical Center

Fort Worth, Texas, 76104, United States

Location

Intermountain Cystic Fibrosis Center

Salt Lake City, Utah, 84113, United States

Location

Seattle Children's Hospital

Seattle, Washington, 98145, United States

Location

University of Washington Medical Center

Seattle, Washington, 98195, United States

Location

Children's Hospital of Wisconsin

Milwaukee, Wisconsin, 53226, United States

Location

MeSH Terms

Conditions

Cystic Fibrosis

Interventions

Azithromycin

Condition Hierarchy (Ancestors)

Pancreatic DiseasesDigestive System DiseasesLung DiseasesRespiratory Tract DiseasesGenetic Diseases, InbornCongenital, Hereditary, and Neonatal Diseases and AbnormalitiesInfant, Newborn, Diseases

Intervention Hierarchy (Ancestors)

ErythromycinMacrolidesPolyketidesLactonesOrganic Chemicals

Results Point of Contact

Title
Arthur Baines
Organization
Seattle Children's Hospital

Study Officials

  • David P Nichols, MD

    National Jewish Health

    PRINCIPAL INVESTIGATOR

Publication Agreements

PI is Sponsor Employee
No
Restrictive Agreement
No

Study Design

Study Type
interventional
Phase
phase 4
Allocation
RANDOMIZED
Masking
QUADRUPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR, OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
OTHER
Responsible Party
PRINCIPAL INVESTIGATOR
PI Title
Associate Professor of Pediatrics

Study Record Dates

First Submitted

January 29, 2016

First Posted

February 9, 2016

Study Start

October 21, 2016

Primary Completion

February 13, 2020

Study Completion

February 13, 2020

Last Updated

June 28, 2021

Results First Posted

March 1, 2021

Record last verified: 2021-06

Locations