NCT02660359

Brief Summary

The purpose of this study is to provide confirmatory evidence of the safety and efficacy of two Dysport® doses (600 units \[U\] and 800 U), compared to placebo in reducing urinary incontinence (UI) in adult subjects treated for neurogenic detrusor overactivity (NDO) due to spinal cord injury (SCI) or multiple sclerosis (MS).

Trial Health

68
Monitor

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
258

participants targeted

Target at P50-P75 for phase_3

Timeline
Completed

Started Jul 2016

Typical duration for phase_3

Geographic Reach
16 countries

82 active sites

Status
terminated

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

January 14, 2016

Completed
7 days until next milestone

First Posted

Study publicly available on registry

January 21, 2016

Completed
6 months until next milestone

Study Start

First participant enrolled

July 8, 2016

Completed
2.3 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

November 9, 2018

Completed
8 months until next milestone

Study Completion

Last participant's last visit for all outcomes

July 4, 2019

Completed
2 years until next milestone

Results Posted

Study results publicly available

June 16, 2021

Completed
Last Updated

September 28, 2022

Status Verified

September 1, 2022

Enrollment Period

2.3 years

First QC Date

January 14, 2016

Results QC Date

May 21, 2021

Last Update Submit

September 15, 2022

Conditions

Outcome Measures

Primary Outcomes (1)

  • Mean Change From Baseline in Weekly Number of UI Episodes at Week 6 of DBPC Cycle

    The weekly number of UI episodes was measured using a 7-day bladder diary. Bladder diaries that contained data recorded on at least 5 days were included in the analysis. The least square (LS) mean of the change in weekly number of UI episodes at 6 weeks after the first study treatment was calculated using a mixed model repeated measures (MMRM) analysis.

    Baseline and Week 6 of DBPC Cycle

Secondary Outcomes (8)

  • Percentage of Subjects With No Episodes of UI at Week 6 of DBPC Cycle

    Baseline and Week 6 of DBPC Cycle

  • Percentage of Subjects With a UI Response at Improvement Levels ≥30%, ≥50%, and ≥75% at Week 6 of the DBPC Cycle

    Baseline and Week 6 of DBPC Cycle

  • Median Time Between Treatments

    Day of first treatment (baseline) to day of retreatment, up to 2 years

  • Mean Change From Baseline in Volume Per Void at Week 6 of DBPC Cycle

    Baseline and Week 6 of DBPC Cycle

  • Mean Change From Baseline in Maximum Cystometric Capacity (MCC) at Week 6 of DBPC Cycle

    Baseline and Week 6 of DBPC Cycle

  • +3 more secondary outcomes

Study Arms (4)

600 U Dysport® Group

EXPERIMENTAL
Biological: Botulinum toxin type A

600 U Dysport® Placebo Group

PLACEBO COMPARATOR
Drug: Placebo

800 U Dysport® Group

EXPERIMENTAL
Biological: Botulinum toxin type A

800 U Dysport® Placebo Group

PLACEBO COMPARATOR
Drug: Placebo

Interventions

600 U intra detrusor injection in two treatment periods (Initial and Retreatment phase) delivered at 30 injection points.

Also known as: AbobotulinumtoxinA (Dysport®), Clostridium BTX-A-haemagglutinin complex
600 U Dysport® Group

AbobotulinumtoxinA Placebo 600 U intra detrusor injection in two treatment periods (Initial and Retreatment phase) delivered at 30 injection points

600 U Dysport® Placebo Group

Eligibility Criteria

Age18 Years - 80 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Urinary Incontinence for at least 3 months prior to Screening as a result of Neurogenic Detrusor Overactivity due to Spinal Cord Injury or Multiple Sclerosis.
  • Subjects with Spinal Cord Injury must have a stable neurological injury at T1 level or below which occurred at least 6 months prior to Screening.
  • Subjects with Multiple Sclerosis must be clinically stable in the investigator's opinion, with no exacerbation (relapse) of MS for at least 3 months prior to Screening.
  • Subjects must have had an inadequate response after at least 4 weeks of oral medications used in the treatment of NDO (e.g. anticholinergics, beta-3 agonists) and/or have intolerable side-effects.
  • Routinely performing Clean Intermittent Catheterization (CIC) to ensure adequate bladder emptying.
  • An average of at least two episodes per day of Urinary Incontinence recorded on the screening bladder diary.

You may not qualify if:

  • Any current condition (other than NDO) that may impact on bladder function.
  • Previous or current, tumour or malignancy affecting the spinal column or spinal cord, or any other unstable cause of SCI.
  • Any condition that will prevent cystoscopic treatment administration or CIC usage, e.g. urethral strictures.
  • Current indwelling bladder catheter, or removal of indwelling bladder catheter less than 4 weeks prior to Screening.
  • BTX-A treatment within 9 months prior to Screening for any urological condition (e.g. detrusor or urethral sphincter treatments).
  • Any neuromodulation/electrostimulation usage for urinary symptoms/incontinence within 4 weeks prior to Screening. Any implanted neuromodulation device must be switched off at least 4 weeks prior to Screening.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (82)

Instituto Urológico Buenos Aires

Buenos Aires, 1060, Argentina

Location

Centro de Urologia

Buenos Aires, C1120AAS, Argentina

Location

Centro Urológico Profesor Bengió

Córdoba, X5000, Argentina

Location

Hospital Privado - Centro Médico de Córdoba

Córdoba, X5016KEH, Argentina

Location

Instituto Médico Rodriguez Alfici

Godoy Cruz, M5501AAP, Argentina

Location

Prince of Wales Hospital (POWH)

Sydney, 2031, Australia

Location

Westmead Hospital

Westmead, 2145, Australia

Location

Antwerp University hospital

Antwerp, Belgium

Location

Hôpital Erasme

Brussels, 1070, Belgium

Location

Ourthe-Amblève

Esneux, 4130, Belgium

Location

Universidade Estadual de Campinas - Cidade Universitária Zeferino Vaz

Campinas, 13083-970, Brazil

Location

Hospital de Clinicas, Federal University of Paraná

Curitiba, 80060-900, Brazil

Location

Hospital São Vicente de Paulo

Passo Fundo, 99010-080, Brazil

Location

Santa Casa de Misericórdia de Porto Alegre - Hospital Santa Clara

Porto Alegre, 90020-090, Brazil

Location

Hospital Moinhos de Vento

Pôrto Alegre, 90560-030, Brazil

Location

Hospital São Lucas da PUCRS

Pôrto Alegre, 90610-000, Brazil

Location

Hospital das Clínicas da Faculdade de Medicina de Ribeirão Preto da Universidade de São Paulo

Ribeirão Preto, 14048-900, Brazil

Location

Faculdade de Medicina do ABC

Santo André, 09060-650, Brazil

Location

Hospital Alemão Oswaldo Cruz

São Paulo, 01323-020, Brazil

Location

Hospital das Clínicas da Faculdade de Medicina da Universidade de São Paulo

São Paulo, 05422-970, Brazil

Location

Clínica Uromed

Santiago, 7500787, Chile

Location

Hospital del Trabajador

Santiago, 7501241, Chile

Location

Clínica Las Condes

Santiago, 7591046, Chile

Location

Solano & Terront Servicios Medicos LTDA- Unidad Integral de Endocrinologia

Bogotá, 110221, Colombia

Location

Fundación Valle del Lili

Cali, 760032, Colombia

Location

Centro Medico Imbanaco

Cali, 760042, Colombia

Location

Asociacion IPS Medicos Internistas de Caldas

Manizales, 170004, Colombia

Location

Centro de Investigaciones Clinicas - CIC

Medellín, 5001000, Colombia

Location

Hôpital Raymond-Poincaré

Garches, France

Location

Centre Hospitalier Régional Universitaire de Lille (CHRU) - Hôpital Claude Huriez

Lille, France

Location

Hôpital de la Conception

Marseille, France

Location

Groupe Hospitalo-Universitaire Pierre Caremau

Nîmes, France

Location

Hopital de la Source

Orléans, France

Location

Hopital Pitie-Salpetriere

Paris, France

Location

Hôpital Tenon

Paris, France

Location

Centre Hospitalier Lyon-Sud

Pierre-Bénite, France

Location

CHU de Rennes - Hôpital Pontchaillou

Rennes, France

Location

CHU de ROUEN - Hôpital Charles Nicolle

Rouen, France

Location

Hôpital Rangueil

Toulouse, France

Location

Universitätsklinikum Bonn Klinik und Poliklinik für Urologie

Bonn, 53127, Germany

Location

Kliniken Maria Hilf GmbH - Krankenhaus St. Franziskus

Mönchengladbach, Germany

Location

Universitätsklinikum Münster

Münster, 48149, Germany

Location

Rambam Medical Center

Haifa, 31096, Israel

Location

Carmel Medical Center

Haifa, 34362, Israel

Location

Meir Medical Center

Kfar Saba, 44281, Israel

Location

Rabin Medical Center - Davidoff Center

Petah Tikva, 49100, Israel

Location

The Chaim Sheba Medical Center

Ramat Gan, 52621, Israel

Location

Estetines Chirurgijos Centas, UAB

Kaunas, 49476, Lithuania

Location

Vilnius University Hospital Santariskiu Klinikos

Vilnius, 8661, Lithuania

Location

Centro Medico Puerta de Hierro - Colima

Colima, 28018, Mexico

Location

Clinstile, S.A. de C.V.

Cuauhtémoc, 06700, Mexico

Location

Hospital Universitario "Dr. José Eleuterio González"

Monterrey, 64460, Mexico

Location

Consultorio Privado

Zapopan, 45040, Mexico

Location

Clínica San Pablo Surco

Lima, 15023, Peru

Location

Clinica Good Hope

Lima, Lima18, Peru

Location

Clinica Internacional Sede Lima

Lima, Lima1, Peru

Location

Clínica Anglo Americana

Lima, Lima27, Peru

Location

Instituto de Ginecología y Reproducción

Lima, Lima33, Peru

Location

Unidad de Investigación de la Clínica Internacional Sede San Borja

Lima, Lima41, Peru

Location

Scientific research institute of urology and interventional radiology n. a. N. A. Lopatkin

Moscow, 105425, Russia

Location

Ministry of healthcare of the Russian Federation

Moscow, 129226, Russia

Location

Penza Regional Clinical Hospital n.a. N.N.Burdenko

Penza, 440026, Russia

Location

Rostov State Medical University

Rostov-on-Don, 344022, Russia

Location

St. Petersburg Research Institute of Phthisiopulmonology

Saint Petersburg, 194064, Russia

Location

Pavlov First Saint Petersburg State Medical University

Saint Petersburg, 197089, Russia

Location

City Hospital No. 40

Saint Petersburg, 197706, Russia

Location

Hospital Orkli

Saint Petersburg, Russia

Location

Complexo Hospitalario Universitario A Coruña

A Coruña, Spain

Location

Fundacio Puigvert

Barcelona, 08025, Spain

Location

Fundació GAEM

Barcelona, Spain

Location

Hospital Universitario Vall d'Hebron

Barcelona, Spain

Location

Hospital Universitario La Paz

Madrid, Spain

Location

Hospital Universitario Virgen del Rocío

Seville, Spain

Location

Hospital Universitari i Politècnic La Fe

Valencia, Spain

Location

Municipal Healthcare Institution "Regional Clinical Center of Urology and Nephrology n.a. V.I. Shapoval", Urology Department

Kharkiv, 61037, Ukraine

Location

Kiev City Clinical Hospital No. 3

Kiev, 02125, Ukraine

Location

NHS Grampian - Aberdeen Royal Infirmary

Aberdeen, AB25 2ZN, United Kingdom

Location

Bedford Hospital

Bedford, MK42 9DJ, United Kingdom

Location

National Hospital for Neurology and Neurosurgery - UCL

London, WC1N 3BG, United Kingdom

Location

Sheffield Teaching Hospitals NHS Foundation Trust - Royal Hallamshire Hospital

Sheffield, S10 2JF, United Kingdom

Location

Royal National Orthopaedic Hospital Trust

Stanmore, HA7 4LP, United Kingdom

Location

The Mid Yorkshire Hospitals NHS Trust - Pinderfields Hospital

Wakefield, WF1 4DG, United Kingdom

Location

Related Publications (1)

  • Kennelly M, Cruz F, Herschorn S, Abrams P, Onem K, Solomonov VK, Del Rosario Figueroa Coz E, Manu-Marin A, Giannantoni A, Thompson C, Vilain C, Volteau M, Denys P; Dysport CONTENT Program Group. Efficacy and Safety of AbobotulinumtoxinA in Patients with Neurogenic Detrusor Overactivity Incontinence Performing Regular Clean Intermittent Catheterization: Pooled Results from Two Phase 3 Randomized Studies (CONTENT1 and CONTENT2). Eur Urol. 2022 Aug;82(2):223-232. doi: 10.1016/j.eururo.2022.03.010. Epub 2022 Apr 7.

MeSH Terms

Conditions

Urinary IncontinenceUrinary Bladder, Overactive

Interventions

Botulinum Toxins, Type AabobotulinumtoxinA

Condition Hierarchy (Ancestors)

Urination DisordersUrologic DiseasesFemale Urogenital DiseasesFemale Urogenital Diseases and Pregnancy ComplicationsUrogenital DiseasesMale Urogenital DiseasesLower Urinary Tract SymptomsUrological ManifestationsSigns and SymptomsPathological Conditions, Signs and SymptomsUrinary Bladder Diseases

Intervention Hierarchy (Ancestors)

Botulinum ToxinsMetalloendopeptidasesEndopeptidasesPeptide HydrolasesHydrolasesEnzymesEnzymes and CoenzymesMetalloproteasesBacterial ProteinsProteinsAmino Acids, Peptides, and ProteinsBacterial ToxinsToxins, BiologicalBiological Factors

Limitations and Caveats

This study was terminated early by the sponsor on 04 October 2018, due to slow subject recruitment (258 subjects randomised compared to 330 planned subjects). Only primary and key secondary efficacy analyses were performed.

Results Point of Contact

Title
Medical Director
Organization
Ipsen

Study Officials

  • Ipsen Medical Director

    Ipsen

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restrictive Agreement
No

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
TRIPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

January 14, 2016

First Posted

January 21, 2016

Study Start

July 8, 2016

Primary Completion

November 9, 2018

Study Completion

July 4, 2019

Last Updated

September 28, 2022

Results First Posted

June 16, 2021

Record last verified: 2022-09

Data Sharing

IPD Sharing
Will share

Qualified researchers may request access to patient level data and related study documents including the clinical study report, study protocol with any amendments, annotated case report form, statistical analysis plan, and dataset specifications. Patient level data will be anonymized, and study documents will be redacted to protect the privacy of study participants. Any requests should be submitted to www.vivli.org for assessment by an independent scientific review board.

Time Frame
Where applicable, data from eligible studies are available 6 months after the studied medicine and indication have been approved in the US and EU or after the primary manuscript describing the results has been accepted for publication, whichever is later.
Access Criteria
Further details on Ipsen's sharing criteria, eligible studies and process for sharing are available here (https://vivli.org/members/ourmembers/).
More information

Locations