NCT02652533

Brief Summary

The investigators plan to investigate the use of US shear wave elastography (SWE), a newly available imaging technology, in children with suspected/known BA.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
41

participants targeted

Target at P25-P50 for all trials

Timeline
Completed

Started Sep 2016

Typical duration for all trials

Geographic Reach
1 country

4 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

December 18, 2015

Completed
25 days until next milestone

First Posted

Study publicly available on registry

January 12, 2016

Completed
8 months until next milestone

Study Start

First participant enrolled

September 1, 2016

Completed
2.3 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

January 1, 2019

Completed
6 months until next milestone

Study Completion

Last participant's last visit for all outcomes

July 1, 2019

Completed
Last Updated

September 23, 2019

Status Verified

March 1, 2018

Enrollment Period

2.3 years

First QC Date

December 18, 2015

Last Update Submit

September 19, 2019

Conditions

Outcome Measures

Primary Outcomes (1)

  • Discrimination of biliary atresia from other liver diseases using ultrasound liver shear wave speed (Aim 1)

    The primary outcome measure will be ultrasound shear wave speed of the liver. The investigators will compare the mean liver shear wave speed measurements in children with biliary atresia to other liver diseases. Sensitivity and specificity of ultrasound for diagnosing biliary atresia will be determined using multiple shear wave speed cut-off values.

    2 years

Secondary Outcomes (1)

  • Predicting long term clinical outcomes in biliary atresia patients using ultrasound liver shear wave speed (aim 2)

    6 years

Interventions

The investigators have recently published a very small study in neonates/infants with suspected BA showing that US liver shear wave speed (i.e. - liver stiffness) can differentiate BA from other causes of cholestasis, potentially with a very high degree of accuracy. Additional research is needed to confirm these very preliminary results and determine if liver shear wave speed measurements either before or after (including longitudinally) Kasai can predict key outcomes.

Eligibility Criteria

AgeUp to 3 Months
Sexall
Healthy VolunteersNo
Age GroupsChild (0-17)
Sampling MethodNon-Probability Sample
Study Population

neonatal cholestasis with concern for BA vs. other liver disease direct bilirubin \>20% of total or ≥2 mg/dL age \<3 months

You may qualify if:

  • neonatal cholestasis with concern for BA vs. other liver disease direct bilirubin \>20% of total or ≥2 mg/dL age \<3 months

You may not qualify if:

  • inability to obtain parent/guardian consent.
  • inability to return for follow up visits as required by the study (these patients will be included in aim 1, but will be unable to participate in aim 2).

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (4)

Lucile Packard Children's Hospital/Stanford University

Stanford, California, 94305, United States

Location

University of Michigan

Ann Arbor, Michigan, 48109, United States

Location

Cincinnati Children's Hospital Medical Center

Cincinnati, Ohio, 45229, United States

Location

Nationwide Children's

Columbus, Ohio, 43205, United States

Location

MeSH Terms

Conditions

Biliary Atresia

Condition Hierarchy (Ancestors)

Bile Duct DiseasesBiliary Tract DiseasesDigestive System DiseasesDigestive System AbnormalitiesCongenital AbnormalitiesCongenital, Hereditary, and Neonatal Diseases and Abnormalities

Study Officials

  • Jonathan Dillman, MD

    Children's Hospital Medical Center, Cincinnati

    PRINCIPAL INVESTIGATOR

Study Design

Study Type
observational
Observational Model
COHORT
Time Perspective
PROSPECTIVE
Sponsor Type
OTHER
Responsible Party
SPONSOR

Study Record Dates

First Submitted

December 18, 2015

First Posted

January 12, 2016

Study Start

September 1, 2016

Primary Completion

January 1, 2019

Study Completion

July 1, 2019

Last Updated

September 23, 2019

Record last verified: 2018-03

Data Sharing

IPD Sharing
Will not share

Locations