Key Insights

Highlights

Success Rate

87% trial completion (above average)

Clinical Risk Assessment

Based on trial outcomes

Moderate Risk

Score: 50/100

Termination Rate

4.9%

3 terminated out of 61 trials

Success Rate

87.0%

+0.5% vs benchmark

Late-Stage Pipeline

8%

5 trials in Phase 3/4

Results Transparency

30%

6 of 20 completed with results

Key Signals

6 with results87% success

Data Visualizations

Phase Distribution

32Total
Not Applicable (13)
Early P 1 (2)
P 1 (6)
P 2 (6)
P 3 (4)
P 4 (1)

Trial Status

Completed20
Unknown16
Recruiting15
Not Yet Recruiting3
Terminated3
Active Not Recruiting2

Trial Success Rate

87.0%

Benchmark: 86.5%

Based on 20 completed trials

Clinical Trials (61)

Showing 20 of 20 trials
NCT05426733Phase 3Enrolling By InvitationPrimary

An Open-label Extension Study to Evaluate Long-term Efficacy and Safety of Odevixibat in Children With Biliary Atresia

NCT04336722Phase 3Active Not RecruitingPrimary

Efficacy and Safety of Odevixibat in Children With Biliary Atresia Who Have Undergone a Kasai HPE (BOLD)

NCT06184971Active Not RecruitingPrimary

Biliary Atresia Research Network Northeast

NCT05848310RecruitingPrimary

Preoperative Serum FGF19 in the Prognosis of Biliary Atresia

NCT06260566Phase 1Not Yet RecruitingPrimary

Tolerability of Enteral NAC in Infants

NCT07250854Early Phase 1RecruitingPrimary

The Use of Near-Infrared Fluorescence Cholangiography With Indocyanine Green (ICG) in the Work Up of Neonatal Cholestasis

NCT07328204CompletedPrimary

Kasai Portoenterostomy Timing and Outcomes in Biliary Atresia

NCT06764082Not ApplicableRecruiting

Nutritional Intervention for Biliary Atresia

NCT06121375Phase 2TerminatedPrimary

Study to Assess Efficacy, Safety, Tolerability, Pharmacokinetics (PK), and Pharmacodynamics (PD) of Obeticholic Acid (OCA) Compared to Placebo in Pediatric Participants With Biliary Atresia, Post-hepatoportoenterostomy

NCT00345553RecruitingPrimary

Biliary Atresia Study in Infants and Children

NCT00061828RecruitingPrimary

A Prospective Database of Infants With Cholestasis

NCT03273049RecruitingPrimary

Mapping Disease Pathways for Biliary Atresia

NCT07139717Not Yet Recruiting

Stool Card in Biliary Atresia

NCT03890536WithdrawnPrimary

Intestinal Microbiome Composition in Infants With Biliary Atresia (BA)

NCT07011199Phase 1Not Yet RecruitingPrimary

Clinical Outcomes of Early Kasai Surgery With Umbilical Cord MSCs in Biliary Atresia

NCT01793168Recruiting

Rare Disease Patient Registry & Natural History Study - Coordination of Rare Diseases at Sanford

NCT04524390Phase 2CompletedPrimary

Evaluation of Maralixibat in Biliary Atresia Response Post-Kasai

NCT06708572Not ApplicableRecruiting

Evaluation of the Use of Granulocyte Colony Stimulating Factor (GCSF) in Post Kasai Type 3 Biliary Atresia

NCT05925309Not ApplicableRecruitingPrimary

Preventive Effect of Prophylactic Oral Antibiotics Against Cholangitis After Kasai Portoenterostomy

NCT06564740Not ApplicableRecruitingPrimary

Stem Cell Applications in Biliary Atresia Patients

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