NCT02608697

Brief Summary

The purpose of this placebo-controlled, double-blind study is to assess the effect of several doses of CAT-2054 on LDL-C in hypercholesterolemic patients on a stable dose of high-intensity statin, and to evaluate the safety and tolerability of different doses of CAT-2054 for 4 weeks.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
153

participants targeted

Target at P75+ for phase_2

Timeline
Completed

Started Oct 2015

Shorter than P25 for phase_2

Geographic Reach
1 country

34 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

October 1, 2015

Completed
1 month until next milestone

First Submitted

Initial submission to the registry

November 11, 2015

Completed
9 days until next milestone

First Posted

Study publicly available on registry

November 20, 2015

Completed
5 months until next milestone

Primary Completion

Last participant's last visit for primary outcome

May 1, 2016

Completed
1 month until next milestone

Study Completion

Last participant's last visit for all outcomes

June 1, 2016

Completed
Last Updated

June 20, 2017

Status Verified

June 1, 2017

Enrollment Period

7 months

First QC Date

November 11, 2015

Last Update Submit

June 14, 2017

Conditions

Outcome Measures

Primary Outcomes (1)

  • Percent change in LDL-C from baseline in patients with hypercholesterolemia.

    4 weeks

Secondary Outcomes (2)

  • Frequency of adverse events

    8 weeks

  • Percent change in TG, non-HDL-C, total cholesterol, HDL-C, apoB from baseline in patients with hypercholesterolemia

    4 weeks

Study Arms (4)

Group 1: CAT-2054 or Placebo Dose 1

EXPERIMENTAL

A run-in phase with 40 mg atorvastatin tablet administered daily for at least 28 days, followed by a 28-day blinded treatment phase with 250 mg CAT-2054 or placebo QD and open label 40 mg atorvastatin tablet administered daily.

Drug: CAT-2054Drug: PlaceboDrug: Atorvastatin

Group 2: CAT-2054 or Placebo Dose 2

EXPERIMENTAL

A run-in phase with 40 mg atorvastatin tablet administered daily for at least 28 days, followed by a 28-day blinded treatment phase with 400 mg CAT-2054 or placebo QD and open label 40 mg atorvastatin tablet administered daily.

Drug: CAT-2054Drug: PlaceboDrug: Atorvastatin

Group 3: CAT-2054 or Placebo Dose 3

EXPERIMENTAL

A run-in phase with 40 mg atorvastatin tablet administered daily for at least 28 days, followed by a 28-day blinded treatment phase with 250 mg CAT-2054 or placebo BID and open label 40 mg atorvastatin tablet administered daily.

Drug: CAT-2054Drug: PlaceboDrug: Atorvastatin

Group 4: CAT-2054 or Placebo Dose 4

EXPERIMENTAL

A run-in phase with 40 mg atorvastatin tablet administered daily for at least 28 days, followed by a 28-day blinded treatment phase with 400 mg CAT-2054 or placebo BID and open label 40 mg atorvastatin tablet administered daily.

Drug: CAT-2054Drug: PlaceboDrug: Atorvastatin

Interventions

Group 1: CAT-2054 or Placebo Dose 1Group 2: CAT-2054 or Placebo Dose 2Group 3: CAT-2054 or Placebo Dose 3Group 4: CAT-2054 or Placebo Dose 4
Group 1: CAT-2054 or Placebo Dose 1Group 2: CAT-2054 or Placebo Dose 2Group 3: CAT-2054 or Placebo Dose 3Group 4: CAT-2054 or Placebo Dose 4
Group 1: CAT-2054 or Placebo Dose 1Group 2: CAT-2054 or Placebo Dose 2Group 3: CAT-2054 or Placebo Dose 3Group 4: CAT-2054 or Placebo Dose 4

Eligibility Criteria

Age18 Years - 74 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Between 18 and 74 years at Screening
  • Hypercholesterolemia (LDL-C ≥ 70 mg/dL and \< 190 mg/dL) plus a stable dose of statin for at least 4 weeks prior to Screening
  • Satisfies one of the following:
  • Female patients of childbearing potential must have used appropriate and highly effective contraception (a regimen which results in a failure rate of \<1% per year) with their partners for 4 weeks prior to Screening, and remain compliant during the treatment phase and until 4 weeks after the last dose of investigational product
  • Male patients must use an acceptable and highly effective contraceptive method during the treatment phase and until 4 weeks after the last dose of investigational product
  • Body mass index (BMI) ≤45 kg/m2

You may not qualify if:

  • History of any major cardiovascular event (stroke, TIA, MI, PTCI, CABG, hospitalization due to heart failure) within 6 months of Screening
  • Type I diabetes mellitus or use of insulin
  • Active peptic ulcer disease or a history of muscle disease or myopathy

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (34)

Unknown Facility

Muscle Shoals, Alabama, 35662, United States

Location

Unknown Facility

Huntington Park, California, 90255, United States

Location

Unknown Facility

Lomita, California, 90717, United States

Location

Unknown Facility

Los Angeles, California, 90057, United States

Location

Unknown Facility

Brooksville, Florida, 34601, United States

Location

Unknown Facility

Hialeah, Florida, 33012, United States

Location

Unknown Facility

Jupiter, Florida, 33458, United States

Location

Unknown Facility

Pembroke Pines, Florida, 33026, United States

Location

Unknown Facility

Winter Park, Florida, 32792, United States

Location

Unknown Facility

Chicago, Illinois, 60607, United States

Location

Unknown Facility

Evanston, Illinois, 60201, United States

Location

Unknown Facility

Indianapolis, Indiana, 46260, United States

Location

Unknown Facility

Kansas City, Kansas, 66160, United States

Location

Unknown Facility

Louisville, Kentucky, 40213, United States

Location

Unknown Facility

Auburn, Maine, 04210, United States

Location

Unknown Facility

Troy, Michigan, 48098, United States

Location

Unknown Facility

Las Vegas, Nevada, 89123, United States

Location

Unknown Facility

New York, New York, 10029, United States

Location

Unknown Facility

Rochester, New York, 14609, United States

Location

Unknown Facility

Cincinnati, Ohio, 45219, United States

Location

Unknown Facility

Cincinnati, Ohio, 45227, United States

Location

Unknown Facility

Cincinnati, Ohio, 45246, United States

Location

Unknown Facility

Columbus, Ohio, 43213, United States

Location

Unknown Facility

Franklin, Ohio, 45005, United States

Location

Unknown Facility

Lyndhurst, Ohio, 44124, United States

Location

Unknown Facility

Marion, Ohio, 43302, United States

Location

Unknown Facility

Willoughby Hills, Ohio, 44094, United States

Location

Unknown Facility

Mt. Pleasant, South Carolina, 29464, United States

Location

Unknown Facility

Summerville, South Carolina, 29485, United States

Location

Unknown Facility

Houston, Texas, 77036, United States

Location

Unknown Facility

Houston, Texas, 77074, United States

Location

Unknown Facility

Orem, Utah, 84058, United States

Location

Unknown Facility

Richmond, Virginia, 23294, United States

Location

Unknown Facility

Olympia, Washington, 98502, United States

Location

MeSH Terms

Conditions

Hypercholesterolemia

Interventions

Atorvastatin

Condition Hierarchy (Ancestors)

HyperlipidemiasDyslipidemiasLipid Metabolism DisordersMetabolic DiseasesNutritional and Metabolic Diseases

Intervention Hierarchy (Ancestors)

PyrrolesAzolesHeterocyclic Compounds, 1-RingHeterocyclic CompoundsHeptanoic AcidsFatty AcidsLipids

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
QUADRUPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR, OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

November 11, 2015

First Posted

November 20, 2015

Study Start

October 1, 2015

Primary Completion

May 1, 2016

Study Completion

June 1, 2016

Last Updated

June 20, 2017

Record last verified: 2017-06

Locations