NCT02591836

Brief Summary

The primary purpose of this placebo-controlled study is to evaluate the low-density lipoprotein cholesterol (LDL-C) efficacy and dose-response of gemcabene 300, 600 and 900 mg/day administered as monotherapy or in combination with atorvastatin 10, 40, and 80 mg/day to hypercholesterolemic patients. Secondary purposes include evaluating the effects of high-sensitivity C-reactive protein (hsCRP), high-density lipoprotein cholesterol (HDL-C), triglycerides (TG) and apolipoprotein B (ApoB), and safety and efficacy of gemcabene monotherapy and gemcabene/atorvastatin combination.

Trial Health

100
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
277

participants targeted

Target at P75+ for phase_2

Timeline
Completed

Started Jan 2003

Shorter than P25 for phase_2

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

January 1, 2003

Completed
5 months until next milestone

Primary Completion

Last participant's last visit for primary outcome

June 1, 2003

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

June 1, 2003

Completed
12.4 years until next milestone

First Submitted

Initial submission to the registry

October 22, 2015

Completed
8 days until next milestone

First Posted

Study publicly available on registry

October 30, 2015

Completed
Last Updated

April 9, 2020

Status Verified

April 1, 2020

Enrollment Period

5 months

First QC Date

October 22, 2015

Last Update Submit

April 8, 2020

Conditions

Keywords

LDL-CLipid Regulator

Outcome Measures

Primary Outcomes (1)

  • LDL-C percent change from baseline

    56 days

Secondary Outcomes (5)

  • HDL-C percent change from baseline

    56 days

  • TG percent change from baseline

    56 days

  • Apolipoprotein-B percent change from baseline

    56 days

  • Adverse Events

    56 days

  • Clinical Laboratory

    56 days

Study Arms (16)

Gemcabene 300 mg

EXPERIMENTAL

Gemcabene 300 mg QD

Drug: Gemcabene

Gemcabene 600 mg

EXPERIMENTAL

Gemcabene 600 mg QD

Drug: Gemcabene

Gemcabene 900 mg

EXPERIMENTAL

Gemcabene 900 mg QD

Drug: Gemcabene

Placebo

PLACEBO COMPARATOR
Drug: Placebo

Atorvastatin 10 mg

ACTIVE COMPARATOR
Drug: Atorvastatin

Atorvastatin 40 mg

ACTIVE COMPARATOR
Drug: Atorvastatin

Atorvastatin 80 mg

ACTIVE COMPARATOR
Drug: Atorvastatin

Gemcabene 300 mg & Atorvastatin 10 mg

EXPERIMENTAL
Drug: GemcabeneDrug: Atorvastatin

Gemcabene 300 mg & Atorvastatin 40 mg

EXPERIMENTAL
Drug: GemcabeneDrug: Atorvastatin

Gemcabene 300 mg & Atorvastatin 80 mg

EXPERIMENTAL
Drug: GemcabeneDrug: Atorvastatin

Gemcabene 600 mg & Atorvastatin 10 mg

EXPERIMENTAL
Drug: GemcabeneDrug: Atorvastatin

Gemcabene 600 mg & Atorvastatin 40 mg

EXPERIMENTAL
Drug: GemcabeneDrug: Atorvastatin

Gemcabene 600 mg & Atorvastatin 80 mg

EXPERIMENTAL
Drug: GemcabeneDrug: Atorvastatin

Gemcabene 900 mg & Atorvastatin 10 mg

EXPERIMENTAL
Drug: GemcabeneDrug: Atorvastatin

Gemcabene 900 mg & Atorvastatin 40 mg

EXPERIMENTAL
Drug: GemcabeneDrug: Atorvastatin

Gemcabene 900 mg & Atorvastatin 80 mg

EXPERIMENTAL
Drug: GemcabeneDrug: Atorvastatin

Interventions

Gemcabene

Gemcabene 300 mgGemcabene 300 mg & Atorvastatin 10 mgGemcabene 300 mg & Atorvastatin 40 mgGemcabene 300 mg & Atorvastatin 80 mgGemcabene 600 mgGemcabene 600 mg & Atorvastatin 10 mgGemcabene 600 mg & Atorvastatin 40 mgGemcabene 600 mg & Atorvastatin 80 mgGemcabene 900 mgGemcabene 900 mg & Atorvastatin 10 mgGemcabene 900 mg & Atorvastatin 40 mgGemcabene 900 mg & Atorvastatin 80 mg

Atorvastatin

Atorvastatin 10 mgAtorvastatin 40 mgAtorvastatin 80 mgGemcabene 300 mg & Atorvastatin 10 mgGemcabene 300 mg & Atorvastatin 40 mgGemcabene 300 mg & Atorvastatin 80 mgGemcabene 600 mg & Atorvastatin 10 mgGemcabene 600 mg & Atorvastatin 40 mgGemcabene 600 mg & Atorvastatin 80 mgGemcabene 900 mg & Atorvastatin 10 mgGemcabene 900 mg & Atorvastatin 40 mgGemcabene 900 mg & Atorvastatin 80 mg
Placebo

Eligibility Criteria

Age18 Years - 70 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Males and Females
  • years old
  • Received a statin as monotherapy while having a LDL-C \>100 mg d/L at initial clinical washout visit OR
  • Received no lipid-altering drugs since the initial clinic washout visit and had a mean LDL-C as follows at 2 qualifying visits:
  • ≥ 130 mg/dL if National Cholesterol Education Program (NCEP) Adult Treatment Panel III (ATP III) Coronary Heard Disease (CHD) risk ≥ 10%; OR
  • ≥ 160 mg/dL if NCEP ATP III CHD risk \< 10%
  • Had variability of 2 qualifying LDL-C \<20% (i.e. lowest value/highest value \>0.8). An additional qualifying visit may have been completed by patients who were washing off lipid medication in order to reassess LDL-C variability; and
  • Had a mean LDL-C \< 250 mg/dL at 2 qualifying visits

You may not qualify if:

  • Women of childbearing potential, pregnant or lactating;
  • Body Mass Index (BMI) \>38kg/m²;
  • TG \>400 mg/dL at Visit B2 or B3
  • Unexplained creatinine phosphokinase (CPK) \> 3 x Upper Limit of Normal (ULN) or those with a history of unexplained myopathy (including rhabdomyolysis);
  • Documented cardiac history of: Myocardial infarction\*, severe or unstable angina pectoris, coronary angioplasty, coronary artery bypass graft, symptomatic carotid artery disease or peripheral artery disease, ventricular arrhythmias, recurrent supraventricular tachycardia, abnormal QTC interval (QT corrected \> 0.44 sec), heart failure or any other major cardiovascular event resulting in hospitalization
  • Uncontrolled hypertension\*
  • Type 1 diabetes mellitus or uncontrolled type 2 diabetes mellitus (HbA1c \>8%) or any diabetic patient who takes insulin and/or thiazolidinediones
  • Renal dysfunction including chronic renal failure or insufficiency, or creatinine \>2.0 mg/dL;
  • Hepatic dysfunction
  • Uncontrolled hypothyroidism
  • Abnormal urinalysis
  • Currently taking any of the following medications:
  • Potent CYP3A4 inhibitors including indinavir, nelfinavir, ritonavir, saquinavir, amiodarone, cimetidine, clarithromycin, erythromycin, erythromycin, fluoxetine, itraconazole, ketoconazole, nefazodone and troleandomycin as well as grapefruit juice;
  • Thiazolidinediones (Avandia, Actos);
  • Immunosuppressive agents;
  • +10 more criteria

Contact the study team to confirm eligibility.

Sponsors & Collaborators

MeSH Terms

Conditions

Hypercholesterolemia

Interventions

gemcabeneAtorvastatin

Condition Hierarchy (Ancestors)

HyperlipidemiasDyslipidemiasLipid Metabolism DisordersMetabolic DiseasesNutritional and Metabolic Diseases

Intervention Hierarchy (Ancestors)

PyrrolesAzolesHeterocyclic Compounds, 1-RingHeterocyclic CompoundsHeptanoic AcidsFatty AcidsLipids

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
QUADRUPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR, OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
FACTORIAL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

October 22, 2015

First Posted

October 30, 2015

Study Start

January 1, 2003

Primary Completion

June 1, 2003

Study Completion

June 1, 2003

Last Updated

April 9, 2020

Record last verified: 2020-04