NCT02504008

Brief Summary

This is a randomized, double-blind, placebo-controlled, 24-week study to evaluate the efficacy and safety of AXS-02 in patients with CRPS-I.

Trial Health

47
At Risk

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Trial has exceeded expected completion date
Enrollment
190

participants targeted

Target at P25-P50 for phase_3

Timeline
Completed

Started Jul 2015

Typical duration for phase_3

Geographic Reach
4 countries

44 active sites

Status
unknown

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

July 1, 2015

Completed
19 days until next milestone

First Submitted

Initial submission to the registry

July 20, 2015

Completed
1 day until next milestone

First Posted

Study publicly available on registry

July 21, 2015

Completed
3.5 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

January 1, 2019

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

January 1, 2019

Completed
Last Updated

March 23, 2018

Status Verified

March 1, 2018

Enrollment Period

3.5 years

First QC Date

July 20, 2015

Last Update Submit

March 21, 2018

Conditions

Keywords

bisphosphonateCRPSRSDnon-opioidCRPS-1acute on chronic painchronic painzoledronic acid

Outcome Measures

Primary Outcomes (1)

  • Change in patient reported pain intensity

    Patient reported pain intensity is recorded as an average daily pain intensity using an 11-point scale (0 = no pain to 10 = worst pain possible).

    Baseline to Week 12

Secondary Outcomes (6)

  • Change in Brief Pain Inventory (BPI) Pain Score

    Baseline to Week 12

  • Patients' Global Impression of Change (PGI-C)

    Baseline to Week 12

  • Clinicians' Global Impression of Change (CGI-C)

    Baseline to Week 12

  • Change in EuroQOL 5-dimensions questionnaire (EQ-5D)

    Baseline to Week 12

  • Change in Short-Form McGill Pain Questionnaire (SF-MPQ-2)

    Baseline to Week 12

  • +1 more secondary outcomes

Study Arms (2)

AXS-02 (oral zoledronate)

EXPERIMENTAL

Administered orally in the morning on Days 1, 8, 15, 22, 29, and 36

Drug: AXS-02 (oral zoledronate)

Placebo

PLACEBO COMPARATOR

Administered orally in the morning on Day 1, 8, 15, 22, 29, and 36

Drug: Placebo

Interventions

Once weekly for 6 weeks

AXS-02 (oral zoledronate)

Once weekly for 6 weeks

Placebo

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Male or female of at least 18 years of age
  • Recently confirmed diagnosis of CRPS-1 (Budapest criteria)
  • Average pain intensity score of ≥ 5 (based on an 11-point scale \[0 - 10\])
  • Willing and able to provide written informed consent

You may not qualify if:

  • Received chronic opioid therapy within 4 weeks
  • Received a sympathetic nerve block within 3 weeks
  • Active litigation or a pending workers' compensation decision
  • Any other clinically significant medical or pain condition (eg, Parkinson's disease, cognitive impairment, or fibromyalgia) or clinical laboratory abnormality that would in the investigator's judgment interfere with the subject's ability to participate in the study

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (44)

Unknown Facility

Tucson, Arizona, United States

Location

Unknown Facility

Hot Springs, Arkansas, United States

Location

Unknown Facility

Encinitas, California, United States

Location

Unknown Facility

La Jolla, California, United States

Location

Unknown Facility

Los Angeles, California, United States

Location

Unknown Facility

Napa, California, United States

Location

Unknown Facility

Temecula, California, United States

Location

Unknown Facility

Denver, Colorado, United States

Location

Unknown Facility

Clermont, Florida, United States

Location

Unknown Facility

Miami, Florida, United States

Location

Unknown Facility

Orlando, Florida, 32827, United States

Location

Unknown Facility

Tampa, Florida, United States

Location

Unknown Facility

West Palm Beach, Florida, United States

Location

Unknown Facility

Canton, Georgia, United States

Location

Unknown Facility

Marietta, Georgia, United States

Location

Unknown Facility

St. Marys, Georgia, 31558, United States

Location

Unknown Facility

Meridian, Idaho, United States

Location

Unknown Facility

Chicago, Illinois, United States

Location

Unknown Facility

Louisville, Kentucky, United States

Location

Unknown Facility

Albuquerque, New Mexico, United States

Location

Unknown Facility

New York, New York, United States

Location

Unknown Facility

Winston-Salem, North Carolina, United States

Location

Unknown Facility

Oklahoma City, Oklahoma, United States

Location

Unknown Facility

Portland, Oregon, United States

Location

Unknown Facility

Dallas, Texas, United States

Location

Unknown Facility

San Antonio, Texas, United States

Location

Unknown Facility

Bellevue, Washington, United States

Location

Unknown Facility

Seattle, Washington, United States

Location

Unknown Facility

Madison, Wisconsin, United States

Location

Unknown Facility

Broadmeadow, New South Wales, Australia

Location

Unknown Facility

Hurstville, New South Wales, Australia

Location

Unknown Facility

Noosa, Queensland, Australia

Location

Unknown Facility

Welland, South Australia, Australia

Location

Unknown Facility

Clayton, Victoria, Australia

Location

Unknown Facility

Nedlands, Western Australia, Australia

Location

Unknown Facility

Sherbrooke, Quebec, Canada

Location

Unknown Facility

Warrington, Cheshire, United Kingdom

Location

Unknown Facility

Darlington, County Durham, United Kingdom

Location

Unknown Facility

Lambeth, London, United Kingdom

Location

Unknown Facility

Liverpool, Merseyside, United Kingdom

Location

Unknown Facility

Norwich, Norfolk, United Kingdom

Location

Unknown Facility

Newcastle upon Tyne, Tyne and Wear, United Kingdom

Location

Unknown Facility

Glasgow, United Kingdom

Location

Unknown Facility

London, United Kingdom

Location

MeSH Terms

Conditions

Complex Regional Pain SyndromesReflex Sympathetic DystrophyChronic Pain

Interventions

Zoledronic Acid

Condition Hierarchy (Ancestors)

Autonomic Nervous System DiseasesNervous System DiseasesPeripheral Nervous System DiseasesNeuromuscular DiseasesPainNeurologic ManifestationsSigns and SymptomsPathological Conditions, Signs and Symptoms

Intervention Hierarchy (Ancestors)

DiphosphonatesOrganophosphonatesOrganophosphorus CompoundsOrganic ChemicalsImidazolesAzolesHeterocyclic Compounds, 1-RingHeterocyclic Compounds

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
DOUBLE
Who Masked
PARTICIPANT, INVESTIGATOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

July 20, 2015

First Posted

July 21, 2015

Study Start

July 1, 2015

Primary Completion

January 1, 2019

Study Completion

January 1, 2019

Last Updated

March 23, 2018

Record last verified: 2018-03

Locations