NCT02428686

Brief Summary

Chronic anemia is the symptom most frequently found at diagnosis in low risk myelodysplastic syndrome. It generates an increased rate of morbidity and mortality in this population of patients whose median age is high and the rate of co-mobidities important. The historical treatment is limited to transfusion support with a significant impact on quality of life and the incidence of secondary haemosiderosis, which contributes to the emergence of co-morbidities, especially cardiovascular. Treatment with rHuEPO allows for overall erythroid response in 40-60% of patients treated. In this trial, the investigators intend to study the interest of a treatment with epoetin beta in patients with anemia \<10 g / dL in the context of a myelodysplastic syndrome with IPSS score \<1. In addition to studying the erythroid response, the investigators will measure the impact on quality of life and functional performance. Patients will receive epoetin beta (60 000UI/week). Response will be assessed after 12 and 24 weeks of treatment.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
50

participants targeted

Target at P25-P50 for phase_2

Timeline
Completed

Started Jun 2010

Typical duration for phase_2

Geographic Reach
1 country

31 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

June 1, 2010

Completed
1.5 years until next milestone

First Submitted

Initial submission to the registry

November 24, 2011

Completed
2.3 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

March 1, 2014

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

March 1, 2014

Completed
1.2 years until next milestone

First Posted

Study publicly available on registry

April 29, 2015

Completed
Last Updated

April 29, 2015

Status Verified

April 1, 2015

Enrollment Period

3.8 years

First QC Date

November 24, 2011

Last Update Submit

April 28, 2015

Conditions

Outcome Measures

Primary Outcomes (1)

  • Assess the level of haematological response according to IWG 2006 criteria with a pattern of administration of high doses epoetin beta (NeoRecormon ®) for 12 and 24 weeks of treatment

    12 and 24 weeks

Study Arms (1)

epoetin beta

EXPERIMENTAL
Drug: Epoetin beta (NeoRecormon)

Interventions

Epoetin beta 60 000 IU/week

Also known as: NeoRecormon
epoetin beta

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Written informed consent
  • Must be 18 years of age or older at the time of screening
  • Myelodysplastic Syndrome of the following subtypes : RA, RAS, RCMD, RCMD-RS, RAEB 1, with IPSS score low or intermediate 1 (IPSS score \< 1 ) and with anemia defined by Hb \< 10 g/dl (with RBC transfusion requirement or not)
  • For women of childbearing potential, need for effective contraception throughout the study period.

You may not qualify if:

  • Myelodysplastic Syndrome with IPSS score \>1
  • EGOG \> 3 ;
  • Other causes of anemia (eg. , Iron deficiency, vitamin B12 or folic acid, hypothyroidism before correction)
  • Uncontrolled arterial hypertension
  • Life expectancy less than 6 months
  • CMML
  • Pregnant or breast feeding female subjects
  • Patients with creatinine clearance less than 30ml/min.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (31)

CHU d'AMIENS

Amiens, 80054, France

Location

CH Angers

Angers, 49 000, France

Location

CH d'Avignon-305 rue Follereau-

Avignon, 84000, France

Location

Hopital de la Cote Basque

Bayonne, 64100, France

Location

Hôpital Avicenne

Bobigny, 93 000, France

Location

Hôpital Boulogne Sur Mer

Boulogne-sur-Mer, 62321, France

Location

CHU de Brest

Brest, 29609, France

Location

CHU Clémenceau

Caen, 14033, France

Location

CH René Dubos

Cergy-Pontoise, 95303, France

Location

Centre Hospitalier du Mans

Le Mans, 72037, France

Location

CHRU Huriez

Lille, 59037, France

Location

Hopital Saint-Vincent de Paul-

Lille, 59160, France

Location

CHRU de Limoges

Limoges, 87046, France

Location

centre hospitalier de Mantes-la-jolie

Mantes-la-Jolie, 78201, France

Location

Institut Paoli Calmette

Marseille, 13273, France

Location

CHU Brabois

Nancy, 54511, France

Location

Hematology Dpt, Hopital de l'Hotel Dieu

Nantes, 44093, France

Location

Hôpital Américain de Paris

Neuilly-sur-Seine, 92200, France

Location

CHU Archet

Nice, 06202, France

Location

Hôpital La Source

Orléans, 45067, France

Location

Hôpital Saint Louis

Paris, 75475, France

Location

Hôpital Saint-Antoine.

Paris, 75571, France

Location

Hopital Cochin

Paris, 75679, France

Location

Hôpital Jean Bernard

Poitiers, 86021, France

Location

Centre Hospitalier de la région d'Annecy

Pringy, 74374, France

Location

CHU de Reims

Reims, 51092, France

Location

Centre Henri Becquerel

Rouen, 76038, France

Location

Centre Hospitalier Universitaire de STRASBOURG

Strasbourg, 67098, France

Location

Chu Purpan

Toulouse, 31059, France

Location

Hopital Bretonneau

Tours, 37044, France

Location

CHU de Bicêtre

Le Kremlin-Bicêtre, Île-de-France Region, 94275, France

Location

MeSH Terms

Conditions

Myelodysplastic Syndromes

Interventions

epoetin beta

Condition Hierarchy (Ancestors)

Bone Marrow DiseasesHematologic DiseasesHemic and Lymphatic Diseases

Study Design

Study Type
interventional
Phase
phase 2
Allocation
NA
Masking
NONE
Purpose
TREATMENT
Intervention Model
SINGLE GROUP
Sponsor Type
OTHER
Responsible Party
SPONSOR

Study Record Dates

First Submitted

November 24, 2011

First Posted

April 29, 2015

Study Start

June 1, 2010

Primary Completion

March 1, 2014

Study Completion

March 1, 2014

Last Updated

April 29, 2015

Record last verified: 2015-04

Locations