NCT02389933

Brief Summary

Novartis has set up this global Multiple Patient Program (MPP) treatment plan to provide access to life-saving treatment with LCZ696 for patients that were not previously exposed to LCZ696 but have no other option to receive LCZ696 in their country prior to market authorization OR commercial availability, based on local regulatory and legal requirements.

Trial Health

73
Monitor

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Strong global presence with extensive site network
Geographic Reach
17 countries

283 active sites

Status
unknown

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

March 10, 2015

Completed
7 days until next milestone

First Posted

Study publicly available on registry

March 17, 2015

Completed
Last Updated

February 15, 2021

Status Verified

February 1, 2021

First QC Date

March 10, 2015

Last Update Submit

February 10, 2021

Conditions

Keywords

Multiple Patient Program, LCZ696, heart failure, heart failure with reduced ejection fraction, HF-rEF

Interventions

LCZ696DRUG

immediate release film coated tablet in 50 mg, 100 mg, 200 mg, and 400 mg strengths for oral administration.

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • The patient(s) for whom the MPP is sought meets all of the following:
  • Is suffering from a serious or life-threatening disease or condition
  • Does not have access to a comparable or satisfactory alternative treatment (i.e., comparable or satisfactory treatment is not available or does not exist)
  • Patient should be on optimized standard of care treatment, including treatment with ARBs or ACEI, beta-blockers and MRA;
  • Intolerance to evidence-based target doses should be documented by the treating physician
  • Meets any other relevant medical criteria for compassionate use of the investigational product
  • Adult patients (but not younger than 18 year old) will be included, upon completion of written informed consent before any assessment is performed.
  • Patients with a diagnosis of CHF NYHA class II-IV and reduced ejection fraction:
  • LVEF ≤ 35% at the time of screening for participation in the program (any local measurement, made within the past 6 months using echocardiography, MUGA, CT scanning, MRI or ventricular angiography is acceptable, provided there are no subsequent measurement above 35%)
  • Patient had a hospitalization for HF within the last 12 months
  • Patients must be on an ACEI or an ARB at a stable dose for at least 4 weeks prior to starting treatment with LCZ696
  • Patients must be treated with a β-blocker, unless contraindicated or not tolerated, at a stable dose for at least 4 weeks prior to starting treatment with LCZ696 (reason should be documented for patients not on CHF target doses per local guidelines, or in absence of that medication).
  • An aldosterone antagonist should also be considered in all patients, taking account of renal function, serum potassium and tolerability. If given, the dose of aldosterone antagonist should be optimized according to guideline recommendations and patient tolerability, and should be stable for at least 4 weeks prior to starting treatment with LCZ696

You may not qualify if:

  • The patient is eligible for participation in any of the IMP's ongoing clinical trials
  • The patient has recently completed a clinical trial that has been terminated and other options (e.g., trial extensions, amendments, etc.) are available to continue a similar treatment.
  • The patient is being transferred from an ongoing clinical trial for which the patient is still eligible for participation
  • History of hypersensitivity or allergy to LCZ696 or to any of its metabolites; to drugs of similar chemical classes, ARBs, or NEP inhibitors; as well as known or suspected contraindications to LCZ696
  • Use of other investigational drugs at the time of enrollment, or within 30 days or 5 half-lives of enrollment, whichever is longer
  • Previous history of intolerance to recommended target doses of ARBs
  • Known history of angioedema
  • Requirement of concomitant treatment with both ACEIs and ARBs
  • Current acute decompensated HF (exacerbation of chronic HF manifested by signs and symptoms that may require intravenous therapy)
  • Symptomatic hypotension and/or a SBP less than 100 mm Hg over the last 4 weeks prior to starting treatment with LCZ696
  • Estimated GFR below 30 mL/min/1.73m2 as measured by the simplified MDRD formula
  • Presence of bilateral renal artery stenosis
  • Serum potassium above 5.2 mmol/L during the week prior to starting treatment with LCZ696
  • Acute coronary syndrome, stroke, transient ischemic attack, cardiac, carotid or other major CV surgery, percutaneous coronary intervention (PCI) or carotid angioplasty within the 3 months prior to starting treatment with LCZ696
  • Coronary or carotid artery disease likely to require surgical or percutaneous intervention within the 6 months after the schedule date to start treatment with LCZ696
  • +22 more criteria

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (286)

Novartis Investigative Site

Vero Beach, Florida, 32960, United States

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Novartis Investigative Site

Darlinghurst, New South Wales, 2010, Australia

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Novartis Investigative Site

North Ryde, New South Wales, 2109, Australia

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Novartis Investigative Site

Perth, Western Australia, 6000, Australia

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Novartis Investigative Site

Krems, A-3500, Austria

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Novartis Investigative Site

Salzburg, Austria

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Novartis Investigative Site

Sankt Pölten, 3100, Austria

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Novartis Investigative Site

Vienna, 1130, Austria

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Novartis Investigative Site

Vienna, A-1090, Austria

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Novartis Investigative Site

Fortaleza, Ceará, 60864-190, Brazil

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Novartis Investigative Site

Salvador, Estado de Bahia, 41180-780, Brazil

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Novartis Investigative Site

Belo Horizonte, Minas Gerais, 30170-040, Brazil

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Novartis Investigative Site

Porto Alegre, Rio Grande do Sul, 90610-000, Brazil

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Novartis Investigative Site

Porto Alegre, Rio Grande do Sul, 90620 001, Brazil

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Novartis Investigative Site

Varaždin, HRV, 42000, Croatia

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Novartis Investigative Site

Limassol, 3021, Cyprus

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Novartis Investigative Site

Nicosia, 1086, Cyprus

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Novartis Investigative Site

Nicosia, 2024, Cyprus

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Novartis Investigative Site

Nicosia, 2029, Cyprus

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Novartis Investigative Site

Nicosia, 2042, Cyprus

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Novartis Investigative Site

Nicosia, 2047, Cyprus

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Novartis Investigative Site

Marseille, Bouches Du Rhone, 13915, France

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Novartis Investigative Site

Bron, Cedex, 69677, France

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Novartis Investigative Site

Caen, Cedex, 14033, France

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Novartis Investigative Site

Saint-Denis, France / La Reunion, 97405, France

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Novartis Investigative Site

Brest Armees, France, 29240, France

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Novartis Investigative Site

Amiens, 80054, France

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Novartis Investigative Site

Amilly, 45200, France

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Novartis Investigative Site

Angers, 49933, France

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Antibes, 06600, France

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Aressy, 64320, France

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Avignon, 84000, France

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Avignon, 84082, France

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Bayeux, 14401, France

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Novartis Investigative Site

Béziers, 34525, France

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Novartis Investigative Site

Bobigny, 93009, France

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Novartis Investigative Site

Brest, 29609, France

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Novartis Investigative Site

Bron, 69677, France

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Novartis Investigative Site

Caen, 14000, France

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Novartis Investigative Site

Caen, 14033, France

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Novartis Investigative Site

Cambrai, 59507, France

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Cannes, 06414, France

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Chambéry, 73011, France

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Chaumont, 52014, France

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Cherbourg Octeville, 50102, France

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Novartis Investigative Site

Clamart, 92140, France

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Clermont-Ferrand, 63003, France

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Compiègne, 60321, France

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Novartis Investigative Site

Contamine-sur-Arve, 74130, France

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Corbeil-Essonnes, 91100, France

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Cornebarrieu, 31700, France

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Dijon, 21000, France

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Eaubonne, 95600, France

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Novartis Investigative Site

Honfleur, 14601, France

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Hyères, 83418, France

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Novartis Investigative Site

La Roche-sur-Yon, 85295, France

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La Seyne-sur-Mer, 83500, France

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La Tronche, 38700, France

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Lille, 59003, France

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Lille, 59037, France

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Limoges, France

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Lyon, 69317, France

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Lyon, 69394, France

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Lyon, F-69001, France

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Marseille, 13008, France

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Novartis Investigative Site

Marseille, 13385, France

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Novartis Investigative Site

Marseille, 13915, France

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Novartis Investigative Site

Mâcon, 71018, France

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Metz, F-57038, France

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Metz-Tessy, 74370, France

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Monaco, 98000, France

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Novartis Investigative Site

Montbéliard, 25209, France

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Novartis Investigative Site

Montpellier, 34295, France

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Novartis Investigative Site

Montpellier, 34960, France

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Novartis Investigative Site

Morlaix, 29672, France

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Moulins, 03006, France

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Mulhouse, 68051, France

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Nantes, 44093, France

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Novartis Investigative Site

Neuilly-sur-Seine, 92200, France

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Novartis Investigative Site

Nice, 06003, France

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Novartis Investigative Site

Nice, 06105, France

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Novartis Investigative Site

Nîmes, 30029, France

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Novartis Investigative Site

Paris, 75475, France

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Novartis Investigative Site

Paris, 75651, France

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Novartis Investigative Site

Paris, 75679, France

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Novartis Investigative Site

Pau, 64046, France

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Perpignan, 66000, France

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Pessac, 33604, France

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Poitiers, 86021, France

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Pont-l'Abbé, 29123, France

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Pontarlier, 25304, France

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Pontoise, F-95300, France

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Rennes, 35033, France

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Rouen, 76031, France

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Novartis Investigative Site

Rumilly, 74150, France

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Novartis Investigative Site

Saint-Denis, 97400, France

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Novartis Investigative Site

Saint-Denis, 97490, France

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Novartis Investigative Site

Saint-Etienne, 42055, France

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Novartis Investigative Site

Saint-Etienne, 42100, France

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Novartis Investigative Site

Saint-Germain-en-Laye, 78105, France

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Novartis Investigative Site

Saint-Palais, 64120, France

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Novartis Investigative Site

St.-Jean, 31240, France

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Novartis Investigative Site

Strasbourg, 67091, France

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Novartis Investigative Site

Thonon-les-Bains, 74203, France

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Novartis Investigative Site

Toulouse, 31054, France

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Novartis Investigative Site

Toulouse, 31059, France

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Novartis Investigative Site

Tours, 37044, France

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Novartis Investigative Site

Valence, 26953, France

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Valenciennes, 59322, France

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Novartis Investigative Site

Vandœuvre-lès-Nancy, 54511, France

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Vichy, 03201, France

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Novartis Investigative Site

Villefranche-sur-Saône, 69655, France

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Novartis Investigative Site

Wattrelos, 59393, France

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Novartis Investigative Site

Süderholz, OT Bartmannshagen, 18516, Germany

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Novartis Investigative Site

Ahlen, 59227, Germany

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Novartis Investigative Site

Augsburg, 86199, Germany

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Novartis Investigative Site

Bad Endbach, 35080, Germany

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Novartis Investigative Site

Bad Homburg, 61348, Germany

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Novartis Investigative Site

Bad Kreuznach, 55543, Germany

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Novartis Investigative Site

Bad Krozingen, 79189, Germany

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Novartis Investigative Site

Bad Oeynhausen, 32545, Germany

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Novartis Investigative Site

Berlin, 10789, Germany

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Novartis Investigative Site

Berlin, 13353, Germany

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Novartis Investigative Site

Bielefeld, 33602, Germany

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Novartis Investigative Site

Bielefeld, 33604, Germany

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Bonn, 53115, Germany

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Novartis Investigative Site

Chemnitz, 09117, Germany

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Novartis Investigative Site

Chemnitz, 09126, Germany

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Novartis Investigative Site

Chemnitz, 09130, Germany

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Novartis Investigative Site

Cologne, 50937, Germany

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Novartis Investigative Site

Cologne, 51105, Germany

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Novartis Investigative Site

Cologne, 51605, Germany

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Novartis Investigative Site

Dessau, 06847, Germany

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Novartis Investigative Site

Diepholz, 49356, Germany

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Dinslaken, 46535, Germany

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Dortmund, 44309, Germany

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Dresden, 01067, Germany

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Dresden, 01277, Germany

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Dresden, 01307, Germany

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Novartis Investigative Site

Düsseldorf, 40477, Germany

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Novartis Investigative Site

Eilenburg, D 04838, Germany

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Novartis Investigative Site

Eschwege, 37269, Germany

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Essen, 45355, Germany

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Frankfurt, 60322, Germany

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Novartis Investigative Site

Frankfurt, 60431, Germany

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Frankfurt, 60439, Germany

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Novartis Investigative Site

Frankfurt, 60590, Germany

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Friedrichroda, 99894, Germany

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Göttingen, 37075, Germany

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Novartis Investigative Site

Gronau, 31028, Germany

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Günzburg, 89312, Germany

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Hamburg, 22457, Germany

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Hanover, 30159, Germany

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Hanover, 30559, Germany

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Haßfurt, 97437, Germany

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Haßloch, 67454, Germany

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Hohenstein-Ernstthal, 09337, Germany

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Jena, 07740, Germany

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Karlsruhe, 76135, Germany

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Kassel, 34121, Germany

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Köthen, 06366, Germany

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Lauchringen, 79787, Germany

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Leipzig, 04103, Germany

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Ludwigshafen, 67063, Germany

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Magdeburg, 39114, Germany

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Magdeburg, 39120, Germany

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Mainz, 55131, Germany

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Mannheim, 68167, Germany

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Marl, 45768, Germany

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München, 80336, Germany

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München, 80636, Germany

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Münster, 48153, Germany

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Oldenburg, 26133, Germany

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Pressath, 92690, Germany

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Rostock, 18107, Germany

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Ulm, 89081, Germany

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Weinheim, 69469, Germany

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Wildeshausen, 27793, Germany

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Wolfratshausen, 82515, Germany

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Würzburg, 97080, Germany

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Novartis Investigative Site

Alexandroupoli, Evros, 681 00, Greece

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Novartis Investigative Site

Heraklion - Crete, Greece, 711 10, Greece

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Novartis Investigative Site

Thesaloniki, Greece, 55134, Greece

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Novartis Investigative Site

Athens, GR, 115 21, Greece

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Novartis Investigative Site

Athens, GR, 115 25, Greece

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Novartis Investigative Site

Athens, GR, 115 27, Greece

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Athens, GR, 14233, Greece

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Ioannina, GR, 451 10, Greece

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Larissa, GR, 411 10, Greece

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Novartis Investigative Site

Thessaloniki, GR, 546 36, Greece

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Novartis Investigative Site

Thessaloniki, GR, 56429, Greece

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Thessaloniki, GR, 570 10, Greece

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Tripoli, GR, 221 00, Greece

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Novartis Investigative Site

Voula, GR, 166 73, Greece

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Novartis Investigative Site

Athens, 106 76, Greece

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Novartis Investigative Site

Athens, 115 21, Greece

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Novartis Investigative Site

Athens, 115 26, Greece

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Novartis Investigative Site

Athens, 115 27, Greece

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Novartis Investigative Site

Athens, 115 28, Greece

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Novartis Investigative Site

Athens, 11521, Greece

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Novartis Investigative Site

Athens, 11526, Greece

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Athens, 11527, Greece

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Novartis Investigative Site

Athens, 145 61, Greece

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Novartis Investigative Site

Athens, 15127, Greece

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Athens, 15562, Greece

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Athens, 176 74, Greece

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Athens, GR14564, Greece

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Chaïdári, 12461, Greece

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Chios, 821 00, Greece

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Corfu, 49100, Greece

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Edessa, 58200, Greece

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Elefsina, 19600, Greece

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Glyfada, 16675, Greece

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Heraklion, 714 09, Greece

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Ioannina, 45001, Greece

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Kalamata, 241 00, Greece

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Karditsa, 43100, Greece

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Katerini, 601 00, Greece

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Kavala, 65 500, Greece

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Kilkis, 611 00, Greece

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Kozani, 50100, Greece

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Marousi, 15125, Greece

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Piraeus, 18454, Greece

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Piraeus, 185 36, Greece

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Rio Patra, 26504, Greece

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Thessaloniki, 54636, Greece

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Thessaloniki, 54642, Greece

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Thessaloniki, 552 36, Greece

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Novartis Investigative Site

Volos, GR 38222, Greece

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Novartis Investigative Site

Co Dublin, Ireland, Ireland

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Dublin, 9, Ireland

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Novartis Investigative Site

Beirut, 11-2555, Lebanon

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Novartis Investigative Site

Beirut, 1107 2020, Lebanon

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Novartis Investigative Site

Beirut, 166378, Lebanon

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Novartis Investigative Site

Beirut, 5544, Lebanon

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Novartis Investigative Site

Beirut, 6301, Lebanon

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Beirut, Lebanon

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Novartis Investigative Site

El Achrafiyé, 166830, Lebanon

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Saida, 652, Lebanon

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Tripoli, Lebanon

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Novartis Investigative Site

Msida, MSD 2090, Malta

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Panama City, Panama

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Manila, National Capital Region, 1000, Philippines

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Novartis Investigative Site

Makati City, 1229, Philippines

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Novartis Investigative Site

Manila, 1000, Philippines

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Novartis Investigative Site

Ljubljana, 1000, Slovenia

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Córdoba, Andalusia, 14004, Spain

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Garanada, Andalusia, 18004, Spain

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Jerez de la Frontera, Andalusia, 11407, Spain

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Seville, Andalusia, 41014, Spain

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Utrera, Andalusia, 41710, Spain

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Baleares, Balearic Islands, 7014, Spain

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Novartis Investigative Site

L'Hospitalet de Llobregat, Barcelona, 08907, Spain

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Bilbao, Basque Country, 48013, Spain

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Novartis Investigative Site

Galdakano, Basque Country, 48960, Spain

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Villamartín, Cadiz, 11650, Spain

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Santander, Cantabria, 39008, Spain

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Novartis Investigative Site

Torrelavega, Cantabria, 39300, Spain

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Novartis Investigative Site

Barcelona, Catalonia, 08035, Spain

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Novartis Investigative Site

Lleida, Catalonia, 25198, Spain

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Novartis Investigative Site

Salt, Catalonia, 17190, Spain

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Novartis Investigative Site

Badajoz, Extremadura, 6011, Spain

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Pontevedra, Galicia, 36001, Spain

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Logroño, La Rioja, 26006, Spain

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Las Palmas de Gran Canaria, Las Palmas de G.C, 35010, Spain

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Novartis Investigative Site

Majadahonda, Madrid, 28222, Spain

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Novartis Investigative Site

San Sebastián de los Reyes, Madrid, 28702, Spain

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Novartis Investigative Site

San Sebastián de los Reyes, Madrid, 28703, Spain

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Novartis Investigative Site

Marbella, Malaga, 29603, Spain

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Novartis Investigative Site

Pamplona, Navarre, 31008, Spain

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Novartis Investigative Site

Badalona, 08911, Spain

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Novartis Investigative Site

El Palmar (Murcia), 30120, Spain

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Novartis Investigative Site

Las Palmas de Gran Canaria, 35010, Spain

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Novartis Investigative Site

Las Palmas de Gran Canaria, 35016, Spain

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Novartis Investigative Site

Madrid, 28023, Spain

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Novartis Investigative Site

Madrid, 28031, Spain

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Novartis Investigative Site

Madrid, 28040, Spain

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Novartis Investigative Site

Madrid, 28046, Spain

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Novartis Investigative Site

Salamanca, 37007, Spain

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Novartis Investigative Site

Seville, 41009, Spain

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Novartis Investigative Site

Seville, 41010, Spain

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Novartis Investigative Site

Zaragoza, 50009, Spain

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Novartis Investigative Site

Zaragoza, 50015, Spain

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Novartis Investigative Site

Lucerne, Canton of Lucerne, 6004, Switzerland

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Novartis Investigative Site

Abu Dhabi, 51900, United Arab Emirates

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Novartis Investigative Site

Ras al-Khaimah, 4727, United Arab Emirates

Location

MeSH Terms

Conditions

Heart Failure

Interventions

sacubitril and valsartan sodium hydrate drug combination

Condition Hierarchy (Ancestors)

Heart DiseasesCardiovascular Diseases

Study Design

Study Type
expanded access
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

March 10, 2015

First Posted

March 17, 2015

Last Updated

February 15, 2021

Record last verified: 2021-02

Locations