NCT02379247

Brief Summary

Investigate the use of BYL719 (alpelisib) as combination therapy with Nab-Paclitaxel in locally recurrent or metastatic HER-2 negative breast cancer.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
43

participants targeted

Target at P50-P75 for phase_1 breast-cancer

Timeline
Completed

Started Feb 2015

Longer than P75 for phase_1 breast-cancer

Geographic Reach
1 country

4 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

January 30, 2015

Completed
2 days until next milestone

Study Start

First participant enrolled

February 1, 2015

Completed
1 month until next milestone

First Posted

Study publicly available on registry

March 4, 2015

Completed
2.6 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

September 21, 2017

Completed
4 years until next milestone

Results Posted

Study results publicly available

September 28, 2021

Completed
5 months until next milestone

Study Completion

Last participant's last visit for all outcomes

March 1, 2022

Completed
Last Updated

June 7, 2022

Status Verified

May 1, 2022

Enrollment Period

2.6 years

First QC Date

January 30, 2015

Results QC Date

May 7, 2021

Last Update Submit

May 16, 2022

Conditions

Keywords

HER-2 NegativeMetastatic Breast Cancer

Outcome Measures

Primary Outcomes (2)

  • Phase I: Recommended Phase II Dose (RP2D) of BYL-719 (Alpelisib) + Nab-paclitaxel to be Used in Combination to Treat Advanced HER2-negative Breast Cancer

    Phase I was a 3+3 dose escalation design (three dose levels of alpelisib: 250mg, 300mg, and 350mg orally once daily, continuous dosing) with dose-limiting toxicities (DLT) assessed during the first treatment cycle. If two or more of the six patients experienced a dose-limiting toxicity, dosing escalation would cease and maximum tolerated dose (MTD) would be reached. RP2D was the next lower dose at which \<1/6 subjects experienced a DLT.

    12 months

  • Phase II: Overall Response Rate (ORR) of Subjects Treated at the Recommended Phase II Dose (RP2D)

    ORR includes complete response (CR) plus partial response (PR). As evaluated per RECIST version 1.1.

    24 months

Secondary Outcomes (4)

  • Clinical Benefit Rate (CBR) at 16 Weeks of Study Treatment

    16 weeks

  • Pharmacokinetics of BYL-719 (Alpelisib) When Administered With Nab-paclitaxel

    In cycle 1 day 1, from prior to alpelisib dosing through 8 hours after alpelisib dosing

  • Pharmacokinetics of (Total) Nab-paclitaxel When Administered With BYL-719 (Alpelisib)

    In cycle 1 day 1, from prior to alpelisib dosing through 8 hours after alpelisib dosing

  • Progression-free Survival (PFS) and Overall Survival (OS)

    36 months

Other Outcomes (1)

  • Correlation of PIK3CA Mutation With Clinical Benefit Rate

    24 months

Study Arms (4)

Dose level 1 BYL-719/alpelisib (250mg)+Nab-paclitaxel

EXPERIMENTAL

BYL-719 (alpelisib): 250mg daily on day 1-28 Nab-paclitaxel: 100mg/m2 IV days 1, 8, 15 of each 28 day cycle (Window for Nab-paclitaxel is +/- 1 day)

Drug: BYL-719 (alpelisib)Drug: Nab-paclitaxel

Dose level 2 BYL-719 (alpelisib) (300mg)+Nab-paclitaxel

EXPERIMENTAL

BYL-719 (alpelisib): 300mg by mouth daily on day 1-28 of each 28 day cycle Nab-paclitaxel: 100mg/m2 given IV on days 1, 8, 15 of each 28 day cycle (Window for Nab-paclitaxel is +/- 1 day)

Drug: BYL-719 (alpelisib)Drug: Nab-paclitaxel

Dose level 3 BYL-719 (alpelisib) (350mg)+Nab-paclitaxel

EXPERIMENTAL

BYL-719 (alpelisib): 350mg by mouth daily on day 1-28 of each 28 day cycle Nab-paclitaxel: 100mg/m2 given IV on days 1, 8, 15 of each 28 day cycle (Window for Nab-paclitaxel is +/- 1 day)

Drug: BYL-719 (alpelisib)Drug: Nab-paclitaxel

BYL-719 (alpelisib) Dose Expansion

EXPERIMENTAL

BYL-719 (alpelisib): RP2D from Phase I by mouth daily on day 1-28 of each 28 day cycle Nab-paclitaxel: 100mg/m2 given IV on days 1, 8, 15 of each 28 day cycle (Window for Nab-paclitaxel is +/- 1 day)

Drug: BYL-719 (alpelisib)Drug: Nab-paclitaxel

Interventions

Oral PI3K inhibitor

Also known as: Piqray
BYL-719 (alpelisib) Dose ExpansionDose level 1 BYL-719/alpelisib (250mg)+Nab-paclitaxelDose level 2 BYL-719 (alpelisib) (300mg)+Nab-paclitaxelDose level 3 BYL-719 (alpelisib) (350mg)+Nab-paclitaxel

IV taxane

Also known as: Abraxane
BYL-719 (alpelisib) Dose ExpansionDose level 1 BYL-719/alpelisib (250mg)+Nab-paclitaxelDose level 2 BYL-719 (alpelisib) (300mg)+Nab-paclitaxelDose level 3 BYL-719 (alpelisib) (350mg)+Nab-paclitaxel

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Ability to understand and the willingness to sign a written Informed Consent Form.
  • Age ≥ 18 years
  • Histologically proven HER-2 negative breast cancer (HER-2 negative defined as HER IHC 0 or 1+ and/or HER-2 FISH negative); HER-2 negative breast cancer includes hormone positive (ER and/or PR positive) breast cancer and TNBC
  • HER-2 negative breast cancer that at the time of study entry is either stage III (locally advanced) disease not amenable to curative therapy or stage IV disease. Histological confirmation of recurrent/metastatic disease is encouraged but not required if clinical evidence of stage IV disease is available
  • Have measurable (defined as at least one lesion that can be accurately measured in at least one dimension \[longest diameter to be recorded\] with minimum lesion size of ≥ 2 cm on conventional measurement techniques or ≥ 1 cm on spiral computed tomography (CT) scan
  • No limitations to number of prior chemotherapies for metastatic disease. Treatment with prior taxanes (except Nab-Paclitaxel) is allowed as long as it has been 6 months or more since exposure to prior taxane.
  • NOTE: For subjects who are, or who have previously received endocrine therapy for breast cancer, the treating investigator will decide how many days should pass between the last dose of endocrine therapy and the first dose of study treatment.
  • All patients should have received at least one line of chemotherapy in either the advanced or adjuvant setting and hormonal therapy (where appropriate)
  • Performance status of 2 or better as per ECOG criteria (See Appendix A for details)
  • Subject is able to swallow and retain oral medicines
  • Adequate marrow and organ function as defined below (labs must be performed within 14 days of subject registration)
  • Absolute neutrophil count ≥ 1500/uL
  • Platelets 100,000/uL (no transfusion allowed within 2 weeks)
  • Hemoglobin \> 9 g/dL (which may be reached by transfusion)
  • Total bilirubin within normal range or ≤ 1.5X IULN if liver metastases are present or total bilirubin ≤ 3.0X IULN with direct bilirubin within normal range in subjects with well-documented Gilbert's Syndrome, which is defined as presence of unconjugated hyperbilirubinemia with normal results from CBC (including normal reticulocyte count and blood smear), normal liver function test results and absence of other contributing disease processes at the time of diagnosis
  • +14 more criteria

You may not qualify if:

  • Subject has any other medical or psychiatric disorder that, in the opinion of the treating physician, would contraindicate the use of drugs in this protocol or place the subject at undue risk for treatment complications
  • Subject is pregnant or lactating
  • Subject has previously been treated with Nab-Paclitaxel NOTE: Subjects who have had previous treatment with Nab-Paclitaxel will NOT be excluded if given in the adjuvant or neoadjuvant setting Only in the metastatic setting, will subjects previously treated with Nab-Paclitaxel be excluded from this trial. Exceptions may be made for subjects who discontinued treatment with a previous Nab-Paclitaxel inhibitor for reasons other than progression and as long as it has been \> 12 months since discontinuation of the previous Nab-Paclitaxel. This exception will require prior approval from the study PI at KUMC.
  • Subject has inflammatory breast cancer
  • Subject has a known hypersensitivity to any of the excipients of Nab-Paclitaxel or BYL719/alpelisib
  • Subject has a concurrent malignancy or malignancy within 3 years of study enrollment (with the exception of adequately treated, basal or squamous cell carcinoma, non-melanomatous skin cancer or curatively resected cervical cancer)
  • Subject has clinically manifest diabetes mellitus or documented steroid-induced diabetes mellitus
  • Subject has impairment of gastrointestinal (GI) function or GI disease that may significantly alter the absorption of the study drugs (e.g. ulcerative diseases, uncontrolled nausea, vomiting, diarrhea, malabsorption syndrome or small bowel resection)
  • Subject is classified into Child-Pugh class C
  • Subject has a known history of HIV infection (testing not mandatory)
  • Subject has active, uncontrolled infection
  • Subject has symptomatic/untreated CNS disease
  • Subject has ≥ Grade 2 peripheral neuropathy
  • Subject has active cardiac disease or a history of cardiac dysfunction including any of the following:
  • Unstable angina pectoris within 6 months prior to study entry
  • +19 more criteria

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (4)

University of Kansas Cancer Center

Kansas City, Kansas, 66205, United States

Location

University of Kansas Cancer Center - Overland Park

Overland Park, Kansas, 66210, United States

Location

University of Kansas Cancer Center - Lee's Summit

Lee's Summit, Missouri, 64064, United States

Location

Vanderbilt-Ingram Cancer Center

Nashville, Tennessee, 37232, United States

Location

Related Publications (1)

  • Sharma P, Abramson VG, O'Dea A, Nye L, Mayer I, Pathak HB, Hoffmann M, Stecklein SR, Elia M, Lewis S, Scott J, De Jong JA, Wang YY, Yoder R, Schwensen K, Finke K, Heldstab J, LaFaver S, Williamson SK, Phadnis MA, Reed GA, Kimler BF, Khan QJ, Godwin AK. Clinical and Biomarker Results from Phase I/II Study of PI3K Inhibitor Alpelisib plus Nab-paclitaxel in HER2-Negative Metastatic Breast Cancer. Clin Cancer Res. 2021 Jul 15;27(14):3896-3904. doi: 10.1158/1078-0432.CCR-20-4879. Epub 2021 Feb 18.

MeSH Terms

Conditions

Breast Neoplasms

Interventions

Alpelisib130-nm albumin-bound paclitaxelAlbumin-Bound Paclitaxel

Condition Hierarchy (Ancestors)

Neoplasms by SiteNeoplasmsBreast DiseasesSkin DiseasesSkin and Connective Tissue Diseases

Intervention Hierarchy (Ancestors)

PaclitaxelTaxoidsCyclodecanesCycloparaffinsHydrocarbons, AlicyclicHydrocarbons, CyclicHydrocarbonsOrganic ChemicalsDiterpenesTerpenesAlbuminsProteinsAmino Acids, Peptides, and Proteins

Results Point of Contact

Title
Dr. Priyanka Sharma
Organization
University of Kansas Medical Center

Study Officials

  • Priyanka Sharma, MD

    University of Kansas Medical Center

    PRINCIPAL INVESTIGATOR

Publication Agreements

PI is Sponsor Employee
No
Restrictive Agreement
No

Study Design

Study Type
interventional
Phase
phase 1
Allocation
NON RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
SINGLE GROUP
Sponsor Type
OTHER
Responsible Party
SPONSOR INVESTIGATOR
PI Title
Medical Doctor

Study Record Dates

First Submitted

January 30, 2015

First Posted

March 4, 2015

Study Start

February 1, 2015

Primary Completion

September 21, 2017

Study Completion

March 1, 2022

Last Updated

June 7, 2022

Results First Posted

September 28, 2021

Record last verified: 2022-05

Locations