NCT02367040

Brief Summary

The purpose of this study was to evaluate whether copanlisib in combination with rituximab is superior to placebo in combination with rituximab in prolonging progression free survival (PFS) in patients with relapsed iNHL who have received one or more lines of treatment, including rituximab and who either had a treatment-free interval of ≥ 12 months after completion of the last rituximab-containing treatment, or who are unwilling to receive chemotherapy/for whom chemotherapy is contraindicated on reason of age, comorbidities, and/or residual toxicity.

Trial Health

98
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Strong global presence with extensive site network
Enrollment
458

participants targeted

Target at P50-P75 for phase_3

Timeline
Completed

Started Aug 2015

Longer than P75 for phase_3

Geographic Reach
36 countries

184 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

February 12, 2015

Completed
8 days until next milestone

First Posted

Study publicly available on registry

February 20, 2015

Completed
5 months until next milestone

Study Start

First participant enrolled

August 3, 2015

Completed
5.1 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

August 31, 2020

Completed
1.3 years until next milestone

Results Posted

Study results publicly available

January 4, 2022

Completed
2.9 years until next milestone

Study Completion

Last participant's last visit for all outcomes

November 15, 2024

Completed
Last Updated

October 14, 2025

Status Verified

September 1, 2025

Enrollment Period

5.1 years

First QC Date

February 12, 2015

Results QC Date

August 27, 2021

Last Update Submit

September 25, 2025

Conditions

Keywords

Clinical trial, Phase IIIPhosphatidylinositol-3-kinaseNon-Hodgkin's lymphomaIndolent B-cell non-Hodgkin's lymphoma

Outcome Measures

Primary Outcomes (1)

  • Progression Free Survival (PFS) Based on Independent Central Review.

    Progression-free survival (PFS) was defined as the time from randomization to progressive disease (PD) or death due to any cause, whichever was earlier according to the Lugano Classification and Response criteria in patients affected by Waldenström macroglobulinemia (kindly refer to the links in the Protocol section).

    From first participant randomization (20-Aug-2015) up to data cut-off at primary completion (31-Aug-2020), approximately 5 years and 2-year follow-up after primary completion at 31-Aug-2022, up to 7 years and final analysis at 15-Nov-2024 up to 9 years

Secondary Outcomes (11)

  • Objective Response Rate (ORR)

    From first participant randomization (20-Aug-2015) up to data cut-off date at primary completion (31-Aug-2020), approximately 5 years and 2-year follow-up after primary completion at 31-Aug-2022, up to 7 years

  • Complete Response Rate (CRR)

    From first participant randomization (20-Aug-2015) up to data cut-off date at primary completion (31-Aug-2020), approximately 5 years and 2-year follow-up after primary completion at 31-Aug-2022, up to 7 years

  • Duration of Response (DOR)

    From first participant randomization (20-Aug-2015) up to data cut-off date at primary completion (31-Aug-2020), approximately 5 years and 2-year follow-up after primary completion at 31-Aug-2022, up to 7 years

  • Disease Control Rate (DCR)

    From first participant randomization (20-Aug-2015) up to data cut-off date at primary completion (31-Aug-2020), approximately 5 years and 2-year follow-up after primary completion at 31-Aug-2022, up to 7 years

  • Time to Progression (TTP)

    From first participant randomization (20-Aug-2015) up to data cut-off date at primary completion (31-Aug-2020), approximately 5 years and 2-year follow-up after primary completion at 31-Aug-2022, up to 7 years

  • +6 more secondary outcomes

Study Arms (2)

Copanlisib + Rituximab

EXPERIMENTAL

Combination of the Copanlisib and rituximab

Drug: Copanlisib (Aliqopa, BAY80-6946)Drug: Rituximab

Placebo + Rituximab

PLACEBO COMPARATOR

Combination of Copanlisib placebo and rituximab

Drug: PlaceboDrug: Rituximab

Interventions

Copanlisib is supplied as lyophilized preparation in a 6 mL injection vial. The total amount of copanlisib per vial is 60 mg. The solution for IV infusions is obtained after reconstitution with normal saline solution. Dosing will be administered on Days 1, 8 and 15 of each 28-day cycle. Copanlisib will be administered before rituximab.

Copanlisib + Rituximab

Placebo is supplied as lyophilized preparation in a 6 mL injection vial. The developed placebo lyophilisate is equivalent to the 60 mg copanlisib formulation, with regard to the composition of excipients and the instructions for reconstitution and dose preparation. Placebo dosing will be administered on Days 1, 8 and 15 of each 28-day cycle. Placebo will be administered before rituximab.

Placebo + Rituximab

Rituximab dose 375 mg/m2 body surface weekly during Cycle 1 on Days 1, 8, 15 and 22, and then on Day 1 of Cycles 3, 5, 7 and 9.The solution for IV infusions is obtained after reconstitution of a calculated concentration of 1 to 4 mg/ml rituximab into an infusion bag containing sterile, pyrogen-free sodium chloride 9 mg/ml (0.9%) solution for injection or 5% D-Glucose in water.

Copanlisib + RituximabPlacebo + Rituximab

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Histologically confirmed diagnosis of Indolent non-Hodgkin's lymphoma (iNHL) in CD20 positive patients, with histological subtype limited to:
  • Follicular lymphoma(FL) grade1-2-3a
  • Small lymphocytic lymphoma(SLL) with absolute lymphocyte count \<5x10\*9/L at study entry
  • Lymphoplasmacytoid lymphoma/Waldenström macroglobulinemia (LPL/WM)
  • Marginal zone lymphoma (MZL) (splenic, nodal, or extra-nodal)
  • Patients must have relapsed (recurrence after complete response or presented progression after partial response) after the last rituximab-, rituximab biosimilars-, or anti-CD20 monoclonal antibody (e.g. obinutuzumab)-containing therapy (other previous treatment lines after rituximab are allowed). A previous regimen is defined as one of the following: at least 2 months of single-agent therapy (less than 2 months of therapy is allowed for patients who responded to single-agent rituximab, rituximab biosimilars, or anti-CD20 monoclonal antibody); at least 2 consecutive cycles of polychemotherapy; autologous transplant; radioimmunotherapy. Previous exposure to PI3K is acceptable (except to copanlisib) provided there is no resistance. Patients with prior intolerance to PI3K inhibitors other than copanlisib are eligible.
  • Non-WM must have at least one bi-dimensionally measurable lesion (which has not been previously irradiated) according to the Lugano Classification. For patients with splenic MZL (Marginal-zone lymphoma) this requirement may be restricted to splenomegaly alone since that is usually the only manifestation of measurable disease.
  • Patients affected by WM who do not have at least one bi-dimensionally measurable lesion in the baseline radiologic assessment must have measurable disease, defined as presence of immunoglobulin M (IgM) paraprotein with a minimum IgM level ≥ 2 x upper limit of normal (ULN) and positive immunofixation test .
  • Male or female patients ≥ 18 years of age
  • Eastern Cooperative Oncology Group (ECOG) performance status ≤ 2
  • Life expectancy of at least 3 months
  • Availability of fresh tumor tissue and/or archival tumor tissue for central pathology(obtained within 5 years of the consent date) at Screening
  • Adequate baseline laboratory values collected no more than 7 days before starting study treatment
  • Left ventricular ejection fraction ≥ 45%
  • Patients must either:
  • +6 more criteria

You may not qualify if:

  • Histologically confirmed diagnosis of follicular lymphoma grade 3b or transformed disease, or chronic lymphocytic leukemia
  • Progression free interval or treatment free interval of less than 12 months since the last rituximab-, rituximab biosimilars-, or anti-CD20 monoclonal antibody (e.g. obinutuzumab)-containing treatment(including maintenance with these drugs). For patients considered unwilling/unfit to receive chemotherapy : progression free interval or treatment free interval of less than 6 months since the last rituximab-, rituximab biosimilars-, or anti-CD20 monoclonal antibody-containing treatment (including maintenance with these drugs), as assessed by the investigator
  • History or concurrent condition of interstitial lung disease of any severity and/or severely impaired lung function
  • Known lymphomatous involvement of the central nervous system
  • Patients with HbA1c \> 8.5% at Screening
  • Known history of human immunodeficiency virus (HIV) infection
  • Hepatitis B (HBV) or hepatitis C (HCV). Patients positive for HBsAg or HBcAb will be eligible if they are negative for HBV-DNA, these patients should receive prophylactic antiviral therapy. Patients positive for anti- HCV antibody will be eligible if they are negative for HCV-RNA
  • Documented evidence of resistance to prior treatment with idelalisib or other PI3K inhibitors.
  • Prior treatment with copanlisib
  • Cytomegalovirus (CMV) infection. Patients who are CMV PCR positive at baseline will not be eligible.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (187)

Unknown Facility

West Covina, California, 91790, United States

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Ashland, Kentucky, 41101, United States

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Louisville, Kentucky, 40207, United States

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Bethesda, Maryland, 20817, United States

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Las Vegas, Nevada, 89169, United States

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Montvale, New Jersey, 07645, United States

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MSK Basking Ridge

New Jersey, New Jersey, United States

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MSK Bergen

New Jersey, New Jersey, United States

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MSK Monmoth

New Jersey, New Jersey, United States

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MSK Westchester

Harrison, New York, United States

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MSK Commack

Long Island City, New York, United States

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MSK Rockville Centre

Long Island City, New York, United States

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New York, New York, 10065, United States

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Canton, Ohio, 44718, United States

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Salt Lake City, Utah, 84106, United States

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Spokane, Washington, 99208, United States

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Buenos Aires, Ciudad Auton. de Buenos Aires, TBC, Argentina

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Rosario, Santa Fe Province, S2000DEJ, Argentina

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San Miguel de Tucumán, Tucumán Province, T4000, Argentina

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Córdoba, X5000AOQ, Argentina

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Ballarat, Victoria, 3350, Australia

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Nedlands, 6009, Australia

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Graz, Styria, 8036, Austria

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Vienna, 1090, Austria

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Vienna, 1130, Austria

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Ottignies, 1340, Belgium

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Passo Fundo, Rio Grande do Sul, 99020-240, Brazil

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Porto Alegre, Rio Grande do Sul, 90850-170, Brazil

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Barretos/SP, São Paulo, 14784-400, Brazil

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Jaú, São Paulo, 17210-120, Brazil

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São Paulo, São Paulo, 01234-030, Brazil

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São Paulo, São Paulo, 08270-070, Brazil

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São Paulo, 05403-000, Brazil

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São Paulo, 05651-901, Brazil

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Plovdiv, 4000, Bulgaria

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Sofia, 1756, Bulgaria

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Varna, 9010, Bulgaria

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Temuco, Región de la Araucanía, 4800827, Chile

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Fuzhou, Fujian, 350000, China

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Guangzhou, Guangdong, 510000, China

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Guangzhou, Guangdong, TBC, China

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Wuhan, Hubei, 430079, China

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Nanjing, Jiangsu, 210000, China

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Suzhou, Jiangsu, 215000, China

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Nanchang, Jiangxi, 330029, China

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Changchun, Jilin, 130061, China

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Shengyang, Liaoning, 110042, China

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Chengdu, Sichuan, 610041, China

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Ürümqi, Xinjiang, 830011, China

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Hangzhou, Zhejiang, 310000, China

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Hangzhou, Zhejiang, 310022, China

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Beijing, 100000, China

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Beijing, 100050, China

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Beijing, 100083, China

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Beijing, 100730, China

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Chongqing, 400030, China

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Chongqing, 400042, China

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Shanghai, 200000, China

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Shanghai, 200025, China

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Shanghai, 200032, China

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Tianjin, 300000, China

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Tianjin, 300121, China

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Medellín, Antioquia, 050034, Colombia

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Bogota, Cundinamarca, 111511, Colombia

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Montería, Departamento de Córdoba, 230002, Colombia

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Cali, Valle del Cauca Department, 760032, Colombia

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Bayonne, 64100, France

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Brest, 29470, France

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Metz, 57085, France

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Nice, 6189, France

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Pessac, 33600, France

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Poitiers, 86021, France

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Saint-Herblain, 44800, France

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München, Bavaria, 81377, Germany

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Recklinghausen, North Rhine-Westphalia, 45659, Germany

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Dresden, Saxony, 1307, Germany

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Halle, Saxony-Anhalt, 6120, Germany

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Berlin, 10967, Germany

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Athens, 106 76, Greece

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Athens, 11527, Greece

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Chaïdári, 12462, Greece

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Pátrai, 26500, Greece

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Chai Wan, 0, Hong Kong

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Hong Kong, MISSING, Hong Kong

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Budapest, 1083, Hungary

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Győr, 9024, Hungary

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Kaposvár, 7400, Hungary

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Pécs, 7623, Hungary

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Tatabánya, 2800, Hungary

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Dublin, D07R2WY, Ireland

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Dublin, D08NHY1, Ireland

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Galway, H91YR71, Ireland

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Udine, Friuli Venezia Giulia, 33038, Italy

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Genoa, Liguria, 16132, Italy

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Milan, Lombardy, 20133, Italy

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Florence, Tuscany, 50134, Italy

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Nagoya, Aichi-ken, 464-8681, Japan

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Nagoya, Aichi-ken, 466-8650, Japan

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Maebashi, Gunma, 371-8511, Japan

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Kobe, Hyōgo, 650-0047, Japan

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Nankoku, Kochi, 783-8505, Japan

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Sendai, Miyagi, 980-8574, Japan

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Ōmura, Nagasaki, 856-8562, Japan

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Kurashiki, Okayama-ken, 710-8602, Japan

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Hirakata, Osaka, 573-1191, Japan

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Izumo, Shimane, 693-8501, Japan

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Chuo-ku, Tokyo, 104-0045, Japan

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Aomori, 030-8553, Japan

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Fukuoka, 811-1395, Japan

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Kumamoto, 860-8556, Japan

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Niigata, 951-8566, Japan

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Osaka, 545-8586, Japan

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Yamagata, 990-9585, Japan

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Kaunas, LT-50009, Lithuania

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Cheras, 56000, Malaysia

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Kota Kinabalu, 88586, Malaysia

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Kuala Lumpur, 59100, Malaysia

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Kuala Selangor, 68000, Malaysia

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Perak, 30450, Malaysia

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Pulau Pinang, 10450, Malaysia

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Morelia, Michoacán, 58260, Mexico

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Monterrey, Nuevo León, 64460, Mexico

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Tauranga, 3112, New Zealand

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City of Taguig, 1102, Philippines

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Pasig, 1605, Philippines

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Gdansk, 80-214, Poland

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Gdynia, 81-519, Poland

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Krakow, 30-727, Poland

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Lublin, 20-090, Poland

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Porto, 4200-072, Portugal

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Porto, 4434-502, Portugal

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Brasov, 500152, Romania

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Bucharest, 10825, Romania

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Bucharest, 20125, Romania

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Bucharest, 22328, Romania

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Bucharest, 30171, Romania

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Cluj-Napoca, 400015, Romania

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Craiova, 200143, Romania

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Târgu Mureş, 540136, Romania

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Chelyabinsk, 454048, Russia

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Irkutsk, 664035, Russia

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Kazan', 420029, Russia

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Kemerovo, 650066, Russia

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Kirov, 610027, Russia

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Novosibirsk, 630087, Russia

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Omsk, 644013, Russia

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Saint Petersburg, 197022, Russia

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Volgograd, 400138, Russia

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Singapore, 119074, Singapore

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Singapore, 168583, Singapore

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Singapore, 169608, Singapore

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Poprad, 058 01, Slovakia

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George, Eastern Cape, 6530, South Africa

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Johannesburg, Gauteng, 2013, South Africa

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Seoul, Seoul Teugbyeolsi, 03722, South Korea

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Seoul, Seoul Teugbyeolsi, 05505, South Korea

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Seoul, Seoul Teugbyeolsi, 3080, South Korea

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Busan, 49201, South Korea

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Busan, 49241, South Korea

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Hwasun Gun, 58128, South Korea

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Seoul, 06351, South Korea

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Majadahonda, Madrid, 28222, Spain

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Málaga, Málaga, 20910, Spain

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Barcelona, 08003, Spain

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Barcelona, 08035, Spain

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Barcelona, 8041, Spain

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Madrid, 28041, Spain

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Salamanca, 37007, Spain

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Changhua, 50006, Taiwan

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Kaohsiung City, 833, Taiwan

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Tainan, 704, Taiwan

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Taipei, 100, Taiwan

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Taipei, 11217, Taiwan

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Chiang Mai, 50200, Thailand

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Pathum Thani, 10120, Thailand

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Ankara, 6100, Turkey (Türkiye)

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Istanbul, 34093, Turkey (Türkiye)

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Izmir, 35100, Turkey (Türkiye)

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Kayseri, 38039, Turkey (Türkiye)

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Trabzon, 61080, Turkey (Türkiye)

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Cherkasy, 18009, Ukraine

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Dnipro, 49102, Ukraine

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Kyiv, 03022, Ukraine

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Lviv, 79044, Ukraine

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Vinnitsa, 21029, Ukraine

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Hà Nội, 10000, Vietnam

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Ho Chi Minh City, 70000, Vietnam

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Related Publications (2)

  • Matasar MJ, Capra M, Ozcan M, Lv F, Li W, Yanez E, Sapunarova K, Lin T, Jin J, Jurczak W, Hamed A, Wang MC, Baker R, Bondarenko I, Zhang Q, Feng J, Geissler K, Lazaroiu M, Saydam G, Szomor A, Bouabdallah K, Galiulin R, Uchida T, Soler LM, Cao A, Hiemeyer F, Mehra A, Childs BH, Shi Y, Zinzani PL. Copanlisib plus rituximab versus placebo plus rituximab in patients with relapsed indolent non-Hodgkin lymphoma (CHRONOS-3): a double-blind, randomised, placebo-controlled, phase 3 trial. Lancet Oncol. 2021 May;22(5):678-689. doi: 10.1016/S1470-2045(21)00145-5. Epub 2021 Apr 10.

  • Morcos PN, Moss J, Veasy J, Hiemeyer F, Childs BH, Garmann D. Model-Based Benefit/Risk Analysis for the Copanlisib Intermittent Dosing Regimen. Clin Pharmacol Ther. 2024 May;115(5):1092-1104. doi: 10.1002/cpt.3173. Epub 2024 Jan 16.

Related Links

MeSH Terms

Conditions

Lymphoma, Non-Hodgkin

Interventions

copanlisibRituximab

Condition Hierarchy (Ancestors)

LymphomaNeoplasms by Histologic TypeNeoplasmsLymphoproliferative DisordersLymphatic DiseasesHemic and Lymphatic DiseasesImmunoproliferative DisordersImmune System Diseases

Intervention Hierarchy (Ancestors)

Antibodies, Monoclonal, Murine-DerivedAntibodies, MonoclonalAntibodiesImmunoglobulinsImmunoproteinsBlood ProteinsProteinsAmino Acids, Peptides, and ProteinsSerum GlobulinsGlobulins

Results Point of Contact

Title
Therapeutic Area Head
Organization
Bayer AG

Study Officials

  • Bayer Study Director

    Bayer

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
LTE60
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
QUADRUPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR, OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

February 12, 2015

First Posted

February 20, 2015

Study Start

August 3, 2015

Primary Completion

August 31, 2020

Study Completion

November 15, 2024

Last Updated

October 14, 2025

Results First Posted

January 4, 2022

Record last verified: 2025-09

Data Sharing

IPD Sharing
Will not share

Availability of this study's data will later be determined according to Bayer's commitment to the EFPIA/PhRMA "Principles for responsible clinical trial data sharing". This pertains to scope, timepoint and process of data access. As such, Bayer commits to sharing upon request from qualified researchers patient-level clinical trial data, study-level clinical trial data, and protocols from clinical trials in patients for medicines and indications approved in the US and EU as necessary for conducting legitimate research. This applies to data on new medicines and indications that have been approved by the EU and US regulatory agencies on or after January 01, 2014. Interested researchers can use www.vivli.org to request access to anonymized patient-level data and supporting documents from clinical studies to conduct research. Information on the Bayer criteria for listing studies and other relevant information is provided in the member section of the portal.

Locations