NCT02202356

Brief Summary

This study will assess the safety, tolerability, pharmacokinetics (PK) and anti-viral effect of single and multiple doses of ALS-008176 in infants hospitalized with respiratory syncytial virus (RSV)

Trial Health

98
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
183

participants targeted

Target at P75+ for phase_1

Timeline
Completed

Started Jul 2014

Typical duration for phase_1

Geographic Reach
14 countries

77 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

July 23, 2014

Completed
Same day until next milestone

Study Start

First participant enrolled

July 23, 2014

Completed
6 days until next milestone

First Posted

Study publicly available on registry

July 29, 2014

Completed
3.6 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

February 15, 2018

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

February 15, 2018

Completed
Last Updated

February 3, 2025

Status Verified

January 1, 2025

Enrollment Period

3.6 years

First QC Date

July 23, 2014

Last Update Submit

January 31, 2025

Conditions

Keywords

RSVRespiratory Syncytial Virus

Outcome Measures

Primary Outcomes (5)

  • Adverse Events

    Baseline through 6 days post-dose

  • Physical Examinations

    Baseline through 6 days post-dose

  • Vital Signs

    Baseline through 6 days post-dose

  • 12-Lead ECGs

    Baseline through 6 days post-dose

  • Clinical Laboratory Results

    Baseline through 6 days post-dose

Secondary Outcomes (6)

  • RSV viral RNA concentrations in nasal aspirates

    Baseline through 6 days post-dose

  • Emergence of resistance

    Baseline through 6 days post-dose

  • Pharmacokinetic parameters, including maximum and minimum drug concentrations

    Baseline through 6 days post-dose

  • Pharmacokinetic parameters, including time to maximum concentration and half-life

    Baseline through 6 days post-dose

  • Pharmacokinetic parameters, including area under concentration-time curves (AUCs)

    Baseline through 6 days post-dose

  • +1 more secondary outcomes

Study Arms (4)

ALS-008176 Single Dose

EXPERIMENTAL

Single dose of ALS-008176 administered orally as a suspension

Drug: ALS-008176

Placebo Single Dose

PLACEBO COMPARATOR

Single dose of placebo administered orally as a suspension

Drug: Placebo

ALS-008176 Multiple Doses

EXPERIMENTAL

Multiple doses of ALS-008176 administered orally as a suspension

Drug: ALS-008176

Placebo Multiple Doses

PLACEBO COMPARATOR

Multiple doses of placebo administered orally as a suspension

Drug: Placebo

Interventions

ALS-008176 Multiple DosesALS-008176 Single Dose
Placebo Multiple DosesPlacebo Single Dose

Eligibility Criteria

AgeUp to 12 Months
Sexall
Healthy VolunteersNo
Age GroupsChild (0-17)

You may qualify if:

  • Male or female infant who is ≥1.0 to ≤12.0 months of age (inclusive), defined at the time of hospital admission, or \<28 days of age (neonate cohort only). Note: all subjects, including neonates, must have been discharged from the hospital after birth and are now being admitted due to an RSV related illness

You may not qualify if:

  • Prematurity
  • Receiving invasive endotracheal mechanical ventilation
  • Poorly functioning gastrointestinal tract
  • Anticipated to be discharged from the hospital in \<24 hours from the time of randomization
  • Prior exposure to palivizumab

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (77)

Children's of Alabama

Birmingham, Alabama, 35233, United States

Location

Arkansas Children's Hospital Research Institute

Little Rock, Arkansas, 72202, United States

Location

Long Beach Memorial Medical Center/Miller Children's and Women's Hospital of Long Beach

Long Beach, California, 90806, United States

Location

Children's Hospital of Orange County

Orange, California, 92868, United States

Location

The University of California at San Diego

San Diego, California, 92093, United States

Location

LSU Health Sciences Center

Shreveport, Louisiana, 71103, United States

Location

Massachusetts General Hospital

Boston, Massachusetts, 02114, United States

Location

The Children's Mercy

Kansas City, Missouri, 64108, United States

Location

University of Rochester

Rochester, New York, 14611, United States

Location

The University of North Carolina at Chapel Hill

Chapel Hill, North Carolina, 27599, United States

Location

Duke University

Durham, North Carolina, 27708, United States

Location

The Research Institute at Nationwide Children's Hospital

Columbus, Ohio, 43205, United States

Location

Children's Hospital/University of Tennessee

Memphis, Tennessee, 38103, United States

Location

UT Southwestern Medical Center

Dallas, Texas, 75390, United States

Location

Texas Children's Hospital/Baylor College of Medicine

Houston, Texas, 77030, United States

Location

The University of Utah

Salt Lake City, Utah, 84112, United States

Location

Seattle Children's Hospital

Seattle, Washington, 98105, United States

Location

The Canberra Hospital

Canberra, Australia

Location

Monash Medical Center

Melbourne, Australia

Location

Women's and Children's Hospital

North Adelaide, Australia

Location

The Royal Children's Hospital Melbourne

Parkville, Australia

Location

Princess Margaret Hospital

Perth, Australia

Location

The Children's Hospital Research Institute of Manitoba

Winnipeg, Manitoba, Canada

Location

Canadian Centre for Vaccinology IWK Health Centre

Halifax, Nova Scotia, Canada

Location

McMaster Children's Hospital

Hamilton, Ontario, Canada

Location

McGill University Health Centre

Montreal, Quebec, Canada

Location

Hospital Dr. Exequiel Gonzalez Cortes

San Miguel, Santiago Metropolitan, Chile

Location

Complejo Asistencial Dr Sotero del Rio

Santiago, Chile

Location

Hospital Padre Hurtado

Santiago, Chile

Location

Fundacion Cardio Infantil Instituto de Cardiologia

Bogotá, Colombia

Location

Hospital Pablo Tobon Uribe

Medellín, Colombia

Location

CHU Pellegrin / Pneumologie pediatrique

Bordeaux, France

Location

Hopital Necker

Paris, France

Location

Hirosaki National Hospital

Hirosaki-shi, Aomori, Japan

Location

Chiba Children's Hospital

Chiba, Chiba, Japan

Location

Ota Memorial Hospital

Ōta, Gunma, 373-8585, Japan

Location

Gunma Children's Medical Center

Shibukawa-shi, Gunma, Japan

Location

NHO Fukuyama Medical Center

Fukuyama, Hiroshima, Japan

Location

Hokkaido P.W.F.A.C. Asahikawa-Kosei General Hospital

Asahikawa-shi, Hokkaido, Japan

Location

NHO Kanazawa Medical Center

Kanazawa, Ishikawa-ken, Japan

Location

NHO Shikoku Medical Center for Children and Adults

Takamatsu, Kagawa-ken, Japan

Location

Okinawa Chubu Hospital

Urumi, Okinawa, Japan

Location

Nakano Children's Hospital

Osaka, Osaka, Japan

Location

National Hospital Organization Saitama National Hospital

Wako, Saitama, 351-0102, Japan

Location

Tokyo Metropolitan Children's Medical Center

Fuchu-shi, Tokyo, Japan

Location

National Center for Child Health and Development

Setagaya-ku, Tokyo, Japan

Location

Fukuoka Children's Hospital

Fukuoka, Japan

Location

NHO Fukuoka Hospital

Fukuoka, Japan

Location

Kochi Health Sciences Center

Kochi, 781-8555, Japan

Location

Saitama Children's Medical Center

Saitama, Japan

Location

Christchurch Clinical Study Trust

Christchurch, New Zealand

Location

Hawke's Bay Hospital

Hastings, New Zealand

Location

Wellington Hospital

Wellington, New Zealand

Location

Hospital Materno Infantil Jose Dominog de Obaldila

David, Chiriquí Province, Panama

Location

Hospital de Especialidades Pediatricas "Omar Torrijos Herrera"

Panama City, Panama

Location

Hospital del Nino

Panama City, Panama

Location

Institute for Mother and Child Care "Alfred Rusescu"

Bucharest, Romania

Location

2 Military Hospital

Cape Town, South Africa

Location

Kingsbury Hospital

Cape Town, South Africa

Location

Tygerberg Academic Hospital

Cape Town, South Africa

Location

Linkou Chang Gung Medical Hospital

Taipei, Taiwan

Location

MacKay Memorial Hospital

Taipei, Taiwan

Location

Chulalongkorn University Department of Pediatrics

Bangkok, Thailand

Location

Phramongkutklao Hospital Department of Pediatrics

Bangkok, Thailand

Location

Siriraj Hospital, Mahidol University Department of Pediatrics

Bangkok, Thailand

Location

Khon Kaen University Department of Pediatrics

Khon Kaen, Thailand

Location

Bristol Royal Hospital for Children

Bristol, England, United Kingdom

Location

Alder Hey Children's Hospital

Liverpool, England, United Kingdom

Location

St. George's University of London

London, England, United Kingdom

Location

University Hospital Southampton NHS Foundation Trust

Southampton, England, United Kingdom

Location

Royal Hospital for Sick Children

Edinburgh, Scotland, United Kingdom

Location

Children's Hospital of Wales

Cardiff, Wales, United Kingdom

Location

Birmingham Children's Hospital

Birmingham, United Kingdom

Location

Royal Alexandra Children's Hospital

Brighton, United Kingdom

Location

Royal Manchester Children's Hospital

Manchester, United Kingdom

Location

Queens Medical Center

Nottingham, United Kingdom

Location

University of Oxford

Oxford, United Kingdom

Location

Related Publications (1)

  • Oey A, McClure M, Symons JA, Chanda S, Fry J, Smith PF, Luciani K, Fayon M, Chokephaibulkit K, Uppala R, Bernatoniene J, Furuno K, Stanley T, Huntjens D, Witek J; 503 and RSV2004 Study Groups. Lumicitabine, an orally administered nucleoside analog, in infants hospitalized with respiratory syncytial virus (RSV) infection: Safety, efficacy, and pharmacokinetic results. PLoS One. 2023 Jul 19;18(7):e0288271. doi: 10.1371/journal.pone.0288271. eCollection 2023.

MeSH Terms

Conditions

Respiratory Syncytial Virus Infections

Interventions

4'-chloromethyl-2'-deoxy-3',5'-di-O-isobutyryl-2'-fluorocytidine

Condition Hierarchy (Ancestors)

Pneumovirus InfectionsParamyxoviridae InfectionsMononegavirales InfectionsRNA Virus InfectionsVirus DiseasesInfections

Study Officials

  • Matthew McClure, M.D.

    Alios BioPharma

    STUDY DIRECTOR

Study Design

Study Type
interventional
Phase
phase 1
Allocation
RANDOMIZED
Masking
QUADRUPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR, OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

July 23, 2014

First Posted

July 29, 2014

Study Start

July 23, 2014

Primary Completion

February 15, 2018

Study Completion

February 15, 2018

Last Updated

February 3, 2025

Record last verified: 2025-01

Locations