NCT02138734

Brief Summary

This is a Phase Ib/IIb, randomized, two-cohort, open-label, multicenter study of intravesical N-803 plus BCG versus BCG alone, in BCG naïve patients with high-grade NMIBC.

Trial Health

78
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
369

participants targeted

Target at P75+ for phase_1

Timeline
156mo left

Started Jul 2014

Longer than P75 for phase_1

Geographic Reach
3 countries

108 active sites

Status
active not recruiting

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Progress48%
Jul 2014Mar 2039

First Submitted

Initial submission to the registry

May 13, 2014

Completed
2 days until next milestone

First Posted

Study publicly available on registry

May 15, 2014

Completed
2 months until next milestone

Study Start

First participant enrolled

July 21, 2014

Completed
12.2 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

September 30, 2026

Expected
12.4 years until next milestone

Study Completion

Last participant's last visit for all outcomes

March 4, 2039

Last Updated

March 31, 2026

Status Verified

March 1, 2026

Enrollment Period

12.2 years

First QC Date

May 13, 2014

Last Update Submit

March 26, 2026

Conditions

Keywords

antitumorBCGbladder cancercancerimmunotherapyinstillationinterleukin-15intravesicalnaivenon-muscle invasivetransitional cell carcinomaALT-803N-803

Outcome Measures

Primary Outcomes (2)

  • Complete Response (CR) Rate

    Patients in Cohort A: compare complete response rate between treatment arms using cystoscopy, confirmatory bladder biopsy and urine cytology.

    6 Months

  • Disease Free Survival (DFS)

    Patients in Cohort B: compare disease-free survival between treatment arms using cystoscopy, confirmatory bladder biopsy and urine cytology.

    13 Years and 3 Months

Secondary Outcomes (14)

  • Progression-free survival (PFS)

    13 Years and 3 Months

  • Overall survival

    13 Years and 3 months

  • Disease specific survival

    13 Years and 3 months

  • Time to disease worsening

    13 Years and 3 Months

  • Cystectomy Free Rate

    13 years and 3 months

  • +9 more secondary outcomes

Other Outcomes (3)

  • Exploratory Endpoints- Immunogenicity: Serum level of anti-N-803 in patient samples

    36 Months

  • Quality of Life Endpoint

    39 Months

  • Exploratory Endpoints- Whole Slide Images (Baseline and any on-study biopsy)

    39 Months

Study Arms (2)

N-803+BCG

EXPERIMENTAL

(Phase Ib and IIb) for BCG-naive patients

Biological: BCG (50mg/instillation) + N-803 (400 μg/instillation)

BCG alone

ACTIVE COMPARATOR

(Phase IIb) for BCG-naive patients

Biological: BCG (50mg/instillation)

Interventions

BCG will be administered via intravesical instillation weekly for 6 consecutive weeks for induction. Phase IIb includes maintenance treatment consisting of BCG for 3 consecutive weeks at 3, 6, 12, 18, 24, 30 and 36 months. An additional 6-week re-induction of BCG for patients with eligible disease at 3 months in phase IIb is included.

BCG alone

BCG and N-803 will be mixed together (with saline) and administered via intravesical instillation weekly for 6 consecutive weeks for induction. Phase IIb includes maintenance treatment consisting of BCG+N-803 for 3 consecutive weeks at 3, 6, 12, 18, 24, 30 and 36 months. An additional 6-week re-induction of BCG+N-803 for patients with eligible disease at 3 months in phase IIb is included.

N-803+BCG

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Histologic confirmation of non-muscle invasive bladder cancer of the transitional cell carcinoma high-grade subtype (mixed histology tumors allowed if transitional cell histology is predominant histology).
  • Cohort A: Histologically confirmed CIS (with or without Ta/T1 disease); Cohort B: Histologically confirmed high-grade papillary disease (Ta/T1 only).
  • Patients are eligible if the diagnostic biopsy was done within 3 months of treatment start and a cystoscopy demonstrating no resectable disease was done within 6 calendar weeks (inclusive of 48 days) of treatment start (residual CIS is acceptable; patients with T1 disease must undergo repeat resection if muscularis propria is not present in each biopsy sample). Patients with high-grade Ta and/or T1 disease should have complete resection before study treatment.
  • Upper tract imaging within 6 months prior to study entry must not be suspicious for upper tract malignancy.
  • Currently eligible for intravesical BCG therapy.
  • Age ≥ 18 years.
  • Performance status: ECOG performance status of 0, 1, or 2.
  • BCG-naive disease as defined as either of the following:
  • Have not received prior intravesical BCG; or
  • Previously received BCG, but stopped receiving more than 3 years before date of randomization.
  • Laboratory tests performed within 21 days of treatment start:
  • Absolute lymphocyte count ≥ Institutional lower limit of normal
  • Absolute neutrophil count (AGC/ANC) ≥ 1,000/μL
  • Platelets ≥ 100,000/µL \[Patients may be transfused to meet this requirement\]
  • Hemoglobin ≥ 8 g/dL \[Patients may be transfused to meet this requirement\]
  • +8 more criteria

You may not qualify if:

  • Prior BCG treatment or known hypersensitivity to BCG. Patients who have received more than a single-dose post-operative treatment of mitomycin-C or gemcitabine following the most recent screening TURBT/biopsy are excluded.
  • Concurrent use of other investigational agents (not including FDA-authorized drugs for the prevention and treatment of COVID-19).
  • History of or evidence of muscle-invasive, locally advanced, metastatic and/or extravesical bladder cancer or any other cancer within the past 5 years, except: adequately treated basal cell or squamous cell skin cancer, in situ cervical cancer, adequately treated stage 1 or 2 cancer from which the patient is currently in complete remission, or stable prostate cancer (under active surveillance or hormone control).
  • Symptomatic congestive heart failure (CHF), NYHA (New York Heart Association) Class III or IV or other clinical signs of severe cardiac dysfunction.
  • Severe/unstable angina pectoris, or myocardial infarction within 6 months prior to study entry.
  • History or evidence of uncontrollable CNS disease.
  • Known HIV-positive.
  • Active systemic infection requiring parenteral antibiotic therapy. All prior infections must have resolved following optimal therapy.
  • Concurrent febrile illness, active urinary tract infection, active tuberculosis, a history of hypotension or anaphylactic reactions.
  • Ongoing chronic systemic steroid therapy required (\>10 mg oral prednisone daily or equivalent).
  • Women who are pregnant or nursing. Female patients of childbearing potential must have a negative pregnancy test and must adhere to using a medically acceptable method of birth control prior to screening and agree to continue its use during the study and for 30 days after the last dose of study drug, or be surgically sterilized (e.g., hysterectomy or tubal ligation). Women of childbearing potential are defined as any female who has experienced menarche and who is NOT permanently sterile or postmenopausal. Postmenopausal is defined as 12 consecutive months with no menses without an alternative medical cause. Males must agree to use barrier methods of birth control while on study and for 90 days post last dose of study drug.
  • Psychiatric illness/social situations that would limit compliance with study requirements.
  • Other illness that in the opinion of the investigator would exclude the patient from participating in this study.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (108)

University of Alabama at Birmingham

Birmingham, Alabama, 35294, United States

Location

Alaska Clinical Research Center

Anchorage, Alaska, 99503, United States

Location

Mayo Clinic

Phoenix, Arizona, 85054, United States

Location

Center for Neurosciences

Tucson, Arizona, 85718, United States

Location

Arkansas Urology

Little Rock, Arkansas, 72211, United States

Location

Hoag Memorial Hospital Presbyterian

Irvine, California, 92618, United States

Location

University of Southern California

Los Angeles, California, 90033, United States

Location

UCLA Department of Urology

Los Angeles, California, 90095, United States

Location

University of California, Irvine Medical Center

Orange, California, 92868, United States

Location

University of California, Davis

Sacramento, California, 95817, United States

Location

Golden State Urology

Sacramento, California, 95823, United States

Location

University of California San Diego

San Diego, California, United States

Location

Skyline Sherman Oaks

Sherman Oaks, California, 91411, United States

Location

Skyline Urology

Torrance, California, 90505, United States

Location

Eastern Connecticut Hematology & Oncology Associates

Norwich, Connecticut, 06360, United States

Location

Memorial Healthcare System

Hollywood, Florida, 33021, United States

Location

Mayo Clinic

Jacksonville, Florida, 32224, United States

Location

Advanced Urology Institute

Oxford, Florida, 34484, United States

Location

Clinical Research Center of Florida

Pompano Beach, Florida, 33060, United States

Location

Florida Urology Partners

Riverview, Florida, 33578, United States

Location

Moffitt Cancer Center

Tampa, Florida, 33612, United States

Location

Emory University

Atlanta, Georgia, 30322, United States

Location

Georgia Urology

Atlanta, Georgia, 30328, United States

Location

University of Hawaii Cancer Center

Honolulu, Hawaii, 96813, United States

Location

Associated Urological Specialists

Chicago, Illinois, 60415, United States

Location

Northwestern University

Chicago, Illinois, 60611, United States

Location

Rush University

Chicago, Illinois, 60612, United States

Location

UroPartners, LLC.

Glenview, Illinois, 60026, United States

Location

Urology of Indiana

Carmel, Indiana, 46032, United States

Location

Kansas University Medical Center

Westwood, Kansas, 66205, United States

Location

Wichita Urology

Wichita, Kansas, 67226, United States

Location

University of Kentucky Markey Cancer Center

Lexington, Kentucky, 40508, United States

Location

Mary Bird Perkins Cancer Center

Metairie, Louisiana, 70002, United States

Location

Anne Arundel Urology

Annapolis, Maryland, 21401, United States

Location

Greater Boston Urology

Plymouth, Massachusetts, 02360, United States

Location

Karmanos Cancer Institute

Detroit, Michigan, 48201, United States

Location

Comprehensive Urology

Royal Oak, Michigan, 48703, United States

Location

Mayo Clinic

Rochester, Minnesota, 55905, United States

Location

Minnesota Urology

Woodbury, Minnesota, 55125, United States

Location

Specialty Clinical Research of St. Louis

St Louis, Missouri, 63141, United States

Location

Adult & Pediatric Urology

Omaha, Nebraska, 68114, United States

Location

Dartmouth-Hitchcock Medical Center

Lebanon, New Hampshire, 03756, United States

Location

Summit Health

Florham Park, New Jersey, 07932, United States

Location

Urology Group of New Mexico (AccumetRx Clinical Research)

Albuquerque, New Mexico, 87109, United States

Location

Winthrop University Hospital

Mineola, New York, 11501, United States

Location

Integrated Medical Professionals

New York, New York, 10016, United States

Location

NYU Langone Health

New York, New York, 10016, United States

Location

Premier Medical Group of the Hudson Valley

Poughkeepsie, New York, 12601, United States

Location

Associated Medical Professionals of NY

Syracuse, New York, 13210, United States

Location

University of North Carolina Chapel Hill

Chapel Hill, North Carolina, 27278, United States

Location

Associated Urologists of North Carolina

Raleigh, North Carolina, 27612, United States

Location

Dayton Physicians Network

Centerville, Ohio, 45459, United States

Location

The Urology Group

Cincinnati, Ohio, 45212, United States

Location

University of Cincinnati Cancer Center

Cincinnati, Ohio, 45267, United States

Location

The Cleveland Clinic Foundation

Cleveland, Ohio, 44195, United States

Location

Central Ohio Urology Group

Gahanna, Ohio, 43230, United States

Location

MidLantic Urology

Bala-Cynwyd, Pennsylvania, 19004, United States

Location

Thomas Jefferson University Hospital

Philadelphia, Pennsylvania, 19141, United States

Location

Lowcountry Urology Clinics

North Charleston, South Carolina, 29406, United States

Location

Erlanger Health

Chattanooga, Tennessee, 37403, United States

Location

Urology Associates, PC

Nashville, Tennessee, 37209, United States

Location

Urology Partners of North Texas

Arlington, Texas, 76017, United States

Location

Texas Oncology

Austin, Texas, 78705, United States

Location

Urology Austin, PLLC

Austin, Texas, 78745, United States

Location

Houston Metro Urology

Houston, Texas, 77027, United States

Location

Urology San Antonio

San Antonio, Texas, 78229, United States

Location

Potomac Urology

Alexandria, Virginia, 22311, United States

Location

Virginia Urology

Richmond, Virginia, 23235, United States

Location

Virginia Commonwealth University

Richmond, Virginia, 23298, United States

Location

Urology of Virginia

Virginia Beach, Virginia, 23462, United States

Location

University of Washington School of Medicine

Seattle, Washington, 98195, United States

Location

Spokane Urology

Spokane, Washington, 99202, United States

Location

HCG Cancer Centre

Visakhapatnam, Andhra Pradesh, 530040, India

Location

Adyar Cancer Institute

Adyār, Chennai, 600036, India

Location

HCG Aastha Cancer Centre

Ahmedabad, Gujarat, 380060, India

Location

Darakh Nursing Home and Kidney Stone Centre

Aurangabad, Maharashtra, 431001, India

Location

Kidney Centre Jasleen Hospital

Nagpur, Maharashtra, 440012, India

Location

Indriyani Hospital & Cancer Institute

Pune, Maharashtra, 412105, India

Location

HCG Manavata Cancer Centre

Mumbai, Nashik, 422002, India

Location

BLK-Max Super Specialty Hospital

New Delhi, National Capital Territory of Delhi, 1100005, India

Location

All India Institute of Medical Sciences,

Bhubaneswar, Odisha, 751019, India

Location

Sri Guru Ram Das Institute of Medical Sciences and Research

Amritsar, Punjab, 143501, India

Location

Urocare Hospital

Guntur, Rajkort, 360002, India

Location

Erode Cancer Centre

Erode, Tamilnadu. India, 638012, India

Location

Pi Health Cancer Hospital

Hyderabad, Telangana, 500032, India

Location

Max Super Specialty Hospital

Ghaziabad, Uttar Pardesh, 201012, India

Location

Pushpanjali Hospital & Research Centre

Agra, Uttar, 282002, India

Location

Swami Harshankaranand JI Hospital and Research Centre

Sunderpur, Varanasi, 221005, India

Location

Govt. Medical College, Kolkata

Kolkata, West Bengal, 700073, India

Location

B J Medical College & Civil Hospital, Asarwa, Ahmedaba

Ahmedabad, India

Location

Basavatarakam Indo American Cancer Hospital & Research Institute

Banjara Hills, India

Location

HCG Bangalore

Bengaluru, 560027, India

Location

SP Medical College and Hospital

Bikaner, 334003, India

Location

Guru Govnid Singh Medical College and Hospital

Farīdkot, 151203, India

Location

Muljibhai Patel Urological Hospital

Gujrāt, India

Location

Binayak Multispecialty Hospital

Kolkata, 700050, India

Location

Chittaranjan National Cancer Institute

Kolkata, India

Location

KR Hospital

Mysuru, 570001, India

Location

KMC Manipal

Nagar, 576104, India

Location

Jasleen Hospital

Nagpur, 440012, India

Location

Onco Life Cancer Center

Pune, 410506, India

Location

Inamdar Hospital Pune

Pune, 411040, India

Location

Urocare Hospital

Rajkot, India

Location

All India Institute of Medical Sciences, Raipur

Rajpura, 492099, India

Location

Uttar Pradesh University of Medical Sciences

Uttar, India

Location

HCG cancer Centre, Vizag

Visakhapatnam, 530040, India

Location

Apollo Vizag

Visakhapatnam, India

Location

SunningHill Hospital

Sandton, 2191, South Africa

Location

Related Publications (1)

  • Chamie K, Chang SS, Rosser CJ, Kramolowski E, Gonzalgo ML, Sexton WJ, Spilman P, Sender L, Reddy S, Soon-Shiong P. N-803 Plus BCG Treatment for BCG-Naive or -Unresponsive Non-Muscle Invasive Bladder Cancer: A Plain Language Review. Future Oncol. 2024;20(31):2307-2317. doi: 10.1080/14796694.2024.2363744. Epub 2024 Jul 2.

MeSH Terms

Conditions

Non-Muscle Invasive Bladder NeoplasmsUrinary Bladder NeoplasmsNeoplasmsCarcinoma, Transitional Cell

Interventions

ALT-803

Condition Hierarchy (Ancestors)

CarcinomaNeoplasms, Glandular and EpithelialNeoplasms by Histologic TypeUrologic NeoplasmsUrogenital NeoplasmsNeoplasms by SiteFemale Urogenital DiseasesFemale Urogenital Diseases and Pregnancy ComplicationsUrogenital DiseasesUrinary Bladder DiseasesUrologic DiseasesMale Urogenital Diseases

Study Officials

  • Bobby Reddy, MD

    ImmunityBio, Inc.

    STUDY DIRECTOR

Study Design

Study Type
interventional
Phase
phase 1
Allocation
RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
PARALLEL
Model Details: Single arm phase Ib. Two-arm phase IIb, two-cohort: each randomized 1:1 via randomization scheme stratified by disease and ECOG status. Cohort A: patients with CIS disease (with or without Ta/T1); planned enrollment = 366 Cohort B: patients with high-grade papillary disease (Ta/T1 only); planned enrollment = 230
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

May 13, 2014

First Posted

May 15, 2014

Study Start

July 21, 2014

Primary Completion (Estimated)

September 30, 2026

Study Completion (Estimated)

March 4, 2039

Last Updated

March 31, 2026

Record last verified: 2026-03

Locations