NCT02105948

Brief Summary

This is a multi-center, randomized, placebo-controlled, double-blind, parallel group trial evaluating mepolizumab 100 mg against placebo given every 4 weeks through subcutaneous (SC) injection. In severe COPD patients, sputum eosinophils levels are elevated similar as those seen in severe asthmatics. It is hypothesized that the reduction of eosinophils with mepolizumab in COPD patients would translate into a reduction of COPD exacerbations. The study will determine the reduction in exacerbations in subjects who are above and below the baseline blood eosinophil count of at least 150 cells/microlitres. The study will evaluate the efficacy and safety of mepolizumab on the frequency of moderate and severe exacerbations in COPD subjects at high risk of exacerbations, despite the use of optimized standard of care background therapy. Overall in this study, a total of 800 subjects will be randomised in 1:1 ratio to receive placebo or mepolizumab (100 milligram (mg)) administered SC. The total duration of this study will be approximately 62 weeks, consisting of a 1 to 2 week screening period, 52-week treatment period and 8-week follow-up period.

Trial Health

98
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Strong global presence with extensive site network
Enrollment
837

participants targeted

Target at P75+ for phase_3

Timeline
Completed

Started Apr 2014

Typical duration for phase_3

Geographic Reach
15 countries

108 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

April 3, 2014

Completed
4 days until next milestone

First Posted

Study publicly available on registry

April 7, 2014

Completed
8 days until next milestone

Study Start

First participant enrolled

April 15, 2014

Completed
2.8 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

January 17, 2017

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

January 17, 2017

Completed
1.2 years until next milestone

Results Posted

Study results publicly available

April 6, 2018

Completed
Last Updated

August 31, 2018

Status Verified

August 1, 2018

Enrollment Period

2.8 years

First QC Date

April 3, 2014

Results QC Date

January 15, 2018

Last Update Submit

August 2, 2018

Conditions

Keywords

eosinophilsSB240563exacerbationsChronic Obstructive Pulmonary Diseasemepolizumab

Outcome Measures

Primary Outcomes (2)

  • Rate of Moderate or Severe Exacerbations in Participants in the High Stratum

    Moderate exacerbations are defined as clinically significant exacerbations that require treatment with oral/systemic corticosteroids and/or antibiotics. Severe exacerbations are defined as clinically significant exacerbations that require in-patient hospitalization ( \>= 24 hours) or result in death. Moderate and severe exacerbations occurring from the start of investigational product (IP) up to the Week 52 visit, including exacerbations reported after early discontinuation from investigational product by subjects who remained in the study, were included in the analysis. The analysis was performed on the mITT high stratum (mITT-H) Population which comprised of participants in the mITT Population (all randomized participants who received at least one dose of study treatment) with blood eosinophil counts \>=150 cells/µL at Screening or \>=300 cells/ µL in the 12 months prior.

    From randomization to Week 52

  • Rate of Moderate or Severe Exacerbations in the mITT Population

    Moderate and severe exacerbations occurring from the start of IP up to the Week 52 visit, including exacerbations reported after early discontinuation from IP by participants who remained in the study, were included in the analysis. The analysis was performed on the mITT Population which comprised of all randomized participants who received at least one dose of trial medication. The strata were combined as pre-specified in the protocol and reporting and analysis plan (RAP).

    From randomization to Week 52

Secondary Outcomes (8)

  • Time to First Moderate/Severe Exacerbation in Participants in the High Stratum

    From randomization to Week 52

  • Rate of COPD Exacerbations Requiring an Emergency Department (ED) Visit and/or Hospitalization (Hosp.) in Participants in the High Stratum

    From randomization to Week 52

  • Change From Baseline in Mean Total St. George's Respiratory Questionnaire (SGRQ) Score in Participants in the High Stratum

    Baseline and Week 52

  • Change From Baseline in Mean COPD Assessment Test (CAT) Score in Participants in the High Stratum

    Baseline and Week 52

  • Time to First Moderate/Severe Exacerbation in the mITT Population

    From randomization to Week 52

  • +3 more secondary outcomes

Study Arms (2)

Arm 1

EXPERIMENTAL

Each subject will receive 100 mg mepolizumab SC injection every 4 weeks (13 administrations during 52 week treatment period) along with optimized standard of care background therapy.

Drug: Mepolizumab

Arm 2

PLACEBO COMPARATOR

Each subject will receive placebo (0.9% sodium chloride) SC injection every 4 weeks (13 administrations during 52 week treatment period) along with optimized standard of care background therapy.

Drug: Placebo

Interventions

Humanised IgG antibody (IgG1, kappa) with human heavy and light chain frameworks, provided as a lyophilised cake in sterile vial. Vial to be reconstituted with Sterile Water for Injection, just prior to use.

Arm 1

Sterile 0.9% sodium chloride solution

Arm 2

Eligibility Criteria

Age40 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • COPD diagnosis: Subjects with a clinically documented history of COPD for at least 1 year in accordance with the definition by the American Thoracic Society/European Respiratory Society.
  • Severity of COPD: Subjects must present with the following: a measured pre and post-salbutamol Forced expiratory volume in one second/ Forced vital capacity (FEV1/FVC) ratio of \<0.70 at Visit 1 to confirm the diagnosis of COPD; a measured post-salbutamol FEV1\>20 percent and \<=80 percent of predicted normal values calculated using National Health and Nutrition Examination Survey (NHANES) III reference equations at Visit 1.
  • History of exacerbations: A well documented history (like medical record verification) in the 12 months prior to Visit 1 of: at least two moderate COPD exacerbations. Moderate is defined as the use of systemic corticosteroids (IM, intravenous, or oral) and/or treatment with antibiotics, or at least one severe COPD exacerbation. Severe is defined as having required hospitalization. Note: At least one exacerbation must have occurred while the subject was taking Inhaled corticosteroid (ICS) plus long acting beta2-agonist (LABA) plus long acting muscarinic antagonist (LAMA). Note: Prior use of antibiotics alone does not qualify as a moderate exacerbation unless the use was specifically for the treatment of worsening symptoms of COPD.
  • Concomitant COPD therapy: A well documented requirement for optimized standard of care (SoC) background therapy that includes ICS plus 2 additional COPD medications (i.e., triple therapy) for the 12 months prior to Visit 1 and meets the following criteria: Immediately prior to Visit 1, minimum of 3 months of use of an inhaled corticosteroid (at a dose \>=500 micrograms (mcg)/day fluticasone propionate dose equivalent plus); or LABA and LAMA.
  • For subjects who are not continually maintained on ICS plus LABA plus LAMA for the entire 12 months prior to Visit 1 use of following is allowed (but not in the 3 months immediately prior to Visit 1): inhaled corticosteroid at a dose \>=500 mcg/day fluticasone propionate dose equivalent plus ; a LABA or a LAMA and use of at least one other class of COPD medication suggested by the 2013 Global Initiative for Chronic Obstructive Lung Disease (GOLD) guidelines for patients who are prone to exacerbation (i.e., phosphodiesterase-4-inhibitors, methylxanthines, or a combination of short acting beta-2-agonist and short acting muscarinic antagonist). Note: Subjects must be willing to stay on their SoC COPD medication for the duration of the study.
  • Informed Consent: Able to give written informed consent prior to participation in the study, which will include the ability to comply with the requirements and restrictions listed in the consent form. Subjects must be able to read, comprehend, and write at a level sufficient to complete study related materials.
  • Gender: Male or Eligible Female; To be eligible for entry into the study females of child bearing potential must commit to consistent and correct use of an acceptable method of birth control from the time of consent, for the duration of the trial, and for 4 months after last study drug administration.
  • Age: At least 40 years of age at Visit 1.
  • Smoking status: Subject with confirmed COPD are eligible to participate independent of their smoking status and smoking history, i.e. current smokers, never smokers or ex-smokers can be enrolled into the study; Current smokers are defined as those with a history of cigarette smoking of \>=10 pack-years \[number of pack years = (number of cigarettes per day / 20) x number of years smoked (e.g., 20 cigarettes per day for 10 years, or 10 cigarettes per day for 20 years)\]; Former smokers are defined as those who meet the definition of a current smoker but have stopped smoking for at least 6 months prior to Visit 1; Never smokers are those that do not meet the definition of a current or former smoker.

You may not qualify if:

  • COPD stability: Subjects with pneumonia, exacerbation, lower respiratory infection within the 4 weeks prior to Visit 1.
  • Lung resection: Subjects with lung volume reduction surgery within the 12 months prior to Visit 1.
  • Pulmonary rehabilitation program: Participation in the acute phase of a pulmonary rehabilitation program within 4 weeks prior to Visit 1. Subjects who are in the maintenance phase of a pulmonary rehabilitation program are not excluded.
  • Oxygen: Subjects receiving treatment with oxygen more than 4.0 Litres/minute (L/min). While breathing supplemental oxygen, subjects should demonstrate an oxyhemoglobin saturation greater than or equal to 89 percent.
  • lead Electrocardiography (ECG) finding: An abnormal and significant ECG finding from the 12-lead ECG conducted at Visit 1 if considered to be clinically significant by the Investigator. 12-lead ECGs will be over-read by a centralized independent cardiologist to assist in consistent evaluation of subject eligibility. Results from the 12-lead ECG over-read must be received prior to assessing eligibility at Visit 2.
  • Unstable or life threatening cardiac disease: Subjects with any of the following would be excluded: Myocardial infarction or unstable angina in the last 6 months ; Unstable or life threatening cardiac arrhythmia requiring intervention in the last 3 months; New York Heart Association (NYHA) Class IV Heart failure.
  • Other diseases/abnormalities: Subjects with (historical or) current evidence of clinically significant, neurological, psychiatric, renal, hepatic, immunological, endocrine (including uncontrolled diabetes or thyroid disease) or haematological abnormalities that are uncontrolled. Significant is defined as any disease that, in the opinion of the investigator, would put the safety of the subject at risk through participation, or which would affect the efficacy or safety analysis if the disease/condition exacerbated during the study.
  • Eosinophilic disease: Subjects with other conditions that could lead to elevated eosinophils such as Hypereosinophilic syndromes including Eosinophilic Granulomatosis with Polyangiitis (EGPA, also known as Churg-Strauss Syndrome), or Eosinophilic Esophagitis.
  • Parasitic infection: Subjects with a pre-existing helminthes infestation within 6 months prior to Visit 1 are also excluded.
  • Malignancy: A current malignancy or previous history of cancer in remission for less than 12 months prior to Visit 1 (Subjects that had localized carcinoma of the skin or cervix which was resected for cure will not be excluded). Note for South Korea: Korean subjects with a diagnosis of malignancy within 5 years of Visit 1 are excluded.
  • Immunodeficiency: A known immunodeficiency e.g. human immunodeficiency virus (HIV), other than that explained by the use of corticosteroids taken for COPD.
  • Liver disease: Unstable liver disease (as defined by the presence of ascites, encephalopathy, coagulopathy, hypoalbuminaemia, esophageal or gastric varices, or persistent jaundice), cirrhosis, and known biliary abnormalities (with the exception of Gilbert's syndrome or asymptomatic gallstones). Chronic stable hepatitis B and C are acceptable if subject otherwise meets entry criteria (e.g. presence of hepatitis B surface antigen or positive hepatitis C test result within 3 months of screening).
  • Monoclonal antibodies: Subjects who have received any monoclonal antibody within 5 half-lives of Visit 1.
  • Investigational medications: Subjects who have received an investigational drug within 30 days of Visit 1, or within 5 drug half-lives of the investigational drug, whichever is longer (this also includes investigational formulations of a marketed product).
  • Hypersensitivity: Subjects with a known allergy or intolerance to another monoclonal antibody or biologic including history of anaphylaxis to another biologic
  • +15 more criteria

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (116)

GSK Investigational Site

Newport Beach, California, 92663, United States

Location

GSK Investigational Site

Rochester, Minnesota, 55905, United States

Location

GSK Investigational Site

Saint Charles, Missouri, 63301, United States

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GSK Investigational Site

New York, New York, 10029, United States

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GSK Investigational Site

Charlotte, North Carolina, 28207, United States

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GSK Investigational Site

Durham, North Carolina, 27705, United States

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GSK Investigational Site

Gastonia, North Carolina, 28054, United States

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GSK Investigational Site

Huntersville, North Carolina, 28078, United States

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GSK Investigational Site

Wilmington, North Carolina, 28401, United States

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GSK Investigational Site

Winston-Salem, North Carolina, 27103, United States

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GSK Investigational Site

Dayton, Ohio, 45459, United States

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GSK Investigational Site

Medford, Oregon, 97504, United States

Location

GSK Investigational Site

Pittsburgh, Pennsylvania, 15213, United States

Location

GSK Investigational Site

Easley, South Carolina, 29640, United States

Location

GSK Investigational Site

Fort Mill, South Carolina, 29707, United States

Location

GSK Investigational Site

Gaffney, South Carolina, 29340, United States

Location

GSK Investigational Site

Greenville, South Carolina, 29615, United States

Location

GSK Investigational Site

Seneca, South Carolina, 29678, United States

Location

GSK Investigational Site

Spartanburg, South Carolina, 29303, United States

Location

GSK Investigational Site

Abingdon, Virginia, 24210, United States

Location

GSK Investigational Site

Cairns, Queensland, 4870, Australia

Location

GSK Investigational Site

Daw Park, South Australia, 5041, Australia

Location

GSK Investigational Site

Clayton, Victoria, 3168, Australia

Location

GSK Investigational Site

Frankston, Victoria, 3199, Australia

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GSK Investigational Site

Murdoch, Western Australia, 6150, Australia

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GSK Investigational Site

Nedlands, Western Australia, 6009, Australia

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GSK Investigational Site

Liverpool, 2107, Australia

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GSK Investigational Site

Brussels, 1000, Belgium

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GSK Investigational Site

Brussels, 1200, Belgium

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GSK Investigational Site

Erpent, 5101, Belgium

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GSK Investigational Site

Leuven, 3000, Belgium

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GSK Investigational Site

Liège, 4000, Belgium

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GSK Investigational Site

Ostend, 8400, Belgium

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GSK Investigational Site

Calgary, Alberta, T2N 4Z6, Canada

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GSK Investigational Site

Sherwood Park, Alberta, T8H 0N2, Canada

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GSK Investigational Site

Winnipeg, Manitoba, R2K 3S8, Canada

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GSK Investigational Site

Toronto, Ontario, M5T 3A9, Canada

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GSK Investigational Site

Windsor, Ontario, N8X 5A6, Canada

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GSK Investigational Site

Gatineau, Quebec, J8Y 6S8, Canada

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GSK Investigational Site

Montreal, Quebec, H2W1T8, Canada

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GSK Investigational Site

Montreal, Quebec, H4J 1C5, Canada

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GSK Investigational Site

Saint-Charles-Borromée, Quebec, J6E 2B4, Canada

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GSK Investigational Site

Sainte-Foy, Quebec, G1V 4G5, Canada

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GSK Investigational Site

Trois-Rivières, Quebec, G8T 7A1, Canada

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GSK Investigational Site

Karlovy Vary, 360 17, Czechia

Location

GSK Investigational Site

Prague, 140 46, Czechia

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GSK Investigational Site

Tábor, 39003, Czechia

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GSK Investigational Site

Teplice, 415 10, Czechia

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GSK Investigational Site

Tallinn, 10138, Estonia

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GSK Investigational Site

Tallinn, 13419, Estonia

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GSK Investigational Site

Tallinn, 13619, Estonia

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GSK Investigational Site

Tartu, 51014, Estonia

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GSK Investigational Site

Bayonne, 64109, France

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GSK Investigational Site

Grenoble, 38043, France

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GSK Investigational Site

Lyon, 69317, France

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GSK Investigational Site

Marseille, 13915, France

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GSK Investigational Site

Montpellier, 34295, France

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GSK Investigational Site

Perpignan, 66000, France

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GSK Investigational Site

Suresnes, 92150, France

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GSK Investigational Site

Athens, 106 76, Greece

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GSK Investigational Site

Athens, 11527, Greece

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GSK Investigational Site

Haidari / Athens, 124 62, Greece

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GSK Investigational Site

Rethymnon, Crete, 74100, Greece

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GSK Investigational Site

Thessaloniki, 56429, Greece

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GSK Investigational Site

Thessaloniki, 57010, Greece

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GSK Investigational Site

Napoli, Campania, 80131, Italy

Location

GSK Investigational Site

Parma, Emilia-Romagna, 43125, Italy

Location

GSK Investigational Site

Pietra Ligure (SV), Liguria, 17027, Italy

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GSK Investigational Site

Milan, Lombardy, 20123, Italy

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GSK Investigational Site

Pisa, Tuscany, 56124, Italy

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GSK Investigational Site

Perugia, Umbria, 06156, Italy

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GSK Investigational Site

Guadalajara, Jalisco, 44100, Mexico

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GSK Investigational Site

Guadalajara, Jalisco, 44500, Mexico

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GSK Investigational Site

Zapopan, Jalisco, 45070, Mexico

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GSK Investigational Site

Monterrey, Nuevo León, 64000, Mexico

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GSK Investigational Site

Monterrey, Nuevo León, 64020, Mexico

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GSK Investigational Site

Monterrey NL, Nuevo León, 64718, Mexico

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GSK Investigational Site

Mexico City, 07760, Mexico

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GSK Investigational Site

México DF, 14050, Mexico

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GSK Investigational Site

Oaxaca City, 68000, Mexico

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GSK Investigational Site

Bodø, 8005, Norway

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GSK Investigational Site

Kløfta, 2040, Norway

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GSK Investigational Site

Trondheim, 7027, Norway

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GSK Investigational Site

Lima, Lima Province, Lima 27, Peru

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GSK Investigational Site

San Martín de Porres, Lima region, Lima 31, Peru

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GSK Investigational Site

San Miguel, Lima region, Lima 32, Peru

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GSK Investigational Site

Santiago de Surco, Lima region, Lima 33, Peru

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GSK Investigational Site

Lima, Lima 18, Peru

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GSK Investigational Site

Lima, Lima 1, Peru

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GSK Investigational Site

Lima, Lima 32, Peru

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GSK Investigational Site

Pueblo Libre, Lima 21, Peru

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GSK Investigational Site

Bialystok, 15-044, Poland

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GSK Investigational Site

Elblag, 82-300, Poland

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GSK Investigational Site

Krakow, 31-024, Poland

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GSK Investigational Site

Ostrów Wielkopolski, 63-400, Poland

Location

GSK Investigational Site

Skierniewice, 96-100, Poland

Location

GSK Investigational Site

Chelyabinsk, 454106, Russia

Location

GSK Investigational Site

Kemerovo, 650000, Russia

Location

GSK Investigational Site

Nizhny Novgorod, 603126, Russia

Location

GSK Investigational Site

Ryazan, 390039, Russia

Location

GSK Investigational Site

Saint Petersburg, 194354, Russia

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GSK Investigational Site

Saint Petersburg, 194356, Russia

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GSK Investigational Site

Saint Petersburg, 195271, Russia

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GSK Investigational Site

Tomsk, 634 050, Russia

Location

GSK Investigational Site

Tomsk, 634001, Russia

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GSK Investigational Site

Yaroslavl, 150003, Russia

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GSK Investigational Site

Alicante, 03004, Spain

Location

GSK Investigational Site

Barcelona, 08025, Spain

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GSK Investigational Site

Barcelona, 08036, Spain

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GSK Investigational Site

L'Hospitalet de Llobregat, 08907, Spain

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GSK Investigational Site

Lugo, 27003, Spain

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GSK Investigational Site

Málaga, 29010, Spain

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GSK Investigational Site

Palma de Mallorca, 07120, Spain

Location

GSK Investigational Site

Pozuelo de Alarcón/Madrid, 28223, Spain

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GSK Investigational Site

Lund, SE-221 85, Sweden

Location

GSK Investigational Site

Stockholm, SE-141 86, Sweden

Location

Related Publications (3)

  • Pavord ID, Chapman KR, Bafadhel M, Sciurba FC, Bradford ES, Schweiker Harris S, Mayer B, Rubin DB, Yancey SW, Paggiaro P. Mepolizumab for Eosinophil-Associated COPD: Analysis of METREX and METREO. Int J Chron Obstruct Pulmon Dis. 2021 Jun 16;16:1755-1770. doi: 10.2147/COPD.S294333. eCollection 2021.

  • Condreay LD, Gao C, Bradford E, Yancey SW, Ghosh S. No genetic associations with mepolizumab efficacy in COPD with peripheral blood eosinophilia. Respir Med. 2019 Aug;155:26-28. doi: 10.1016/j.rmed.2019.07.004. Epub 2019 Jul 5.

  • Pavord ID, Chanez P, Criner GJ, Kerstjens HAM, Korn S, Lugogo N, Martinot JB, Sagara H, Albers FC, Bradford ES, Harris SS, Mayer B, Rubin DB, Yancey SW, Sciurba FC. Mepolizumab for Eosinophilic Chronic Obstructive Pulmonary Disease. N Engl J Med. 2017 Oct 26;377(17):1613-1629. doi: 10.1056/NEJMoa1708208. Epub 2017 Sep 11.

Related Links

MeSH Terms

Conditions

Pulmonary Disease, Chronic Obstructive

Interventions

mepolizumab

Condition Hierarchy (Ancestors)

Lung Diseases, ObstructiveLung DiseasesRespiratory Tract DiseasesChronic DiseaseDisease AttributesPathologic ProcessesPathological Conditions, Signs and Symptoms

Results Point of Contact

Title
GSK Response Center
Organization
GlaxoSmithKline

Study Officials

  • GSK Clinical Trials

    GlaxoSmithKline

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
TRIPLE
Who Masked
PARTICIPANT, INVESTIGATOR, OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

April 3, 2014

First Posted

April 7, 2014

Study Start

April 15, 2014

Primary Completion

January 17, 2017

Study Completion

January 17, 2017

Last Updated

August 31, 2018

Results First Posted

April 6, 2018

Record last verified: 2018-08

Data Sharing

IPD Sharing
Will share

IPD for this study will be made available via the Clinical Study Data Request site.

Shared Documents
STUDY PROTOCOL, SAP, ICF, CSR
Time Frame
IPD is available via the Clinical Study Data Request site (click on the link provided below)
Access Criteria
Access is provided after a research proposal is submitted and has received approval from the Independent Review Panel and after a Data Sharing Agreement is in place. Access is provided for an initial period of 12 months but an extension can be granted, when justified, for up to another 12 months.
More information

Locations