NCT02081534

Brief Summary

Randomized. double blind, placebo controlled, parallel arms dose finding study with a 4 weeks treatment period

Trial Health

90
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
162

participants targeted

Target at P75+ for phase_2

Timeline
Completed

Started Mar 2014

Shorter than P25 for phase_2

Geographic Reach
4 countries

41 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

March 1, 2014

Completed
5 days until next milestone

First Submitted

Initial submission to the registry

March 6, 2014

Completed
1 day until next milestone

First Posted

Study publicly available on registry

March 7, 2014

Completed
8 months until next milestone

Primary Completion

Last participant's last visit for primary outcome

November 1, 2014

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

November 1, 2014

Completed
5.9 years until next milestone

Results Posted

Study results publicly available

September 14, 2020

Completed
Last Updated

September 14, 2020

Status Verified

August 1, 2020

Enrollment Period

8 months

First QC Date

March 6, 2014

Results QC Date

August 6, 2020

Last Update Submit

August 25, 2020

Conditions

Keywords

S-phosphate, hyperphosphatemia, hemodialysis, ESRD

Outcome Measures

Primary Outcomes (1)

  • Change in Serum Phosphate Levels

    Change in serum phosphate levels from the end of wash out (pre randomization value) to end of treatment

    End of wash out (pre randomization value) to end of treatment (Day 29)

Secondary Outcomes (1)

  • Change From Baseline in Calcium x Phosphorus Product

    End of wash out (pre randomization value) to end of treatment (Day 29)

Study Arms (7)

1 mg bid

EXPERIMENTAL

1 mg AZD1722 bid

Drug: AZD1722

3 mg bid

EXPERIMENTAL

3 mg AZD1722 bid

Drug: AZD1722

10 mg bid

EXPERIMENTAL

10 mg AZD1722 bid

Drug: AZD1722

30 mg bid

EXPERIMENTAL

30 mg AZD1722 bid

Drug: AZD1722

3 mg od

EXPERIMENTAL

3 mg AZD1722 od

Drug: AZD1722

30 mg od

EXPERIMENTAL

30 mg AZD1722 od

Drug: AZD1722

Placebo

PLACEBO COMPARATOR

Placebo (double dummy technique)

Drug: Placebo

Interventions

AZD1722, oral tablet

1 mg bid10 mg bid3 mg bid3 mg od30 mg bid30 mg od

Placebo bid, double dummy technique

Placebo

Eligibility Criteria

Age18 Years - 85 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Females and males aged ≥18 years
  • Chronic maintenance hemodialysis 3 x/week for a at least 3 months
  • Prescribed and taking at least 3 doses of phosphate binder per day
  • Serum phosphate levels should be between 3.5 and 8.0 mg/dL ; 1.13 mmol/L and 2.58 mmol/L (inclusive) at screening
  • Total serum calcium levels 2.0 - 2.6 mmol/L inclusive at screening
  • For randomization in the study, after up to 3 weeks wash out of phosphate binders, patients must have serum phosphate levels of at least 6. 0 mg/dL (1.94 mmol/L) but below 10 mg/dL (3.23 mmol/L) and have had an increase of at least 1.5 mg/dL (0.48 mmol/L) vs pre wash out

You may not qualify if:

  • Severe hyperphosphatemia defined as \>10 mg/dL on Phosphate-binders at all time points during clinical routine monitoring for the 3 preceding months before screening visit.
  • Serum parathyroid hormone \>1200 pg/mL
  • Significant metabolic acidosis
  • Clinical signs of hypovolemia at randomization

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (41)

Research Site

Downey, California, United States

Location

Research Site

Los Angeles, California, United States

Location

Research Site

Sacramento, California, United States

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Research Site

Whittier, California, United States

Location

Research Site

Denver, Colorado, United States

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Research Site

Pembroke Pines, Florida, United States

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Research Site

Tampa, Florida, United States

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Research Site

Winter Park, Florida, United States

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Research Site

Springfield, Massachusetts, United States

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Research Site

Detroit, Michigan, United States

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Research Site

Voorhees Township, New Jersey, United States

Location

Research Site

Flushing, New York, United States

Location

Research Site

Maspeth, New York, United States

Location

Research Site

Charlotte, North Carolina, United States

Location

Research Site

Cincinnati, Ohio, United States

Location

Research Site

San Antonio, Texas, United States

Location

Research Site

Bialystok, Poland

Location

Research Site

Częstochowa, Poland

Location

Research Site

Działdowo, Poland

Location

Research Site

Legnica, Poland

Location

Research Site

Lublin, Poland

Location

Research Site

Radom, Poland

Location

Research Site

Szczecin, Poland

Location

Research Site

Warsaw, Poland

Location

Research Site

Wroclaw, Poland

Location

Research Site

Zamość, Poland

Location

Research Site

Zgierz, Poland

Location

Research Site

Żary, Poland

Location

Research Site

Banská Bystrica, Slovakia

Location

Research Site

Bratislava, Slovakia

Location

Research Site

Hlohovec, Slovakia

Location

Research Site

Košice, Slovakia

Location

Research Site

Piešťany, Slovakia

Location

Research Site

Púchov, Slovakia

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Research Site

Senica, Slovakia

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Research Site

Birmingham, United Kingdom

Location

Research Site

Doncaster, United Kingdom

Location

Research Site

Exeter, United Kingdom

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Research Site

Hull, United Kingdom

Location

Research Site

Leicester, United Kingdom

Location

Research Site

London, United Kingdom

Location

Related Publications (2)

  • Sprague SM, Weiner DE, Tietjen DP, Pergola PE, Fishbane S, Block GA, Silva AL, Fadem SZ, Lynn RI, Fadda G, Pagliaro L, Zhao S, Edelstein S, Spiegel DM, Rosenbaum DP. Tenapanor as Therapy for Hyperphosphatemia in Maintenance Dialysis Patients: Results from the OPTIMIZE Study. Kidney360. 2024 May 1;5(5):732-742. doi: 10.34067/KID.0000000000000387. Epub 2024 Feb 7.

  • Block GA, Rosenbaum DP, Yan A, Greasley PJ, Chertow GM, Wolf M. The effects of tenapanor on serum fibroblast growth factor 23 in patients receiving hemodialysis with hyperphosphatemia. Nephrol Dial Transplant. 2019 Feb 1;34(2):339-346. doi: 10.1093/ndt/gfy061.

MeSH Terms

Conditions

HyperphosphatemiaKidney Failure, Chronic

Interventions

tenapanor

Condition Hierarchy (Ancestors)

Phosphorus Metabolism DisordersMetabolic DiseasesNutritional and Metabolic DiseasesRenal Insufficiency, ChronicRenal InsufficiencyKidney DiseasesUrologic DiseasesFemale Urogenital DiseasesFemale Urogenital Diseases and Pregnancy ComplicationsUrogenital DiseasesMale Urogenital DiseasesChronic DiseaseDisease AttributesPathologic ProcessesPathological Conditions, Signs and Symptoms

Results Point of Contact

Title
Chief Development Officer
Organization
Ardelyx

Study Officials

  • Geoffrey A Block, MD

    Denver Nephrology PC, Denver, CO 80230

    PRINCIPAL INVESTIGATOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
GT60
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
DOUBLE
Who Masked
PARTICIPANT, INVESTIGATOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

March 6, 2014

First Posted

March 7, 2014

Study Start

March 1, 2014

Primary Completion

November 1, 2014

Study Completion

November 1, 2014

Last Updated

September 14, 2020

Results First Posted

September 14, 2020

Record last verified: 2020-08

Locations