NCT02073409

Brief Summary

Isolation of nontuberculous mycobacteria (NTM) from the sputum of individuals with CF is an increasingly common finding, and the lack of an evidenced-based approach to the diagnosis of NTM disease has been identified as one of the greatest unmet needs within the CF community. Current evidence predicts that the prevalence of NTM will remain relatively high in the CF population. Approaches to NTM disease diagnosis differ widely between centers. This study is observational and follows current best practices. The study will help standardize the diagnosis and collect relevant data associated with the diagnosis of NTM disease to build a framework for future therapeutic trials.

Trial Health

55
Monitor

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Trial has exceeded expected completion date
Enrollment
200

participants targeted

Target at P75+ for all trials

Timeline
Completed

Started Dec 2013

Longer than P75 for all trials

Geographic Reach
1 country

19 active sites

Status
enrolling by invitation

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

December 1, 2013

Completed
3 months until next milestone

First Submitted

Initial submission to the registry

February 24, 2014

Completed
3 days until next milestone

First Posted

Study publicly available on registry

February 27, 2014

Completed
11 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

March 1, 2025

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

March 1, 2025

Completed
Last Updated

April 2, 2024

Status Verified

March 1, 2024

Enrollment Period

11.3 years

First QC Date

February 24, 2014

Last Update Submit

March 30, 2024

Conditions

Keywords

Nontuberculous Mycobacteria

Outcome Measures

Primary Outcomes (1)

  • Proportion meeting the diagnosis of NTM disease

    12 months intervals following study enrollment

Secondary Outcomes (5)

  • Adherence to PREDICT protocol: number of respiratory cultures obtained per participant per year, withdrawals and major deviations from protocol

    12 months intervals following study enrollment

  • Incidence and prevalence of NTM species/subspecies by geographical region

    12 months intervals following study enrollment

  • Proportion of eligible NTM positive individuals with CF enrolling in PREDICT by site

    12 months intervals following study enrollment

  • Proportion of PREDICT participants with NTM disease diagnosis who enroll in Part B PATIENCE

    12 months intervals following study enrollment

  • Clinical parameters and outcomes (FEV1, growth parameters, CFQ-R)

    12 months intervals following study enrollment

Study Arms (1)

CF patients

Male and female subjects with CF age 6 years and older who have a positive sputum culture for NTM.

Eligibility Criteria

Age6 Years - 99 Years
Sexall
Healthy VolunteersNo
Age GroupsChild (0-17), Adult (18-64), Older Adult (65+)
Sampling MethodNon-Probability Sample
Study Population

Male and female subjects with CF age 6 years and older who have a positive sputum culture for NTM.

You may qualify if:

  • Written informed consent (and assent when applicable) obtained from participant or participant's legal representative
  • Enrolled in the CFF Patient Registry (CFF PR)
  • Be willing and able to adhere to study procedures in the context of clinical care, and other protocol requirements
  • Male or female participant ≥ 6 years of age at enrollment
  • Diagnosis of CF consistent with the 2017 CFF Guidelines
  • NTM positive for a species or sub-species in the 2 years prior to enrollment that has never been treated.
  • Willing to discontinue chronic azithromycin use for the duration of the study

You may not qualify if:

  • Prior or ongoing antibiotic treatment of the same NTM species or sub-species for which the patient is being considered for this study
  • History of solid organ or hematological transplantation
  • Has any other condition that, in the opinion of the Site Investigator/designee, would preclude informed consent or assent, make study participation unsafe, complicate interpretation of study outcome data, or otherwise interfere with achieving the study objectives

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (19)

CFF Pediatric Program, University of Alabama

Birmingham, Alabama, 35233, United States

Location

Children's Hospital of Los Angeles

Los Angeles, California, United States

Location

University of California San Diego

San Diego, California, United States

Location

Children's Hospital Colorado

Aurora, Colorado, 80045, United States

Location

National Jewish Health

Denver, Colorado, 80206, United States

Location

University of Florida

Gainesville, Florida, United States

Location

Northwestern University

Chicago, Illinois, United States

Location

CFF Adult Program, Johns Hopkins University

Baltimore, Maryland, 21205, United States

Location

Boston Children's Hospital, Brigham & Women's Hospital

Boston, Massachusetts, United States

Location

CFF Pediatric Program University of Michigan

Ann Arbor, Michigan, 48109, United States

Location

Dartmouth Hitchcock Medical Center

Lebanon, New Hampshire, United States

Location

CFF Pediatric Program, Columbia University

New York, New York, 10032, United States

Location

CFF Adult Program, University of North Carolina at Chapel Hill

Chapel Hill, North Carolina, 27517, United States

Location

Nationwide Children's Hospital

Columbus, Ohio, United States

Location

University of Pittsburgh Medical Center

Pittsburgh, Pennsylvania, United States

Location

CFF Adult Program, The University of Texas Southwestern Medical Center at Dallas

Dallas, Texas, 75390-8558, United States

Location

University of Vermont Medical Center

Burlington, Vermont, United States

Location

CFF Pediatric Program Seattle Children's Hospital

Seattle, Washington, 98105, United States

Location

CFF Adult Program, University of Washington

Seattle, Washington, 98195, United States

Location

Related Publications (1)

  • Martiniano SL, Caceres SM, Poch K, Rysavy NM, Lovell VK, Armantrout E, Jones M, Anthony M, Keck A, Nichols DP, Vandalfsen JM, Sagel SD, Wagner B, Xie J, Weaver K, Heltshe SL, Daley CL, Davidson RM, Nick JA; Investigators of the Cystic Fibrosis NTM Consortium. Prospective evaluation of nontuberculous mycobacteria disease in cystic fibrosis: The design of the PREDICT study. J Cyst Fibros. 2024 Jan;23(1):50-57. doi: 10.1016/j.jcf.2023.08.007. Epub 2023 Sep 4.

Biospecimen

Retention: SAMPLES WITHOUT DNA

Samples collected may include serum, sputum, whole blood, breath, urine, and NTM isolates.

MeSH Terms

Conditions

Cystic Fibrosis

Condition Hierarchy (Ancestors)

Pancreatic DiseasesDigestive System DiseasesLung DiseasesRespiratory Tract DiseasesGenetic Diseases, InbornCongenital, Hereditary, and Neonatal Diseases and AbnormalitiesInfant, Newborn, Diseases

Study Officials

  • Jerry A Nick, MD

    National Jewish Health

    PRINCIPAL INVESTIGATOR
  • Stacey Martiniano, MD

    Children's Hospital Colorado

    PRINCIPAL INVESTIGATOR

Study Design

Study Type
observational
Observational Model
CASE ONLY
Time Perspective
PROSPECTIVE
Sponsor Type
OTHER
Responsible Party
PRINCIPAL INVESTIGATOR
PI Title
Professor of Medicine

Study Record Dates

First Submitted

February 24, 2014

First Posted

February 27, 2014

Study Start

December 1, 2013

Primary Completion

March 1, 2025

Study Completion

March 1, 2025

Last Updated

April 2, 2024

Record last verified: 2024-03

Locations