NCT02050347

Brief Summary

Patients have a type of lymph gland cancer called Non-Hodgkin Lymphoma (NHL), acute lymphocytic leukemia (ALL) or chronic lymphocytic leukemia (CLL) (these diseases will be referred to as "lymphoma" or "leukemia"). The lymphoma or leukemia has come back or has not gone away after treatment (including the best treatment known for these cancers). Because there is no standard treatment for this cancer at this time, subjects are asked to volunteer to be in a gene transfer research study using special immune cells. The body has different ways of fighting infection and disease. No one way seems perfect for fighting cancers. This research study combines two different ways of fighting disease, antibodies and T cells, hoping that they will work together. Both antibodies and T cells have been used to treat patients with cancers; they have shown promise, but have not been strong enough to cure most patients. T cells can kill tumor cells but there normally are not enough of them to kill all the tumor cells. Some researchers have taken T cells from a person's blood, grown more of them in the laboratory and then given them back to the person. The antibody used in this study is called anti-CD19. This antibody sticks to cancer cells because of a substance on the outside of these cells called CD19. CD19 antibodies have been used to treat people with lymphoma and leukemia. For this study, the CD19 antibody has been changed so that instead of floating free in the blood it is now joined to the T cells. When an antibody is joined to a T cell in this way it is called a chimeric receptor. The T lymphocytes will also contain CD28, which stimulates T cells and makes them last longer. Treatment with CD19/CD28 chimeric receptor-T cells has had activity against lymphoma and leukemia when the cells are made from the patients affected by these diseases. In this study, investigators are going to see if this treatment works even better when they make these cells from a healthy stem cell donor. If investigators are not able to collect blood from the stem cell donor, they will collect blood from the subject to make the CD19/CD28 chimeric receptor-T cells. These CD19/CD28 chimeric receptor T cells are investigational products not approved by the FDA. The purpose of this study is to find the biggest dose of chimeric T Cells that is safe, to see how long T cells with this chimeric receptor last, to learn what the side effects are, and to see whether this therapy might help people with lymphoma or leukemia after a stem cell transplantation from a donor.

Trial Health

75
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
7

participants targeted

Target at below P25 for phase_1

Timeline
56mo left

Started Apr 2014

Longer than P75 for phase_1

Geographic Reach
1 country

2 active sites

Status
active not recruiting

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Progress73%
Apr 2014Dec 2030

First Submitted

Initial submission to the registry

January 29, 2014

Completed
1 day until next milestone

First Posted

Study publicly available on registry

January 30, 2014

Completed
2 months until next milestone

Study Start

First participant enrolled

April 1, 2014

Completed
5.5 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

October 1, 2019

Completed
11.2 years until next milestone

Study Completion

Last participant's last visit for all outcomes

December 1, 2030

Expected
Last Updated

November 14, 2025

Status Verified

November 1, 2025

Enrollment Period

5.5 years

First QC Date

January 29, 2014

Last Update Submit

November 12, 2025

Conditions

Keywords

CD19.CAR-CD28zetachimeric antigen receptorhematopoietic stem cell transplant

Outcome Measures

Primary Outcomes (1)

  • Number of patients with dose limiting toxicity

    Toxicity is evaluated using CTCAE, version 4.0. Dose limiting toxicity (DLT) will be defined as any of the following that is NOT (1) pre-existing, or (2) due to infection (to which patients with CLL and NHL are predisposed), or (3) due to underlying malignancy, and that may, after consultation with the FDA when indicated, be considered possibly, probably, or definitely related to the study cellular products: * Development of Grade III-IV GVHD or Grade II GVHD unresponsive to front line treatment; * Non-hematologic DLT is any grade 3 or grade 4 non-hematologic toxicity, including allergic reactions to T cell infusions. * Hematologic DLT is defined as any grade 4 hematologic toxicity, including secondary graft failure (as defined per protocol). * Patients with evidence of bone marrow disease (metastases or diffuse infiltration) are not evaluable for hematologic dose limiting toxicity.

    6 weeks

Secondary Outcomes (2)

  • Number of patients with tumor response

    8 weeks

  • Frequency of T cell products

    Up to 15 years

Study Arms (4)

Subgroup A1

EXPERIMENTAL

Patients with residual or relapsed B-cell ALL and with an HLA-matched related donor will receive CD19.CAR-CD28Z T Cells - dose escalation 1

Genetic: CD19.CAR-CD28Z T Cells - dose escalation 2

Subgroup B1

EXPERIMENTAL

Patients with other B-cell malignancies and with an HLA-matched related donor will receive CD19.CAR-CD28Z T Cells - dose escalation 1

Genetic: CD19.CAR-CD28Z T Cells - dose escalation 2

Subgroup A2

EXPERIMENTAL

Patients with residual or relapsed B-cell ALL and with an unrelated or HLA-mismatched donor will receive CD19.CAR-CD28Z T Cells - dose escalation 2

Genetic: CD19.CAR-CD28Z T Cells - dose escalation 1

Subgroup B2

EXPERIMENTAL

Patients with other B cell malignancies and with an unrelated or HLA-mismatched donor will receive CD19.CAR-CD28Z T Cells - dose escalation 2

Genetic: CD19.CAR-CD28Z T Cells - dose escalation 1

Interventions

Patients will receive one of the following dose levels: Dose Level 1: 5 ×10\^5 cells/kg Dose Level 2: 1×10\^6 cells/kg Dose Level 3: 5×10\^6 cells/kg

Subgroup A1Subgroup B1

Patients will receive one of the following doses: Dose Level one: 1x10\^5 cells/kg Dose Level 2: 5x10\^5 cells/kg Dose Level 3: 1x10\^6 cells/kg

Subgroup A2Subgroup B2

Eligibility Criteria

Sexall
Healthy VolunteersNo
Age GroupsChild (0-17), Adult (18-64), Older Adult (65+)

You may qualify if:

  • PROCUREMENT
  • Group A: CD19+ B-ALL undergoing allogeneic HSCT or Group B: CD19+ B cell CLL or NHL undergoing allogeneic HSCT
  • Life expectancy of ≥12 weeks.
  • Patient has an appropriate donor identified for hematopoietic stem cell transplantation
  • TREATMENT
  • Any patient regardless of sex or age with CD19+ B-ALL undergoing allogeneic HSCT (Group A) OR any patient regardless of sex or age with CD19+ B-CLL or NHL undergoing allogeneic HSCT (Group B)
  • Residual disease at the time of transplant (bulky or minimal) or post transplant relapse as evidenced by PCR positivity, specific cytogenetic abnormalities, an abnormal population on flow cytometry or increased blasts on bone marrow biopsy or in the peripheral blood. MRD will be defined as detection in blood or marrow of any of the following:
  • Any leukemia specific marker (such as t(9:22) or t(4:11)) documented in the patient's leukemia cells pre transplant on a post transplant evaluation.
  • An immune globulin rearrangement known to be a disease marker for this patient post transplant.
  • A leukemia specific phenotype post transplant at a level of ≥ 0.01%
  • Mixed donor chimerism (any level)
  • Life expectancy ≥ 6 weeks
  • Karnofsky/Lansky score ≥ 50%.
  • Bilirubin ≤ 2 times the upper limit of normal.
  • AST ≤ 3 times the upper limit of normal.
  • +7 more criteria

You may not qualify if:

  • Severe intercurrent infection.
  • Evidence of GVHD \> grade II.
  • Pregnant or lactating.
  • History of hypersensitivity reactions to murine protein-containing products.
  • Currently taking corticosteroids (\>0.5 mg/kg/day prednisone or equivalent) for therapy of GVHD.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (2)

Houston Methodist Hospital

Houston, Texas, 77030, United States

Location

Texas Children's Hospital

Houston, Texas, 77030, United States

Location

MeSH Terms

Conditions

Lymphoma, Non-HodgkinBurkitt LymphomaLeukemia, B-Cell

Condition Hierarchy (Ancestors)

LymphomaNeoplasms by Histologic TypeNeoplasmsLymphoproliferative DisordersLymphatic DiseasesHemic and Lymphatic DiseasesImmunoproliferative DisordersImmune System DiseasesEpstein-Barr Virus InfectionsHerpesviridae InfectionsDNA Virus InfectionsVirus DiseasesInfectionsTumor Virus InfectionsLymphoma, B-CellLeukemia, LymphoidLeukemiaHematologic Diseases

Study Officials

  • Carlos A Ramos, MD

    Baylor College of Medicine

    PRINCIPAL INVESTIGATOR

Study Design

Study Type
interventional
Phase
phase 1
Allocation
NON RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
OTHER
Responsible Party
PRINCIPAL INVESTIGATOR
PI Title
Assistant Professor

Study Record Dates

First Submitted

January 29, 2014

First Posted

January 30, 2014

Study Start

April 1, 2014

Primary Completion

October 1, 2019

Study Completion (Estimated)

December 1, 2030

Last Updated

November 14, 2025

Record last verified: 2025-11

Locations