NCT02043860

Brief Summary

In this phase I trial, patients with multiple myeloma will receive standard high dose melphalan with autologous stem cell rescue. In addition the pre-transplant conditioning will include targeted total marrow irradiation (TMI). This conventional 3+3 phase I trial will increase the dose of TMI until the maximum tolerated dose (MTD) is reached. Initial patients enrolled will receive the lowest possible dose of 3Gy. Maximum dose will be 12Gy.

Trial Health

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Monitor

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
3

participants targeted

Target at below P25 for phase_1 multiple-myeloma

Timeline
Completed

Started Jan 2014

Shorter than P25 for phase_1 multiple-myeloma

Geographic Reach
1 country

1 active site

Status
terminated

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

January 10, 2014

Completed
11 days until next milestone

First Submitted

Initial submission to the registry

January 21, 2014

Completed
2 days until next milestone

First Posted

Study publicly available on registry

January 23, 2014

Completed
2.8 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

November 7, 2016

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

November 7, 2016

Completed
2.9 years until next milestone

Results Posted

Study results publicly available

October 14, 2019

Completed
Last Updated

October 14, 2019

Status Verified

September 1, 2019

Enrollment Period

2.8 years

First QC Date

January 21, 2014

Results QC Date

February 20, 2019

Last Update Submit

September 23, 2019

Conditions

Keywords

Multiple MyelomaHigh RiskIntermediate RiskSymptomatic

Outcome Measures

Primary Outcomes (1)

  • Progression Free Survival No Results Due to 1 Subject Came Off Treatment Within 7 Days and 1 Subject Came Off Treatment Within 5 Days. Not Enough Data to Analyze

    To evaluate progression free survival (PFS) and in patients with multiple myeloma undergoing autologous stem cell transplant using the combination of high dose melphalan and total marrow irradiation.

    Up to 1 year post-transplant.

Study Arms (1)

Total Marrow Irradiation

EXPERIMENTAL

Escalating doses of total marrow irradiation (3Gy, 6Gy, 9Gy, or 12Gy) with standard high dose melphalan prior to autologous stem cell rescue.

Radiation: Total Marrow IrradiationProcedure: Autologous TransplantDrug: MelphalanDrug: Filgrastim (G-CSF)

Interventions

Subjects in this trial will receive total body irradiation (3Gy) per day for up to four days and as little as one day. Total IMT doses: 3Gy, 6Gy, 9Gy, or 12Gy.

Total Marrow Irradiation

Subjects will receive standard melphalan 200mg/m\^2 (100mg/m\^2 day-2 and day-1) conditioning with escalating doses of total marrow irradiation prior to autologous stem cell rescue.

Total Marrow Irradiation

Subjects will receive standard melphalan 200mg/m\^2 (100mg/m\^2 day-2 and day-1) conditioning therapy prior to transplant.

Also known as: Alkeran ®
Total Marrow Irradiation

Subjects to begin GCSF 5 μg/kg/d SC or IV on Day 5 and continue until ANC \> 1000/mm\^3 over period of 3 days.

Also known as: Neupogen®
Total Marrow Irradiation

Eligibility Criteria

Age18 Years - 75 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Patients meeting criteria for symptomatic myeloma
  • Patients must be high or intermediate risk of disease progression as defined by having one of the following criteria: 2.1 ISS stage 2 or 3 disease 2.2 Abnormal metaphase cytogenetics 2.3 Presence of FISH abnormalities aside from hyperdiploidy
  • Patients who have received at least 2 cycles of systemic treatment of any kind in the preceding 12 months
  • Patient age 18-75 years at time of enrollment
  • Karnofsky performance status of ≥70
  • Cardiac function: LVEF \>40%
  • Hepatic: Bilirubin \<2x upper limit of normal and ALT and AST \< 2.5x the upper limit of normal
  • Renal: Creatinine clearance of ≥30mL/min, estimated or calculated
  • Pulmonary: DLCO, FEV1, FVC \>50% of predicted (after correction for hemoglobin)

You may not qualify if:

  • Patients with diagnosis of plasma cell leukemia
  • Patients with myeloma who have had any disease progression prior to enrollment
  • Patients with truly non secretory myeloma (patients with light chain disease are eligible)
  • Pregnant or breast-feeding
  • Uncontrolled viral, fungal or bacterial infection Note: Infection is permitted if there is evidence of response to medication. Eligibility of HIV infected patients will be determined on a case-by-case basis.
  • Patients who have undergone prior allograft or autologous transplant
  • Prior solid organ transplant
  • Patients receiving prior radiation to more than 20% of bone marrow containing areas

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (1)

UIC Cancer Center

Chicago, Illinois, 60612, United States

Location

MeSH Terms

Conditions

Multiple Myeloma

Interventions

Transplantation, AutologousMelphalanFilgrastimGranulocyte Colony-Stimulating Factor

Condition Hierarchy (Ancestors)

Neoplasms, Plasma CellNeoplasms by Histologic TypeNeoplasmsHemostatic DisordersVascular DiseasesCardiovascular DiseasesParaproteinemiasBlood Protein DisordersHematologic DiseasesHemic and Lymphatic DiseasesHemorrhagic DisordersLymphoproliferative DisordersImmunoproliferative DisordersImmune System Diseases

Intervention Hierarchy (Ancestors)

TransplantationSurgical Procedures, OperativeNitrogen Mustard CompoundsMustard CompoundsHydrocarbons, HalogenatedHydrocarbonsOrganic ChemicalsPhenylalanineAmino Acids, AromaticAmino Acids, CyclicAmino AcidsAmino Acids, Peptides, and ProteinsColony-Stimulating FactorsGlycoproteinsGlycoconjugatesCarbohydratesHematopoietic Cell Growth FactorsCytokinesIntercellular Signaling Peptides and ProteinsPeptidesProteinsBiological Factors

Limitations and Caveats

Only 2 subjects received total marrow irradiation at 3Gy dose

Results Point of Contact

Title
Annette Kinsella, RN, CCRC, QA Education Specialist
Organization
UIC Cancer Center Clinical Trials Office

Study Officials

  • Pritesh Patel, MD

    University of Illinois at Chicago

    PRINCIPAL INVESTIGATOR

Publication Agreements

PI is Sponsor Employee
No
Restrictive Agreement
No

Study Design

Study Type
interventional
Phase
phase 1
Allocation
NA
Masking
NONE
Purpose
TREATMENT
Intervention Model
SINGLE GROUP
Sponsor Type
OTHER
Responsible Party
PRINCIPAL INVESTIGATOR
PI Title
Faculty, Assistant Professor

Study Record Dates

First Submitted

January 21, 2014

First Posted

January 23, 2014

Study Start

January 10, 2014

Primary Completion

November 7, 2016

Study Completion

November 7, 2016

Last Updated

October 14, 2019

Results First Posted

October 14, 2019

Record last verified: 2019-09

Locations