NCT01995513

Brief Summary

The purpose of this study is to determine if continued treatment with Enzalutamide is effective in patients with metastatic prostate cancer.

Trial Health

98
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
509

participants targeted

Target at P75+ for phase_4 prostate-cancer

Timeline
Completed

Started Oct 2013

Longer than P75 for phase_4 prostate-cancer

Geographic Reach
11 countries

95 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

October 22, 2013

Completed
27 days until next milestone

First Submitted

Initial submission to the registry

November 18, 2013

Completed
8 days until next milestone

First Posted

Study publicly available on registry

November 26, 2013

Completed
3 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

November 15, 2016

Completed
1 year until next milestone

Results Posted

Study results publicly available

November 17, 2017

Completed
4.8 years until next milestone

Study Completion

Last participant's last visit for all outcomes

August 31, 2022

Completed
Last Updated

September 18, 2023

Status Verified

August 1, 2023

Enrollment Period

3.1 years

First QC Date

November 18, 2013

Results QC Date

October 13, 2017

Last Update Submit

August 22, 2023

Conditions

Outcome Measures

Primary Outcomes (1)

  • Progression Free Survival (PFS)

    PFS = time from randomization to first documentation of radiographic progression (RP),unequivocal clinical progression or death due to any cause (death within 112 days of treatment discontinuation without objective evidence of RP),whichever occurred first as per investigator. Unequivocal disease progression was pain requiring chronic administration of analgesics, decline of prostate cancer of Eastern Cooperative Oncology Group (ECOG) performance status score to 3 or higher or initiation of new anticancer therapy/radiation therapy or surgical intervention due to tumor progression. ECOG score range= 0(no severity) to 5(maximum severity).RP for bone disease was evaluated by appearance of 2 or more new bone lesions as per Prostate Cancer Clinical Trials Working Group 2 (PCWG2) or for soft tissue disease according to Response Evaluation Criteria in Solid Tumor version 1.1. Participants with no PFS event at analysis date were censored at last tumor assessment date prior to data cutoff date.

    From randomization until disease progression, last tumor assessment without disease progression or death due to any cause, whichever occurred first (maximum up to 20.3 months)

Secondary Outcomes (12)

  • Time to Prostate Specific Antigen (PSA) Progression

    From randomization until disease progression, last tumor assessment without disease progression, whichever occurred first (maximum up to 11.1 months)

  • Prostate Specific Antigen (PSA) Response Rate

    From randomization until disease progression, last tumor assessment without disease progression, whichever occurred first (maximum up to 11.1 months)

  • Objective Response Rate (ORR)

    From randomization until CR or PR, whichever occurred first (maximum up to 21.3 months)

  • Rate of Pain Progression

    Month 6

  • Time to First Use of New Antineoplastic Therapy for Prostate Cancer

    From randomization until date of first use of any antineoplastic therapy (after last dose date of Period 2, maximum up to 22.3 months

  • +7 more secondary outcomes

Other Outcomes (4)

  • Percentage of Participants With Treatment-Emergent Adverse Events (AEs) and Serious Adverse Events (SAEs)

    Baseline up to 30 days after the last dose of study drug or before initiation of a new antitumor treatment, whichever occurred first (maximum of 99.4 months)

  • Percentage of Participants With Adverse Events (AEs) Leading to Study Drug Discontinuation

    Baseline up to 30 days after the last dose of study drug or before initiation of a new antitumor treatment, whichever occurred first (maximum of 99.4 months)

  • Percentage of Participants With Adverse Events (AEs) Leading to Death

    Baseline up to 30 days after the last dose of study drug or before initiation of a new antitumor treatment, whichever occurred first (maximum of 99.4 months)

  • +1 more other outcomes

Study Arms (2)

Enzalutamide & Abiraterone/prednisone

EXPERIMENTAL

Enzalutamide (160 mg) administered as four 40-mg capsules by mouth once daily in combination with abiraterone (1000 mg) administered as four 250-mg tablets by mouth once daily and prednisone (10 mg) administered as one 5-mg tablet by mouth twice daily

Drug: EnzalutamideDrug: AbirateroneDrug: Prednisone

Enzalutamide placebo & Abiraterone/prednisone

ACTIVE COMPARATOR

Enzalutamide placebo (placebo) capsules (identical in appearance to enzalutamide) administered as 4 capsules by mouth once daily in combination with abiraterone (1000 mg) administered as four 250-mg tablets by mouth once daily and prednisone (10 mg) administered as one 5-mg tablet by mouth twice daily.

Drug: AbirateroneDrug: Placebo for EnzalutamideDrug: Prednisone

Interventions

160 mg by mouth once daily

Also known as: MDV3100, Xtandi
Enzalutamide & Abiraterone/prednisone

1000 mg by mouth once daily

Also known as: Abiraterone acetate, Zytiga
Enzalutamide & Abiraterone/prednisoneEnzalutamide placebo & Abiraterone/prednisone

Sugar pill manufactured to mimic Enzalutamide 40 mg capsule

Enzalutamide placebo & Abiraterone/prednisone

5 mg by mouth twice daily

Also known as: prednisolone
Enzalutamide & Abiraterone/prednisoneEnzalutamide placebo & Abiraterone/prednisone

Eligibility Criteria

Age18 Years+
Sexmale(Gender-based eligibility)
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Men with metastatic castration-resistant prostate cancer
  • Progressive disease on androgen deprivation therapy
  • Patients must agree to continue androgen deprivation therapy with a GnRH agonist/antagonist throughout the study or have had a prior bilateral orchiectomy
  • ECOG performance score ≤ 1
  • Estimated life expectancy of ≥ 12 months

You may not qualify if:

  • Prior cytotoxic chemotherapy, aminoglutethimide, ketoconazole, abiraterone, or enzalutamide for the treatment of prostate cancer
  • Prior participation in a clinical trial of an investigational agent that inhibits the androgen receptor or androgen synthesis (unless the treatment was placebo)
  • History of brain metastasis, active leptomeningeal disease or seizure
  • Severe cardiovascular or hepatic disease
  • Pituitary or adrenal dysfunction

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (95)

Beth Israel Deaconess Medical Center

Boston, Massachusetts, 02115, United States

Location

Brigham & Women's Hospital

Boston, Massachusetts, 02115, United States

Location

Beth Israel Deaconess Medical Center

Boston, Massachusetts, 02215, United States

Location

Dana Farber Cancer Institute

Boston, Massachusetts, 02215, United States

Location

eResearch Technology

Philadelphia, Pennsylvania, 19103, United States

Location

Urology of Virginia, PLLC

Virginia Beach, Virginia, 23462, United States

Location

Border Medical Oncology Research Unit

Albury, New South Wales, 2640, Australia

Location

Ramsay Health Care Australia Pty Ltd

Albury, New South Wales, 2640, Australia

Location

Regional Imaging Border

Albury, New South Wales, 2640, Australia

Location

Terry White Chemist

Albury, New South Wales, 2640, Australia

Location

Concord Cancer Centre, Medical Oncology Department

Concord, New South Wales, 2139, Australia

Location

Concord Hospital Clinical Trials Pharmacy

Concord, New South Wales, 2139, Australia

Location

Epic Pharmacy Lismore

Lismore, New South Wales, 2480, Australia

Location

Macquarie University Hospital Pharmacy

North Ryde, New South Wales, 2109, Australia

Location

Macquarie University

North Ryde, New South Wales, 2109, Australia

Location

Epic Pharmacy Port Macquarie base hospital

Port Macquarie, New South Wales, 2444, Australia

Location

Port Macquarie Base Hospital,North Coast Cancer Institute

Port Macquarie, New South Wales, 2444, Australia

Location

North Shore Radiology and Nuclear Medicine

St Leonards, New South Wales, 2065, Australia

Location

Royal North Shore Hospital

St Leonards, New South Wales, 2065, Australia

Location

Sydney Adventist Hospital

Sydney, New South Wales, 2076, Australia

Location

Northern NSW Local Health District

Tweed Heads, New South Wales, 2485, Australia

Location

Queensland Diagnostic Imaging

Tweed Heads, New South Wales, 2485, Australia

Location

Sydney Adventist Hospital

Wahroonga, New South Wales, 2076, Australia

Location

Regional Imaging

West Albury, New South Wales, 2640, Australia

Location

Westmead Hospital

Westmead, New South Wales, 2145, Australia

Location

Icon Cancer Care Wesley

Auchenflower, Queensland, 4066, Australia

Location

River City Pharmacy - APHS

Auchenflower, Queensland, 4066, Australia

Location

Icon Cancer Care Chermside

Chermside, Queensland, 4032, Australia

Location

Gold Coast Radiology PTY LTD

Hope Island, Queensland, 4212, Australia

Location

Icon Cancer Care South Brisbane

South Brisbane, Queensland, 4101, Australia

Location

Icon Cancer Care

South Brisbane, Queensland, 4101, Australia

Location

South Coast Radiology

Tugun, Queensland, 4224, Australia

Location

Adelaide Cancer Centre

Kurralta Park, South Australia, 5037, Australia

Location

Ashford Cancer Centre Research

Kurralta Park, South Australia, 5037, Australia

Location

Cancer Care SA Pty Ltd

Kurralta Park, South Australia, 5037, Australia

Location

Tenpharm Pty Ltd trading as EPIC Pharmacy Tennyson

Kurralta Park, South Australia, 5037, Australia

Location

Moorabbin Radiology

Bentleigh East, Victoria, 3165, Australia

Location

Box Hill Hospital

Box Hill, Victoria, 3128, Australia

Location

Monash Medical Centre

Clayton, Victoria, 3168, Australia

Location

Cabrini Health - Cabrini Hospital

Malvern, Victoria, 3144, Australia

Location

Border Medical Oncology

Wodonga, Victoria, 3690, Australia

Location

Algemeen Ziekenhuis Groeninge

Kortrijk, West-vlaanderen, 8500, Belgium

Location

Cliniques universitaires saint-Luc

Brussels, 1200, Belgium

Location

Universitaire Ziekenhuizen Leuven

Leuven, 3000, Belgium

Location

Rigshospitalet CPC 7521

Copenhagen, Norrebro, 2200, Denmark

Location

Arhus Universitetshospital

Arhus N, 8200, Denmark

Location

Rigshospitalet

Copenhagen, 2100, Denmark

Location

Frederiksberg Hospital

Frederiksberg, 2000, Denmark

Location

Helsingin yliopistollinen keskussairaala, Meilahden sairaala

Helsinki, 00290, Finland

Location

Oulun yliopistollinen sairaala

Oulu, 90220, Finland

Location

Tampereen yliopistollinen Sairaala

Tampere, 33520, Finland

Location

Institut Gustave Roussy - Service d'Urologie

Villejuif, 94805, France

Location

U.O. Oncologia Medica, IRCCS Istituto Scientifico Romagnolo per lo Studio e la Cura

Meldola, FC, 47014, Italy

Location

Medicina Nucleare, Azienda Ospedaliera "Istituti Ospitalieri" di Cremona

Cremona, 26100, Italy

Location

Servizio di Radiologia, Azienda Ospedaliera "Istituti Ospitalieri" di Cremona

Cremona, 26100, Italy

Location

Struttura Complessa di Oncologia, Azienda Socio Sanitaria Territoriale di Cremona

Cremona, 26100, Italy

Location

Laboratorio Farmaci Antiblastici

Meldola (FC), 47014, Italy

Location

UO Radiologia

Meldola (FC), 47014, Italy

Location

SCDU Oncologia Medica II Pad, A.O.U. San Luigi Gonzaga

Orbassano to, 10043, Italy

Location

SCDU Radiodiagnostica, A.O.U. San Luigi Gonzaga

Orbassano to, 10043, Italy

Location

SS Medicina Nucleare, A.O.U. San Luigi Gonzaga

Orbassano to, 10043, Italy

Location

Azienda Ospedaliera S. Camillo Forlanini, UOC per il governo clinico in Oncologia Medica

Roma, 00152, Italy

Location

UOC Radiologia Piasta, Azienda Ospedaliera S. Camillo Forlanini

Roma, 00512, Italy

Location

Fakultna nemocnica s poliklinikou F.D. Roosevelta

Banská Bystrica, 975 17, Slovakia

Location

Institut nuklearnej a molekularnej mediciny

Banská Bystrica, 975 17, Slovakia

Location

Fakultna nemocnica s poliklinikou F.D. Roosevelta

Banská Bystrica, 97517, Slovakia

Location

Bratislavske radiodiagnosticke centrum,a.s.

Bratislava, 814 99, Slovakia

Location

CUIMED, s.r.o., urologicka ambulancia

Bratislava, 851 05, Slovakia

Location

Univerzitna nemocnica martin

Martin, 036 59, Slovakia

Location

Jessenius-diagnosticke centrum, a.s.

Nitra, 949 01, Slovakia

Location

Uroexam, spol. s r.o., Urologicka ambulancia

Nitra, 949 01, Slovakia

Location

IZOTOPCENTRUM, s.r.o.

Nitra, 950 01, Slovakia

Location

GAMMALAB, spol.s r.o., Oddelenie nuklearnej mediciny

Trnava, 917 01, Slovakia

Location

Hospital Universitario Son Espases

Palma, Balearic Islands, 07120, Spain

Location

CO Badalona-Instituto Germans Trias i Pujol

Badalona, Barcelona, 08916, Spain

Location

ICO Badalona-Instituto Germans Trias i Pujol

Badalona, Barcelona, 08916, Spain

Location

ALTAHIA, Xarxa Assistencial Universitaria de Manresa

Manresa, Barcelona, 08243, Spain

Location

Hospital Universitari Parc Tauli

Sabadell, Barcelona, 08208, Spain

Location

ICO Badalona-Instituto Germans Trias i Pujol

Badalona, Barcelon, 08916, Spain

Location

Hospital del Mar

Barcelona, 08003, Spain

Location

Hospital Clinic de Barcelona

Barcelona, 08036, Spain

Location

Hospital Universitario Madrid Sanchinarro

Madrid, 28050, Spain

Location

Urologmottagningen

Gothenburg, 41345, Sweden

Location

Urologiska kliniken

Malmo, 20502, Sweden

Location

Oriola

Mölnlycke, 435 25, Sweden

Location

Apoteket AB Kliniska Provningar Molnlycke

Mölnlycke, 435 33, Sweden

Location

Rontgenkliniken

Örebro, 701 85, Sweden

Location

Urologmottagningen

Örebro, 701 85, Sweden

Location

East and North Hertfordshire NHS Trust

Northwood, Middlesex, HA6 2RN, United Kingdom

Location

The Royal Marsden NHS Foundation Trust

Sutton, Surrey, SM2 5PT, United Kingdom

Location

Velindre NHS Trust

Cardiff, CF14 2TL, United Kingdom

Location

University College Hospitals NHS Trust

London, NW1 2BU, United Kingdom

Location

The Royal Marsden NHS Foundation Trust

London, SW3 6JJ, United Kingdom

Location

University College London Hospitals NHS Foundation Trust

London, WC1E 6AG, United Kingdom

Location

Oxford University Hospitals NHS Trust

Oxford, OX3 7LE, United Kingdom

Location

Related Publications (1)

  • Attard G, Borre M, Gurney H, Loriot Y, Andresen-Daniil C, Kalleda R, Pham T, Taplin ME; PLATO collaborators. Abiraterone Alone or in Combination With Enzalutamide in Metastatic Castration-Resistant Prostate Cancer With Rising Prostate-Specific Antigen During Enzalutamide Treatment. J Clin Oncol. 2018 Sep 1;36(25):2639-2646. doi: 10.1200/JCO.2018.77.9827. Epub 2018 Jul 20.

MeSH Terms

Conditions

Prostatic Neoplasms

Interventions

enzalutamideabirateroneAbiraterone AcetatePrednisonePrednisolone

Condition Hierarchy (Ancestors)

Genital Neoplasms, MaleUrogenital NeoplasmsNeoplasms by SiteNeoplasmsGenital Diseases, MaleGenital DiseasesUrogenital DiseasesProstatic DiseasesMale Urogenital Diseases

Intervention Hierarchy (Ancestors)

AndrostenesAndrostanesSteroidsFused-Ring CompoundsPolycyclic CompoundsPregnadienediolsPregnadienesPregnanesPregnadienetriols

Results Point of Contact

Title
Pfizer ClinicalTrials.gov Call Center
Organization
Pfizer, Inc.

Study Officials

  • Pfizer CT.gov Call Center

    Pfizer

    STUDY DIRECTOR
  • Medical Director

    Medviation, Inc.

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 4
Allocation
RANDOMIZED
Masking
QUADRUPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR, OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

November 18, 2013

First Posted

November 26, 2013

Study Start

October 22, 2013

Primary Completion

November 15, 2016

Study Completion

August 31, 2022

Last Updated

September 18, 2023

Results First Posted

November 17, 2017

Record last verified: 2023-08

Data Sharing

IPD Sharing
Will share

Pfizer will provide access to individual de-identified participant data and related study documents (e.g. protocol, Statistical Analysis Plan (SAP), Clinical Study Report (CSR)) upon request from qualified researchers, and subject to certain criteria, conditions, and exceptions. Further details on Pfizer's data sharing criteria and process for requesting access can be found at: https://www.pfizer.com/science/clinical\_trials/trial\_data\_and\_results/data\_requests.

More information

Locations