NCT01991041

Brief Summary

This is a registry study, where sites will enter patients with LGS who require a modification in anti-epileptic therapy (either the addition of another anti-epileptic drug, or the change of one drug to another). This will include patients who are started on rufinamide. Patients will be reviewed according to local practice, but it is envisaged that review will occur at approximately one month, three months and six months, and then every six months. Upon entry to the registry baseline details concerning disease severity, diagnosis, prior therapy, and developmental assessment will be recorded. On each subsequent visit the patient (usually through their caregiver) will be asked about current medication, general seizure profile, any seizures deemed to be of medical significance, tolerability, AEs (including suicidal-related events), and healthcare resource utilisation.

Trial Health

93
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
109

participants targeted

Target at P50-P75 for all trials

Timeline
Completed

Started Jun 2008

Longer than P75 for all trials

Geographic Reach
8 countries

49 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

June 1, 2008

Completed
5.5 years until next milestone

First Submitted

Initial submission to the registry

November 18, 2013

Completed
7 days until next milestone

First Posted

Study publicly available on registry

November 25, 2013

Completed
1.8 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

October 1, 2015

Completed
1 month until next milestone

Study Completion

Last participant's last visit for all outcomes

November 1, 2015

Completed
Last Updated

May 4, 2016

Status Verified

May 1, 2016

Enrollment Period

7.3 years

First QC Date

November 18, 2013

Last Update Submit

May 3, 2016

Conditions

Keywords

Lennox-Gastaut Syndrome

Outcome Measures

Primary Outcomes (1)

  • Safety during the use of rufinamide and other anti-epileptic drugs

    Evaluation of the incidence of seizures of medical significance (including status epilepticus, new / worsening of seizure types and withdrawal seizures) during exposure to anti-epileptic drugs, including rufinamide, in patients with LGS; incidence of hypersensitivity reactions during the exposure to anti-epileptic drugs, including rufinamide; common AEs identified with anti-epileptic drugs, as they may be related to this specific population; including sedation, neurological AEs, suicidal-related events, events associated with blood dyscrasias, and the potential increased risk of infections.

    At least three years

Secondary Outcomes (1)

  • Long term use of rufinamide, and other anti-epileptic drugs

    At least three years

Study Arms (2)

Rufinamide

Anti-Epileptic Drugs

Includes those used off label as part of local clinical practice

Eligibility Criteria

Age4 Years+
Sexall
Healthy VolunteersNo
Age GroupsChild (0-17), Adult (18-64), Older Adult (65+)
Sampling MethodNon-Probability Sample
Study Population

Participation in this study will be offered to any patient of four years or older, who has a known diagnosis of LGS, who requires a change in anti-epileptic therapy. This will include patients who are started on rufinamide, as an adjuvant therapy.

You may qualify if:

  • Patients will be four years and older
  • Patients will have an established diagnosis of Lennox-Gastaut syndrome, and:
  • Documented history or current presence of multiple seizure types associated with LGS (including tonic or atonic seizures (drop attacks) and atypical absences)
  • Documented history or current presence of typical EEG abnormalities (e.g., bursts of slow spike and wave activity)
  • Presence of intellectual / learning disability (a variable degree is permitted)
  • Patients entered on the registry will be those requiring a modification in their current anti-epileptic medication. This includes but is not limited to patients who are commenced on rufinamide as adjuvant therapy

You may not qualify if:

  • Female patients who are pregnant, lactating, or whom are planning to become pregnant
  • Female patients, of child bearing potential, who are not willing to use appropriate contraception (This is at the discretion of the investigator)
  • Those starting rufinamide and for whom the investigator considers it necessary to administer in contradiction to the indications, and warnings within the current Summary of Product Characteristics (SPC).

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (49)

Unknown Facility

Graz, Austria

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Innsbruck, Austria

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Linz, Austria

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Mödling, Austria

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Steyr, Austria

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Vienna, Austria

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Wein, Austria

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Copenhagen, Denmark

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Dianalund, Denmark

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Besançon, France

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Lyon, France

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Marseille, France

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Paris, France

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Reims, France

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Strasbourg, France

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Tain-l'Hermitage, France

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Berlin, Germany

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Bernau, Germany

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Bielefeld, Germany

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Bonn, Germany

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Erlangen, Germany

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Freiburg im Breisgau, Germany

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Hamburg, Germany

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Heidelberg, Germany

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Jena, Germany

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Kehl, Germany

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Kiel, Germany

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Münster, Germany

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Stuttgart, Germany

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Tübingen, Germany

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Vogtareuth, Germany

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Mantova, Italy

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Milan, Italy

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Padua, Italy

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Roma, Italy

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Trieste, Italy

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Verona, Italy

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Barcelona, Spain

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Córdoba, Spain

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Esplugues de Llobregat, Spain

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Madrid, Spain

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Málaga, Spain

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Pamplona, Spain

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Lund, Sweden

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Birmingham, United Kingdom

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Cardiff, United Kingdom

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London, United Kingdom

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Manchester, United Kingdom

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West Yorkshire, United Kingdom

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Related Publications (1)

  • Nikanorova M, Brandt C, Auvin S, McMurray R. Real-world data on rufinamide treatment in patients with Lennox-Gastaut syndrome: Results from a European noninterventional registry study. Epilepsy Behav. 2017 Nov;76:63-70. doi: 10.1016/j.yebeh.2017.08.026. Epub 2017 Sep 15.

MeSH Terms

Conditions

Lennox Gastaut Syndrome

Condition Hierarchy (Ancestors)

Epileptic SyndromesEpilepsyBrain DiseasesCentral Nervous System DiseasesNervous System DiseasesGenetic Diseases, InbornCongenital, Hereditary, and Neonatal Diseases and Abnormalities

Study Design

Study Type
observational
Observational Model
COHORT
Time Perspective
PROSPECTIVE
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

November 18, 2013

First Posted

November 25, 2013

Study Start

June 1, 2008

Primary Completion

October 1, 2015

Study Completion

November 1, 2015

Last Updated

May 4, 2016

Record last verified: 2016-05

Locations