NCT01969799

Brief Summary

To demonstrate the safety and efficacy of adjunctive therapy with the Amikacin fosfomycin inhalation system (AFIS) versus aerosolized placebo to treat Gram-negative pneumonia in mechanically ventilated patients receiving IV antibiotics.

Trial Health

93
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
143

participants targeted

Target at P75+ for phase_2

Timeline
Completed

Started Dec 2013

Geographic Reach
7 countries

41 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

October 22, 2013

Completed
3 days until next milestone

First Posted

Study publicly available on registry

October 25, 2013

Completed
1 month until next milestone

Study Start

First participant enrolled

December 1, 2013

Completed
2.2 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

March 1, 2016

Completed
1 month until next milestone

Study Completion

Last participant's last visit for all outcomes

April 1, 2016

Completed
1.3 years until next milestone

Results Posted

Study results publicly available

July 2, 2017

Completed
Last Updated

July 2, 2017

Status Verified

March 1, 2016

Enrollment Period

2.2 years

First QC Date

October 22, 2013

Results QC Date

July 8, 2016

Last Update Submit

June 4, 2017

Conditions

Keywords

Gram-negative pneumoniaAerosol antibioticsMechanical ventilationAmikacinFosfomycinPneumonia, BacterialPneumoniaBacterial InfectionsLung DiseasesRespiratory Tract DiseasesRespiratory Tract InfectionsAnti-Bacterial AgentsAnti-Infective AgentsTherapeutic UsesPharmacologic Actions

Outcome Measures

Primary Outcomes (1)

  • Change From Baseline in Clinical Pulmonary Infection Score (CPIS) For Each Patient, Value Obtained From a Daily Assessment Over the 10 Day Study Period Was Compared to Baseline, and the LSM Data Represent the Change From Baseline Data Over All Days .

    Change from baseline in Clinical Pulmonary Infection Score (CPIS) For each patient, value obtained from a daily assessment over the 10 day study period was compared to baseline, and the LSM data represent the change from baseline data over all days. Daily CPIS will be determined by one blinded, central reviewer in order to minimize inter-observer variability. The scale ranges from 0 to 13, with 13 being the worst. The value of zero would be a healthy patient with no evidence of pneumonia. For each patient, there was a daily assessment for the 10 day study period.

    10 day treatment period.

Secondary Outcomes (7)

  • Composite Endpoint of Mortality and Clinical Cure

    Day 1 - Day 28

  • Composite Endpoint of Mortality and Ventilator-free Days

    Day 1- Day 28

  • Number of Days Free of Mechanical Ventilation From Day 1 Through Day 28

    Day 1 - Day 28

  • Number of ICU Days From Day 1 Through Day 28

    Day 1 - Day 28

  • Microbiological Response Rates in Patients Positive for Multi-drug Resistant Gram-negative Bacteria

    Day 14

  • +2 more secondary outcomes

Study Arms (2)

Amikacin fosfomycin inhalation solution

EXPERIMENTAL

300 mg of amikacin and 120 mg of fosfomycin twice daily for 10 days to be administered by aerosol via the eFlow Inline System.

Drug: Amikacin fosfomycin inhalation solution

Aerosolized placebo

PLACEBO COMPARATOR

Aerosolized placebo twice daily for 10 days administered using the eFlow Inline System

Drug: Aerosolized placebo

Interventions

300 mg of amikacin and 120 mg of fosfomycin twice daily for 10 days to be administered by aerosol via the eFlow Inline System

Also known as: Amikacin fosfomycin inhalation system (AFIS), eFlow Inline System
Amikacin fosfomycin inhalation solution

Placebo twice daily for 10 days to be administered by aerosol the eFlow Inline System

Also known as: eFlow Inline System
Aerosolized placebo

Eligibility Criteria

Age18 Years - 80 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Males and non-pregnant, non-lactating females, ≥ 18 years and ≤ 80 years of age
  • Intubated and mechanically ventilated
  • Diagnosis of pneumonia, defined as presence of a new or progressive infiltrate(s) on the most recent chest radiograph prior to screening, as determined by the treating physician
  • Signs of infection (within 24 hours prior to screening):
  • Fever (\> 38ºC or \> 100.4ºF); or
  • Leukopenia (\< 4,000 WBC/mm3) or leukocytosis (≥ 12,000 WBC/mm3)
  • Impaired oxygenation (within 24 hours prior to screening):
  • a. PaO2/FiO2 ≤ 350 mmHg
  • Acute Physiology and Chronic Health Evaluation (APACHE) II score \> 10 (within 24 hours prior to screening)
  • Presence, or high suspicion, of Gram-negative organism(s) by either Gram stain or culture of respiratory secretions from a sample obtained within the previous 7 days (enrollment can occur before culture results are available)

You may not qualify if:

  • History of hypersensitivity to amikacin, other aminoglycosides, fosfomycin, imipenem, meropenem, or colistin
  • Received systemic antibiotic therapy for this episode of Gram-negative pneumonia for greater than 72 hours at the time of randomization
  • PaO2/FiO2 ≤ 100 mmHg and diffuse infiltrates on Chest X-ray
  • Refractory septic shock (severe sepsis plus unstable hypotension, in spite of adequate fluid resuscitation and vasopressors)
  • Any of the following conditions that interfere with the assessment or interpretation of the diagnosis or response to therapy:
  • chest trauma with ongoing loss of stability of the thoracic cage following a fracture of the sternum, ribs, or both;
  • increased amounts of fluid in the lung cavities requiring chest tube drainage;
  • lung cancer within the last 2 years;
  • lung abscess(s);
  • anatomical bronchial obstruction;
  • suspected atypical pneumonia;
  • chemical pneumonitis (e.g., inhalation injury);
  • cystic fibrosis
  • Immunocompromised patients, including those with neutropenia NOT due to the current infection (absolute neutrophil count \< 500/mm3), leukemia, lymphoma, human immunodeficiency virus (HIV) infection with CD4 count \< 200 cells/mm3, or splenectomy; those who are early post-transplantation (\< 3 months post-transplant, or \> 3 months post-transplant with evidence of organ rejection by clinical criteria, pathologic confirmation, or modification of immunosuppression within the past 4 weeks), are on cytotoxic chemotherapy, or are on high-dose steroids (e.g., \> 40 mg of prednisone or its equivalent \[\> 160 mg hydrocortisone, \> 32 mg methylprednisolone, \> 6 mg dexamethasone, \> 200 mg cortisone\] daily for \> 2 weeks)
  • Evidence of significant renal impairment (serum creatinine \> 4.0 mg/dL within 24 hours prior to screening). If serum creatinine is \>2.0 mg/dL, site must be capable of performing continuous renal replacement therapy, if clinically indicated. Patients with serum creatinine \> 4.0 mg/dL and being treated with continuous renal replacement therapy (continuous venous-venous hemofiltration or continuous venous-venous hemodialysis) or chronic hemodialysis are eligible
  • +6 more criteria

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (41)

Unknown Facility

Los Angeles, California, 90033, United States

Location

Unknown Facility

Gainesville, Florida, 32610, United States

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Unknown Facility

Jacksonville, Florida, 32209, United States

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Unknown Facility

Chicago, Illinois, 60612, United States

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Unknown Facility

Hazard, Kentucky, 41701, United States

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Unknown Facility

Lexington, Kentucky, 21686, United States

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Unknown Facility

Boston, Massachusetts, 02119, United States

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Unknown Facility

Burlington, Massachusetts, 01805, United States

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Unknown Facility

Springfield, Massachusetts, 01199, United States

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Unknown Facility

Detroit, Michigan, 48202, United States

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Unknown Facility

St Louis, Missouri, 63110, United States

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Unknown Facility

Omaha, Nebraska, 60198, United States

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Unknown Facility

Oklahoma City, Oklahoma, 73104, United States

Location

Unknown Facility

Knoxville, Tennessee, 37920, United States

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Unknown Facility

El Paso, Texas, 79905, United States

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Unknown Facility

Houston, Texas, 77030, United States

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Unknown Facility

Limoges, Limousin, 87042, France

Location

Unknown Facility

Orléans, Loiret, 45000, France

Location

Unknown Facility

Vandœuvre-lès-Nancy, Meurthe-et-Moselle, 54500, France

Location

Unknown Facility

Tours, 37044, France

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Unknown Facility

Colombes, Île-de-France Region, 92701, France

Location

Unknown Facility

Alexandroupoli, Evros, 68100, Greece

Location

Unknown Facility

Athens, 10676, Greece

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Unknown Facility

Athens, 11527, Greece

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Unknown Facility

Athens, 12462, Greece

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Unknown Facility

Athens, 15227, Greece

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Unknown Facility

Ioannina, 45500, Greece

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Unknown Facility

Larissa, 41334, Greece

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Unknown Facility

Debrecen, Hajdú-Bihar, 4012, Hungary

Location

Unknown Facility

Debrecen, Hajdú-Bihar, 4043, Hungary

Location

Unknown Facility

Budapest, 1081, Hungary

Location

Unknown Facility

Budapest, 1125, Hungary

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Unknown Facility

San Juan, 00921, Puerto Rico

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Unknown Facility

Palma de Majorca, Balearic Islands, 07010, Spain

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Unknown Facility

Getafe, Madrid, 28905, Spain

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Unknown Facility

Barcelona, 08036, Spain

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Unknown Facility

Ankara, Ankara, 06100, Turkey (Türkiye)

Location

Unknown Facility

Ankara, 06110, Turkey (Türkiye)

Location

Unknown Facility

Istanbul, 34098, Turkey (Türkiye)

Location

Unknown Facility

Istanbul, 34760, Turkey (Türkiye)

Location

Unknown Facility

Trabzon, 61080, Turkey (Türkiye)

Location

Related Publications (1)

  • Kollef MH, Ricard JD, Roux D, Francois B, Ischaki E, Rozgonyi Z, Boulain T, Ivanyi Z, Janos G, Garot D, Koura F, Zakynthinos E, Dimopoulos G, Torres A, Danker W, Montgomery AB. A Randomized Trial of the Amikacin Fosfomycin Inhalation System for the Adjunctive Therapy of Gram-Negative Ventilator-Associated Pneumonia: IASIS Trial. Chest. 2017 Jun;151(6):1239-1246. doi: 10.1016/j.chest.2016.11.026. Epub 2016 Nov 24.

Related Links

MeSH Terms

Conditions

Pneumonia, BacterialPneumoniaBacterial InfectionsLung DiseasesRespiratory Tract DiseasesRespiratory Tract Infections

Condition Hierarchy (Ancestors)

Bacterial Infections and MycosesInfections

Results Point of Contact

Title
Bruce Montgomery, MD
Organization
Cardeas Pharma

Study Officials

  • Marin Kollef, M.D.

    Washington University School of Medicine

    PRINCIPAL INVESTIGATOR

Publication Agreements

PI is Sponsor Employee
No
Restrictive Agreement
No

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
QUADRUPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR, OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

October 22, 2013

First Posted

October 25, 2013

Study Start

December 1, 2013

Primary Completion

March 1, 2016

Study Completion

April 1, 2016

Last Updated

July 2, 2017

Results First Posted

July 2, 2017

Record last verified: 2016-03

Locations