NCT01966289

Brief Summary

This study will be looking at whether CY/GVAX in combination with SGI-110 is effective (recruits CD45RO+ T cells to the tumor which may be a marker of anti-tumor activity) and safe in patients with metastatic colon or rectum cancers.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
18

participants targeted

Target at P25-P50 for phase_1

Timeline
Completed

Started Apr 2014

Longer than P75 for phase_1

Geographic Reach
1 country

1 active site

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

October 10, 2013

Completed
11 days until next milestone

First Posted

Study publicly available on registry

October 21, 2013

Completed
6 months until next milestone

Study Start

First participant enrolled

April 14, 2014

Completed
6.2 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

June 6, 2020

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

June 6, 2020

Completed
Last Updated

March 30, 2021

Status Verified

March 1, 2021

Enrollment Period

6.2 years

First QC Date

October 10, 2013

Last Update Submit

March 26, 2021

Conditions

Keywords

Colorectal NeoplasmsIntestinal NeoplasmsGastrointestinal NeoplasmsDigestive System NeoplasmsNeoplasms by SiteNeoplasmsDigestive System DiseasesGastrointestinal DiseasesColonic DiseasesIntestinal DiseasesRectal Diseases

Outcome Measures

Primary Outcomes (2)

  • Difference in CD45RO+ tumor infiltrating lymphocytes (TILs) measured by immunohistochemistry in pre and post-treatment tumor biopsies from patients with metastatic colorectal cancer

    4 years

  • Number of Participants with Adverse Events as a Measure of Safety and Tolerability

    4 years

Secondary Outcomes (3)

  • Overall Survival (OS)

    4 years

  • Time To Progression (TTP)

    4 years

  • Progression Free Survival (PFS)

    4 years

Study Arms (4)

Cohort 1:CY/GVAX concurrently with SGI-110

EXPERIMENTAL

During each of the four cycles, Cyclophosphamide (CY) is administered on Day 1 at 200 mg/m2, the colon cancer tumor vaccine (GVAX) is administered on Day 2 at 5E8 colon cancer cells + 5E7 Granulocyte macrophage-colony stimulating factor (GM-CSF) secreting cells, and SGI-110 is administered on Days 1-5 at 60 mg/m2. Each cycle is 28 days. Enrollment will begin first in Cohort 1 and 2. If a response to the treatment is seen in Cohorts 1 and 2, enrollment in Cohort 3 and 4 will begin.

Drug: CYBiological: GVAXDrug: SGI-110

Cohort 2: CY/GVAX after SGI-110

EXPERIMENTAL

During each of the four cycles, SGI-110 is administered on Days 1-5 at 60 mg/m2, Cyclophosphamide (CY) is administered on Day 8 at 200 mg/m2, and the colon cancer tumor vaccine (GVAX) is administered on Day 9 at 5E8 colon cancer cells + 5E7 GM-CSF secreting cells. Each cycle is 28 days. Enrollment will begin first in Cohort 1 and 2. If a response to the treatment is seen in Cohorts 1 and 2, enrollment in Cohort 3 and 4 will begin.

Drug: CYBiological: GVAXDrug: SGI-110

Cohort 3: CY/GVAX

EXPERIMENTAL

During each of the four cycles, Cyclophosphamide (CY) is administered on Day 1 at 200 mg/m2 and the colon cancer tumor vaccine (GVAX) is administered on Day 2 at 5E8 colon cancer cells + 5E7 GM-CSF secreting cells. Each cycle is 28 days. Enrollment will begin first in Cohort 1 and 2. If a response to the treatment is seen in Cohorts 1 and 2, enrollment in Cohort 3 and 4 will begin.

Drug: CYBiological: GVAX

Cohort 4: SGI-110

EXPERIMENTAL

During each of the four cycles, SGI-110 is administered on Days 1-5 at 60 mg/m2. Each cycle is 28 days. Enrollment will begin first in Cohort 1 and 2. If a response to the treatment is seen in Cohorts 1 and 2, enrollment in Cohort 3 and 4 will begin.

Drug: SGI-110

Interventions

CYDRUG

CY is administered intravenously at 200 mg/m2

Also known as: Cyclophosphamide, Cytoxan
Cohort 1:CY/GVAX concurrently with SGI-110Cohort 2: CY/GVAX after SGI-110Cohort 3: CY/GVAX
GVAXBIOLOGICAL

GVAX is administered intradermally at 5E8 colon cancer cells + 5E7 GM-CSF secreting cells

Also known as: Colon cancer tumor vaccine
Cohort 1:CY/GVAX concurrently with SGI-110Cohort 2: CY/GVAX after SGI-110Cohort 3: CY/GVAX

SGI-110 is administered subcutaneously at 60 mg/m2

Cohort 1:CY/GVAX concurrently with SGI-110Cohort 2: CY/GVAX after SGI-110Cohort 4: SGI-110

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Documented cancer of the colon or rectum who have received and are stable on first or second-line therapy regimens for metastatic colorectal cancer
  • Eastern Cooperative Oncology Group (ECOG) Performance Status of 0 to 1
  • Adequate organ function as defined by study-specified laboratory tests
  • Must use acceptable form of birth control through the study and for 28 days after final dose of study drug
  • Signed informed consent form
  • Willing and able to comply with study procedures

You may not qualify if:

  • Currently have or have history of certain study-specified heart, liver, kidney, lung, neurological, immune or other medical conditions
  • Systemically active steroid use
  • Another investigational product within 28 days prior to receiving study drug
  • Major surgery or significant traumatic injury (or unhealed surgical wounds) occurring within 28 days prior to receiving study drug
  • Chemotherapy, radiation, hormonal, or biological cancer therapy within 28 days prior to receiving study drug
  • Pregnant or lactating
  • Unwilling or unable to comply with study procedures

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (1)

Sidney Kimmel Comprehensive Cancer Center at Johns Hopkins

Baltimore, Maryland, 21231, United States

Location

Related Publications (1)

  • Bever KM, Thomas DL 2nd, Zhang J, Diaz Rivera EA, Rosner GL, Zhu Q, Nauroth JM, Christmas B, Thompson ED, Anders RA, Judkins C, Liu M, Jaffee EM, Ahuja N, Zheng L, Azad NS. A feasibility study of combined epigenetic and vaccine therapy in advanced colorectal cancer with pharmacodynamic endpoint. Clin Epigenetics. 2021 Feb 2;13(1):25. doi: 10.1186/s13148-021-01014-8.

MeSH Terms

Conditions

Colorectal NeoplasmsIntestinal NeoplasmsGastrointestinal NeoplasmsDigestive System NeoplasmsNeoplasms by SiteNeoplasmsDigestive System DiseasesGastrointestinal DiseasesColonic DiseasesIntestinal DiseasesRectal Diseases

Interventions

Cyclophosphamideguadecitabine

Intervention Hierarchy (Ancestors)

Phosphoramide MustardsNitrogen Mustard CompoundsMustard CompoundsHydrocarbons, HalogenatedHydrocarbonsOrganic ChemicalsPhosphoramidesOrganophosphorus Compounds

Study Officials

  • Nilofer Azad, MD

    The Sidney Kimmel Comprehensive Cancer Center at Johns Hopkins

    PRINCIPAL INVESTIGATOR

Study Design

Study Type
interventional
Phase
phase 1
Allocation
RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
OTHER
Responsible Party
SPONSOR

Study Record Dates

First Submitted

October 10, 2013

First Posted

October 21, 2013

Study Start

April 14, 2014

Primary Completion

June 6, 2020

Study Completion

June 6, 2020

Last Updated

March 30, 2021

Record last verified: 2021-03

Locations