NCT01846663

Brief Summary

The purpose of the study is to evaluate the safety of Rifaximin or placebo in subjects with severe hepatic impairment and Hepatic Encephalopathy.

Trial Health

57
Monitor

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
6

participants targeted

Target at below P25 for phase_4

Timeline
Completed

Started Apr 2013

Typical duration for phase_4

Geographic Reach
1 country

28 active sites

Status
terminated

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

April 3, 2013

Completed
21 days until next milestone

First Submitted

Initial submission to the registry

April 24, 2013

Completed
9 days until next milestone

First Posted

Study publicly available on registry

May 3, 2013

Completed
2.8 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

February 22, 2016

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

February 22, 2016

Completed
7.9 years until next milestone

Results Posted

Study results publicly available

January 9, 2024

Completed
Last Updated

January 9, 2024

Status Verified

January 1, 2024

Enrollment Period

2.9 years

First QC Date

April 24, 2013

Results QC Date

December 15, 2023

Last Update Submit

January 8, 2024

Conditions

Keywords

Hepatic EncephalopathyLiver FailureHepatic InsufficiencyLiver DiseasesBrain DiseasesRifaximinCirrhosis

Outcome Measures

Primary Outcomes (1)

  • Proportion of Participants With Hepatic Encephalopathy (HE) Breakthrough Episode

    6 Months

Secondary Outcomes (1)

  • Proportion of Participants With HE-related Hospitalization

    6 Months

Study Arms (2)

Rifaximin

EXPERIMENTAL

Rifaximin, oral, 550 mg BID, 6 months of treatment

Drug: Rifaximin

Placebo

PLACEBO COMPARATOR

Placebo, oral, 0 mg BID, 6 months of treatment

Drug: Placebo

Interventions

Placebo, oral, 0 mg BID, 6 months of treatment

Placebo

Rifaximin, oral, 550 mg BID, 6 months treatment

Also known as: XIFAXAN® Tablets
Rifaximin

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Male or non-pregnant, non-breast feeding female ≥ 18 years old
  • In remission from demonstrated overt HE
  • Had ≥1 episode of overt HE associated with liver disease within the last 6 months
  • MELD score of ≥ 19
  • Has a close family member or other personal contact who is familiar with the subject's HE, can provide continuing oversight to the subject and is willing to be available to the subject during the conduct of the trial

You may not qualify if:

  • HIV
  • History of tuberculosis infection
  • Chronic respiratory insufficiency
  • Current infection and receiving antibiotics
  • Renal insufficiency requiring dialysis
  • Active spontaneous bacterial peritonitis infection
  • Intestinal obstruction or has inflammatory bowel disease
  • Active malignancy within the last 5 years
  • Current GI bleeding or has had a GI hemorrhage within past 3 months
  • Anemia

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (28)

The University of Alabama at Birmingham

Birmingham, Alabama, 35294-0111, United States

Location

Banner Research

Phoenix, Arizona, 85016, United States

Location

University Of Arizona Liver Research Institute

Tucson, Arizona, 85724, United States

Location

Southern California Liver Centers

Coronado, California, 92118, United States

Location

UCSD Clinical & Translational Research Institute

La Jolla, California, 92037, United States

Location

Loma Linda University Medical Center Transplantation Institute

Loma Linda, California, 92324, United States

Location

University of Southern Califorina Keck School Of Medicine

Los Angeles, California, 90033, United States

Location

Cedars-Sinai Medical Center

Los Angeles, California, 90048, United States

Location

Inland Empire Liver Foundation

Rialto, California, 92377, United States

Location

University of Colorado Denver

Aurora, Colorado, 80045, United States

Location

Salix Site

New Haven, Connecticut, 06520, United States

Location

Salix Site

Tampa, Florida, 33606, United States

Location

Piedmont Atlanta Hospital

Atlanta, Georgia, 30309, United States

Location

Northwestern University-Comprehensive Transplant Center

Chicago, Illinois, 60611, United States

Location

Rush University Medical Center

Chicago, Illinois, 60612, United States

Location

Tulane Abdominal Transplant Research Office

New Orleans, Louisiana, 70112, United States

Location

Mayo Clinic

Rochester, Minnesota, 55905, United States

Location

Washington University

St Louis, Missouri, 63110, United States

Location

New York University School of Medicine

New York, New York, 10016, United States

Location

Salix Site

Portland, Oregon, 97239, United States

Location

Vanderbilt University Medical Center

Nashville, Tennessee, 37212-1610, United States

Location

The Liver Institute at Methodist Dallas Medical Center

Dallas, Texas, 75203, United States

Location

Brook Army Medical Center

Fort Sam Houston, Texas, 78234, United States

Location

Salix Site

Galveston, Texas, 77555, United States

Location

The Methodist Hospital

Houston, Texas, 77030, United States

Location

McGuire VA Medical Center

Richmond, Virginia, 23249, United States

Location

VCU/MCV Health Systems

Richmond, Virginia, 23298, United States

Location

Swedish Medical Center

Seattle, Washington, 98122, United States

Location

MeSH Terms

Conditions

Hepatic EncephalopathyLiver FailureHepatic InsufficiencyLiver DiseasesBrain DiseasesFibrosis

Interventions

Rifaximin

Condition Hierarchy (Ancestors)

Digestive System DiseasesBrain Diseases, MetabolicCentral Nervous System DiseasesNervous System DiseasesMetabolic DiseasesNutritional and Metabolic DiseasesPathologic ProcessesPathological Conditions, Signs and Symptoms

Intervention Hierarchy (Ancestors)

RifamycinsHeterocyclic Compounds, 4 or More RingsHeterocyclic Compounds, Fused-RingHeterocyclic CompoundsLactams, MacrocyclicMacrocyclic CompoundsPolycyclic Compounds

Results Point of Contact

Title
Study Director
Organization
Bausch Health Americas, Inc

Study Officials

  • Varsha Bhatt, Ph.D.

    Bausch Health Americas, Inc.

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 4
Allocation
RANDOMIZED
Masking
QUADRUPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR, OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

April 24, 2013

First Posted

May 3, 2013

Study Start

April 3, 2013

Primary Completion

February 22, 2016

Study Completion

February 22, 2016

Last Updated

January 9, 2024

Results First Posted

January 9, 2024

Record last verified: 2024-01

Data Sharing

IPD Sharing
Will share

Locations