NCT01843374

Brief Summary

This is a Phase 2b, randomized, double-blind, parallel-group study. Subjects with unresectable pleural or peritoneal malignant mesothelioma will be randomized in a 2:1 ratio to receive either tremelimumab or placebo. Approximately 564 subjects will be enrolled at study centers in multiple countries. The study consists of a screening period, a treatment period, a 90-day follow-up period for safety, and a long-term survival follow-up period.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Strong global presence with extensive site network
Enrollment
571

participants targeted

Target at P75+ for phase_2

Timeline
10mo left

Started May 2013

Longer than P75 for phase_2

Geographic Reach
19 countries

104 active sites

Status
active not recruiting

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Progress94%
May 2013May 2027

First Submitted

Initial submission to the registry

April 22, 2013

Completed
8 days until next milestone

First Posted

Study publicly available on registry

April 30, 2013

Completed
17 days until next milestone

Study Start

First participant enrolled

May 17, 2013

Completed
2.7 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

January 24, 2016

Completed
1.6 years until next milestone

Results Posted

Study results publicly available

August 17, 2017

Completed
9.8 years until next milestone

Study Completion

Last participant's last visit for all outcomes

May 31, 2027

Expected
Last Updated

July 27, 2026

Status Verified

June 1, 2026

Enrollment Period

2.7 years

First QC Date

April 22, 2013

Results QC Date

April 10, 2017

Last Update Submit

July 8, 2026

Conditions

Keywords

tremelimumabpleural, peritonealmalignant mesotheliomaCTLA-4

Outcome Measures

Primary Outcomes (1)

  • Overall Survival (OS)

    Overall survival (OS) by treatment arm

    3 years.

Secondary Outcomes (9)

  • OS Rate at 18 Months by Treatment Arm

    18 months

  • Progression-free Survival by Treatment Arm

    Time from randomization to disease progression or death, whichever occurs first, assessed up to 3 years.

  • Overall Response Rate by Treatment Arm

    Time from randomization to best response to treatment, assessed up to 3 years.

  • Duration of Response by Treatment Arm

    Duration of response from the first documentation of objcetive response (confirmed CR or PR) to the first documented disease progression, assessed up to 14 weeks after the initial response.

  • Disease Control Rate by Treatment Arm

    Time from randomization to disease progression or death, whichever occurs first, assessed up to 3 years.

  • +4 more secondary outcomes

Study Arms (2)

Tremelimumab

EXPERIMENTAL

Tremelimumab

Drug: Tremelimumab

Placebo

PLACEBO COMPARATOR

Placebo

Drug: Placebo

Interventions

Tremelimumab is to be administered as an IV solution, followed by observation.

Tremelimumab

Placebo is to be administered as an IV solution, followed by observation.

Placebo

Eligibility Criteria

Age18 Years - 99 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Histologically and/or cytologically confirmed pleural or peritoneal malignant mesothelioma;
  • Disease not amenable to curative surgery;
  • Age 18 and over at the time of consent;
  • ECOG Performance status 0-1;
  • Progressed after previous receipt of 1-2 prior systemic treatments for advanced disease that included a first-line pemetrexed (or anti-folate)-based regimen in combination with platinum agent.
  • Recovered from all toxicities associated with prior treatment, to acceptable baseline status, or a NCI CTCAE Grade of 0 or 1, except for toxicities not considered a safety risk,
  • Measurable diseaseby modified RECIST for pleural mesothelioma or RECIST v1.1 for peritoneal mesothelioma;
  • Adequate bone marrow, hepatic, and renal function determined within 14 days prior to randomization defined as:
  • Negative screening test results for human immunodeficiency virus (HIV), hepatitis A, B and C.
  • Written informed consent and any locally required authorization (eg, HIPAA in the USA, EU Data Privacy Directive authorization in the EU) obtained from the subject/legal representative prior to performing any protocol- related procedures, including screening evaluations;
  • Females of childbearing potential who are sexually active with a nonsterilized male partner must use a highly effective method of contraception for 28 days prior to the first dose of investigational product, and must agree to continue using such precautions for 6 months after the final dose of investigational product; cessation of contraception after this point should be discussed with a responsible physician.
  • Nonsterilized males who are sexually active with a female partner of childbearing potential must use a highly effective method of contraception from Days 1 through 90 post last dose. In addition, they must refrain from sperm donation for 90 days after the final dose of investigational product.

You may not qualify if:

  • Subjects who failed more than 2 prior systemic treatment regimens for advanced malignant mesothelioma;
  • Received any prior mAb against CTLA-4, programmed cell death 1 (PD1) or programmed cell death 1 ligand 1 (PD-L1);
  • History of chronic inflammatory or autoimmune disease with symptomatic disease within the last 3 years prior to randomization.
  • Active, untreated central nervous system (CNS) metastasis
  • Any serious uncontrolled medical disorder or active infection that would impair the subject's ability to receive investigational product;
  • History of other malignancy unless the subject has been disease-free for at least 3 years;
  • Pregnant or breast feeding at time of consent;
  • Any condition that would prohibit the understanding or rendering of information and consent and compliance with the requirements of this protocol;
  • Active or history of diverticulitis;
  • Active or history of inflammatory bowel disease, irritable bowel disease, celiac disease or other serious gastrointestinal chronic conditions associated with diarrhea. Active or history of systemic lupus erythematosus or granulomatosis with polyangiitis;
  • History of sarcoidosis syndrome;
  • Currently receiving systemic corticosteroids or other immunosuppressive medications or has a medical condition that requires the chronic use of corticosteroids.
  • Subjects should not be vaccinated with live attenuated vaccines within one month prior to starting tremelimumab treatment;
  • The last dose of prior chemotherapy or radiation therapy was received less than 2 weeks prior to randomization;
  • Any unresolved toxicity NCI CTCAE Grade ≥ 2 from previous anticancer therapy with the exception of vitiligo and alopecia;
  • +4 more criteria

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (104)

Research Site

Scottsdale, Arizona, 85259, United States

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La Jolla, California, 92093, United States

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Los Angeles, California, 90025, United States

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San Francisco, California, 94143, United States

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Santa Monica, California, 90404, United States

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New Haven, Connecticut, 06511, United States

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Newark, Delaware, 19718, United States

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Tampa, Florida, 33612, United States

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Augusta, Georgia, 30912, United States

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Chicago, Illinois, 60637, United States

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Peoria, Illinois, 61615, United States

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Baltimore, Maryland, 21201, United States

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Baltimore, Maryland, 21231, United States

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Minneapolis, Minnesota, 55445, United States

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New York, New York, 10065, United States

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Rochester, New York, 14642, United States

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Durham, North Carolina, 27710, United States

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Canton, Ohio, 44710, United States

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Philadelphia, Pennsylvania, 19104, United States

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Dallas, Texas, 75390, United States

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Houston, Texas, 77030, United States

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Adelaide, 5000, Australia

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Auchenflower, 4066, Australia

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Box Hill, 3128, Australia

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Chermside, 4032, Australia

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East Bentleigh, 3165, Australia

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Gosford, 2250, Australia

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Heidelberg, 3084, Australia

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Nedlands, 6009, Australia

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Saint Leonards, 2065, Australia

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Waratah, 2298, Australia

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Edegem, 2650, Belgium

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Ghent, 9000, Belgium

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Leuven, 3000, Belgium

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Toronto, Ontario, M5G 2M9, Canada

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Sainte-Foy, Quebec, G1V 4G5, Canada

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Copenhagen, 2100, Denmark

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Caen, 14076, France

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Le Mans, 72037, France

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Lille, 59037, France

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Nice, 06189, France

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Rennes, 35033, France

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Toulouse, 31059, France

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Villejuif, 94805, France

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Berlin, 13125, Germany

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Esslingen a.N., 73730, Germany

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Freiburg im Breisgau, 79106, Germany

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Gauting, 82131, Germany

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Großhansdorf, 22927, Germany

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Hamburg, 21075, Germany

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Hemer, 58675, Germany

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Karlsruhe, 76137, Germany

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Löwenstein, 74245, Germany

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Lübeck, 23538, Germany

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Gyöngyös - Mátraháza, 3200, Hungary

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Törökbálint, 2045, Hungary

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Beersheba, 84101, Israel

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Alessandria, 15100, Italy

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Aviano, 33081, Italy

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Bergamo, 24125, Italy

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Bologna, 40138, Italy

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Candiolo, 10060, Italy

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Genova, 16132, Italy

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Meldola, 47014, Italy

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Milan, 20133, Italy

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Orbassano, 10043, Italy

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Padova, 35128, Italy

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Rozzano, 20089, Italy

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Siena, 53100, Italy

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Breda, 4818 CK, Netherlands

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Eindhoven, 5623EJ, Netherlands

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Rotterdam, 3015 GD, Netherlands

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Gdansk, 80-952, Poland

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Poznan, 60-693, Poland

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Szczecin, 70-891, Poland

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Warsaw, 02-781, Poland

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Craiova, 200385, Romania

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Moscow, 115478, Russia

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Nizhny Novgorod, 603006, Russia

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Saint Petersburg, 197022, Russia

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Kraaifontein, 7570, South Africa

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Pretoria, 0081, South Africa

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Pretoria, 0181, South Africa

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Jeonnam, 58128, South Korea

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Seoul, 03722, South Korea

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Seoul, 05505, South Korea

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Seoul, 06351, South Korea

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Barcelona, 08035, Spain

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Donostia / San Sebastian, 20014, Spain

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Madrid, 28040, Spain

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Sabadell (Barcelona), 08208, Spain

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Seville, 41013, Spain

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Linköping, 58185, Sweden

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Lund, 22185, Sweden

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Umeå, SE90185, Sweden

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Leeds, LS9 7TF, United Kingdom

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Leicester, LE1 5WW, United Kingdom

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London, EC1A 7BE, United Kingdom

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London, SE1 9RT, United Kingdom

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Maidstone, ME16 9QQ, United Kingdom

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Manchester, M23 9LT, United Kingdom

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Metropolitan Borough of Wirral, CH63 4JY, United Kingdom

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Plymouth, PL6 8DH, United Kingdom

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Southampton, SO16 6YD, United Kingdom

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Related Publications (2)

  • Baverel P, Roskos L, Tatipalli M, Lee N, Stockman P, Taboada M, Vicini P, Horgan K, Narwal R. Exposure-Response Analysis of Overall Survival for Tremelimumab in Unresectable Malignant Mesothelioma: The Confounding Effect of Disease Status. Clin Transl Sci. 2019 Sep;12(5):450-458. doi: 10.1111/cts.12633. Epub 2019 Apr 12.

  • Maio M, Scherpereel A, Calabro L, Aerts J, Perez SC, Bearz A, Nackaerts K, Fennell DA, Kowalski D, Tsao AS, Taylor P, Grosso F, Antonia SJ, Nowak AK, Taboada M, Puglisi M, Stockman PK, Kindler HL. Tremelimumab as second-line or third-line treatment in relapsed malignant mesothelioma (DETERMINE): a multicentre, international, randomised, double-blind, placebo-controlled phase 2b trial. Lancet Oncol. 2017 Sep;18(9):1261-1273. doi: 10.1016/S1470-2045(17)30446-1. Epub 2017 Jul 17.

Related Links

MeSH Terms

Conditions

Mesothelioma, MalignantDiabetes Mellitus, Insulin-Dependent, 12

Interventions

tremelimumab

Condition Hierarchy (Ancestors)

MesotheliomaAdenomaNeoplasms, Glandular and EpithelialNeoplasms by Histologic TypeNeoplasmsNeoplasms, MesothelialLung NeoplasmsRespiratory Tract NeoplasmsThoracic NeoplasmsNeoplasms by SitePleural NeoplasmsLung DiseasesRespiratory Tract Diseases

Limitations and Caveats

Baseline characteristics and efficacy outcomes are from the primary analysis reported in the main CSR based on a DCO of 24th January 2016. Participant flow and AE results are from the CSR Addendum based on a DBL of 23 January 2017.

Results Point of Contact

Title
Paul Stockman, MD, PhD
Organization
AstraZeneca

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
QUADRUPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR, OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

April 22, 2013

First Posted

April 30, 2013

Study Start

May 17, 2013

Primary Completion

January 24, 2016

Study Completion (Estimated)

May 31, 2027

Last Updated

July 27, 2026

Results First Posted

August 17, 2017

Record last verified: 2026-06

Data Sharing

IPD Sharing
Will share

Qualified researchers can request access to anonymized individual patient-level data from AstraZeneca group of companies sponsored clinical trials via the request portal. All request will be evaluated as per the AZ disclosure commitment: https://astrazenecagrouptrials.pharmacm.com/ST/Submission/Disclosure

Shared Documents
STUDY PROTOCOL, SAP
Time Frame
AstraZeneca will meet or exceed data availability as per the commitments made to the EFPIA Pharma Data Sharing Principles. For details of our timelines, please rerefer to our disclosure commitment at https://astrazenecagrouptrials.pharmacm.com/ST/Submission/Disclosure
Access Criteria
When a request has been approved AstraZeneca will provide access to the de-identified individual patient-level data in an approved sponsored tool . Signed Data Sharing Agreement (non-negotiable contract for data accessors) must be in place before accessing requested information. Additionally, all users will need to accept the terms and conditions of the SAS MSE to gain access. For additional details, please review the Disclosure Statements at https://astrazenecagrouptrials.pharmacm.com/ST/Submission/Disclosure
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