NCT01716442

Brief Summary

Anti-CD20 agent has been proposed as a rescue therapy for refractory nephrotic syndrome(NS) on the basis of favorable clinical observations. Yet the long-term effect on maintaining remission or the likelihood of becoming rituximab-dependent is unclear and the information on the safety profile of rituximab is limited. This trial was designed to investigate the safety and efficacy of Rituximab in children with refractory NS.

Trial Health

43
At Risk

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Trial has exceeded expected completion date
Enrollment
88

participants targeted

Target at P50-P75 for phase_2

Timeline
Completed

Started Aug 2012

Shorter than P25 for phase_2

Geographic Reach
1 country

1 active site

Status
unknown

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

August 1, 2012

Completed
3 months until next milestone

First Submitted

Initial submission to the registry

October 25, 2012

Completed
4 days until next milestone

First Posted

Study publicly available on registry

October 29, 2012

Completed
10 months until next milestone

Primary Completion

Last participant's last visit for primary outcome

September 1, 2013

Completed
2 months until next milestone

Study Completion

Last participant's last visit for all outcomes

November 1, 2013

Completed
Last Updated

October 29, 2012

Status Verified

October 1, 2012

Enrollment Period

1.1 years

First QC Date

October 25, 2012

Last Update Submit

October 26, 2012

Conditions

Keywords

rituximabnephroticrefractory

Outcome Measures

Primary Outcomes (2)

  • The remission rate of steroid-resistant nephrotic syndrome patients after rituximab treatment

    within 6 months from the initiation of treatment

  • The rate of maintaining remission in steroid-dependent nephrotic syndrome patients

    within 6 months from the initiation of treatment versus placebo control

Study Arms (3)

steroid-resistant

ACTIVE COMPARATOR

Steroid-resistant group: n=27 , enroll all for treatment

Drug: Rituximab

steroid-dependent-rituximab

ACTIVE COMPARATOR

steroid-responsive group: n=38

Drug: Rituximab

steroid-dependent-placebo

PLACEBO COMPARATOR

steroid-responsive group: n=23

Drug: Placebo

Interventions

Per dose: Rituximab 375 mg/m2 (max.500mg/day). efficacy monitored by CD19 cell count. If CD19 cells are not depleted, second or third doses are given at 2-3 weeks interval.

Also known as: Mabthera, 2005110300291 (rituximab)
steroid-dependent-rituximabsteroid-resistant
steroid-dependent-placebo

Eligibility Criteria

Age1 Year - 18 Years
Sexall
Healthy VolunteersNo
Age GroupsChild (0-17), Adult (18-64)

You may qualify if:

  • (A)steroid/calcineurin inhibitor resistant nephrotic syndrome
  • steroid resistance: no remission after 4 weeks of daily oral corticosteroid (60mg/m2/day)
  • calcineurin inhibitor resistance: no remission after 3 months of therapeutic dose administration of cyclosporine and/or tacrolimus
  • no remission defined by persistent proteinuria of nephrotic range for the last 3 months
  • post-transplant patients were included in the study
  • (B)steroid-dependent nephrotic syndrome
  • Steroid-dependent patients who had been on various known medications (such as corticosteroids, cyclophosphamide, chlorambucil, calcineurin inhibitors, levamisole ..) continuously for more than 2 years
  • definition of dependency: more than two consecutive relapse events in 2 weeks after discontinuation of steroid or calcineurin inhibitor
  • no improvement in relapsing frequency with calcineurin inhibitor use
  • unable to continue with calcineurin inhibitor due to side effects
  • unable to continue with calcineurin inhibitor due to prolonged use (over 2 years)
  • other conditions in which the clinician considers difficult to control disease with steroids or calcineurin inhibitors only.

You may not qualify if:

  • previous rituximab use
  • secondary nephrotic syndrome
  • estimated GFR \<60mL/min/1.73m2 or under 50% of age-matched standard GFR
  • chronic or acute active infection (e.g. hepatitis B,C, herpes, varicella zoster)
  • prior live vaccine inoculation within 1 month (from the study enrollment)
  • cardiovascular diseases, pulmonary or pleural diseases
  • uncontrolled hypertension
  • leukocytopenia (absolute neutrophil count \<1500/mm3) or thrombocytopenia (\<75000/mm3)
  • pregnancy

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (1)

Seoul National University Children's Hospital

Seoul, 110-740, South Korea

RECRUITING

Related Publications (2)

  • Liu ID, Willis NS, Craig JC, Hodson EM. Interventions for idiopathic steroid-resistant nephrotic syndrome in children. Cochrane Database Syst Rev. 2025 May 8;5(5):CD003594. doi: 10.1002/14651858.CD003594.pub7.

  • Larkins NG, Hahn D, Liu ID, Willis NS, Craig JC, Hodson EM. Non-corticosteroid immunosuppressive medications for steroid-sensitive nephrotic syndrome in children. Cochrane Database Syst Rev. 2024 Nov 8;11(11):CD002290. doi: 10.1002/14651858.CD002290.pub6.

MeSH Terms

Conditions

Nephrotic Syndrome

Interventions

Rituximab

Condition Hierarchy (Ancestors)

NephrosisKidney DiseasesUrologic DiseasesFemale Urogenital DiseasesFemale Urogenital Diseases and Pregnancy ComplicationsUrogenital DiseasesMale Urogenital Diseases

Intervention Hierarchy (Ancestors)

Antibodies, Monoclonal, Murine-DerivedAntibodies, MonoclonalAntibodiesImmunoglobulinsImmunoproteinsBlood ProteinsProteinsAmino Acids, Peptides, and ProteinsSerum GlobulinsGlobulins

Study Officials

  • Hee Gyung Kang A. Kang, M.D., Ph.D.

    Seoul National University Children's Hospital

    PRINCIPAL INVESTIGATOR

Central Study Contacts

Hee Gyung A. Kang, M.D., Ph.D.

CONTACT

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
SINGLE
Who Masked
PARTICIPANT
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
OTHER
Responsible Party
PRINCIPAL INVESTIGATOR
PI Title
Associate Professor

Study Record Dates

First Submitted

October 25, 2012

First Posted

October 29, 2012

Study Start

August 1, 2012

Primary Completion

September 1, 2013

Study Completion

November 1, 2013

Last Updated

October 29, 2012

Record last verified: 2012-10

Locations