NCT01684761

Brief Summary

The purpose of this study is to determine whether Tcelna (imilecleucel-T, autologous T-Cell Immunotherapy) is effective in the treatment of secondary progressive multiple sclerosis (SPMS).

Trial Health

90
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
183

participants targeted

Target at P75+ for phase_2

Timeline
Completed

Started Aug 2012

Typical duration for phase_2

Geographic Reach
2 countries

36 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

August 1, 2012

Completed
1 month until next milestone

First Submitted

Initial submission to the registry

September 11, 2012

Completed
2 days until next milestone

First Posted

Study publicly available on registry

September 13, 2012

Completed
4.1 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

October 1, 2016

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

October 1, 2016

Completed
Last Updated

January 10, 2017

Status Verified

January 1, 2017

Enrollment Period

4.2 years

First QC Date

September 11, 2012

Last Update Submit

January 9, 2017

Conditions

Keywords

Multicenter StudyRandomized Controlled TrialIndividualized MedicineImmunotherapyMyelin ProteinsBiological Agents

Outcome Measures

Primary Outcomes (1)

  • Brain Atrophy

    The percentage of brain volume change (atrophy) as measured on 24 month MRIs calculated by the central MRI facility.

    2 Years

Secondary Outcomes (1)

  • Disease Progression

    2 Years

Study Arms (2)

Tcelna

EXPERIMENTAL

30-45 x 10E6 total cells in 2 ml. Subjects receive two annual courses of 5 subcutaneous doses each year (at 0, 4, 8, 12 and 24 weeks).

Biological: Tcelna

Placebo

PLACEBO COMPARATOR

Tcelna inactive ingredients (without cells) totaling 2 ml per dose. Administered subcutaneously with same two year treatment regimen as experimental treatment arm.

Biological: Placebo

Interventions

TcelnaBIOLOGICAL

Autologous pool of myelin reactive T-cells (MRTC) expanded ex vivo with immunodominant epitopes selected from the three myelin antigens, MBP, PLP and MOG on a per subject basis. Attenuated by irradiation to prevent further proliferation before releasing product for administration.

Tcelna
PlaceboBIOLOGICAL

2 ml of Tcelna excipients, prepared daily as individual doses and irradiated before releasing product for administration.

Placebo

Eligibility Criteria

Age18 Years - 60 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64)

You may qualify if:

  • Diagnosed with MS as defined by the modified McDonald criteria
  • SPMS defined as relapsing-remitting disease with recent progression in MS-related neurological deficits
  • EDSS score 3.0 - 6.0, inclusively
  • Presence of myelin reactive T-cells

You may not qualify if:

  • Diagnosed with primary progressive MS
  • Treatment with beta-interferon, glatiramer acetate or dimethyl fumarate 30 days prior to screening
  • Treatment with ACTH, any over-the-counter or prescription corticosteroids 60 days prior to screening
  • Treatment with IVIG, plasmapheresis or cytopheresis 90 days prior to screening
  • Treatment with mitoxantrone, teriflunomide, fingolimod, natalizumab, azathioprine, cyclosporine, methotrexate or mycophenolate mofetil 1 year prior to baseline
  • Any prior treatment with cladribine, cyclophosphamide, total lymphoid irradiation, T cell or T cell receptor products, or any therapeutic monoclonal antibody, except natalizumab
  • Previous treatment with any other MS investigational drug 1 year prior to screening
  • All non-MS investigational drugs must have a minimum washout of 30 days prior to screening or 5 half-lives, whatever is the longest period of time.
  • HIV or hepatitis infection
  • History of cancer
  • Any other significant medical condition that, in the opinion of the investigator, could cause CNS tissue damage or limit its repair.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (36)

HOPE Research Institute

Phoenix, Arizona, 85050, United States

Location

Northwest NeuroSpecialists, LLC

Tucson, Arizona, 85741, United States

Location

Alta Bates Summit Medical Center, The Research and Education Development Institute

Berkeley, California, 94705, United States

Location

Neurology Associates, P.A.

Maitland, Florida, 32751, United States

Location

University of Miami

Miami, Florida, 33136, United States

Location

Collier Neurologic Specialists, LLC

Naples, Florida, 34102, United States

Location

Neurological Services of Orlando

Orlando, Florida, 32806, United States

Location

Meridien Research

Tampa, Florida, 33606, United States

Location

Vero Beach Neurology

Vero Beach, Florida, 32960, United States

Location

Shepherd Center

Atlanta, Georgia, 30309, United States

Location

Consultants In Neurology, Ltd.

Northbrook, Illinois, 60062, United States

Location

Fort Wayne Neurological Center

Fort Wayne, Indiana, 46804, United States

Location

Josephson Wallack Munshower Neurology, PC

Indianapolis, Indiana, 46256, United States

Location

University of Kansas Medical Center

Kansas City, Kansas, 66160, United States

Location

Associates in Neurology

Lexington, Kentucky, 40503, United States

Location

Saint Elizabeth's Medical Center

Boston, Massachusetts, 02135, United States

Location

Island Neurological Assoicates, PC

Plainview, New York, 11803, United States

Location

University Hospital and Medical Center Stony Brook New York

Stony Brook, New York, 11794-8121, United States

Location

The Neurological Institute, PA

Charlotte, North Carolina, 28204, United States

Location

Carolinas Medical Center Neurology

Charlotte, North Carolina, 28207, United States

Location

PMG Research of Charlotte

Charlotte, North Carolina, 28209, United States

Location

Neurology Specialists, Inc

Dayton, Ohio, 45408, United States

Location

Providence Medical Group - Medford

Medford, Oregon, 97504, United States

Location

Providence St. Vincent Medical Center - Northwest MS Center

Portland, Oregon, 97225, United States

Location

University of Pennsylvania

Philadelphia, Pennsylvania, 19104, United States

Location

The Maxine Mesinger MS Clinic/Baylor College of Medicine

Houston, Texas, 77030, United States

Location

Central Texas Neurology

Round Rock, Texas, 78681, United States

Location

Integra Clinical Research, LLC

San Antonio, Texas, 78229, United States

Location

Fletcher Allen Health Care - Neurology Service

Burlington, Vermont, 05401, United States

Location

Hampton Roads Neurology

Newport News, Virginia, 23601, United States

Location

Neurological Associates, Inc

Richmond, Virginia, 23226, United States

Location

Swedish Neuroscience Institute

Issaquah, Washington, 98029, United States

Location

Swedish Neuroscience Institute

Seattle, Washington, 98122, United States

Location

University of Ottawa

Ottawa, Ontario, K1H 8L6, Canada

Location

Recherche Sepmus Inc.

Greenfield Park, Quebec, J4V 2J2, Canada

Location

Montreal Neurological Institute and Hospital

Montreal, Quebec, H3A 2B4, Canada

Location

Related Links

MeSH Terms

Conditions

Autoimmune Diseases of the Nervous SystemMultiple SclerosisMultiple Sclerosis, Chronic ProgressiveDisease Progression

Condition Hierarchy (Ancestors)

Nervous System DiseasesAutoimmune DiseasesImmune System DiseasesDemyelinating Autoimmune Diseases, CNSDemyelinating DiseasesChronic DiseaseDisease AttributesPathologic ProcessesPathological Conditions, Signs and Symptoms

Study Officials

  • Jessica Jackson

    Opexa Therapeutics, Inc.

    STUDY DIRECTOR

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
QUADRUPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR, OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

September 11, 2012

First Posted

September 13, 2012

Study Start

August 1, 2012

Primary Completion

October 1, 2016

Study Completion

October 1, 2016

Last Updated

January 10, 2017

Record last verified: 2017-01

Locations