NCT01597297

Brief Summary

The objectives of this study in Multiple Sclerosis (MS) participants treated with prolonged-released fampridine (BIIB041) 10 mg twice daily compared with participants treated with placebo are to assess the effect over 24 weeks on the following parameters to explore endpoints for the Phase 3 study: self-assessed walking disability, dynamic and static balance, subjective impression of well-being, and participants' global impression of change in walking . Another purpose of this study is to evaluate the safety and tolerability of prolonged-release fampridine.

Trial Health

93
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
132

participants targeted

Target at P75+ for phase_2 multiple-sclerosis

Timeline
Completed

Started Aug 2012

Shorter than P25 for phase_2 multiple-sclerosis

Geographic Reach
6 countries

23 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

May 10, 2012

Completed
4 days until next milestone

First Posted

Study publicly available on registry

May 14, 2012

Completed
3 months until next milestone

Study Start

First participant enrolled

August 1, 2012

Completed
1 year until next milestone

Primary Completion

Last participant's last visit for primary outcome

August 1, 2013

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

August 1, 2013

Completed
Last Updated

January 9, 2017

Status Verified

January 1, 2017

Enrollment Period

1 year

First QC Date

May 10, 2012

Last Update Submit

January 5, 2017

Conditions

Outcome Measures

Primary Outcomes (7)

  • Change from baseline in self-assessed walking disability as reported on the Multiple Sclerosis Walking Scale-12 (MSWS-12)

    Day 1, up to 24 weeks

  • Change from baseline in static balance as assessed by Berg Balance Scale (BBS)

    Day 1, up to 24 weeks

  • Change from baseline in dynamic balance as assessed by the Timed Up and Go (TUG) scale)

    Day 1, up to 24 weeks

  • Change from baseline in subjective impression of well-being measured by Multiple Sclerosis Impact Scale-29 (MSIS-29)

    Day 1, up to 24 weeks

  • Change from baseline in subjective impression of well-being measured by Euro Quality of Life-5D (EQ-5D)

    Day 1, up to 24 weeks

  • Participant's global impression of change in walking as reported on the Patient Global Impression of Change Scale (PGIC)

    Day 1, up to 24 weeks

  • Summary of Participants with adverse events (AEs) and serious adverse events (SAEs)

    Day 1 Up to 26 weeks

Study Arms (2)

Fampridine-PR

EXPERIMENTAL

Prolonged-Release Fampridine (Fampridine-PR) 10 mg twice daily (every 12 hours) for up to 24 weeks.

Drug: BIIB041 (PR Fampridine)

Placebo

PLACEBO COMPARATOR

Matched placebo twice daily (every 12 hours) for up to 24 weeks.

Other: Placebo

Interventions

10 mg twice daily, given orally. Doses of study treatment must be spaced at least 12 hours apart. If a dose of study treatment is delayed or missed, the participant should not dose again until their next scheduled dose. Tablets must be swallowed whole and should be taken without food.

Also known as: Fampridine-PR (prolonged-release), Dalfampridine-ER (extended-release), FAMPYRA®, AMPYRA®
Fampridine-PR
PlaceboOTHER

Twice daily, given orally. Doses of study treatment must be spaced at least 12 hours apart. If a dose of study treatment is delayed or missed, the participant should not dose again until their next scheduled dose. Tablets must be swallowed whole and should be taken without food.

Placebo

Eligibility Criteria

Age18 Years - 70 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Must be able to understand the purpose and risk of the study and provide signed and dated informed consent and authorization to use protected health information (PHI) in accordance with national and local subject privacy regulations
  • Diagnosis of primary-progressive, secondary progressive, progressive-remitting, or relapsing-remitting Multiple Sclerosis of at least 3-month duration
  • EDSS 4 to 7
  • Female patients of childbearing potential must practice effective contraception during the study and be willing and able to continue contraception for 30 days after their last dose of study treatment
  • Must be able to understand and comply with the requirements of the protocol

You may not qualify if:

  • Known allergy to pyridine-containing substances or to any of the inactive ingredients in the prolonged release fampridine (BIIB041) tablet
  • Any history of seizure, epilepsy, or other convulsive disorder, with the exception of febrile seizures in childhood
  • An estimated creatinine clearance (CrCl) of \<80 mL/minute (using the Cockcroft-Gault formula)
  • Known history of Human Immunodeficiency Virus, hepatitis C, or hepatitis B. Subjects who have evidence of prior hepatitis infection that has been serologically confirmed as resolved based on previous testing documented in the subjects' medical history are not excluded from study participation
  • History of malignant disease including solid tumors and hematologic malignancies (with the exception of basal cell and squamous cell carcinomas of the skin that have been completely excised and are considered cured) within the 5 years prior to the Screening Visit, or at any time during the screening period
  • Onset of MS exacerbation within the 60 days prior to the Screening Visit, or at any time during the screening period
  • History of any major surgical intervention (with the exception of skin biopsy) within the 30 days prior to the Screening Visit, or at any time during the screening period
  • Any non-MS-related condition or factor (as determined by the Investigator) that is likely to interfere with walking ability including, but not limited to, previous major surgery of the foot, leg, or hip; any significant trauma; or known peripheral neuropathy of the lower limb
  • Presence of pulmonary disease including, but not limited to, chronic obstructive pulmonary disease that could impede the subject's daily activities (as determined by the Investigator)
  • Presence of any psychiatric disorder, including clinical depression, that is likely to interfere with the subject's participation in the study (as determined by the Investigator)
  • Uncontrolled hypertension (as determined by the Investigator) at the Screening Visit, any time during the screening period, or Day 1
  • History of any clinically significant endocrinologic, hematologic, immunologic, metabolic, urologic, neurologic (except for MS, but including events indicative of a potentially lower seizure threshold), dermatologic, or other major disease (as determined by the Investigator)
  • Clinically significant abnormal laboratory values (as determined by the Investigator)
  • A Body Mass Index ≥40
  • Use of off label MS treatment including rituximab, alemtuzumab, daclizumab, or antibody (except natalizumab) within the 3 months prior to the Screening Visit, or any time during the screening period, or scheduled use during study participation
  • +16 more criteria

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (23)

Research Site

Ath, Belgium

Location

Research Site

Bruges, Belgium

Location

Research Site

Brussels, Belgium

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Research Site

Leuven, Belgium

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Research Site

Yvoir, Belgium

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Research Site

Halifax, Nova Scotia, Canada

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Research Site

London, Ontario, Canada

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Research Site

Gatineau, Quebec, Canada

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Research Site

Greenfield Park, Quebec, Canada

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Research Site

Montreal, Quebec, Canada

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Research Site

Ancona, AN, Italy

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Research Site

Brescia, BS, Italy

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Research Site

Empoli, FI, Italy

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Research Site

Palermo, PA, Italy

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Research Site

Roma, RM, Italy

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Research Site

Breda, Netherlands

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Research Site

Sittard-Geleen, Netherlands

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Research Site

Gothenburg, Sweden

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Research Site

Stockholm, Sweden

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Research Site

Edgbaston, Birmingham, United Kingdom

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Research Site

Poole, Dorset, United Kingdom

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Research Site

Swansea, Glamorgan, United Kingdom

Location

Research Site

London, United Kingdom

Location

Related Publications (1)

  • Hupperts R, Lycke J, Short C, Gasperini C, McNeill M, Medori R, Tofil-Kaluza A, Hovenden M, Mehta LR, Elkins J. Prolonged-release fampridine and walking and balance in MS: randomised controlled MOBILE trial. Mult Scler. 2016 Feb;22(2):212-21. doi: 10.1177/1352458515581436. Epub 2015 Apr 28.

    PMID: 25921050BACKGROUND

Related Links

MeSH Terms

Conditions

Multiple Sclerosis

Interventions

4-Aminopyridine

Condition Hierarchy (Ancestors)

Demyelinating Autoimmune Diseases, CNSAutoimmune Diseases of the Nervous SystemNervous System DiseasesDemyelinating DiseasesAutoimmune DiseasesImmune System Diseases

Intervention Hierarchy (Ancestors)

AminopyridinesAminesOrganic ChemicalsPyridinesHeterocyclic Compounds, 1-RingHeterocyclic Compounds

Study Officials

  • Medical Director

    Biogen

    STUDY DIRECTOR

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
DOUBLE
Who Masked
PARTICIPANT, INVESTIGATOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

May 10, 2012

First Posted

May 14, 2012

Study Start

August 1, 2012

Primary Completion

August 1, 2013

Study Completion

August 1, 2013

Last Updated

January 9, 2017

Record last verified: 2017-01

Locations