NCT01652703

Brief Summary

The primary objective is to evaluate the effect of 12 weeks of subcutaneous evolocumab every 2 weeks or every 4 weeks, compared with placebo, on percent change from baseline in low-density lipoprotein cholesterol (LDL-C) when used in addition to statin therapy in Japanese adults with hypercholesterolemia and high cardiovascular risk.

Trial Health

80
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
310

participants targeted

Target at P75+ for phase_2

Geographic Reach
1 country

42 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

July 10, 2012

Completed
16 days until next milestone

First Submitted

Initial submission to the registry

July 26, 2012

Completed
4 days until next milestone

First Posted

Study publicly available on registry

July 30, 2012

Completed
10 months until next milestone

Primary Completion

Last participant's last visit for primary outcome

May 14, 2013

Completed
2.4 years until next milestone

Results Posted

Study results publicly available

October 5, 2015

Completed
Last Updated

November 28, 2018

Status Verified

November 1, 2018

Enrollment Period

10 months

First QC Date

July 26, 2012

Results QC Date

September 3, 2015

Last Update Submit

November 1, 2018

Conditions

Keywords

Japanese, hypercholesterolemia, high risk for cardiovascular events

Outcome Measures

Primary Outcomes (1)

  • Percent Change From Baseline in Low-Density Lipoprotein Cholesterol (LDL-C) at Week 12

    LDL-C was measured using ultracentrifugation.

    Baseline and Week 12

Secondary Outcomes (7)

  • Change From Baseline in Low-Density Lipoprotein Cholesterol (LDL-C) at Week 12

    Baseline and Week 12

  • Percentage of Participants With an LDL-C Response at Week 12

    Week 12

  • Percent Change From Baseline to Week 12 in Non-HDL-C

    Baseline and Week 12

  • Percent Change From Baseline to Week 12 in Apolipoprotein B

    Baseline and Week 12

  • Percent Change From Baseline to Week 12 in VLDL-C

    Baseline and Week 12

  • +2 more secondary outcomes

Study Arms (6)

Placebo Q2W

PLACEBO COMPARATOR

Participants received placebo subcutaneous injection once every 2 weeks (Q2W) for 12 weeks.

Other: Placebo

Placebo Q4W

PLACEBO COMPARATOR

Participants received placebo subcutaneous injection once every 4 weeks (Q4W) for 12 weeks.

Other: Placebo

Evolocumab 70 mg Q2W

EXPERIMENTAL

Participants received 70 mg evolocumab by subcutaneous injection once every 2 weeks for 12 weeks.

Biological: Evolocumab

Evolocumab 140 mg Q2W

EXPERIMENTAL

Participants received 140 mg evolocumab by subcutaneous injection once every 2 weeks for 12 weeks.

Biological: Evolocumab

Evolocumab 280 mg Q4W

EXPERIMENTAL

Participants received 280 mg evolocumab by subcutaneous injection once every 4 weeks for 12 weeks.

Biological: Evolocumab

Evolocumab 420 mg Q4W

EXPERIMENTAL

Participants received 420 mg evolocumab by subcutaneous injection once every 4 weeks for 12 weeks.

Biological: Evolocumab

Interventions

EvolocumabBIOLOGICAL

Administered by subcutaneous injection

Also known as: AMG 145, Repatha
Evolocumab 140 mg Q2WEvolocumab 280 mg Q4WEvolocumab 420 mg Q4WEvolocumab 70 mg Q2W
PlaceboOTHER

Administered by subcutaneous injection

Placebo Q2WPlacebo Q4W

Eligibility Criteria

Age20 Years - 80 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (42)

Research Site

Nagoya, Aichi-ken, 454-0933, Japan

Location

Research Site

Nagoya, Aichi-ken, 455-8530, Japan

Location

Research Site

Nagoya, Aichi-ken, 462-0825, Japan

Location

Research Site

Fukui-shi, Fukui, 910-0067, Japan

Location

Research Site

Fukui-shi, Fukui, 910-0803, Japan

Location

Research Site

Fukui-shi, Fukui, 910-0837, Japan

Location

Research Site

Kasuga-shi, Fukuoka, 816-0864, Japan

Location

Research Site

Gifu, Gifu, 500-8384, Japan

Location

Research Site

Fujioka-shi, Gunma, 375-0015, Japan

Location

Research Site

Maebashi, Gunma, 371-0022, Japan

Location

Research Site

Maebashi, Gunma, 371-0046, Japan

Location

Research Site

Takasaki-shi, Gunma, 370-0829, Japan

Location

Research Site

Kawanishi, Hyōgo, 666-0125, Japan

Location

Research Site

Kobe, Hyōgo, 657-0068, Japan

Location

Research Site

Hitachi-shi, Ibaraki, 317-0077, Japan

Location

Research Site

Koga-shi, Ibaraki, 306-0041, Japan

Location

Research Site

Mito, Ibaraki, 311-4198, Japan

Location

Research Site

Komatsu-shi, Ishikawa-ken, 923-8560, Japan

Location

Research Site

Takamatsu, Kagawa-ken, 760-8557, Japan

Location

Research Site

Kochi, Kochi, 781-8555, Japan

Location

Research Site

Kumamoto, Kumamoto, 860-8556, Japan

Location

Research Site

Kyoto, Kyoto, 613-0911, Japan

Location

Research Site

Kyoto, Kyoto, 615-8125, Japan

Location

Research Site

Ina-shi, Nagano, 396-8555, Japan

Location

Research Site

Matsumoto-shi, Nagano, 390-0848, Japan

Location

Research Site

Suwa-shi, Nagano, 392-8510, Japan

Location

Research Site

Ibaraki-shi, Osaka, 567-0876, Japan

Location

Research Site

Suita-shi, Osaka, 565-0871, Japan

Location

Research Site

Toyonaka-shi, Osaka, 560-0082, Japan

Location

Research Site

Hanyu-shi, Saitama, 348-8505, Japan

Location

Research Site

Sayama-shi, Saitama, 350-1305, Japan

Location

Research Site

Toda-shi, Saitama, 335-0023, Japan

Location

Research Site

Ōtsu, Shiga, 520-0113, Japan

Location

Research Site

Bunkyo-ku, Tokyo, 113-8421, Japan

Location

Research Site

Bunkyo-ku, Tokyo, 113-8519, Japan

Location

Research Site

Chiyoda-ku, Tokyo, 101-0041, Japan

Location

Research Site

Chuo-ku, Tokyo, 103-0027, Japan

Location

Research Site

Hachioji-shi, Tokyo, 192-0918, Japan

Location

Research Site

Itabashi-ku, Tokyo, 173-8610, Japan

Location

Research Site

Shinagawa-ku, Tokyo, 141-0001, Japan

Location

Research Site

Taito-ku, Tokyo, 111-0052, Japan

Location

Research Site

Toshima-ku, Tokyo, 171-0021, Japan

Location

Related Publications (3)

  • Hirayama A, Yamashita S, Inomata H, Kassahun H, Cyrille M, Ruzza A, Yoshida M, Kiyosue A, Ma Y, Teramoto T. One-Year Efficacy and Safety of Evolocumab in Japanese Patients - A Pooled Analysis From the Open-Label Extension OSLER Studies. Circ J. 2017 Jun 23;81(7):1029-1035. doi: 10.1253/circj.CJ-16-1016. Epub 2017 Mar 29.

    PMID: 28367845BACKGROUND
  • Toth PP, Descamps O, Genest J, Sattar N, Preiss D, Dent R, Djedjos C, Wu Y, Geller M, Uhart M, Somaratne R, Wasserman SM; PROFICIO Investigators. Pooled Safety Analysis of Evolocumab in Over 6000 Patients From Double-Blind and Open-Label Extension Studies. Circulation. 2017 May 9;135(19):1819-1831. doi: 10.1161/CIRCULATIONAHA.116.025233. Epub 2017 Mar 1.

    PMID: 28249876BACKGROUND
  • Kasichayanula S, Grover A, Emery MG, Gibbs MA, Somaratne R, Wasserman SM, Gibbs JP. Clinical Pharmacokinetics and Pharmacodynamics of Evolocumab, a PCSK9 Inhibitor. Clin Pharmacokinet. 2018 Jul;57(7):769-779. doi: 10.1007/s40262-017-0620-7.

    PMID: 29353350BACKGROUND

Related Links

MeSH Terms

Conditions

Hypercholesterolemia

Interventions

evolocumab

Condition Hierarchy (Ancestors)

HyperlipidemiasDyslipidemiasLipid Metabolism DisordersMetabolic DiseasesNutritional and Metabolic Diseases

Results Point of Contact

Title
Study Director
Organization
Amgen Inc.

Study Officials

  • MD

    Amgen

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
TRIPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

July 26, 2012

First Posted

July 30, 2012

Study Start

July 10, 2012

Primary Completion

May 14, 2013

Last Updated

November 28, 2018

Results First Posted

October 5, 2015

Record last verified: 2018-11

Locations