NCT01613599

Brief Summary

This prospective observational study will evaluate the long-term safety of MabThera/Rituxan (rituximab) in participants with granulomatosis with polyangiitis (Wegener's) or microscopic polyangiitis. Data will be collected for a maximum of 4 years from participants initiated on MabThera/Rituxan therapy by their physician according to prescribing information.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
100

participants targeted

Target at P50-P75 for all trials

Timeline
Completed

Started Jun 2012

Longer than P75 for all trials

Geographic Reach
1 country

15 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

June 4, 2012

Completed
3 days until next milestone

First Posted

Study publicly available on registry

June 7, 2012

Completed
13 days until next milestone

Study Start

First participant enrolled

June 20, 2012

Completed
3.1 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

July 13, 2015

Completed
1.1 years until next milestone

Results Posted

Study results publicly available

August 17, 2016

Completed
8 months until next milestone

Study Completion

Last participant's last visit for all outcomes

April 28, 2017

Completed
Last Updated

July 26, 2018

Status Verified

July 1, 2018

Enrollment Period

3.1 years

First QC Date

June 4, 2012

Results QC Date

July 6, 2016

Last Update Submit

July 24, 2018

Conditions

Outcome Measures

Primary Outcomes (1)

  • Incidence Rate of Serious Infections

    A serious infection was defined as an infection that was a serious adverse event (SAE) or a non-SAE infection that required treatment with intravenous antimicrobials. A SAE was defined as any adverse event that fulfilled at least one of the following criteria: •Was fatal (results in death) •Was life-threatening •Required in-patient hospitalization or prolongation of existing hospitalization •Resulted in persistent or significant disability/incapacity •Was a congenital anomaly/birth defect •Was medically significant or required intervention to prevent one or other of the outcomes listed above. Multiple events reported in the same participant were counted multiple times in the calculation of incidence. Incidence rate is defined as events per 100 patient years.

    From first dose until participant withdrawal or the date of last participant, last visit (up to 4.32 years)

Secondary Outcomes (9)

  • Percentage of Participants With a Serious Infusion-related Reaction

    From the start of an infusion up to 24 hours following infusion completion (Up to 4.32 years)

  • Incidence Rate of Serious Cardiac Adverse Events

    From first dose until participant withdrawal or the date of last participant, last visit (up to 4.32 years)

  • Percentage of Participants With Any Serious Adverse Events During or Within 24 Hours After Any Rituximab Infusion

    From the start of an infusion up to 24 hours following infusion completion (Up to 4.32 years)

  • Incidence Rate of Serious Vascular Adverse Events

    From first dose until participant withdrawal or the date of last participant, last visit (up to 4.32 years)

  • Incidence Rate of Malignancy, Excluding Non-melanoma Skin Cancer

    From first dose until participant withdrawal or the date of last participant, last visit (up to 4.32 years)

  • +4 more secondary outcomes

Study Arms (1)

Rituximab

Participants with granulomatosis with polyangiitis (GPA) (Wegener's granulomatosis) or microscopic polyangiitis (MPA) who received rituximab as per investigator's discretion were followed for a maximum of 4 years.

Drug: Rituximab

Interventions

Participants received rituximab at the discretion of their treating physicians.

Also known as: Rituxan
Rituximab

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)
Sampling MethodNon-Probability Sample
Study Population

Participants with granulomatosis with polyangiitis or microscopic polyangiitis treated with MabThera/Rituxan

You may qualify if:

  • Adult participants, \>/= 18 years of age
  • Granulomatosis with polyangiitis (GPA) or microscopic polyangiitis (MPA), according to Chapel Hill Consensus Conference Definitions for MPA and American College of Rheumatology (ACR) Criteria for the Classification of GPA
  • Disease severity requiring rituximab treatment per the investigator's assessment

You may not qualify if:

  • Prior use of rituximab (except if received within 4 weeks of screening)
  • Known hypersensitivity to rituximab, to any component of the product, or to murine proteins
  • Pregnant or breastfeeding women
  • Diagnosis of Churg-Strauss syndrome

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (15)

Mayo Clinic Arizona

Scottsdale, Arizona, 85025, United States

Location

Cedars-Sinai Medical Center

Los Angeles, California, 90048, United States

Location

Mayo Clinic

Jacksonville, Florida, 32224, United States

Location

Rush University Medical Center

Chicago, Illinois, 60612, United States

Location

Johns Hopkins Asthma&Allergy

Baltimore, Maryland, 21224, United States

Location

Mass. General Hospital

Boston, Massachusetts, 02114, United States

Location

Boston Medical Center

Boston, Massachusetts, 02118-2393, United States

Location

Mayo Clinic Rochester; Int.Med - Div. of Pul

Rochester, Minnesota, 55905, United States

Location

Weill Medical College of Cornell University; Hospital for Special Surgery

New York, New York, 10065, United States

Location

UNC- Chapel Hill

Chapel Hill, North Carolina, 27516, United States

Location

Duke Univ Medical Center

Durham, North Carolina, 27710, United States

Location

Cleveland Clinic Foundation

Cleveland, Ohio, 44915, United States

Location

University of Pennsylvania

Philadelphia, Pennsylvania, 19104, United States

Location

University of Pittsburgh

Pittsburgh, Pennsylvania, 15261, United States

Location

University of Utah; Division of Rheumatology

Salt Lake City, Utah, 84132, United States

Location

Related Publications (1)

  • Merkel PA, Niles JL, Mertz LE, Lehane PB, Pordeli P, Erblang F. Long-Term Safety of Rituximab in Granulomatosis With Polyangiitis and in Microscopic Polyangiitis. Arthritis Care Res (Hoboken). 2021 Sep;73(9):1372-1378. doi: 10.1002/acr.24332. Epub 2021 Aug 13.

MeSH Terms

Conditions

Granulomatosis with PolyangiitisMicroscopic Polyangiitis

Interventions

Rituximab

Condition Hierarchy (Ancestors)

Lung Diseases, InterstitialLung DiseasesRespiratory Tract DiseasesAnti-Neutrophil Cytoplasmic Antibody-Associated VasculitisSystemic VasculitisVasculitisVascular DiseasesCardiovascular DiseasesSkin Diseases, VascularSkin DiseasesSkin and Connective Tissue DiseasesAutoimmune DiseasesImmune System DiseasesCerebral Small Vessel DiseasesCerebrovascular DisordersBrain DiseasesCentral Nervous System DiseasesNervous System Diseases

Intervention Hierarchy (Ancestors)

Antibodies, Monoclonal, Murine-DerivedAntibodies, MonoclonalAntibodiesImmunoglobulinsImmunoproteinsBlood ProteinsProteinsAmino Acids, Peptides, and ProteinsSerum GlobulinsGlobulins

Results Point of Contact

Title
Medical Communications
Organization
Hoffman-La Roche

Study Officials

  • Clinical Trials

    Genentech, Inc.

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
observational
Observational Model
COHORT
Time Perspective
PROSPECTIVE
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

June 4, 2012

First Posted

June 7, 2012

Study Start

June 20, 2012

Primary Completion

July 13, 2015

Study Completion

April 28, 2017

Last Updated

July 26, 2018

Results First Posted

August 17, 2016

Record last verified: 2018-07

Locations