NCT01521780

Brief Summary

The purpose of this study is to characterize the baseline variability of a panel of tissue (tumor and adjacent) and blood-based biomarkers obtained from participants with hepatocellular carcinoma (HCC). The primary hypothesis is that the upper bound of the 80% Confidence Interval of log beta-catenin protein or messenger RNA (mRNA) expression from one core needle biopsy (CNB) equivalent is =\< 0.65.

Trial Health

55
Monitor

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
12

participants targeted

Target at below P25 for phase_1 hepatocellular-carcinoma

Timeline
Completed

Started Apr 2012

Shorter than P25 for phase_1 hepatocellular-carcinoma

Status
terminated

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

December 16, 2011

Completed
2 months until next milestone

First Posted

Study publicly available on registry

January 31, 2012

Completed
2 months until next milestone

Study Start

First participant enrolled

April 1, 2012

Completed
5 months until next milestone

Primary Completion

Last participant's last visit for primary outcome

September 1, 2012

Completed
2 months until next milestone

Study Completion

Last participant's last visit for all outcomes

November 1, 2012

Completed
12 months until next milestone

Results Posted

Study results publicly available

October 28, 2013

Completed
Last Updated

November 2, 2015

Status Verified

October 1, 2015

Enrollment Period

5 months

First QC Date

December 16, 2011

Results QC Date

August 14, 2013

Last Update Submit

October 30, 2015

Conditions

Keywords

hepatocellular carcinomaMRIpharmacogenomicsbeta-catenin

Outcome Measures

Primary Outcomes (2)

  • Expression Levels of Beta-catenin mRNA From Core Needle Biopsy (CNB) Equivalents of Resected HCC.

    Resected tumors were fixed with formalin in paraffin embedded (FFPE) blocks, which were used to prepare multiple serial slide sections. The sections were to be analyzed for beta-catenin messenger RNA (mRNA) by quantitative reverse transcription polymerase chain reaction (qRT-PCR).

    Visit 3, approximately 7 days after screening Visit 1.

  • Expression Levels of Beta-catenin Protein From Core Needle Biopsy (CNB) Equivalents of Resected HCC.

    Resected tumors were fixed in FFPE blocks, which were used to prepare multiple serial slide sections. The sections were to be analyzed for beta-catenin protein by automated image analysis.

    Visit 3, approximately 7 days after screening Visit 1.

Secondary Outcomes (5)

  • Tumor Volumes From Repeated MRI Measurements of HCC.

    Visit 2, approximately 7 days after screening Visit 1.

  • Median Apparent Diffusion Coefficient (Median ADC) of Tumors From Repeated MRI Measurements of HCC.

    Visit 2, approximately 7 days after screening Visit 1.

  • Expression Levels of Beta-catenin mRNA From CNB Equivalents of Liver Adjacent to HCC.

    Visit 3, approximately 7 days after screening Visit 1.

  • Expression Levels of Beta-catenin Protein From CNB Equivalents of Liver Adjacent to HCC.

    Visit 3, approximately 7 days after screening Visit 1.

  • Expression Levels of Low Density Lipoprotein Receptor (LDL-R) in Resected HCC and Adjacent Liver From Whole Tissue Sections.

    Visit 3, approximately 7 days after screening Visit 1.

Study Arms (3)

Imaging

EXPERIMENTAL

Magnetic resonance imaging (MRI) of HCC tumor.

Procedure: MRIProcedure: Blood Samples

Pathology

EXPERIMENTAL

Pathology samples from surgical resection of HCC tumor and adjacent liver.

Procedure: PathologyProcedure: Blood Samples

Imaging/Pathology

EXPERIMENTAL

MRI of HCC tumor, followed by pathology samples from surgical resection of HCC tumor and adjacent liver.

Procedure: MRIProcedure: PathologyProcedure: Blood Samples

Interventions

MRIPROCEDURE

Participants undergo volumetric \& diffusion weighted (DW) MRI. Participants are scanned twice, with an intervening fifteen minute walk between the scans.

ImagingImaging/Pathology
PathologyPROCEDURE

Participants who are undergoing surgical resection of HCC per their standard of care treatment, will submit tumor samples for biomarker analysis.

Imaging/PathologyPathology
Blood SamplesPROCEDURE

Blood is collected from participants during screening Visit 1 - 24.5 ml. During Visit 3, blood samples totaling 22 ml, are collected at least 6-18 hours post-resection, and every other day up to a week until discharge. At follow up Visit 4, 5.5 ml of blood is collected.

Imaging/PathologyPathology

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Diagnosed with HCC.
  • Candidate for surgical resection or has no contraindications to MRI procedures.

You may not qualify if:

  • Prior loco-regional treatment of tumor, unless there is untreated tumor present representing a distinct untreated nodule.
  • Confirmed or suspected diagnosis of fibrolamellar HCC, mixed HCC/cholangiocarcinoma or metastatic tumor.
  • Had a liver transplant.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

MeSH Terms

Conditions

Carcinoma, Hepatocellular

Interventions

Blood Specimen Collection

Condition Hierarchy (Ancestors)

AdenocarcinomaCarcinomaNeoplasms, Glandular and EpithelialNeoplasms by Histologic TypeNeoplasmsLiver NeoplasmsDigestive System NeoplasmsNeoplasms by SiteDigestive System DiseasesLiver Diseases

Intervention Hierarchy (Ancestors)

Specimen HandlingClinical Laboratory TechniquesDiagnostic Techniques and ProceduresDiagnosisPuncturesSurgical Procedures, OperativeInvestigative Techniques

Limitations and Caveats

The study was terminated early.

Results Point of Contact

Title
Senior Vice President, Global Clinical Development
Organization
Merck Sharp & Dohme Corp.

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 1
Allocation
NON RANDOMIZED
Masking
NONE
Purpose
DIAGNOSTIC
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

December 16, 2011

First Posted

January 31, 2012

Study Start

April 1, 2012

Primary Completion

September 1, 2012

Study Completion

November 1, 2012

Last Updated

November 2, 2015

Results First Posted

October 28, 2013

Record last verified: 2015-10