NCT01496313

Brief Summary

The purpose of this study is to give patients with medullary thyroid cancer either 300mg/day or 150mg/day vandetanib and compare how well each dose affects how their cancer responds. It will also help the investigators understand the side effects of different doses in these patients.

Trial Health

93
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
81

participants targeted

Target at P25-P50 for phase_4

Timeline
Completed

Started Jun 2012

Longer than P75 for phase_4

Geographic Reach
9 countries

30 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

December 2, 2011

Completed
19 days until next milestone

First Posted

Study publicly available on registry

December 21, 2011

Completed
6 months until next milestone

Study Start

First participant enrolled

June 8, 2012

Completed
1.8 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

April 2, 2014

Completed
1.7 years until next milestone

Results Posted

Study results publicly available

November 27, 2015

Completed
8.6 years until next milestone

Study Completion

Last participant's last visit for all outcomes

July 11, 2024

Completed
Last Updated

October 3, 2025

Status Verified

September 1, 2025

Enrollment Period

1.8 years

First QC Date

December 2, 2011

Results QC Date

April 1, 2015

Last Update Submit

September 16, 2025

Conditions

Keywords

medullary thyroid cancermetastaticthyroid cancercarcinoma of the thyroidreceptor tyrosine kinase inhibitorVEGFRUnresectable locally advanced thyroid cancer

Outcome Measures

Primary Outcomes (1)

  • Overall Response Rate (ORR) for Vandetanib 150 and 300mg With Responses Determined by the Investigator

    ORR=proportion of patients with a best response of complete or partial response as per Response Evaluation Criteria in Solid Tumors(RECIST)1.1

    Randomisation to week 60 (maximum)

Secondary Outcomes (5)

  • Best Objective Response

    Randomisation to week 60 (maximum)

  • Duration of Objective Response (RECIST 1.1) by Treatment Arm

    Randomization to Week 60 (maximum)

  • Time to Objective Response (RECIST 1.1) by Treatment Arm

    Randomization to Week 60 (maximum)

  • Percentage Change From Baseline in Target Lesion Size (RECIST 1.1) by Treatment Arm

    Randomization to Week 60 (maximum)

  • Plasma Concentration of Vandetanib in the Bloodstream (Cmax) for Patients by Treatment Arm.

    Week 3 to week 60 (maximum)

Study Arms (2)

300mg vandetanib

ACTIVE COMPARATOR
Drug: 300mg vandetanib

150mg vandetanib

ACTIVE COMPARATOR
Drug: 150mg vandetanib

Interventions

Oral blinded tablets taken once daily. At objective disease progression or 14 months (whichever is earlier), patient may be unblinded to treatment Dosing with unblinded study treatment can continue until 24 months after patient was randomised. At any time dosing may be interrupted for up to 6 weeks due to toxicity. Dosing may restart at a reduced dose (200mg/day). Once reduced, dose increases are not permitted and dosing must stop if further toxicities occur.

Also known as: SAR390530
300mg vandetanib

Oral blinded tablets taken once daily. At objective disease progression or 14 months (whichever is earlier), patient may be unblinded to treatment. Patients who have not dose reduced at the time of unblinding may have their dose increased to 300mg Dosing with unblinded study treatment can continue until 24 months after patient was randomised At any time dosing may be interrupted for up to 6 weeks due to toxicity. Dosing may restart at a reduced dose (100mg/day) \[OR 300 reduced to 200mg/day if dose was increased at unblinding.\] Once reduced, dose increases are not permitted and dosing must stop if further toxicities occur.

Also known as: SAR390530
150mg vandetanib

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Written consent from Female or male patients aged 18 years and over. Previously confirmed histological diagnosis of unresectable, locally advanced or metastatic, hereditary or sporadic MTC Objective disease progression within the previous 14 months prior to enrolment, and/or
  • Have one or more symptoms that the Investigator believes to be related to the patient's MTC.
  • World Health Organisation (WHO) or Eastern Cooperative Oncology Group (ECOG) Performance status 0-2.
  • Has measurable disease (at least one lesion, not irradiated within 12 weeks of study randomisation, with longest diameter more or equal 10mm (lymph nodes minimum more or equal 15 mm) with CT or MRI).
  • Lesions must be amenable to accurate and repeat measurement.

You may not qualify if:

  • Prior treatment (major surgery, radiation therapy, chemotherapy, or other investigational drugs) received within 28 days before randomization.
  • Abnormal liver function tests (bilirubin more than 1.5xULRR, and ALT, AST, or ALP more than 2.5xULRR or 5.0xULRR if related to liver metastases).
  • Significant cardiac conditions or events such as reduced cardiac functions, symptomatic cardiac arrhythmia requiring treatment, congenital long QT syndrome, history of drug-induced QT prolongation, or QTcF correction unmeasurable or more than 450 ms.
  • Abnormal electrolytes such as potassium, magnesium and calcium, or abnormal organ functions such as decreased creatinine clearance.
  • For women only - currently pregnant or breast feeding.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (30)

Research Site

Houston, Texas, United States

Location

Investigational Site Number : 1903

Olomouc, 77900, Czechia

Location

Research Site

Olomouc, Czechia

Location

Investigational Site Number : 1901

Prague, 15006, Czechia

Location

Research Site

Prague, Czechia

Location

Research Site

Bangalore Karnataka, India

Location

Research Site

Vellore, India

Location

Research Site

Beersheba, Israel

Location

Research Site

Haifa, Israel

Location

Research Site

Jerusalem, Israel

Location

Research Site

Petah Tikva, Israel

Location

Research Site

Catania, Italy

Location

Research Site

Milan, Italy

Location

Research Site

Palermo, Italy

Location

Research Site

Pisa, Italy

Location

Research Site

Roma, Italy

Location

Research Site

Siena, Italy

Location

Research Site

Torino, Italy

Location

Research Site

Groningen, Netherlands

Location

Research Site

Leiden, Netherlands

Location

Investigational Site Number : 5704

Warsaw, Masovian Voivodeship, 02-781, Poland

Location

Investigational Site Number : 5703

Gliwice, 44-101, Poland

Location

Research Site

Gliwice, Poland

Location

Research Site

Warsaw, Poland

Location

Research Site

Zgierz, Poland

Location

Research Site

Saint Petersburg, Russia

Location

Research Site

Cardiff, United Kingdom

Location

Research Site

Greater London, United Kingdom

Location

Research Site

London, United Kingdom

Location

Research Site

Tyne & Wear, United Kingdom

Location

Related Links

MeSH Terms

Conditions

Thyroid NeoplasmsCarcinoma, MedullaryNeoplasm Metastasis

Interventions

vandetanib

Condition Hierarchy (Ancestors)

Endocrine Gland NeoplasmsNeoplasms by SiteNeoplasmsHead and Neck NeoplasmsEndocrine System DiseasesThyroid DiseasesCarcinoma, NeuroendocrineNeuroendocrine TumorsNeuroectodermal TumorsNeoplasms, Germ Cell and EmbryonalNeoplasms by Histologic TypeAdenocarcinomaCarcinomaNeoplasms, Glandular and EpithelialNeoplasms, Ductal, Lobular, and MedullaryNeoplasms, Nerve TissueNeoplastic ProcessesPathologic ProcessesPathological Conditions, Signs and Symptoms

Results Point of Contact

Title
Trial Transparency Team
Organization
Sanofi aventis recherche & développement

Study Officials

  • Clinical Sciences & Operations

    Sanofi

    STUDY CHAIR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 4
Allocation
RANDOMIZED
Masking
TRIPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

December 2, 2011

First Posted

December 21, 2011

Study Start

June 8, 2012

Primary Completion

April 2, 2014

Study Completion

July 11, 2024

Last Updated

October 3, 2025

Results First Posted

November 27, 2015

Record last verified: 2025-09

Locations