NCT01472939

Brief Summary

The aim of this study is to establish a dose-related effect of a selective 5-HT4 receptor agonist compared to placebo on residual symptoms (regurgitation with or without heartburn) in subjects with GERD who have persistent symptoms while on PPI therapy.

Trial Health

93
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
480

participants targeted

Target at P75+ for phase_2

Timeline
Completed

Started Feb 2012

Shorter than P25 for phase_2

Geographic Reach
6 countries

88 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

November 14, 2011

Completed
3 days until next milestone

First Posted

Study publicly available on registry

November 17, 2011

Completed
3 months until next milestone

Study Start

First participant enrolled

February 27, 2012

Completed
1.2 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

May 14, 2013

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

May 14, 2013

Completed
11 months until next milestone

Results Posted

Study results publicly available

April 15, 2014

Completed
Last Updated

June 9, 2021

Status Verified

May 1, 2021

Enrollment Period

1.2 years

First QC Date

November 14, 2011

Results QC Date

March 4, 2014

Last Update Submit

May 14, 2021

Conditions

Outcome Measures

Primary Outcomes (1)

  • Change From Baseline in Percent Regurgitation-Free Days Over Weeks 5-8

    Baseline and over weeks 5-8

Secondary Outcomes (5)

  • Change From Baseline in Heartburn-Free Days Over Weeks 5-8

    Baseline and over weeks 5-8

  • Change From Baseline in the Persistent Reflux Integrated Symptom Measurement (PRISM) Liquid and Food Domain Scores Over Weeks 5-8

    Baseline and over weeks 5-8

  • Area Under the Steady-state Plasma Concentration-time Curve (AUC) of SSP-002358

    Over 8 hours post-dose (week 2 or later)

  • Steady State Maximum Plasma Concentration (Cmax) of SSP-002358

    Over 8 hours post-dose (week 2 or later)

  • Time to Maximum Plasma Concentration (Tmax) of SSP-002358

    Over 8 hours post-dose (week 2 or later)

Study Arms (4)

SSP-002358 (0.1 mg) + Proton Pump Inhibitor (PPI)

ACTIVE COMPARATOR
Drug: SSP-002358 (0.1 mg) + PPI

SSP-002358 (0.5 mg) + PPI

ACTIVE COMPARATOR
Drug: SSP-002358 (0.5 mg) + PPI

SSP-002358 (2.0 mg) + PPI

ACTIVE COMPARATOR
Drug: SSP-002358 (2.0 mg) + PPI

Placebo + PPI

PLACEBO COMPARATOR
Drug: Placebo + PPI

Interventions

0.1 mg tablet three times daily (t.i.d.) taken in addition to a PPI

Also known as: SPD557
SSP-002358 (0.1 mg) + Proton Pump Inhibitor (PPI)

0.5 mg tablet t.i.d. taken in addition to a PPI

SSP-002358 (0.5 mg) + PPI

2.0 mg tablet t.i.d. taken in addition to a PPI

SSP-002358 (2.0 mg) + PPI

Placebo t.i.d. taken in addition to a PPI

Placebo + PPI

Eligibility Criteria

Age18 Years - 70 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Written Informed Consent Form signed voluntarily before the first study-related activity.
  • Aged between 18 and 70 years, inclusive.
  • Subjects with a history of the cardinal symptoms of GERD (both heartburn and regurgitation) prior to PPI therapy.
  • Subjects with symptoms of GERD for at least 6 months prior to the Screening Visit.
  • Subjects who have persistent symptoms of regurgitation for 3 or more days over the past week with or without heartburn while on PPI.
  • Subjects have at least some improvement to the symptom of heartburn while on PPI therapy.
  • Subjects on PPI therapy for at least 8 weeks prior to the Screening Visit of which the last 4 weeks are on a stable labeled dose for any GERD indication according to the country label, where a change of PPI therapy would not impact the symptoms (twice-daily dosing of PPI is not allowed in the last 4 weeks)

You may not qualify if:

  • Subjects who show no response to heartburn while on PPI therapy.
  • Subjects with dyspepsia symptoms that are more predominant than their GERD symptoms (heartburn and/or regurgitation).
  • Subjects with prior endoscopic anti-reflux procedure or major GI surgery or subjects with major GI disorders.
  • Presence of severe and clinically uncontrolled cardiovascular, liver, lung or neurologic disease, cancer or AIDS.
  • Alarm symptoms suggestive of malignancies or organic disease.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (88)

HOPE Research Institute

Phoenix, Arizona, 85050, United States

Location

Genova Clinical Research

Tucson, Arizona, 85704, United States

Location

Lynn Institute of the Ozarks

Little Rock, Arkansas, 72205, United States

Location

Preferred Research Partners, Inc

Little Rock, Arkansas, 72211, United States

Location

Arkansas Gastroenterology

North Little Rock, Arkansas, 72117, United States

Location

Anaheim Clinical Trials

Anaheim, California, 92801-2417, United States

Location

Southern California Research Institute Medical Group Inc

Los Angeles, California, 90045, United States

Location

Medical Center for Clinical Research

San Diego, California, 92108, United States

Location

Clinicos

Colorado Springs, Colorado, 80904, United States

Location

Connecticut Gastroenterology Institute

Bristol, Connecticut, 06010, United States

Location

Stamford Therapeutics Consortium

Stamford, Connecticut, 06905, United States

Location

Medical Research Unlimited, LLC

Aventura, Florida, 33180, United States

Location

Consultants for Clinical Research of South Florida

Boynton Beach, Florida, 33426, United States

Location

PAB Clinical Research

Brandon, Florida, 33511, United States

Location

Avail Clinical Research, LLC

DeLand, Florida, 32720, United States

Location

S & W Clinical Research

Fort Lauderdale, Florida, 33306, United States

Location

Medical Research Unlimited, LLC

Hialeah, Florida, 33012, United States

Location

Jupiter Research

Jupiter, Florida, 33458, United States

Location

Pines Clinical Research, Inc.

Pembroke Pines, Florida, 33028, United States

Location

Radiant Research

Pinellas Park, Florida, 33781, United States

Location

Accord Clinical Research, LLC

Port Orange, Florida, 32129, United States

Location

Meridien Research

St. Petersburg, Florida, 33709, United States

Location

Gastrointestinal Specialists of GA, PC

Marietta, Georgia, 30060, United States

Location

Digestive Research Associates

Newnan, Georgia, 30263, United States

Location

Rockford Gastroenterology Associates, Ltd

Rockford, Illinois, 61107, United States

Location

Professional Research Network of Kansas, LLC

Wichita, Kansas, 67203, United States

Location

Research Integrity

Owensboro, Kentucky, 42303, United States

Location

Clinical Trials Management

Metairie, Louisiana, 70006, United States

Location

Louisiana Research Center, LLC

Shreveport, Louisiana, 71103, United States

Location

Meritus Medical Center

Hagerstown, Maryland, 21742, United States

Location

Beacon Clinical Research

Brockton, Massachusetts, 02301, United States

Location

Center for Digestive and Liver Diseases

Mexico, Missouri, 65265, United States

Location

Clinical Research Group of Montana

Bozeman, Montana, 59718, United States

Location

Meridian Clinical Research

Omaha, Nebraska, 68134, United States

Location

Clinical Research Center of Nevada

Las Vegas, Nevada, 89104, United States

Location

New Jersey Physicians, LLC

Clifton, New Jersey, 07012, United States

Location

UNC Hospitals

Chapel Hill, North Carolina, 27599, United States

Location

Carolinas Research Associates

Davidson, North Carolina, 28036, United States

Location

Cumberland Research Associates

Fayetteville, North Carolina, 28314, United States

Location

Vital Research, Inc.

Greensboro, North Carolina, 27408, United States

Location

Carolinas Research Associates

Harrisburg, North Carolina, 28075, United States

Location

Peters Medical Research

High Point, North Carolina, 27262, United States

Location

Wake Research Associates

Raleigh, North Carolina, 27612, United States

Location

Prestige Clinical Research

Franklin, Ohio, 45005, United States

Location

Oklahoma Foundation for Digestive Research Sciences Center

Oklahoma City, Oklahoma, 73104, United States

Location

Family Medical Associates

Levittown, Pennsylvania, 19056, United States

Location

Guthrie Clinic, Ltd.

Sayre, Pennsylvania, 18840, United States

Location

Omega Medical Research

Warwick, Rhode Island, 02886, United States

Location

Meridian Clinical Research

Dakota Dunes, South Dakota, 57049, United States

Location

Clinsearch, LLC

Chattanooga, Tennessee, 37421, United States

Location

Radiant Research Dallas-North

Dallas, Texas, 75231, United States

Location

GI Consultants, P.A.

Houston, Texas, 77034, United States

Location

Pasadena Gastroenterology Assoc, dba Digestive Health Center

Pasadena, Texas, 77505, United States

Location

Office Based Practitioner

San Antonio, Texas, 78229, United States

Location

Advanced Research Institute

Clinton, Utah, 84015, United States

Location

Advanced Research Institute

Logan, Utah, 84341, United States

Location

Advanced Research Institute

Ogden, Utah, 84405, United States

Location

Advanced Research Institute

Sandy City, Utah, 84094, United States

Location

New River Valley Research Institute

Christiansburg, Virginia, 24073, United States

Location

Blue Ridge Medical Center

Lynchburg, Virginia, 24502, United States

Location

Ramstad Medical Associates

Suffolk, Virginia, 23435, United States

Location

Aurora Wilkinson Medical Clinic

Summit, Wisconsin, 53066, United States

Location

Hepato-Gastroenterology HK s.r.o.

Hradec Králové, 50012, Czechia

Location

Nemocnice Valasske Mezirici a.s.

Valašské Meziříčí, 75742, Czechia

Location

Praxis Dr. Andreas Schwittay-Facharzt fuer Innere Medizin

Böhlen, 4564, Germany

Location

Zentrum fur Innere Medizin, Klinikum Garmisch Partenkirchen

Garmisch-Partenkirchen, 82467, Germany

Location

Haus der Gesundheit

Ludwigshafen, 67067, Germany

Location

Praxis für Gastroenterologie und fachärztliche Innere Medizin

Ludwigshafen, 67067, Germany

Location

Medizinische Fakultät der Otto-von-Guericke Universität

Magdeburg, 39120, Germany

Location

Gemeinschaftspraxis Dres. Brandt

Potsdam, 14482, Germany

Location

Gemeinschaftspraxis Dres Josef und Wilma Großkopf

Wallerfing, 94574, Germany

Location

Daugavpils Regional Hospital

Daugavpils, 5417, Latvia

Location

Pauls Stradins Clinical University Hospital

Riga, 1002, Latvia

Location

Digestive Disease Centre "Gastro"

Riga, 1006, Latvia

Location

Vidzemes Hospital

Valmiera, 4201, Latvia

Location

NZOZ Specjalistyczne Centrum Gastrologii Gastromed

Bialystok, 15-351, Poland

Location

Centrum Medyczne im Swietego Lukasza Sp. z o.o.

Częstochowa, 42-202, Poland

Location

NZOZ ''Salvia''

Katowice, 40-772, Poland

Location

Centrum Medyczne Szpital sw. Rodziny Sp. z o.o.

Lodz, 90-302, Poland

Location

Gastromed Sp. K. NZOZ

Lublin, 20-607, Poland

Location

Endoskopia Sp. z o.o.

Sopot, 81-756, Poland

Location

NZOZ Vivamed

Warsaw, 03-580, Poland

Location

Lexmedica

Wroclaw, 53-025, Poland

Location

Aktywne Centrum Zdrowia NZOZ ZAWIDAWIE Sp. z o.o.

Wroclaw, 54-239, Poland

Location

Brasov County Hospital

Brasov, 500326, Romania

Location

Centrul Medical Galenus

Târgu Mureş, 540098, Romania

Location

Cabinet Particular Policlinic Algomed SRL

Timișoara, 300002, Romania

Location

Policlinica "Dr. Citu" SRL

Timișoara, 300594, Romania

Location

Related Publications (1)

  • Shaheen NJ, Adler J, Dedrie S, Johnson D, Malfertheiner P, Miner P, Meulemans A, Poole L, Tack J, Thielemans L, Troy S, Vakil N, Zerbib F, Ruth M. Randomised clinical trial: the 5-HT4 agonist revexepride in patients with gastro-oesophageal reflux disease who have persistent symptoms despite PPI therapy. Aliment Pharmacol Ther. 2015 Apr;41(7):649-61. doi: 10.1111/apt.13115. Epub 2015 Feb 19.

MeSH Terms

Conditions

Gastroesophageal Reflux

Interventions

revexepride

Condition Hierarchy (Ancestors)

Esophageal Motility DisordersDeglutition DisordersEsophageal DiseasesGastrointestinal DiseasesDigestive System Diseases

Results Point of Contact

Title
Study Director
Organization
Shire

Study Officials

  • Study Director

    Takeda

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
DOUBLE
Who Masked
PARTICIPANT, INVESTIGATOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

November 14, 2011

First Posted

November 17, 2011

Study Start

February 27, 2012

Primary Completion

May 14, 2013

Study Completion

May 14, 2013

Last Updated

June 9, 2021

Results First Posted

April 15, 2014

Record last verified: 2021-05

Locations