NCT01442129

Brief Summary

The main purpose of this research is to determine whether injecting mesenchymal precursor cells (MPC) into the heart during surgery to implant a left ventricular assist device (LVAD) is safe. MPCs are normally present in human bone marrow, and have been shown to increase the development of blood vessels and new heart muscle cells in the heart. In addition, this research is being done to test whether injecting the MPCs into the heart is effective in improving heart function.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
30

participants targeted

Target at P25-P50 for phase_2 heart-failure

Timeline
Completed

Started Apr 2012

Geographic Reach
1 country

11 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

September 26, 2011

Completed
2 days until next milestone

First Posted

Study publicly available on registry

September 28, 2011

Completed
6 months until next milestone

Study Start

First participant enrolled

April 1, 2012

Completed
11 months until next milestone

Primary Completion

Last participant's last visit for primary outcome

March 1, 2013

Completed
5 months until next milestone

Study Completion

Last participant's last visit for all outcomes

August 1, 2013

Completed
1.2 years until next milestone

Results Posted

Study results publicly available

October 13, 2014

Completed
Last Updated

May 1, 2015

Status Verified

April 1, 2015

Enrollment Period

11 months

First QC Date

September 26, 2011

Results QC Date

October 7, 2014

Last Update Submit

April 10, 2015

Conditions

Keywords

Heart FailureLeft Ventricular Assist DeviceHeart TransplantationCardiomyopathyDestination TherapyCell Therapy

Outcome Measures

Primary Outcomes (1)

  • Intervention Related Adverse Events

    The primary safety endpoint of this study is the incidence of the following potential study-intervention related adverse events within 90 days post intervention (LVAD implantation + intramyocardial injection of study product): infectious myocarditis, myocardial rupture, neoplasm, hypersensitivity reaction, and immune sensitization.

    90 days

Secondary Outcomes (1)

  • Functional Status and Ventricular Function

    90 days

Study Arms (2)

MPC Intramyocardial injection

EXPERIMENTAL

Intramyocardial injections of 25 million Mesenchymal Precursor Cells (MPCs)

Biological: MPC Intramyocardial injection

Control Solution

SHAM COMPARATOR

Intramyocardial injections of 50% Alpha-MEM/42.5% ProFreeze NAO Freezing Medium/7.5% DMSO

Biological: Control Solution

Interventions

Intramyocardial injection of 25 million mesenchymal precursor cells at the time of LVAD implantation

Also known as: RevascorTM
MPC Intramyocardial injection

Injection of control solution during the LVAD implantation.

Also known as: Cryoprotective media
Control Solution

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Signed informed consent, inclusive of release of medical information, and Health Insurance Portability and Accountability Act (HIPAA) documentation;
  • Age 18 years or older;
  • If the subject or partner is of childbearing potential, he or she must be willing to use adequate contraception (hormonal or barrier method or abstinence) from the time of screening and for a period of at least 16 weeks after procedure;
  • Female subjects of childbearing potential must have a negative serum pregnancy test at screening;
  • Admitted to the clinical center at the time of randomization;
  • Clinical indication and accepted candidate for implantation of an FDA approved implantable, non-pulsatile LVAD as a bridge to transplantation or for destination therapy.

You may not qualify if:

  • Planned percutaneous LVAD implantation;
  • Anticipated requirement for biventricular mechanical support;
  • Cardiothoracic surgery within 30 days prior to randomization;
  • Myocardial infarction within 30 days prior to randomization;
  • Prior cardiac transplantation, LV reduction surgery, or cardiomyoplasty;
  • Acute reversible cause of heart failure (e.g. myocarditis, profound hypothyroidism);
  • Stroke within 30 days prior to randomization;
  • Platelet count \< 100,000/ul within 24 hours prior to randomization;
  • Active systemic infection within 48 hours prior to randomization;
  • Presence of \>10% anti-human leukocyte antigen (anti-HLA) antibody titers with known specificity to the MPC donor HLA antigens;
  • A known hypersensitivity to dimethyl sulfoxide (DMSO), murine, and/or bovine products;
  • History of cancer prior to screening (excluding basal cell carcinoma);
  • Acute or chronic infectious disease, including but not limited to human immunodeficiency virus (HIV);
  • Received investigational intervention within 30 days prior to randomization;
  • Treatment and/or an incompleted follow-up treatment of any investigational cell based therapy within 6 months prior to randomization;
  • +3 more criteria

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (11)

University of Florida

Gainsville, Florida, 32610, United States

Location

University of Maryland

Baltimore, Maryland, 21201, United States

Location

Minneapolis Heart Institute Foundation

Minneapolis, Minnesota, 55407, United States

Location

Columbia University Medical Center

New York, New York, 10032, United States

Location

Montefiore Einstein Heart Center

The Bronx, New York, 10467, United States

Location

Duke University

Durham, North Carolina, 27710, United States

Location

Cleveland Clinic Foundation

Cleveland, Ohio, 44195, United States

Location

Ohio State University

Columbus, Ohio, 43210, United States

Location

University of Pennsylvania

Philadelphia, Pennsylvania, 19104, United States

Location

Baylor Research Institute

Dallas, Texas, 75230, United States

Location

Texas Heart Institute

Houston, Texas, 77030, United States

Location

Related Publications (1)

  • Ascheim DD, Gelijns AC, Goldstein D, Moye LA, Smedira N, Lee S, Klodell CT, Szady A, Parides MK, Jeffries NO, Skerrett D, Taylor DA, Rame JE, Milano C, Rogers JG, Lynch J, Dewey T, Eichhorn E, Sun B, Feldman D, Simari R, O'Gara PT, Taddei-Peters WC, Miller MA, Naka Y, Bagiella E, Rose EA, Woo YJ. Mesenchymal precursor cells as adjunctive therapy in recipients of contemporary left ventricular assist devices. Circulation. 2014 Jun 3;129(22):2287-96. doi: 10.1161/CIRCULATIONAHA.113.007412. Epub 2014 Mar 28.

Related Links

MeSH Terms

Conditions

Heart FailureCardiomyopathiesVentricular Dysfunction

Condition Hierarchy (Ancestors)

Heart DiseasesCardiovascular Diseases

Results Point of Contact

Title
Deborah D. Ascheim, MD, Associate Professor, Clinical Director of Research, InCHOIR
Organization
Mount Sinai

Study Officials

  • Timothy Gardner, MD

    Christiana Care Health Services

    STUDY CHAIR
  • Patrick O'Gara, MD

    Brigham and Women's Hospital

    STUDY CHAIR

Publication Agreements

PI is Sponsor Employee
No
Restrictive Agreement
No

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
QUADRUPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR, OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
OTHER
Responsible Party
SPONSOR INVESTIGATOR
PI Title
Associate Professor, Clinical Director of Research, InCHOIR

Study Record Dates

First Submitted

September 26, 2011

First Posted

September 28, 2011

Study Start

April 1, 2012

Primary Completion

March 1, 2013

Study Completion

August 1, 2013

Last Updated

May 1, 2015

Results First Posted

October 13, 2014

Record last verified: 2015-04

Locations