NCT01441375

Brief Summary

This study is a retrospective chart review of sickle cell patients and will include patients whom have received blood transfusions and those whom have not. Of the transfused patients, it will also include those whom have received chelation therapy and those whom have not.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
261

participants targeted

Target at P75+ for all trials

Timeline
Completed

Started Jul 2011

Shorter than P25 for all trials

Geographic Reach
1 country

2 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

July 1, 2011

Completed
2 months until next milestone

First Submitted

Initial submission to the registry

September 7, 2011

Completed
20 days until next milestone

First Posted

Study publicly available on registry

September 27, 2011

Completed
9 months until next milestone

Primary Completion

Last participant's last visit for primary outcome

July 1, 2012

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

July 1, 2012

Completed
Last Updated

October 18, 2012

Status Verified

October 1, 2012

Enrollment Period

1 year

First QC Date

September 7, 2011

Last Update Submit

October 17, 2012

Conditions

Keywords

Sickle cell anemia

Outcome Measures

Primary Outcomes (1)

  • Sickle cell complications

    average of 5 years

Secondary Outcomes (5)

  • Utilization of health care delivery to treat sickle cell complications

    average of 5 years

  • Overall survival

    average of 5 years

  • Utilization of blood transfusions (patients with frequent transfusions only)

    average of 5 years

  • Burden of iron overload (patients with frequent transfusions only)

    average of 5 years

  • Utilization of Iron Chelation Therapies (ICTs) (patients receiving deferoxamine or deferasirox [Exjade®] only)

    average of 5 years

Study Arms (3)

Sickle cell patients non-transfused

Sickle cell patients transfused with no ICT

Sickle cell patients transfused with ICT

Eligibility Criteria

Age16 Years+
Sexall
Healthy VolunteersNo
Age GroupsChild (0-17), Adult (18-64), Older Adult (65+)
Sampling MethodNon-Probability Sample
Study Population

Patients with Sickle cell anemia

You may qualify if:

  • Patients with a diagnosis of Sickle Cell Disease (SCD) and a confirmed genotype
  • Patients ≥ 16 years of age
  • Patients with ≥ 6 months of follow-up data available from first SCD treatment at the center after they reach 16 years old
  • At least one SF reading during a non-acute phase on or after the first SCD treatment at the center after they reach 16 years old

You may not qualify if:

  • Patients who participated in a clinical trial for an iron chelating medication or in a clinical trial for transfusions for SCD (1) within the six months before the index date or (2) during the patient observation period
  • Patients with sickle cell trait

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (2)

Tulane University

New Orleans, Louisiana, 70112, United States

Location

Universit of Tennessee

Memphis, Tennessee, 38163, United States

Location

MeSH Terms

Conditions

Anemia, Sickle Cell

Condition Hierarchy (Ancestors)

Anemia, Hemolytic, CongenitalAnemia, HemolyticAnemiaHematologic DiseasesHemic and Lymphatic DiseasesHemoglobinopathiesGenetic Diseases, InbornCongenital, Hereditary, and Neonatal Diseases and Abnormalities

Study Officials

  • Novartis Pharmaceuticals

    Novartis Pharmaceuticals

    STUDY DIRECTOR

Study Design

Study Type
observational
Observational Model
COHORT
Time Perspective
RETROSPECTIVE
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

September 7, 2011

First Posted

September 27, 2011

Study Start

July 1, 2011

Primary Completion

July 1, 2012

Study Completion

July 1, 2012

Last Updated

October 18, 2012

Record last verified: 2012-10

Locations