NCT01418352

Brief Summary

The goal of the current trial is to determine efficacy and safety of once-weekly aripiprazole in reducing Total Tic Severity (TTS) score in children and adolescents with Tourette's Disorder.

Trial Health

93
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
83

participants targeted

Target at below P25 for phase_3

Timeline
Completed

Started Aug 2011

Typical duration for phase_3

Geographic Reach
5 countries

35 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

August 1, 2011

Completed
1 day until next milestone

Study Start

First participant enrolled

August 2, 2011

Completed
15 days until next milestone

First Posted

Study publicly available on registry

August 17, 2011

Completed
2.6 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

March 12, 2014

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

March 12, 2014

Completed
7.6 years until next milestone

Results Posted

Study results publicly available

October 7, 2021

Completed
Last Updated

October 7, 2021

Status Verified

September 1, 2021

Enrollment Period

2.6 years

First QC Date

August 1, 2011

Results QC Date

September 7, 2021

Last Update Submit

September 10, 2021

Conditions

Keywords

Tourette's DisorderTic disorders

Outcome Measures

Primary Outcomes (1)

  • Mean Change From Baseline to Week 8 in Yale Global Tic Severity Scale (YGTSS) Total Tic Score

    The YGTSS is a semi-structured clinical interview designed to measure the tic severity. This scale consisted of a tic inventory, with 5 separate rating scales to rate the severity of symptoms, and an impairment ranking. Ratings were made along 5 different dimensions on a scale of 0 to 5 for motor and vocal tics, each including number, frequency, intensity, complexity, and interference. The YGTSS TTS was the summation of the severity scores of motor and vocal tics. The total tic score (TTS) ranged from 0 (none) to 50 (severe) with higher score represent more severe symptoms (greater reduction from baseline for greater improvement).

    Baseline and Week 8

Secondary Outcomes (2)

  • Mean Change From Baseline in Clinical Global Impressions Scale for Tourette's Syndrome (CGI-TS) Score

    Baseline and Week 8

  • Mean Change From Baseline in Gilles de la Tourette Quality of Life (GTS-QOL) Overall Score at Week 8

    Baseline and Week 8

Study Arms (4)

Matching Placebo

PLACEBO COMPARATOR

Participants received aripiprazole matching placebo, tablets, orally, once weekly for 8 weeks in the Double-blind Treatment Period.

Drug: Placebo

Aripiprazole 52.5 mg

EXPERIMENTAL

Participants received aripiprazole 52.5 mg, tablets, orally, once weekly for 8 weeks in the Double-blind Treatment Period.

Drug: Aripiprazole

Aripiprazole 77.5 mg

EXPERIMENTAL

Participants received aripiprazole 77.5 mg, tablets, orally, once weekly for 8 weeks in the Double-blind Treatment Period.

Drug: Aripiprazole

Aripiprazole 110 mg

EXPERIMENTAL

Participants received aripiprazole 110 mg, tablets, orally, once weekly for 8 weeks in the Double-blind Treatment Period.

Drug: Aripiprazole

Interventions

Aripiprazole tablets once weekly for 8 weeks.

Also known as: ABILIFY
Aripiprazole 110 mgAripiprazole 52.5 mgAripiprazole 77.5 mg

Aripiprazole matching-placebo once-weekly for 8 weeks.

Matching Placebo

Eligibility Criteria

Age7 Years - 17 Years
Sexall
Healthy VolunteersNo
Age GroupsChild (0-17)

You may qualify if:

  • to 17 year old with diagnostic and statistical manual of mental disorders, fourth edition -text revision (DSM-IV-TR) diagnostic criteria for Tourette's disorder (TD), confirmed by the kiddie schedule for affective disorders and schizophrenia - present and lifetime version (K-SADS-PL), including the Diagnostic Supplement 5
  • Has a total tic score (TTS) ≥20 on the yale global tic severity scale (YGTSS) at Screening and Baseline
  • Presenting tic symptoms cause impairment in the participant's normal routines, which include academic achievement, occupational functioning, social activities, and/or relationships
  • Females of childbearing potential must have a negative pregnancy test, must be practicing acceptable double-barrier methods of contraception, and must not be pregnant or lactating.
  • Written informed consent form (ICF) obtained from a legally acceptable representative \& informed assent at Screening as applicable by study center's Institutional review board/independent ethics committee (IRB/IEC)
  • The participant, designated guardian(s) or caregiver(s) are able to comprehend and satisfactorily comply with the protocol requirements, as evaluated by the investigator.

You may not qualify if:

  • Clinical presentation and/or history, consistent with another neurologic condition that may have accompanying abnormal movements.
  • History of schizophrenia, bipolar disorder, or other psychotic disorder.
  • Participant receiving psychostimulants for treatment of attention-deficit disorder/Attention-deficit hyperactivity disorder (ADD/ADHD) and who have developed and/or had exacerbations of tic disorder after initiation of stimulant treatment.
  • Currently meets DSM-IV-TR criteria for a primary mood disorder.
  • Severe obsessive-compulsive disorder (OCD), per children's yale-brown obsessive compulsive scale (CY-BOCS) score \>16.
  • Taken aripiprazole within 30 days of the Screening visit.
  • Received any investigational agent in a clinical trial within 30 days prior to Screening or who were randomized into a clinical trial with Once-weekly aripiprazole at any time.
  • History of neuroleptic malignant syndrome.
  • Sexually active participants not using 2 approved methods of contraception; breastfeeding or pregnant.
  • Risk of committing suicide
  • Bodyweight lower than 16 kg
  • Taken neuroleptic or antiparkinson drugs \<14 days prior to randomization.
  • Requiring cognitive-behavioral therapy (CBT) for TD during study.
  • Participant meets DSM-IV-TR criteria for any significant psychoactive substance use disorder within the past 3 months.
  • Positive drug screen
  • +4 more criteria

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (35)

Unknown Facility

Dothan, Alabama, 36303, United States

Location

Unknown Facility

San Francisco, California, 94143, United States

Location

Unknown Facility

Gainesville, Florida, 32610, United States

Location

Unknown Facility

Miami, Florida, 33126, United States

Location

Unknown Facility

Atlanta, Georgia, 30308, United States

Location

Unknown Facility

Atlanta, Georgia, 30329, United States

Location

Unknown Facility

Chicago, Illinois, 60612, United States

Location

Unknown Facility

Omaha, Nebraska, 68131, United States

Location

Unknown Facility

Manhasset, New York, 11030, United States

Location

Unknown Facility

Cincinnati, Ohio, 45229-3039, United States

Location

Unknown Facility

Oklahoma City, Oklahoma, 73112, United States

Location

Unknown Facility

Charlottesville, Virginia, 22903, United States

Location

Unknown Facility

La Crosse, Wisconsin, 54601, United States

Location

Unknown Facility

Rousse, 7004, Bulgaria

Location

Unknown Facility

Sofia, 1431, Bulgaria

Location

Unknown Facility

Varna, 9010, Bulgaria

Location

Unknown Facility

Aachen, 52074, Germany

Location

Unknown Facility

Dresden, 01307, Germany

Location

Unknown Facility

Hanover, 30625, Germany

Location

Unknown Facility

München, 80336, Germany

Location

Unknown Facility

Ulm, 89075, Germany

Location

Unknown Facility

Bucharest, 041914, Romania

Location

Unknown Facility

Cluj-Napoca, 400660, Romania

Location

Unknown Facility

Craiova, 200620, Romania

Location

Unknown Facility

Iași, 700282, Romania

Location

Unknown Facility

Donetsk, 83008, Ukraine

Location

Unknown Facility

Kharkiv, 61068, Ukraine

Location

Unknown Facility

Kharkiv, 61153, Ukraine

Location

Unknown Facility

Kyiv, 01030, Ukraine

Location

Unknown Facility

Kyiv, 03049, Ukraine

Location

Unknown Facility

Kyiv, 04209, Ukraine

Location

Unknown Facility

Luhansk, 91045, Ukraine

Location

Unknown Facility

Poltava, 36006, Ukraine

Location

Unknown Facility

Stepanovka, 73488, Ukraine

Location

Unknown Facility

Vinnytsia, 21005, Ukraine

Location

MeSH Terms

Conditions

Tourette SyndromeTic Disorders

Interventions

Aripiprazole

Condition Hierarchy (Ancestors)

Basal Ganglia DiseasesBrain DiseasesCentral Nervous System DiseasesNervous System DiseasesMovement DisordersHeredodegenerative Disorders, Nervous SystemNeurodegenerative DiseasesGenetic Diseases, InbornCongenital, Hereditary, and Neonatal Diseases and AbnormalitiesNeurodevelopmental DisordersMental Disorders

Intervention Hierarchy (Ancestors)

PiperazinesHeterocyclic Compounds, 1-RingHeterocyclic CompoundsQuinolonesQuinolinesHeterocyclic Compounds, 2-RingHeterocyclic Compounds, Fused-Ring

Limitations and Caveats

Limitations of the trial such as small numbers of subjects analyzed or technical problems leading to unreliable data.

Results Point of Contact

Title
Global Clinical Development
Organization
Otsuka Pharmaceutical Development & Commercialization, Inc.

Study Officials

  • Eva Kohegyi, MD

    Otsuka Pharmaceutical Development & Commercialization, Inc.

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
QUADRUPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR, OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

August 1, 2011

First Posted

August 17, 2011

Study Start

August 2, 2011

Primary Completion

March 12, 2014

Study Completion

March 12, 2014

Last Updated

October 7, 2021

Results First Posted

October 7, 2021

Record last verified: 2021-09

Data Sharing

IPD Sharing
Will share

Anonymized Individual participant data (IPD) that underlie the results of this study will be shared with researchers to achieve aims pre-specified in a methodologically sound research proposal. Small studies with less than 25 participants are excluded from data sharing.

Shared Documents
STUDY PROTOCOL, SAP, CSR
Time Frame
Data will be available after marketing approval in global markets, or beginning 1-3 years following article publication. There is no end date to the availability of the data.
Access Criteria
Otsuka will share data on the Vivli data sharing platform which can be found here: https://vivli.org/ourmember/Otsuka/.
More information

Locations