NCT01395914

Brief Summary

The administration of Anamorelin HCl in patients with Non-Small Cell Lung Cancer-Cachexia (NSCLC-C) is expected to increase appetite, lean body mass, weight gain, and muscle strength.

Trial Health

98
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
513

participants targeted

Target at P75+ for phase_3

Timeline
Completed

Started Jul 2011

Typical duration for phase_3

Geographic Reach
16 countries

69 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

June 30, 2011

Completed
1 day until next milestone

Study Start

First participant enrolled

July 1, 2011

Completed
17 days until next milestone

First Posted

Study publicly available on registry

July 18, 2011

Completed
2.9 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

June 1, 2014

Completed
8 months until next milestone

Study Completion

Last participant's last visit for all outcomes

February 1, 2015

Completed
2.4 years until next milestone

Results Posted

Study results publicly available

July 11, 2017

Completed
Last Updated

September 14, 2017

Status Verified

August 1, 2017

Enrollment Period

2.9 years

First QC Date

June 30, 2011

Results QC Date

March 15, 2017

Last Update Submit

August 16, 2017

Conditions

Outcome Measures

Primary Outcomes (1)

  • Percentage of Participants With Treatment-emergent Adverse Events

    To Evaluate the Safety and Tolerability of Anamorelin HCl.

    Over the 12-week treatment period

Secondary Outcomes (3)

  • Change in Body Weight

    Change in body weight from baseline of the original trial through Week 12 of this extension trial.

  • Change in Handgrip Strength of the Non-Dominant Hand

    Change in HGS from baseline of the original trial through Week 12 of this extension trial.

  • Change in A/CS Domain Score

    Change in FAACT A/CS Domain Score from baseline of the original trial through Week 12 of this extension trial

Study Arms (2)

100 mg QD

EXPERIMENTAL

100 mg yellow coated, oval tablet; oral administration once daily

Drug: Anamorelin HCl

Placebo

PLACEBO COMPARATOR

Placebo tablets identical in appearance to active tablets; oral administration once daily

Drug: Placebo

Interventions

100 mg QD
Placebo

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Has completed the Day 85 Visit in the original trial (Study HT-ANAM-301 or HT-ANAM-302) and is considered appropriate to continue to receive additional study drug; must start dosing on the extension study within 5 days of completing dosing on the original trial
  • ECOG performance status ≤2
  • Life expectancy of \>4 months at time of screening
  • If woman of childbearing potential or a fertile man, he/she must agree to use an effective form of contraception during the study and for 30 days following the last dose of study drug (an effective form of contraception is abstinence, a hormonal contraceptive, or a double-barrier method)
  • Must be willing and able to give signed informed consent and, in the opinion of the Investigator, to comply with the protocol tests and procedures

You may not qualify if:

  • Women who are pregnant or breast-feeding
  • Had major surgery (central venous access placement and tumor biopsies are not considered major surgery) within 4 weeks prior to enrollment into the extension study; patients must be well recovered from acute effects of surgery prior to screening; patients should not have plans to undergo major surgical procedures during the treatment period
  • Currently taking prescription medications intended to increase appetite or treat weight loss; these include, but are not limited to, testosterone, androgenic compounds, megestrol acetate, methylphenidate, and dronabinol
  • Inability to readily swallow oral tablets; patients with severe gastrointestinal disease (including esophagitis, gastritis, malabsorption, or obstructive symptoms) or intractable or frequent vomiting are excluded
  • Has an active, uncontrolled infection
  • Has known or symptomatic brain metastases
  • Receiving strong CYP3A4 inhibitors
  • Receiving tube feedings or parenteral nutrition (either total or partial); patients must have discontinued these treatments for at least 6 weeks prior to Day 1, and throughout the study duration
  • Other clinical diagnosis, ongoing or intercurrent illness that in the Investigator's opinion would prevent the patient's participation
  • Patients actively receiving a concurrent investigational agent, other than Anamorelin HCl

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (72)

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Corona, California, United States

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Fountain Valley, California, United States

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Fullerton, California, United States

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Glendale, California, United States

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La Jolla, California, United States

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Riverside, California, United States

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Washington D.C., District of Columbia, United States

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Orange City, Florida, United States

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Quincy, Illinois, United States

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Indianapolis, Indiana, United States

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Louisville, Kentucky, United States

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Boston, Massachusetts, United States

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Lake Success, New York, United States

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Durham, North Carolina, United States

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Cleveland, Ohio, United States

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Sylvania, Ohio, United States

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West Reading, Pennsylvania, United States

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Charleston, South Carolina, United States

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Falls Church, Virginia, United States

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Prairiewood, New South Wales, Australia

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Adelaide, Australia

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East Bentleigh, Australia

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Victoria, Australia

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Brest, Belarus

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Lesnoy, Belarus

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Minsk, Belarus

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Antwerp, Belgium

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Brussels, Belgium

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Genk, Belgium

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Ghent, Belgium

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Liège, Belgium

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Edmonton, Alberta, Canada

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Sault Ste. Marie, Ontario, Canada

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Toronto, Ontario, Canada

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Montreal, Quebec, Canada

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Benešov, Czechia

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Brno, Czechia

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Hlučín, Czechia

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Liberec, Czechia

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Nymburk, Czechia

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Lyon, France

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Villejuif, France

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Großhansdorf, Germany

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Halle, Germany

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Budapest, Hungary

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Kassai, Hungary

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Beersheba, Israel

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Petach Tikvah, Israel

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Tel Litwinsky, Israel

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Ẕerifin, Israel

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Piacenza, Italy

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Bydgoszcz, Poland

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Grudziądz, Poland

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Katowice, Poland

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Krakow, Poland

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Lodz, Poland

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Lublin, Poland

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Szczecin, Poland

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Warsaw, Poland

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Krasnodar, Russia

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Moscow, Russia

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Saint Petersburg, Russia

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Yekaterinburg, Russia

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Belgrade, Serbia

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Kamenitz, Serbia

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Ljubljana, Slovenia

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Barcelona, Spain

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Seville, Spain

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Valencia, Spain

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Dnipropetrovsk, Ukraine

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Kharkiv, Ukraine

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Kyiv, Ukraine

Location

Related Publications (1)

  • Currow D, Temel JS, Abernethy A, Milanowski J, Friend J, Fearon KC. ROMANA 3: a phase 3 safety extension study of anamorelin in advanced non-small-cell lung cancer (NSCLC) patients with cachexia. Ann Oncol. 2017 Aug 1;28(8):1949-1956. doi: 10.1093/annonc/mdx192.

MeSH Terms

Conditions

CachexiaCarcinoma, Non-Small-Cell Lung

Condition Hierarchy (Ancestors)

Weight LossBody Weight ChangesBody WeightSigns and SymptomsPathological Conditions, Signs and SymptomsThinnessCarcinoma, BronchogenicBronchial NeoplasmsLung NeoplasmsRespiratory Tract NeoplasmsThoracic NeoplasmsNeoplasms by SiteNeoplasmsLung DiseasesRespiratory Tract Diseases

Results Point of Contact

Title
Richard K. Bourne, Ph.D.
Organization
Helsinn Therapeutics (US), Inc.

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
QUADRUPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR, OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

June 30, 2011

First Posted

July 18, 2011

Study Start

July 1, 2011

Primary Completion

June 1, 2014

Study Completion

February 1, 2015

Last Updated

September 14, 2017

Results First Posted

July 11, 2017

Record last verified: 2017-08

Locations