NCT01394029

Brief Summary

This study will observe patients with transfusional hemosiderosis treated with deferasirox in actual practice setting.

Trial Health

90
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
120

participants targeted

Target at P50-P75 for all trials

Timeline
Completed

Started Jul 2011

Longer than P75 for all trials

Geographic Reach
4 countries

10 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

July 1, 2011

Completed
11 days until next milestone

First Submitted

Initial submission to the registry

July 12, 2011

Completed
2 days until next milestone

First Posted

Study publicly available on registry

July 14, 2011

Completed
4.2 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

October 1, 2015

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

October 1, 2015

Completed
Last Updated

February 2, 2016

Status Verified

February 1, 2016

Enrollment Period

4.3 years

First QC Date

July 12, 2011

Last Update Submit

February 1, 2016

Conditions

Keywords

iron overloadiron chelationdeferasiroxobservational

Outcome Measures

Primary Outcomes (2)

  • Serum Creatinine and liver enzyme levels

    Observed over 3 years for each patient

    3 years

  • Adverse Drug Reactions

    Observed over 3 years for each patient

    3 years

Study Arms (1)

deferasirox

Drug: deferasirox

Interventions

Also known as: ICL670
deferasirox

Eligibility Criteria

Age2 Years+
Sexall
Healthy VolunteersNo
Age GroupsChild (0-17), Adult (18-64), Older Adult (65+)
Sampling MethodNon-Probability Sample
Study Population

Patients treated with deferasirox for transfusional hemosiderosis according to the local prescribing information.

You may qualify if:

  • Patients treated with deferasirox for transfusional hemosiderosis according to the local prescribing information.
  • (the patients are either beginning treatment with deferasirox at the time of enrollment in the sentinel site monitoring or are currently under treatment with deferasirox and have started the treatment under prescription up to twelve months prior to enrollment in the sentinal site monitoring.

You may not qualify if:

  • Patients with non-transfusional hemosiderosis
  • Patients treated with deferasirox in an interventional clinical trial

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (10)

Novartis Investigative Site

Cairo, Cairo Governorate, 11566, Egypt

Location

Novartis Investigative Site

Cairo, Egypt

Location

Novartis Investigative Site

Amman, 11195, Jordan

Location

Novartis Investigative Site

Barcelona, Catalonia, 08916, Spain

Location

Novartis Investigative Site

Barcelona, Catalonia, Spain

Location

Novartis Investigative Site

Oviedo, Principality of Asturias, 33006, Spain

Location

Novartis Investigative Site

West Midlands, Birmingham, B4 6NH, United Kingdom

Location

Novartis Investigative Site

London, N18 1QX, United Kingdom

Location

Novartis Investigative Site

London, N19 5NF, United Kingdom

Location

Novartis Investigative Site

London, SE5 9RS, United Kingdom

Location

MeSH Terms

Conditions

Iron Overload

Interventions

Deferasirox

Condition Hierarchy (Ancestors)

Iron Metabolism DisordersMetabolic DiseasesNutritional and Metabolic Diseases

Intervention Hierarchy (Ancestors)

BenzoatesAcids, CarbocyclicCarboxylic AcidsOrganic ChemicalsBenzene DerivativesHydrocarbons, AromaticHydrocarbons, CyclicHydrocarbonsTriazolesAzolesHeterocyclic Compounds, 1-RingHeterocyclic Compounds

Study Officials

  • Novartis Pharmaceuticals

    Novartis Pharmaceuticals

    STUDY DIRECTOR

Study Design

Study Type
observational
Observational Model
COHORT
Time Perspective
RETROSPECTIVE
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

July 12, 2011

First Posted

July 14, 2011

Study Start

July 1, 2011

Primary Completion

October 1, 2015

Study Completion

October 1, 2015

Last Updated

February 2, 2016

Record last verified: 2016-02

Locations