NCT00466063

Brief Summary

This registry will evaluate long-term safety and efficacy of deferasirox in children with transfusional iron overload.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
108

participants targeted

Target at P50-P75 for all trials

Timeline
Completed

Started May 2007

Longer than P75 for all trials

Geographic Reach
1 country

23 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

April 25, 2007

Completed
2 days until next milestone

First Posted

Study publicly available on registry

April 27, 2007

Completed
4 days until next milestone

Study Start

First participant enrolled

May 1, 2007

Completed
8.2 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

July 1, 2015

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

July 1, 2015

Completed
Last Updated

December 29, 2015

Status Verified

December 1, 2015

Enrollment Period

8.2 years

First QC Date

April 25, 2007

Last Update Submit

December 26, 2015

Conditions

Keywords

Iron overloadchildrendeferasiroxTransfusion-dependent anemia

Outcome Measures

Primary Outcomes (1)

  • Safety - renal and hepatic function monitoring.

    5 years

Secondary Outcomes (3)

  • Adverse events

    5 years

  • Longitudinal ferritin levels

    5 years

  • Assessment of auditory and ophthalmologic status

    5 years

Study Arms (1)

ICL670

ICL670

Drug: Deferasirox

Interventions

ICL670

Eligibility Criteria

Age2 Years - 5 Years
Sexall
Healthy VolunteersNo
Age GroupsChild (0-17)
Sampling MethodNon-Probability Sample
Study Population

200 unselected children aged from 2 to \<6 years at enrolment with chronic iron overload due to repeated blood transfusions. The participating countries were selected on the basis of both a high incidence of young children with thalassemia or other transfusion dependent anemias and on the basis that the drug is approved and 'on the market' in the country selected.

You may qualify if:

  • History of transfusion-dependent anemia.
  • History of iron overload

You may not qualify if:

  • Patients with non-transfusional hemosiderosis.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (23)

University of South Alabama Medical Center

Mobile, Alabama, 36604, United States

Location

Children's Hospital Los Angeles

Los Angeles, California, 90027, United States

Location

Children's Hospital Oakland

Oakland, California, 94609, United States

Location

Children's Hospital of Orange County

Orange, California, 92868-3874, United States

Location

Stanford University Medical Center

Stanford, California, 94304, United States

Location

MD Anderson Cancer Center - Orlando

Orlando, Florida, 32806, United States

Location

St. Joseph's Children's Hospital of Tampa

Tampa, Florida, 33609, United States

Location

Children's Memorial Hospital

Chicago, Illinois, 60614-3394, United States

Location

Children's Hospital Boston

Boston, Massachusetts, 02115, United States

Location

Hackensack University Medical Center

Hackensack, New Jersey, 07601, United States

Location

St. Joseph's Children's Hospital

Paterson, New Jersey, 07503, United States

Location

The Brooklyn Hospital Center

Brooklyn, New York, 11201, United States

Location

Schneider Children's Hospital

New York, New York, 11040, United States

Location

SUNY - Upstate Medical University

Syracuse, New York, 13210, United States

Location

East Carolina University

Greenville, North Carolina, 27858, United States

Location

Akron Children's Hospital

Akron, Ohio, 44308-1062, United States

Location

Children's Medical Center

Dayton, Ohio, 45404, United States

Location

Oklahoma State University Health Sciences Center

Oklahoma City, Oklahoma, 73104, United States

Location

Penn State University / Milton S. Hershey Medical Center

Hershey, Pennsylvania, 17033-0850, United States

Location

St. Jude Children's Research Hospital Memphis

Memphis, Tennessee, 38105-2794, United States

Location

Cook's Children's Medical Center

Fort Worth, Texas, 76104, United States

Location

Texas Children's Hospital

Houston, Texas, 77030, United States

Location

Children's Hospital of the King's Daughters

Norfolk, Virginia, 23507, United States

Location

MeSH Terms

Conditions

AnemiaIron Overload

Interventions

Deferasirox

Condition Hierarchy (Ancestors)

Hematologic DiseasesHemic and Lymphatic DiseasesIron Metabolism DisordersMetabolic DiseasesNutritional and Metabolic Diseases

Intervention Hierarchy (Ancestors)

BenzoatesAcids, CarbocyclicCarboxylic AcidsOrganic ChemicalsBenzene DerivativesHydrocarbons, AromaticHydrocarbons, CyclicHydrocarbonsTriazolesAzolesHeterocyclic Compounds, 1-RingHeterocyclic Compounds

Study Officials

  • Novartis Pharmaceuticals

    Novartis Pharmaceuticals

    STUDY DIRECTOR

Study Design

Study Type
observational
Observational Model
COHORT
Time Perspective
PROSPECTIVE
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

April 25, 2007

First Posted

April 27, 2007

Study Start

May 1, 2007

Primary Completion

July 1, 2015

Study Completion

July 1, 2015

Last Updated

December 29, 2015

Record last verified: 2015-12

Locations