NCT01295710

Brief Summary

The study objective is to compare the efficacy and safety of US-ATG-F as a supplement to standard of care prophylaxis versus standard of care prophylaxis alone in moderate to severe chronic GVHD-free survival.

Trial Health

90
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
260

participants targeted

Target at P50-P75 for phase_3

Timeline
Completed

Started Oct 2011

Typical duration for phase_3

Geographic Reach
2 countries

28 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

February 9, 2011

Completed
5 days until next milestone

First Posted

Study publicly available on registry

February 14, 2011

Completed
8 months until next milestone

Study Start

First participant enrolled

October 10, 2011

Completed
4 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

October 15, 2015

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

October 15, 2015

Completed
3.4 years until next milestone

Results Posted

Study results publicly available

March 20, 2019

Completed
Last Updated

April 9, 2019

Status Verified

March 1, 2019

Enrollment Period

4 years

First QC Date

February 9, 2011

Results QC Date

January 22, 2019

Last Update Submit

March 29, 2019

Conditions

Keywords

adult acute myeloid leukemiaadult acute lymphoid leukemiaadult myelodysplastic syndromeallogenic stem cell transplantationunrelated donorGVHDUS-ATG-F (Anti-human-T-lymphocyte Immune Globulin, Rabbit)

Outcome Measures

Primary Outcomes (1)

  • Number of Participants With First Occurrence of Moderate to Severe Chronic GVHD According to 2005 NIH Criteria as Determined by the Independent Endpoint Committee or Death From Any Cause After Allogeneic Stem Cell Transplantation

    Participants with first occurrence of moderate to severe chronic GVHD according to 2005 NIH criteria as determined by the Independent Endpoint Committee or death from any cause after allogeneic stem cell transplantation, with a target of 124 total events of moderate or severe chronic GVHD, or death from any cause

    Time from first study drug administration until the first occurrence of moderate to severe chronic GVHD according to 2005 NIH criteria as determined by the Independent Endpoint Committee, or death from any cause, assessed up to 48 months

Secondary Outcomes (11)

  • Overall Survival

    Time from first study drug administration until the occurrence of death from any cause, assessed up to 48 months

  • Number of Participants With Chronic GVHD Mild to Severe

    Time from first study drug administration until the first occurrence of mild to severe chronic GVHD according to 2005 NIH criteria as determined by the Investigators, with death and re transplantation as competing risks, assessed up to 48 months

  • Number of Participants With Chronic GVHD Moderate to Severe

    Time from first study drug administration until the first occurrence of moderate to severe chronic GVHD according to 2005 NIH criteria as determined by the Investigators, with death and re transplantation as competing risks, assessed up to 48 months

  • Number of Participants With Chronic GVHD Severe

    Time from first study drug administration until the first occurrence of severe chronic GVHD according to 2005 NIH criteria as determined by the Investigators, with death and re transplantation as competing risks, assessed up to 48 months

  • Number of Participants With Acute GVHD Grade I-IV

    Time from first study drug administration until the first occurrence of acute GVHD grade I-IV as determined by the Investigators, with death and re transplantation as competing risks, assessed up to 48 months

  • +6 more secondary outcomes

Study Arms (2)

US-ATG-F

ACTIVE COMPARATOR

20 mg/kg body weight per day, diluted in 250 mL normal saline, IV infusion over 6-16 hours 3 days prior to transplantation

Biological: US-ATG-F

Placebo

PLACEBO COMPARATOR

250 mL normal saline, IV infusion over 6-16 hours 3 days prior to transplantation

Biological: Placebo

Interventions

US-ATG-FBIOLOGICAL

20 mg/kg body weight per day, diluted in 250 mL normal saline, IV infusion over 6-16 hours 3 days prior to transplantation

Also known as: Anti-human-T-lymphocyte Immune Globulin, Rabbit
US-ATG-F
PlaceboBIOLOGICAL

250 mL normal saline, IV infusion over 6-16 hours 3 days prior to transplantation

Placebo

Eligibility Criteria

Age18 Years - 65 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Patients designated to undergo allogeneic peripheral blood or bone marrow stem cell transplantation following the diagnosis of one of the primary diseases in early or intermediate disease status (i.e., acute myeloid leukemia, acute lymphoid leukemia, and myelodysplastic syndrome)
  • Patients with an unrelated HLA-A,-B, -C and -DRBI matched donor
  • Patients with a Karnofsky Performance Score ≥ 70%

You may not qualify if:

  • Clinically significant concomitant diseases (i.e., cardiac, pulmonary, renal and CNS)
  • Bacterial, viral, or fungal infections
  • Known positive for Hepatitis B surfaces antigen, or Hepatitis C antibody, or who have been tested positive for HIV
  • Patients with any concurrent malignancy. Cancer treated with curative intent \< 5 years previously will not be allowed except for patients with resected basal cell carcinoma or treated cervical carcinoma in situ
  • Known contraindications to the administration of rabbit immunoglobulin antibodies
  • Hypersensitivity to methylprednisolone, tacrolimus, methotrexate or any excipients contains in these products

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (28)

City of Hope

Duarte, California, 91019, United States

Location

Stanford University Medical Center, BMT

Stanford, California, 94305, United States

Location

University of Florida Shands Cancer Center

Gainesville, Florida, 32610, United States

Location

Moffitt Cancer Center

Tampa, Florida, 33612, United States

Location

University of Chicago Medical Center

Chicago, Illinois, 60637, United States

Location

Loyola University Medical Center

Maywood, Illinois, 60153, United States

Location

University of Kansas Medical Center

Westwood, Kansas, 66205, United States

Location

Tulane University Health Sciences Center

New Orleans, Louisiana, 70112, United States

Location

Beth Israel Deaconess Medical Center

Boston, Massachusetts, 02215, United States

Location

Dana-Farber Cancer Institute

Boston, Massachusetts, 02215, United States

Location

Massachusetts General Hospital

Boston, Massachusetts, 02215, United States

Location

Mayo Clinic

Rochester, Minnesota, 55905, United States

Location

Washington University Medical Center

St Louis, Missouri, 63110, United States

Location

Weill Cornell Medical Center

New York, New York, 10065, United States

Location

University of North Carolina Hospitals

Chapel Hill, North Carolina, 27599, United States

Location

Duke University Medical Center

Durham, North Carolina, 27710, United States

Location

University of Oklahoma Health Sciences Center

Oklahoma City, Oklahoma, 73104, United States

Location

Oregon Health and Science University

Portland, Oregon, 97239, United States

Location

Penn State Hershey Cancer Institute

Hershey, Pennsylvania, 17033, United States

Location

Abramson Cancer Center of the University at Perlman Center for Advanced Medicine

Philadelphia, Pennsylvania, 19104, United States

Location

Vanderbilt University Medical Center, Vanderbilt Ingram Cancer Center

Nashville, Tennessee, 37232, United States

Location

University of Texas Southwestern Medical Center

Dallas, Texas, 75390, United States

Location

Texas Transplant Physician's Group

San Antonio, Texas, 78229, United States

Location

University of Utah School of Medicine

Salt Lake City, Utah, 84132, United States

Location

VA Puget Sound Healthcare System

Seattle, Washington, 98108, United States

Location

Fred Hutchinson Cancer Research Center

Seattle, Washington, 98109, United States

Location

Royal Adelaide Hospital

Adelaide, South Australia, 5000, Australia

Location

Royal Melbourne Hospital

Parkville, Victoria, 03050, Australia

Location

Related Publications (1)

  • Chakupurakal G, Freudenberger P, Skoetz N, Ahr H, Theurich S. Polyclonal anti-thymocyte globulins for the prophylaxis of graft-versus-host disease after allogeneic stem cell or bone marrow transplantation in adults. Cochrane Database Syst Rev. 2023 Jun 21;6(6):CD009159. doi: 10.1002/14651858.CD009159.pub3.

MeSH Terms

Conditions

Leukemia, Myeloid, AcutePrecursor Cell Lymphoblastic Leukemia-LymphomaMyelodysplastic SyndromesAnemia, Refractory, with Excess of Blasts

Condition Hierarchy (Ancestors)

Leukemia, MyeloidLeukemiaNeoplasms by Histologic TypeNeoplasmsHematologic DiseasesHemic and Lymphatic DiseasesLeukemia, LymphoidLymphoproliferative DisordersLymphatic DiseasesImmunoproliferative DisordersImmune System DiseasesBone Marrow DiseasesAnemia, RefractoryAnemia

Results Point of Contact

Title
Anne Kuan
Organization
Neovii

Study Officials

  • Anne Kuan

    Neovii Biotech

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restrictive Agreement
No

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
QUADRUPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR, OUTCOMES ASSESSOR
Purpose
PREVENTION
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

February 9, 2011

First Posted

February 14, 2011

Study Start

October 10, 2011

Primary Completion

October 15, 2015

Study Completion

October 15, 2015

Last Updated

April 9, 2019

Results First Posted

March 20, 2019

Record last verified: 2019-03

Locations