NCT01284062

Brief Summary

This study represents the first investigation of anrukinzumab in patients with active ulcerative colitis (UC) and will evaluate proof of mechanism by changes in the mechanism based biomarker (YKL 40) and pharmacodynamic biomarkers (fecal calprotectin, lactoferrin and hs-CRP). It will provide further assessment of the safety, tolerability, and pharmacokinetics (PK) by administration of multiple intravenous (IV) doses of anrukinzumab.

Trial Health

98
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
84

participants targeted

Target at P50-P75 for phase_2

Timeline
Completed

Started Mar 2011

Geographic Reach
11 countries

76 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

January 25, 2011

Completed
1 day until next milestone

First Posted

Study publicly available on registry

January 26, 2011

Completed
1 month until next milestone

Study Start

First participant enrolled

March 1, 2011

Completed
2.1 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

April 1, 2013

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

April 1, 2013

Completed
1.6 years until next milestone

Results Posted

Study results publicly available

November 18, 2014

Completed
Last Updated

November 18, 2014

Status Verified

November 1, 2014

Enrollment Period

2.1 years

First QC Date

January 25, 2011

Results QC Date

November 10, 2014

Last Update Submit

November 10, 2014

Conditions

Keywords

Active Ulcerative ColitisPhase 2ADouble-blindRandomizedPK/PD Biomarker Study

Outcome Measures

Primary Outcomes (1)

  • Fold Change From Baseline in Fecal Calprotectin at Week 14

    The fold change from baseline in fecal calprotectin at Week 14, is the ratio of the measurement of fecal calprotectin at Week 14 to baseline measurement; this was calculated as the change from baseline in natural log transformed fecal calprotectin at Week 14.

    Baseline, Week 14

Secondary Outcomes (12)

  • Maximum Observed Plasma Concentration (Cmax) for Anrukinzumab

    Pre-dose to end of the dosing interval after Day 1, Week 12

  • Minimum Observed Plasma Trough Concentration (Cmin) for Anrukinzumab

    Pre-dose to end of the dosing interval after Day 1, Week 12

  • Area Under the Curve From Time Zero to End of Dosing Interval (AUCtau) for Anrukinzumab

    Pre-dose, within 1 hour post-end of infusion on Day 1; Day 2, 4, 7, pre-dose on Week 2

  • Plasma Decay Half-Life (t1/2) for Anrukinzumab

    Within 1 hour post-end of infusion on Week 12; Week 14, 16, 18, 20, 22, 24, 26, 28, 30, 32

  • Systemic Clearance (CL) for Anrukinzumab

    Pre-dose, within 1 hour post-end of infusion on Week 12; Week 14, 16, 18, 20, 22, 24, 26, 28, 30, 32

  • +7 more secondary outcomes

Other Outcomes (5)

  • Clinical Response Rate at Week 14

    Week 14

  • Clinical Remission Rate at Week 14

    Week 14

  • Change From Baseline in Total Mayo Score at Week 14

    Baseline, Week 14

  • +2 more other outcomes

Study Arms (4)

Arm 1

EXPERIMENTAL

200 mg PF-05230917, Anrukinzumab active dose level

Biological: Anrukinzumab

Arm 2

EXPERIMENTAL

400 mg PF-05230917, Anrukinzumab active dose level

Biological: Anrukinzumab

Arm 3

EXPERIMENTAL

600 mg PF-05230917, Anrukinzumab active dose level

Biological: Anrukinzumab

Arm 4

PLACEBO COMPARATOR

Matching placebo - administered at matching dose level 200 mg, 400 mg or 600 mg.

Other: placebo

Interventions

AnrukinzumabBIOLOGICAL

200 mg sterile liquid vial, administered intravenously, one-hour infusion on Day 1, Week 2, 4, 8, and 12

Also known as: PF-05230917
Arm 1
placeboOTHER

200 mg liquid sterile vial, administered at matching dose level 200 mg, 400 mg or 600 mg intravenously, one-hour infusion on Day 1, Week 2, 4, 8, and 12

Arm 4

Eligibility Criteria

Age18 Years - 65 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Male or Female, Age \>=18 and \<=65 years
  • Active ulcerative colitis (UC) beyond the rectum based upon Mayo Score
  • women of childbearing potential with highly effective method of contraception

You may not qualify if:

  • Indeterminate disease status, Crohn's disease, ischemic colitis, positive HIV, positive or history of tuberculosis infection, active enteric infections, transplant organ recipient, concomitant steroids, immunosuppressives or anti-TNFs.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (76)

The Kirkland Clinic

Birmingham, Alabama, 35233, United States

Location

UAB Hospital

Birmingham, Alabama, 35233, United States

Location

UAB Hospital Department of Pharmacy

Birmingham, Alabama, 35249, United States

Location

Administrative Offices

Birmingham, Alabama, 35294, United States

Location

UAB ACIP

Birmingham, Alabama, 35294, United States

Location

Arizona Surgical Center

Phoenix, Arizona, 85006, United States

Location

Dedicated Phase I, Inc.

Phoenix, Arizona, 85013, United States

Location

AGMG Endoscopy Center

Anaheim, California, 92801, United States

Location

Anaheim Clinical Trials, LLC

Anaheim, California, 92801, United States

Location

West Coast Radiology Center

Santa Ana, California, 92705, United States

Location

Endoscopy Center of Connecticut, LLC

Hamden, Connecticut, 06518, United States

Location

Gastroenterology Center of Connecticut, PC

Hamden, Connecticut, 06518, United States

Location

Medical Research Center of Connecticut, LLC

Hamden, Connecticut, 06518, United States

Location

International Clinical Research - US, LLC

Sanford, Florida, 32771, United States

Location

Gastrointestinal Specialists of Georgia, PC

Marietta, Georgia, 30060, United States

Location

GI Diagnostics

Marietta, Georgia, 30067, United States

Location

Gastrointestinal Associates, PA

Jackson, Mississippi, 39202, United States

Location

Gastrointestional Associates, PA

Jackson, Mississippi, 39202, United States

Location

St. Dominic Hospital

Jackson, Mississippi, 39216, United States

Location

Digestive Health Specialists, PA

Tupelo, Mississippi, 38801, United States

Location

North Mississippi Medical Center

Tupelo, Mississippi, 38801, United States

Location

Premier Medical Group of the Hudson Valley

Poughkeepsie, New York, 12601, United States

Location

Piedmont Gastroenterology Specialists

Winston-Salem, North Carolina, 27103, United States

Location

PMG Research of Winston-Salem

Winston-Salem, North Carolina, 27103, United States

Location

University Hospitals Case Medical Center - Division of Gastroenterology and Liver Disease

Cleveland, Ohio, 44106, United States

Location

Wheeler and Stuckey, Inc.

Oklahoma City, Oklahoma, 73103, United States

Location

Oklahoma Foundation for Digestive Research

Oklahoma City, Oklahoma, 73104, United States

Location

OU Physicians Building

Oklahoma City, Oklahoma, 73104, United States

Location

Memphis Gastroenterology Group, PC

Germantown, Tennessee, 38138, United States

Location

The West Clinic

Memphis, Tennessee, 38120, United States

Location

Centennial Medical Center Physicians Park

Nashville, Tennessee, 37203, United States

Location

Centennial Medical Center Tower Medical Imaging

Nashville, Tennessee, 37203, United States

Location

Columbia Medical Group - The First Clinic Inc.

Nashville, Tennessee, 37203, United States

Location

Radiology Alliance

Nashville, Tennessee, 37203, United States

Location

Professional Quality Research, Inc.

Austin, Texas, 78705, United States

Location

Austin Endoscopy Center

Austin, Texas, 78757, United States

Location

Austin Gastroenterology, PA

Austin, Texas, 78757, United States

Location

Texas Center for Drug Development, Inc.

Houston, Texas, 77081, United States

Location

Austin Gastroenterology, PA

Round Rocks, Texas, 78681, United States

Location

Cardiology Clinic of San Antonio

San Antonio, Texas, 78229, United States

Location

Gastroenterology Research of San Antonio

San Antonio, Texas, 78229, United States

Location

San Antonio Endoscopy Center

San Antonio, Texas, 78229, United States

Location

CNS Pharmacy

Murray, Utah, 84123, United States

Location

RGL Medical Services

Salt Lake City, Utah, 84084, United States

Location

Alpine Medical Group

Salt Lake City, Utah, 84102, United States

Location

Wasatch Clinical Research

Salt Lake City, Utah, 84107, United States

Location

Wasatch Endoscopy Center

Salt Lake City, Utah, 84124, United States

Location

University of Utah Hospital

Salt Lake City, Utah, 84132, United States

Location

Krankenhaus der Elisabethinen Linz GmbH

Linz, 4020, Austria

Location

Landesklinikum St. Poelten

Sankt Pölten, 3100, Austria

Location

AKH Wien Universitaetsklinik fuer Innere Medizin III

Vienna, 1090, Austria

Location

MBAL Ruse / MHAT Ruse, Terapevtichno, gastroenterologichno i hematologichno otdelenie

Rousse, 7002, Bulgaria

Location

MBAL Voennomeditsinska Akademia / MMA HAT, Klinika po gastroenterologia i hepatologia

Sofia, 1606, Bulgaria

Location

DKTs Sveta Anna, Gastroenterologichen cabinet

Sofia, 1750, Bulgaria

Location

Heritage Medical Research Clinic - University of Calgary

Calgary, Alberta, T2N 4Z6, Canada

Location

Vancouver Coastal Health - Vancouver General Hospital

Vancouver, British Columbia, V5Z 1M9, Canada

Location

Vancouver General Hospital - The Gordon and Leslie Diamond Centre

Vancouver, British Columbia, V5Z 1M9, Canada

Location

The Religious Hospitallers of St. Joseph of the Hotel Dieu of Kingston

Kingston, Ontario, K7L 5G2, Canada

Location

Sunnybrook Health Sciences Centre

Toronto, Ontario, M4N 3M5, Canada

Location

CHU Hopital Nord

Amiens, 80054, France

Location

Hopital Beaujon

Clichy, 92110, France

Location

CHU Hotel-Dieu

Nantes, 44093, France

Location

Charite - Campus Berlin Mitte

Berlin, 10117, Germany

Location

Universitaetsklinikum Heidelberg

Heidelberg, 69120, Germany

Location

Universitaetsklinikum Schleswig-Holstein, Campus Kiel

Kiel, 24105, Germany

Location

Gastroenterologische Gemeinschaftspraxis Minden

Minden, 32423, Germany

Location

Szent Janos Korhaz es Eszak-budai Egyesitett Korhazak/I. Belgyogyaszati-Gasztroenterologiai Osztaly

Budapest, 1125, Hungary

Location

Pannonia Maganorvosi Centrum Kft.

Budapest, 1136, Hungary

Location

Clinfan Kft.

Szekszárd, 7100, Hungary

Location

VU Medisch Centrum

Amsterdam, 1081 HV, Netherlands

Location

Academic Medical Center - University of Amsterdam, Dept. of Gastroenterology

Amsterdam, 1105 AZ, Netherlands

Location

Academisch Ziekenhuis Maastricht

Maastricht, 6229 HX, Netherlands

Location

Centralny Szpital Kliniczny MSWiA, Klinika Chorob Wewnetrznych i Gastroenterologii

Warsaw, 02-507, Poland

Location

Sectia Clinica Medicina Interna II

Bucharest, 010816, Romania

Location

Hospital Clinic I Provincial de Barcelona

Barcelona, Barcelona, 08036, Spain

Location

Hospital General Universitario Gregorio Marañon

Madrid, Madrid, 28007, Spain

Location

Related Publications (1)

  • Reinisch W, Panes J, Khurana S, Toth G, Hua F, Comer GM, Hinz M, Page K, O'Toole M, Moorehead TM, Zhu H, Sun Y, Cataldi F. Anrukinzumab, an anti-interleukin 13 monoclonal antibody, in active UC: efficacy and safety from a phase IIa randomised multicentre study. Gut. 2015 Jun;64(6):894-900. doi: 10.1136/gutjnl-2014-308337. Epub 2015 Jan 7.

Related Links

MeSH Terms

Conditions

Colitis, Ulcerative

Interventions

anrukinzumab

Condition Hierarchy (Ancestors)

ColitisGastroenteritisGastrointestinal DiseasesDigestive System DiseasesInflammatory Bowel DiseasesColonic DiseasesIntestinal Diseases

Results Point of Contact

Title
Pfizer ClinicalTrials.gov Call Center
Organization
Pfizer, Inc.

Study Officials

  • Pfizer CT.gov Call Center

    Pfizer

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
TRIPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

January 25, 2011

First Posted

January 26, 2011

Study Start

March 1, 2011

Primary Completion

April 1, 2013

Study Completion

April 1, 2013

Last Updated

November 18, 2014

Results First Posted

November 18, 2014

Record last verified: 2014-11

Locations